Substudy 02C: Safety and Efficacy of Pembrolizumab in Combination With Investigational Agents or Pembrolizumab Alone in Participants With Stage III Melanoma Who Are Candidates for Neoadjuvant Therapy (MK-3475-02C/KEYMAKER-U02)

NCT ID: NCT04303169

Last Updated: 2025-10-27

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1/PHASE2

Total Enrollment

146 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-06-26

Study Completion Date

2025-09-24

Brief Summary

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Substudy 02C is part of a larger research study that is testing experimental treatments for melanoma, a type of skin cancer. The larger study is the umbrella study.

The goal of substudy 02C is to evaluate the safety and efficacy of investigational treatment arms in participants with Stage III melanoma who are candidates for neoadjuvant therapy to identify the investigational agent(s) that, when used in combination, are superior to the current treatment options/historical control available.

Arm 1: Pembrolizumab + Vibostolimab, Arm 2: Pembrolizumab + Gebasaxturev, and Arm 3: Pembrolizumab were added in the base protocol on 13-Nov-2019, and enrollment into those arms has been completed. Arm 4: Pembrolizumab + MK-4830 was added in Amendment 04 on 20-Dec-2021, and enrollment into that arm has been completed. Arm 5: Favezelimab + Pembrolizumab and Arm 6: Pembrolizumab + all-trans retinoic acid (ATRA) were added in Amendment 06 on 25-Jun-2022, and enrollment is ongoing.

Detailed Description

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Conditions

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Melanoma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Pembrolizumab + Vibostolimab

Prior to tumor resection surgery, in the neoadjuvant phase, participants will receive pembrolizumab intravenously (IV) plus vibostolimab IV at specified doses on specified days. After surgery, in the adjuvant phase, participants will receive pembrolizumab IV at a specified dose on specified days.

Participants will receive treatments in the neoadjuvant and adjuvant phase for a total treatment duration of up to approximately 1 year.

Group Type EXPERIMENTAL

Pembrolizumab

Intervention Type BIOLOGICAL

Administered via IV infusion at a specified dose on specified days

Vibostolimab

Intervention Type BIOLOGICAL

Administered via IV infusion at a specified dose on specified days

Pembrolizumab + Gebasaxturev

Prior to tumor resection surgery, in the neoadjuvant phase, participants will receive pembrolizumab IV plus gebasaxturev (V937) intratumorally (IT) at specified doses on specified days. After surgery, in the adjuvant phase, participants will receive pembrolizumab IV at a specified dose on specified days.

Participants will receive treatments in the neoadjuvant and adjuvant phase for a total treatment duration of up to approximately 1 year.

Group Type EXPERIMENTAL

Pembrolizumab

Intervention Type BIOLOGICAL

Administered via IV infusion at a specified dose on specified days

Gebasaxturev

Intervention Type BIOLOGICAL

Administered via IT injection at a specified dose on specified days

Pembrolizumab

Prior to tumor resection surgery, in the neoadjuvant phase, participants will receive pembrolizumab IV at a specified dose on specified days. After surgery, in the adjuvant phase, participants will receive pembrolizumab IV at a specified dose on specified days.

Participants will receive treatments in the neoadjuvant and adjuvant phase for a total treatment duration of up to approximately 1 year.

Group Type EXPERIMENTAL

Pembrolizumab

Intervention Type BIOLOGICAL

Administered via IV infusion at a specified dose on specified days

Pembrolizumab + MK-4830

Prior to tumor resection surgery, in the neoadjuvant phase, participants will receive pembrolizumab IV plus MK-4830 IV at specified doses on specified days. After surgery, in the adjuvant phase, participants will receive pembrolizumab IV at a specified dose on specified days.

Participants will receive treatments in the neoadjuvant and adjuvant phase for a total treatment duration of up to approximately 1 year.

Group Type EXPERIMENTAL

Pembrolizumab

Intervention Type BIOLOGICAL

Administered via IV infusion at a specified dose on specified days

MK-4830

Intervention Type BIOLOGICAL

Administered via IV infusion at a specified dose on specified days

Favezelimab + Pembrolizumab

Prior to tumor resection surgery, in the neoadjuvant phase, participants will receive MK-4280A (favezelimab and pembrolizumab administered as a co-formulation) IV at specified doses on specified days. After surgery, in the adjuvant phase, participants will receive pembrolizumab IV at a specified dose on specified days.

Participants will receive treatments in the neoadjuvant and adjuvant phase for a total treatment duration of up to approximately 1 year.

Group Type EXPERIMENTAL

Favezelimab + Pembrolizumab

Intervention Type BIOLOGICAL

Administered via IV infusion at a specified dose on specified days

Pembrolizumab + all-trans retinoic acid (ATRA)

Prior to tumor resection surgery, in the neoadjuvant phase, participants will receive pembrolizumab IV plus ATRA orally at specified doses on specified days. After surgery, in the adjuvant phase, participants will receive pembrolizumab IV at a specified dose on specified days.

Participants will receive treatments in the neoadjuvant and adjuvant phase for a total treatment duration of up to approximately 1 year.

Group Type EXPERIMENTAL

Pembrolizumab

Intervention Type BIOLOGICAL

Administered via IV infusion at a specified dose on specified days

ATRA

Intervention Type DRUG

Administered via oral capsules at a specified dose on specified days

Interventions

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Pembrolizumab

Administered via IV infusion at a specified dose on specified days

Intervention Type BIOLOGICAL

Vibostolimab

Administered via IV infusion at a specified dose on specified days

Intervention Type BIOLOGICAL

Gebasaxturev

Administered via IT injection at a specified dose on specified days

Intervention Type BIOLOGICAL

MK-4830

Administered via IV infusion at a specified dose on specified days

Intervention Type BIOLOGICAL

Favezelimab + Pembrolizumab

Administered via IV infusion at a specified dose on specified days

Intervention Type BIOLOGICAL

ATRA

Administered via oral capsules at a specified dose on specified days

Intervention Type DRUG

Other Intervention Names

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MK-3475 KEYTRUDA® MK-7684 Coxsackievirus A21 (CVA21) Formerly known as CAVATAK® CAV21 V937 MK-4280A Tretinoin Vesanoid®

Eligibility Criteria

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Inclusion Criteria

* Has histologically or cytologically confirmed melanoma
* Has clinically detectable and resectable Stage IIIB or IIIC or IIID melanoma amenable to surgery
* Has been untreated for Stage IIIB, IIIC or IIID melanoma

* surgical resection of primary melanoma is allowed
* prior radiotherapy to the primary melanoma is allowed
* Has provided a baseline tumor biopsy
* Male participants who receive gebasaxturev are abstinent from heterosexual intercourse or agree to use contraception during the intervention period and for at least 120 days after the last dose of gebasaxturev
* Male participants who receive ATRA are abstinent from heterosexual intercourse or agree to use contraception during the intervention period and for at least 7 days after the last dose of ATRA
* Female participants are not pregnant or breastfeeding and are either not a woman of child-bearing potential (WOCBP) OR use a contraceptive method that is highly effective or are abstinent from heterosexual intercourse during the intervention period and for at least 120 days after the last dose of pembrolizumab, vibostolimab, gebasaxturev, or MK-4830, favezelimab + pembrolizumab, or 30 days after the last dose of ATRA, whichever occurs last
* Has adequate organ function
* Has resolution of toxic effect(s) of the most recent prior therapy to Grade 1 or less (except alopecia)

Exclusion Criteria

* Has a diagnosis of immunodeficiency or is receiving immunosuppressive therapy within 7 days before the first dose of study intervention
* Has a known additional malignancy that is progressing or requires active treatment within the past 2 years
* Has known central nervous system (CNS) metastases and/or carcinomatous meningitis
* Has ocular or mucosal melanoma
* Has known hypersensitivity including previous clinically significant hypersensitivity reaction to treatment with another monoclonal antibody (mAb)
* Has an active autoimmune disease that has required systemic treatment in the past 2 years
* Has an active infection requiring systemic therapy
* Has known history of human immunodeficiency virus (HIV)
* Has known history of hepatitis B
* Has a history of (noninfectious) pneumonitis
* Has a history of active tuberculosis (TB)
* Has received prior systemic anticancer therapy within 4 weeks prior to randomization
* Has received prior radiotherapy within 2 weeks of first dose of study intervention
* Has had major surgery \<3 weeks prior to first dose of study intervention
* Has received a live or live-attenuated vaccine within 30 days before the first dose of study intervention
* Has participated in a study of an investigational agent within 4 weeks prior to the first dose of study intervention
* Has had an allogeneic tissue/solid organ transplant
* Has only mucosal lesions
* Is not naïve to Talimogene laherparepvec (TVEC) and other oncolytic viruses
Minimum Eligible Age

18 Years

Maximum Eligible Age

120 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Merck Sharp & Dohme LLC

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Medical Director

Role: STUDY_DIRECTOR

Merck Sharp & Dohme LLC

Locations

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The Angeles Clinic and Research Institute ( Site 3009)

Los Angeles, California, United States

Site Status

Providence Saint John's Health Center ( Site 3010)

Santa Monica, California, United States

Site Status

University of Colorado, Anschutz Cancer Pavilion ( Site 3012)

Aurora, Colorado, United States

Site Status

Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins ( Site 3022)

Baltimore, Maryland, United States

Site Status

NYU Clinical Cancer Center ( Site 3002)

New York, New York, United States

Site Status

Duke Cancer Institute ( Site 3005)

Durham, North Carolina, United States

Site Status

Martha Morehouse Tower ( Site 3020)

Columbus, Ohio, United States

Site Status

Oregon Health & Science University ( Site 3013)

Portland, Oregon, United States

Site Status

University of Pennsylvania Abramson Cancer Center ( Site 3008)

Philadelphia, Pennsylvania, United States

Site Status

West Cancer Center - East Campus ( Site 3014)

Germantown, Tennessee, United States

Site Status

Inova Schar Cancer Institute ( Site 3011)

Fairfax, Virginia, United States

Site Status

Melanoma Institute Australia ( Site 3402)

Wollstonecraft, New South Wales, Australia

Site Status

Tasman Oncology Research Pty Ltd ( Site 3403)

Southport, Queensland, Australia

Site Status

Fiona Stanley Hospital ( Site 3401)

Murdoch, Western Australia, Australia

Site Status

Hopital La Timone ( Site 3103)

Marseille, Bouches-du-Rhone, France

Site Status

Institut Claudius Regaud ( Site 3105)

Toulouse, Haute-Garonne, France

Site Status

Centre Hospitalier Lyon Sud ( Site 3102)

Pierre-Bénite, Rhone, France

Site Status

A.P.H. Paris, Hopital Saint Louis ( Site 3107)

Paris, , France

Site Status

Gustave Roussy ( Site 3101)

Villejuif, Île-de-France Region, France

Site Status

HaEmek Medical Center ( Site 3703)

Afula, , Israel

Site Status

Rambam Health Care Campus-Oncology ( Site 3704)

Haifa, , Israel

Site Status

Hadassah Ein Karem Jerusalem ( Site 3702)

Jerusalem, , Israel

Site Status

Rabin Medical Center-Oncology ( Site 3705)

Petah Tikva, , Israel

Site Status

Chaim Sheba Medical Center ( Site 3701)

Ramat Gan, , Israel

Site Status

Istituto Europeo di Oncologia ( Site 3301)

Milan, , Italy

Site Status

Policlinico Le Scotte - A.O. Senese ( Site 3377)

Siena, , Italy

Site Status

Hôpitaux Universitaires de Genève (HUG)-Oncology ( Site 3603)

Geneva, Canton of Geneva, Switzerland

Site Status

CHUV Centre Hospitalier Universitaire Vaudois ( Site 3602)

Lausanne, Canton of Vaud, Switzerland

Site Status

Universitaetsspital Zuerich ( Site 3601)

Zuerich Flughafen, Canton of Zurich, Switzerland

Site Status

Countries

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United States Australia France Israel Italy Switzerland

References

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Dummer R, Robert C, Scolyer RA, Taube JM, Tetzlaff MT, Menzies AM, Hill A, Grob JJ, Portnoy DC, Lebbe C, Khattak MA, Cohen J, Bar-Sela G, Mehmi I, Shapira-Frommer R, Meyer N, Webber AL, Ren Y, Fukunaga-Kalabis M, Krepler C, Long GV. Neoadjuvant anti-PD-1 alone or in combination with anti-TIGIT or an oncolytic virus in resectable stage IIIB-D melanoma: a phase 1/2 trial. Nat Med. 2025 Jan;31(1):144-151. doi: 10.1038/s41591-024-03411-x. Epub 2025 Jan 7.

Reference Type RESULT
PMID: 39775043 (View on PubMed)

Related Links

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Other Identifiers

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MK-3475-02C

Identifier Type: OTHER

Identifier Source: secondary_id

KEYMAKER-U02

Identifier Type: OTHER

Identifier Source: secondary_id

2023-506314-51-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

U1111-1293-5665

Identifier Type: REGISTRY

Identifier Source: secondary_id

2019-003978-22

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

3475-02C

Identifier Type: -

Identifier Source: org_study_id

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