A Phase 2b/3a Study to Evaluate the Efficacy and Safety of JointStem in Patients Diagnosed as Knee Osteoarthritis

NCT ID: NCT04368806

Last Updated: 2025-07-24

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2/PHASE3

Total Enrollment

140 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-05-26

Study Completion Date

2026-12-31

Brief Summary

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This study is a double-blind, randomized, placebo controlled, multi-center, superiority study to evaluate the efficacy and safety of JointStem, autologous adipose tissue derived mesenchymal stem cells (AdMSC), in patients diagnosed as knee osteoarthritis. Following a 2-week screening period, approximately 140 subjects will be randomly assigned into one of the following two arms in a 1:1 ratio (1 JointStem : 1 Placebo). After each subject completes 48-Weeks visit (Visit 8) and the data management team confirms all individual data have no issue, the individual database will be locked and the blinding will be open for the statistical analysis.

Detailed Description

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Study Procedures:

* Visit 1 (Week -7) - Screening
* Visit 2 (Week -5) - Baseline and Randomization (Lipoaspiration)
* Visit 3 (Week 0) - Treatment (Intra-articular injection)
* Visit 4 (Week 4) - 4 weeks follow-up
* Visit 5 (Week 12) - 12 weeks follow-up
* Visit 6 (Week 24) - 24 weeks follow-up
* Visit 7 (Week 36) - 36 weeks follow-up
* Visit 8 (Week 48) - 48 weeks follow-up (End of Study)

Conditions

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Osteoarthritis, Knee

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors

Study Groups

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JointStem

Autologous Adipose tissue derived Mesenchymal Stem Cells(AdMSC)

Group Type EXPERIMENTAL

JointStem

Intervention Type DRUG

Autologous Adipose tissue derived Mesenchymal Stem Cells (AdMSC)

Placebo

Normal Saline with Autologous Serum

Group Type PLACEBO_COMPARATOR

Placebo Control

Intervention Type OTHER

Normal Saline with autologous Serum

Interventions

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JointStem

Autologous Adipose tissue derived Mesenchymal Stem Cells (AdMSC)

Intervention Type DRUG

Placebo Control

Normal Saline with autologous Serum

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

1. Male or female of any race, adult aged 18 years or older
2. Subject who had osteoarthritis of knee diagnosed (according to the clinical and American College of Rheumatology Criteria)
3. Subject who has ≥ 45 on WOMAC function score at Screening and Baseline
4. Subject who has knee pain ≥ 70 mm for the study knee out of 100 mm on VAS (Visual Analog Scale) at Screening and Baseline
5. Subject who has radiographic evidence of grade 3 osteoarthritis in the study knee based on the Kellgren and Lawrence radiographic criteria
6. Subject who has a varus angle of 5 degrees or less confirmed through radiography
7. Subjects whose knee pain persists for at least 12 weeks (about 3 months) prior to Screening and does not improve symptoms with non-operative treatment options
8. Subject who is willing to discontinue all pain medications for osteoarthritis except rescue medication (acetaminophen \< 3.25 g per day) at least 72 hours prior to Screening and throughout the duration of study
9. Subject who is willing and able to give written informed consent for participation in the study

Exclusion Criteria

1. Subject who has Body Mass Index (BMI) \> 35 kg/m2
2. Subject judged by the investigator to have a history of clinically significant disease(s) (i.e., uncontrolled comorbid disease, kidney diseases, liver diseases, endocrine diseases, etc., but not limited to these diseases) that may affect the patient's participation in the study.
3. Subject who has any of following clinically significant diseases:

* Autoimmune diseases
* Paget's disease, ochronosis, acromegaly, hemochromatosis, or Wilson's disease
* Genetic diseases (hyperkinesia, collagen gene abnormality, etc.)
* Inflammatory joint disorders (e.g., rheumatoid inflammation)
* Infectious joint disorders (e.g., septic arthritis)
* Other joint disorders (e.g., gout, recurrent pseudogout, articular fracture, primary osteochondrosis, villonodular synovitis)
4. Subject who has any history of cancer and/or currently receiving treatment for a current cancer diagnosis.
5. Subject who is positive in pathogenic test (HIV, viral hepatitis, or syphilis)
6. Subject who has heart diseases (myocardial infarction, coronary artery bypass graft surgery, arrhythmia, or other serious heart diseases) or has history of heart diseases within 6 months prior to Screening
7. Subject who has received any intra-articular therapy in any joint within 6 months prior to Screening, or surgery on the relevant knee including articular endoscopic procedures within 6 months prior to Screening
8. Subject who has history of prolotherapy, or platelet rich plasma injection within 6 months prior to Screening
9. Subject who has received long-acting hyaluronic acid injection (e.g., Synvisc-One®, etc.) within 6 months prior to Screening
10. Subject who has history of stem cell therapy
11. Subject who has significant lab abnormalities for the following parameters (If the value is within 10% of the listed laboratory exclusion criterion value and the value is considered not to be clinically significant by the investigator, the subject can be considered for enrollment):

* Serum ALT and AST \> 2 x upper limit of normal
* Serum creatinine out of normal range
* PT/INR out of normal range
* Hemoglobin \< 10 g/dL for female subject and hemoglobin \< 11 g/dL for male subject
* Platelets out of normal range
12. Subject for whom the investigator judges the lipoaspiration can cause any problem
13. Subject who has history of local anesthetic allergy
14. Subject who has taken anti-inflammatory drugs (prescription and non-prescription NSAIDs), symptomatic slow acting drugs (glucosamine, chondroitin sulfate, diacerhein etc.), or oral steroids (prednisone etc.) within 14 days prior to Screening (however, those who undergo a 14-day wash-out period can participate.)
15. Subject who is an active drug/alcohol abuser
16. Pregnant or breast-feeding women, or women or men who are not using appropriate method of contraception (appropriate method includes hormones, bilateral tubal ligation, and barrier method with spermicide, and intra-uterine device for women and vasectomy and barrier method with spermicide for men; subjects should agree to use appropriate method)
17. Subject who is enrolled in any other clinical trials within 3 months from screening
18. Subject who received the COVID-19 vaccines within 1 week from Visit 2 (Lipoaspiration, baseline)
19. Subject who the principal investigator considers inappropriate for the study due to any other reasons than those listed above
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Nature Cell Co. Ltd.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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TriWest Research Associates

El Cajon, California, United States

Site Status RECRUITING

BioSolutions Clinical Research Center

La Mesa, California, United States

Site Status RECRUITING

Neurovations Research

Napa, California, United States

Site Status RECRUITING

Newport Therapeutics

Newport Beach, California, United States

Site Status RECRUITING

Source Healthcare

Santa Monica, California, United States

Site Status RECRUITING

Keimyung University Dongsan Hospital

Daegu, Korea, South Korea

Site Status RECRUITING

Kyung Hee University Medical Center

Seoul, Korea, South Korea

Site Status RECRUITING

Kyung Hee University Hospital At Gangdong

Seoul, Korea, South Korea

Site Status RECRUITING

Smg-Snu Boramae Medical Center

Seoul, Korea, South Korea

Site Status RECRUITING

Countries

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United States South Korea

Central Contacts

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Hugh Lee

Role: CONTACT

301-540-2600

Christine Lee

Role: CONTACT

301-540-2600

Facility Contacts

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Arthur R. Mabaquiao, M.D.

Role: primary

619-334-4735

David C. Ruiz, Phlebotomist

Role: backup

619-334-4735

Peter B. Hanson, M.D.

Role: primary

619-637-0770

Tamara Packard, L.V.N.

Role: backup

619-637-0770

Eric Grigsby, M.D.

Role: primary

707-252-9666

Louiza Khedim

Role: backup

707-252-9606

Richard Paicius, M.D.

Role: primary

949-644-5800

Zeyn White

Role: backup

949-644-5800

Timothy T. Davis, M.D.

Role: primary

310-574-2777

Afrida Sara, B.S.

Role: backup

310-574-2777

Ki-Cheor Bae, M.D.

Role: primary

82-53-250-7729

Yu-gyeong Ahn

Role: backup

+82-53-258-6654

Sang-Jun Song, M.D., PhD

Role: primary

+82-2-958-9489

Chae-hong Lee

Role: backup

KANG-IL Kim, M.D., PhD

Role: primary

+82-2-440-6151

Hyun-Mi Cho

Role: backup

Moon-Jong Chang, M.D., PhD

Role: primary

+82-2-870-2317

Hyewon Kim

Role: backup

+82+2870+3931

Other Identifiers

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JS-OAP3-US01

Identifier Type: -

Identifier Source: org_study_id

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