Trial Outcomes & Findings for Large-scale Brain Organization During Cognitive Control in ADHD (NCT NCT04349917)

NCT ID: NCT04349917

Last Updated: 2021-01-12

Results Overview

Assessment of network topology during a resting state using functional connectivity estimates. Modularity will be determined by applying graph theoretical methods to functional connectivity estimates acquired during functional magnetic resonance imaging (fMRI) scans. Modularity is measured on a -1 to 1 scale, with higher scores indicating stronger community structure, or a stronger tendency of clusters of brain regions to separate into distinct, highly interconnected networks with sparse connections across networks. The optimal modularity value depends on the context. For example, during complex tasks lower modularity is better, while during basic, automatic tasks higher modularity is better.

Recruitment status

COMPLETED

Study phase

PHASE4

Target enrollment

37 participants

Primary outcome timeframe

1 to 3 hours after administration of intervention

Results posted on

2021-01-12

Participant Flow

Participants were recruited between December 2016 and March 2020.

A total of 47 participants were screened during a behavioral visit. Of those not randomized, 8 did not meet inclusion criteria and 2 withdrew from study.

Participant milestones

Participant milestones
Measure
Methylphenidate, Then Placebo
Participants received a single, low dose of methylphenidate (0.3 mg/kg) before the first MRI scan. Approximately one week later, participants received a matching placebo pill before the second MRI scan.
Placebo, Then Methylphenidate
Participants received a matching placebo pill before the first MRI scan. Approximately one week later, participants received a single, low dose of methylphenidate (0.3 mg/kg) before the second MRI scan.
First Intervention (2-4 Hours)
STARTED
19
18
First Intervention (2-4 Hours)
Received Intervention
19
17
First Intervention (2-4 Hours)
COMPLETED
19
16
First Intervention (2-4 Hours)
NOT COMPLETED
0
2
Washout Period (4-20 Days)
STARTED
19
16
Washout Period (4-20 Days)
COMPLETED
19
16
Washout Period (4-20 Days)
NOT COMPLETED
0
0
Second Intervention (2-4 Hours)
STARTED
19
16
Second Intervention (2-4 Hours)
Received Intervention
19
16
Second Intervention (2-4 Hours)
COMPLETED
19
16
Second Intervention (2-4 Hours)
NOT COMPLETED
0
0

Reasons for withdrawal

Reasons for withdrawal
Measure
Methylphenidate, Then Placebo
Participants received a single, low dose of methylphenidate (0.3 mg/kg) before the first MRI scan. Approximately one week later, participants received a matching placebo pill before the second MRI scan.
Placebo, Then Methylphenidate
Participants received a matching placebo pill before the first MRI scan. Approximately one week later, participants received a single, low dose of methylphenidate (0.3 mg/kg) before the second MRI scan.
First Intervention (2-4 Hours)
Withdrawal by Subject
0
1
First Intervention (2-4 Hours)
Unable to Swallow Pill
0
1

Baseline Characteristics

Large-scale Brain Organization During Cognitive Control in ADHD

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Methylphenidate, Then Placebo
n=19 Participants
Participants received a single, low dose of methylphenidate (0.3 mg/kg) before the first MRI scan. Approximately one week later, participants received a matching placebo pill before the second MRI scan.
Placebo, Then Methylphenidate
n=18 Participants
Participants received a matching placebo pill before the first MRI scan. Approximately one week later, participants received a single, low dose of methylphenidate (0.3 mg/kg) before the second MRI scan.
Total
n=37 Participants
Total of all reporting groups
Age, Continuous
9.71 years
STANDARD_DEVIATION 0.92 • n=5 Participants
9.75 years
STANDARD_DEVIATION 1.41 • n=7 Participants
9.73 years
STANDARD_DEVIATION 1.17 • n=5 Participants
Sex: Female, Male
Female
9 Participants
n=5 Participants
9 Participants
n=7 Participants
18 Participants
n=5 Participants
Sex: Female, Male
Male
10 Participants
n=5 Participants
9 Participants
n=7 Participants
19 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
2 Participants
n=5 Participants
1 Participants
n=7 Participants
3 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
17 Participants
n=5 Participants
16 Participants
n=7 Participants
33 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
1 Participants
n=7 Participants
1 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
1 Participants
n=5 Participants
1 Participants
n=7 Participants
2 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
1 Participants
n=5 Participants
0 Participants
n=7 Participants
1 Participants
n=5 Participants
Race (NIH/OMB)
White
17 Participants
n=5 Participants
14 Participants
n=7 Participants
31 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
3 Participants
n=7 Participants
3 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Region of Enrollment
United States
19 Participants
n=5 Participants
18 Participants
n=7 Participants
37 Participants
n=5 Participants

PRIMARY outcome

Timeframe: 1 to 3 hours after administration of intervention

Population: Participants excluded due to excessive head motion (mean framewise displacement (FD) \> 0.5mm or fewer than 150 timepoints remaining after scrubbing all timepoints with FD \> 0.2mm), incomplete brain coverage, or poor-quality fMRI data. Participants must have good data from both methylphenidate and placebo scan days to be included in this analysis.

Assessment of network topology during a resting state using functional connectivity estimates. Modularity will be determined by applying graph theoretical methods to functional connectivity estimates acquired during functional magnetic resonance imaging (fMRI) scans. Modularity is measured on a -1 to 1 scale, with higher scores indicating stronger community structure, or a stronger tendency of clusters of brain regions to separate into distinct, highly interconnected networks with sparse connections across networks. The optimal modularity value depends on the context. For example, during complex tasks lower modularity is better, while during basic, automatic tasks higher modularity is better.

Outcome measures

Outcome measures
Measure
Methylphenidate
n=22 Participants
Participants received a single, low dose of methylphenidate (0.3 mg/kg) before MRI scan
Placebo
n=22 Participants
Participants received a matching placebo pill before MRI scan.
Resting State Brain Network Organization
0.223 units on a scale
Standard Deviation 0.026
0.228 units on a scale
Standard Deviation 0.034

PRIMARY outcome

Timeframe: 1 to 3 hours after administration of intervention

Population: Participants excluded due to excessive head motion (mean framewise displacement \[FD\] \> 0.5mm or fewer than 150 timepoints remaining after scrubbing all timepoints with FD \> 0.2mm), incomplete brain coverage, or poor-quality fMRI data. Participants must have good data from both methylphenidate and placebo scan days to be included in this analysis.

Assessment of network topology during the Go/No-go (GNG) regular and GNG reward tasks. Subjects see a series of sports balls and are told to respond to most balls (go trials), but not to some specific balls (no-go trials). GNG tasks are identical, except in the rewarded task, correct fast go responses and correct withholding on no-go trials are rewarded with 1 cent and 5 cents respectively. Graph theoretical methods are applied to functional connectivity estimates from fMRI scans to determine modularity during each task. Modularity (-1 to 1 scale) measures the degree to which the whole-brain system separates into distinct communities, such that greater modularity reflects stronger community structure, or stronger tendency of brain regions to separate into distinct, highly interconnected networks with few connections across networks. Optimal modularity value depends on context. During complex tasks lower modularity is better, while higher modularity is better for basic tasks.

Outcome measures

Outcome measures
Measure
Methylphenidate
n=23 Participants
Participants received a single, low dose of methylphenidate (0.3 mg/kg) before MRI scan
Placebo
n=23 Participants
Participants received a matching placebo pill before MRI scan.
Task-Based Brain Network Organization
GNG regular
0.213 units on a scale
Standard Deviation 0.041
0.218 units on a scale
Standard Deviation 0.040
Task-Based Brain Network Organization
GNG reward
0.235 units on a scale
Standard Deviation 0.051
0.213 units on a scale
Standard Deviation 0.055

PRIMARY outcome

Timeframe: 1 to 3 hours after administration of intervention

Population: Participants excluded due to excessive head motion (mean framewise displacement \[FD\] \> 0.5mm or fewer than 150 timepoints remaining after scrubbing all timepoints with FD \> 0.2mm), incomplete brain coverage, or poor-quality fMRI data. Participants must have good data from both scan days and all tasks being compared to be included in this analysis.

Assessment of reconfiguration of network topology between the GNG regular task and the resting state and GNG reward task and resting state. In the GNG tasks, subjects see a series of sports balls and are told to respond to most of the balls (go trials), but not to some specific balls (no-go trials). GNG tasks are identical, except in the rewarded task, correct fast go responses and correct withholding on no-go trials are rewarded with 1 cent and 5 cents respectively. Normalized mutual information will be determined by applying the same graph theoretical methods to functional connectivity estimates acquired during fMRI scans for each rest-task pair. Normalized mutual information is measured on a 0 to 1 scale, with higher scores indicating more similarity in network structure across task and rest conditions.

Outcome measures

Outcome measures
Measure
Methylphenidate
n=22 Participants
Participants received a single, low dose of methylphenidate (0.3 mg/kg) before MRI scan
Placebo
n=22 Participants
Participants received a matching placebo pill before MRI scan.
Rest-Task Reconfiguration
GNG regular
0.104 units on a scale
Standard Deviation 0.055
0.119 units on a scale
Standard Deviation 0.058
Rest-Task Reconfiguration
GNG reward
0.122 units on a scale
Standard Deviation 0.074
0.150 units on a scale
Standard Deviation 0.074

PRIMARY outcome

Timeframe: 1 to 3 hours after administration of intervention

Population: Participants excluded due to excessive head motion (mean framewise displacement \[FD\] \> 0.5 mm or fewer than 150 timepoints remaining after scrubbing all timepoints with FD \> 0.2 mm), incomplete brain coverage, or poor-quality fMRI data. Participants excluded if incomplete behavioral GNG data. Must have good data from both scan days to be included.

Assessment of how changes in brain network topology relate to improvements in behavioral performance on the GNG regular and reward tasks, in which subjects respond to go stimuli and withhold responses to no-go stimuli. GNG tasks are identical, except subjects are rewarded for good performance on the reward task. Brain measures include change in modularity during rest, GNG regular, and GNG reward (Outcome Measures 1, 2); behavioral measures include change in commission rate, omission rate, and coefficient of variation of response time during GNG tasks (Outcome Measures 5-7). Pearson correlations are used to relate change in brain measures with change in behavioral measures from the placebo to the methylphenidate scans. Positive correlations indicate that subjects with greater change in the brain measure had greater change in the behavioral measure. Negative correlations indicate that subjects with less change in the brain measure had greater change in the behavioral measure.

Outcome measures

Outcome measures
Measure
Methylphenidate
n=18 Participants
Participants received a single, low dose of methylphenidate (0.3 mg/kg) before MRI scan
Placebo
Participants received a matching placebo pill before MRI scan.
Drug-induced Normalization
Delta rest mod vs delta GNG reg commission rate
-0.361 correlation coefficient
Interval -0.693 to 0.097
Drug-induced Normalization
Delta rest mod vs delta GNG reg omission rate
0.508 correlation coefficient
Interval 0.084 to 0.776
Drug-induced Normalization
Delta rest mod vs delta GNG reg RT variability
0.287 correlation coefficient
Interval -0.178 to 0.647
Drug-induced Normalization
Delta rest mod vs delta GNG rew commission rate
0.162 correlation coefficient
Interval -0.303 to 0.564
Drug-induced Normalization
Delta rest mod vs delta GNG rew omission rate
-0.224 correlation coefficient
Interval -0.606 to 0.243
Drug-induced Normalization
Delta rest mod vs delta GNG rew RT variability
0.003 correlation coefficient
Interval -0.44 to 0.445
Drug-induced Normalization
Delta GNG reg mod vs delta GNG reg commission rate
-0.033 correlation coefficient
Interval -0.468 to 0.416
Drug-induced Normalization
Delta GNG reg mod vs delta GNG reg omission rate
-0.170 correlation coefficient
Interval -0.57 to 0.271
Drug-induced Normalization
Delta GNG reg mod vs delta GNG reg RT variability
-0.195 correlation coefficient
Interval -0.587 to 0.271
Drug-induced Normalization
Delta GNG rew mod vs delta GNG rew commission rate
0.220 correlation coefficient
Interval -0.246 to 0.604
Drug-induced Normalization
Delta GNG rew mod vs delta GNG rew omission rate
-0.276 correlation coefficient
Interval -0.64 to 0.189
Drug-induced Normalization
Delta GNG rew mod vs delta GNG rew RT variability
-0.027 correlation coefficient
Interval -0.464 to 0.42

SECONDARY outcome

Timeframe: 1 to 3 hours after administration of intervention

Population: Participants must have good data from both methylphenidate and placebo scan days to be included in this analysis. Participants included if they completed at least one task.

Evaluation of commission errors assessed during the GNG regular and GNG reward tasks. In the GNG tasks, subjects see a series of sports balls and are told to respond to most of the balls (go trials), but not to some specific balls (no-go trials). GNG tasks are identical, except in the rewarded task, correct fast go responses and correct withholding on no-go trials are rewarded with 1 cent and 5 cents respectively. In both tasks, commission errors occur on trials on which participants respond to a stimulus ("go" response) when they are supposed to withhold a response ("no-go" trial). Commission errors are scored from 0 (no commission errors) to 1 (100% commission errors), with lower values indicating better performance.

Outcome measures

Outcome measures
Measure
Methylphenidate
n=33 Participants
Participants received a single, low dose of methylphenidate (0.3 mg/kg) before MRI scan
Placebo
n=33 Participants
Participants received a matching placebo pill before MRI scan.
Go/No-go (GNG) Commission Rate
GNG regular
0.396 units on a scale
Standard Deviation 0.213
0.403 units on a scale
Standard Deviation 0.206
Go/No-go (GNG) Commission Rate
GNG reward
0.292 units on a scale
Standard Deviation 0.176
0.348 units on a scale
Standard Deviation 0.181

SECONDARY outcome

Timeframe: 1 to 3 hours after administration of intervention

Population: Participants must have good data from both methylphenidate and placebo scan days to be included in this analysis. Participants included if they completed at least one task.

Evaluation of omission errors assessed during the GNG regular and GNG reward tasks. In the GNG tasks, subjects see a series of sports balls and are told to respond to most of the balls (go trials), but not to some specific balls (no-go trials). GNG tasks are identical, except in the rewarded task, correct fast go responses and correct withholding on no-go trials are rewarded with 1 cent and 5 cents respectively. In both tasks, omission errors occur on trials on which participants do not respond to a "go" stimulus to which they are supposed to respond. Omission errors are scored from 0 (no omission errors) to 1 (100% omission errors), with lower values indicating better performance.

Outcome measures

Outcome measures
Measure
Methylphenidate
n=33 Participants
Participants received a single, low dose of methylphenidate (0.3 mg/kg) before MRI scan
Placebo
n=33 Participants
Participants received a matching placebo pill before MRI scan.
Go/No-go (GNG) Omission Rate
GNG regular
0.071 units on a scale
Standard Deviation 0.116
0.104 units on a scale
Standard Deviation 0.119
Go/No-go (GNG) Omission Rate
GNG reward
0.040 units on a scale
Standard Deviation 0.055
0.101 units on a scale
Standard Deviation 0.111

SECONDARY outcome

Timeframe: 1 to 3 hours after administration of intervention

Population: Participants must have good data from both methylphenidate and placebo scan days to be included in this analysis. Participants included if they completed at least one task.

Evaluation of response time variability assessed during the GNG regular and GNG reward tasks. In the GNG tasks, subjects see a series of sports balls and are told to respond to most of the balls (go trials), but not to some specific balls (no-go trials). GNG tasks are identical, except in the rewarded task, correct fast go responses and correct withholding on no-go trials are rewarded with 1 cent and 5 cents respectively. Coefficient of variation (standard deviation / mean) will be calculated for response time in GNG regular and GNG reward tasks separately to account for group differences in mean response time.

Outcome measures

Outcome measures
Measure
Methylphenidate
n=33 Participants
Participants received a single, low dose of methylphenidate (0.3 mg/kg) before MRI scan
Placebo
n=33 Participants
Participants received a matching placebo pill before MRI scan.
Go/No-go (GNG) Response Time Variability
GNG regular
0.298 coefficient of variation
Standard Deviation 0.104
0.344 coefficient of variation
Standard Deviation 0.155
Go/No-go (GNG) Response Time Variability
GNG reward
0.253 coefficient of variation
Standard Deviation 0.071
0.342 coefficient of variation
Standard Deviation 0.146

Adverse Events

Methylphenidate

Serious events: 0 serious events
Other events: 11 other events
Deaths: 0 deaths

Placebo

Serious events: 0 serious events
Other events: 9 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Methylphenidate
n=35 participants at risk
Participants received a single, low dose of methylphenidate (0.3 mg/kg) before MRI scan
Placebo
n=36 participants at risk
Participants received a matching placebo pill before MRI scan.
Cardiac disorders
Heart Racing
0.00%
0/35 • From the First Intervention through 24-48 hours following the Second Intervention, an overall total of between 5-22 days depending on the length of the Washout Period (Washout Period range: 4-20 days).
Safety Population includes all participants who received at least one dose of intervention
2.8%
1/36 • From the First Intervention through 24-48 hours following the Second Intervention, an overall total of between 5-22 days depending on the length of the Washout Period (Washout Period range: 4-20 days).
Safety Population includes all participants who received at least one dose of intervention
Gastrointestinal disorders
Nausea
2.9%
1/35 • From the First Intervention through 24-48 hours following the Second Intervention, an overall total of between 5-22 days depending on the length of the Washout Period (Washout Period range: 4-20 days).
Safety Population includes all participants who received at least one dose of intervention
2.8%
1/36 • From the First Intervention through 24-48 hours following the Second Intervention, an overall total of between 5-22 days depending on the length of the Washout Period (Washout Period range: 4-20 days).
Safety Population includes all participants who received at least one dose of intervention
Gastrointestinal disorders
Stomachache
0.00%
0/35 • From the First Intervention through 24-48 hours following the Second Intervention, an overall total of between 5-22 days depending on the length of the Washout Period (Washout Period range: 4-20 days).
Safety Population includes all participants who received at least one dose of intervention
2.8%
1/36 • From the First Intervention through 24-48 hours following the Second Intervention, an overall total of between 5-22 days depending on the length of the Washout Period (Washout Period range: 4-20 days).
Safety Population includes all participants who received at least one dose of intervention
General disorders
Fatigue
20.0%
7/35 • From the First Intervention through 24-48 hours following the Second Intervention, an overall total of between 5-22 days depending on the length of the Washout Period (Washout Period range: 4-20 days).
Safety Population includes all participants who received at least one dose of intervention
11.1%
4/36 • From the First Intervention through 24-48 hours following the Second Intervention, an overall total of between 5-22 days depending on the length of the Washout Period (Washout Period range: 4-20 days).
Safety Population includes all participants who received at least one dose of intervention
General disorders
Increased Energy
0.00%
0/35 • From the First Intervention through 24-48 hours following the Second Intervention, an overall total of between 5-22 days depending on the length of the Washout Period (Washout Period range: 4-20 days).
Safety Population includes all participants who received at least one dose of intervention
2.8%
1/36 • From the First Intervention through 24-48 hours following the Second Intervention, an overall total of between 5-22 days depending on the length of the Washout Period (Washout Period range: 4-20 days).
Safety Population includes all participants who received at least one dose of intervention
Metabolism and nutrition disorders
Change in Appetite
2.9%
1/35 • From the First Intervention through 24-48 hours following the Second Intervention, an overall total of between 5-22 days depending on the length of the Washout Period (Washout Period range: 4-20 days).
Safety Population includes all participants who received at least one dose of intervention
2.8%
1/36 • From the First Intervention through 24-48 hours following the Second Intervention, an overall total of between 5-22 days depending on the length of the Washout Period (Washout Period range: 4-20 days).
Safety Population includes all participants who received at least one dose of intervention
Nervous system disorders
Dizziness
2.9%
1/35 • From the First Intervention through 24-48 hours following the Second Intervention, an overall total of between 5-22 days depending on the length of the Washout Period (Washout Period range: 4-20 days).
Safety Population includes all participants who received at least one dose of intervention
0.00%
0/36 • From the First Intervention through 24-48 hours following the Second Intervention, an overall total of between 5-22 days depending on the length of the Washout Period (Washout Period range: 4-20 days).
Safety Population includes all participants who received at least one dose of intervention
Nervous system disorders
Headache
8.6%
3/35 • From the First Intervention through 24-48 hours following the Second Intervention, an overall total of between 5-22 days depending on the length of the Washout Period (Washout Period range: 4-20 days).
Safety Population includes all participants who received at least one dose of intervention
5.6%
2/36 • From the First Intervention through 24-48 hours following the Second Intervention, an overall total of between 5-22 days depending on the length of the Washout Period (Washout Period range: 4-20 days).
Safety Population includes all participants who received at least one dose of intervention
Psychiatric disorders
Changes in Mood
11.4%
4/35 • From the First Intervention through 24-48 hours following the Second Intervention, an overall total of between 5-22 days depending on the length of the Washout Period (Washout Period range: 4-20 days).
Safety Population includes all participants who received at least one dose of intervention
2.8%
1/36 • From the First Intervention through 24-48 hours following the Second Intervention, an overall total of between 5-22 days depending on the length of the Washout Period (Washout Period range: 4-20 days).
Safety Population includes all participants who received at least one dose of intervention
Psychiatric disorders
Difficulty Falling Asleep
2.9%
1/35 • From the First Intervention through 24-48 hours following the Second Intervention, an overall total of between 5-22 days depending on the length of the Washout Period (Washout Period range: 4-20 days).
Safety Population includes all participants who received at least one dose of intervention
2.8%
1/36 • From the First Intervention through 24-48 hours following the Second Intervention, an overall total of between 5-22 days depending on the length of the Washout Period (Washout Period range: 4-20 days).
Safety Population includes all participants who received at least one dose of intervention

Additional Information

Jessica R. Cohen, PhD

University of North Carolina at Chapel Hill

Phone: (919) 843-3753

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place