Trial Outcomes & Findings for Treatment of POEMS Syndrome With Daratumumab (NCT NCT04396496)

NCT ID: NCT04396496

Last Updated: 2023-11-13

Results Overview

There is a one-point improvement in ECOG performance score; and/or ≥ 50% reduction in ONLS score at Day 360.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

2 participants

Primary outcome timeframe

360 days

Results posted on

2023-11-13

Participant Flow

Participant milestones

Participant milestones
Measure
Daratumumab Injection
Up to 12 four-week cycles of Daratumumab (DARA), in combination with the immunomodulatory drug (IMiD) lenalidomide. DARA is injected. Dosage calculated by weight.On Cycles 1 and 2, DARA is given on Days 1, 8,15 and 22. On Cycles 3-6,DARA is given on Days 1 and 15. On Cycles 7-12, DARA is given on Day 1. Lenalidomide is taken by mouth. 15 mg on Days 1-21 of each cycle. Daratumumab Injection: DARA is a human monoclonal antibody that specifically recognizes the CD38 molecule that is expressed at a high level in a variety of hematological malignancies, including myeloma cells. DARA injection will be given with oral lenalidomide for up to 12 four week cycles.
Overall Study
STARTED
2
Overall Study
COMPLETED
2
Overall Study
NOT COMPLETED
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Treatment of POEMS Syndrome With Daratumumab

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Daratumumab Injection
n=2 Participants
Up to 12 four-week cycles of Daratumumab (DARA), in combination with the immunomodulatory drug (IMiD) lenalidomide. DARA is injected. Dosage calculated by weight.On Cycles 1 and 2, DARA is given on Days 1, 8,15 and 22. On Cycles 3-6,DARA is given on Days 1 and 15. On Cycles 7-12, DARA is given on Day 1. Lenalidomide is taken by mouth. 15 mg on Days 1-21 of each cycle. Daratumumab Injection: DARA is a human monoclonal antibody that specifically recognizes the CD38 molecule that is expressed at a high level in a variety of hematological malignancies, including myeloma cells. DARA injection will be given with oral lenalidomide for up to 12 four week cycles.
Age, Categorical
<=18 years
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
2 Participants
n=5 Participants
Age, Categorical
>=65 years
0 Participants
n=5 Participants
Sex: Female, Male
Female
1 Participants
n=5 Participants
Sex: Female, Male
Male
1 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
0 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=5 Participants
Race (NIH/OMB)
White
1 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
1 Participants
n=5 Participants
Region of Enrollment
United States
2 participants
n=5 Participants

PRIMARY outcome

Timeframe: 360 days

There is a one-point improvement in ECOG performance score; and/or ≥ 50% reduction in ONLS score at Day 360.

Outcome measures

Outcome measures
Measure
Daratumumab Injection
n=2 Participants
Up to 12 four-week cycles of Daratumumab (DARA), in combination with the immunomodulatory drug (IMiD) lenalidomide. DARA is injected. Dosage calculated by weight.On Cycles 1 and 2, DARA is given on Days 1, 8,15 and 22. On Cycles 3-6,DARA is given on Days 1 and 15. On Cycles 7-12, DARA is given on Day 1. Lenalidomide is taken by mouth. 15 mg on Days 1-21 of each cycle. Daratumumab Injection: DARA is a human monoclonal antibody that specifically recognizes the CD38 molecule that is expressed at a high level in a variety of hematological malignancies, including myeloma cells. DARA injection will be given with oral lenalidomide for up to 12 four week cycles.
Treatment Success
0 Participants

Adverse Events

Daratumumab Injection

Serious events: 1 serious events
Other events: 2 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Daratumumab Injection
n=2 participants at risk
Up to 12 four-week cycles of Daratumumab (DARA), in combination with the immunomodulatory drug (IMiD) lenalidomide. DARA is injected. Dosage calculated by weight.On Cycles 1 and 2, DARA is given on Days 1, 8,15 and 22. On Cycles 3-6,DARA is given on Days 1 and 15. On Cycles 7-12, DARA is given on Day 1. Lenalidomide is taken by mouth. 15 mg on Days 1-21 of each cycle. Daratumumab Injection: DARA is a human monoclonal antibody that specifically recognizes the CD38 molecule that is expressed at a high level in a variety of hematological malignancies, including myeloma cells. DARA injection will be given with oral lenalidomide for up to 12 four week cycles.
Respiratory, thoracic and mediastinal disorders
Allergic rhinitis
50.0%
1/2 • Number of events 1 • 3 years
General disorders
Chills
50.0%
1/2 • Number of events 1 • 3 years
Vascular disorders
Thromboembolic event
50.0%
1/2 • Number of events 1 • 3 years

Other adverse events

Other adverse events
Measure
Daratumumab Injection
n=2 participants at risk
Up to 12 four-week cycles of Daratumumab (DARA), in combination with the immunomodulatory drug (IMiD) lenalidomide. DARA is injected. Dosage calculated by weight.On Cycles 1 and 2, DARA is given on Days 1, 8,15 and 22. On Cycles 3-6,DARA is given on Days 1 and 15. On Cycles 7-12, DARA is given on Day 1. Lenalidomide is taken by mouth. 15 mg on Days 1-21 of each cycle. Daratumumab Injection: DARA is a human monoclonal antibody that specifically recognizes the CD38 molecule that is expressed at a high level in a variety of hematological malignancies, including myeloma cells. DARA injection will be given with oral lenalidomide for up to 12 four week cycles.
Gastrointestinal disorders
Vomiting
50.0%
1/2 • Number of events 1 • 3 years
Gastrointestinal disorders
Constipation
100.0%
2/2 • Number of events 2 • 3 years
General disorders
Fever
100.0%
2/2 • Number of events 2 • 3 years
General disorders
Fatigue
50.0%
1/2 • Number of events 1 • 3 years
Injury, poisoning and procedural complications
Infusion related reaction
100.0%
2/2 • Number of events 2 • 3 years
Investigations
Neutrophil count decreased
50.0%
1/2 • Number of events 1 • 3 years
Investigations
White blood cell decreased
50.0%
1/2 • Number of events 1 • 3 years
Nervous system disorders
Headache
50.0%
1/2 • Number of events 1 • 3 years
Respiratory, thoracic and mediastinal disorders
Laryngospasm
50.0%
1/2 • Number of events 1 • 3 years
Respiratory, thoracic and mediastinal disorders
Rhinorrhea
50.0%
1/2 • Number of events 1 • 3 years
Respiratory, thoracic and mediastinal disorders
Allergic rhinitis
50.0%
1/2 • Number of events 1 • 3 years
Respiratory, thoracic and mediastinal disorders
Cough
100.0%
2/2 • Number of events 2 • 3 years
Respiratory, thoracic and mediastinal disorders
Dyspnea
50.0%
1/2 • Number of events 2 • 3 years
Respiratory, thoracic and mediastinal disorders
Nasal congestion
50.0%
1/2 • Number of events 1 • 3 years
Skin and subcutaneous tissue disorders
Rash maculo-papular
50.0%
1/2 • Number of events 2 • 3 years
Skin and subcutaneous tissue disorders
Skin and subcutaneous tissue disorders, Other, specify
50.0%
1/2 • Number of events 3 • 3 years
Vascular disorders
Flushing
50.0%
1/2 • Number of events 1 • 3 years
Vascular disorders
Thromboembolic event
50.0%
1/2 • Number of events 1 • 3 years

Additional Information

Beth Scanlan

University of Arkansas for Medical Sciences

Phone: 5016868274

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place