Safety Study of BJ-001, an IL-15 Fusion Protein, for Locally Advanced/Metastatic Solid Tumors

NCT ID: NCT04294576

Last Updated: 2023-11-09

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

PHASE1

Total Enrollment

92 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-12-04

Study Completion Date

2024-10-22

Brief Summary

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The purpose of this study is to assess the safety and tolerability of BJ-001, a human IL-15 fusion protein, administered via subcutaneous injections, as a single agent and in combination with pembrolizumab in adult patients with Locally Advanced/Metastatic Solid Tumors

Detailed Description

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Conditions

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Locally Advanced/Metastatic Solid Tumors

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SEQUENTIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

no masking is used. All involved know the identity of the intervention assignment.

Study Groups

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Arm 1; BJ-001

Phase 1a Part 1, Part 2, and Part 4: dose escalation for BJ-001 as single agent

Group Type EXPERIMENTAL

BJ-001

Intervention Type DRUG

BJ-001 dosed via SC injection as single agent. One cycle is 6 weeks.

Arm 2; BJ-001 and pembrolizumab

Phase 1a Part 3 and Part 5: dose escalation for BJ-001 in combination with Pembrolizumab

Phase 1b: expansion cohorts for the combination of BJ-001 and pembrolizumab

Group Type EXPERIMENTAL

BJ-001

Intervention Type DRUG

BJ-001 dosed via SC injection as single agent. One cycle is 6 weeks.

Pembrolizumab

Intervention Type DRUG

BJ-001 dosed via SC injection in combination with Pembrolizumab

One cycle is 6 weeks.

Interventions

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BJ-001

BJ-001 dosed via SC injection as single agent. One cycle is 6 weeks.

Intervention Type DRUG

Pembrolizumab

BJ-001 dosed via SC injection in combination with Pembrolizumab

One cycle is 6 weeks.

Intervention Type DRUG

Other Intervention Names

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Keytruda

Eligibility Criteria

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Inclusion Criteria

* Phase 1a patients must have locally advanced or metastatic solid tumors,
* Phase 1b patients must have locally advanced or metastatic and/or non-resectable head and neck squamous cell carcinoma, cholangiocarcinoma, stomach cancer, melanoma, pancreatic cancer, NSCLC (as high expression of αVβ3, αVβ5, or αVβ6 have been reported for these tumors)

* Measurable disease: For Phase 1a patients can have non-measurable or measurable disease. For all other parts: measurable disease defined by RECIST v1.1 is required
* For Phase 1a Part 3 and Phase 1b patients (combination treatment) must be refractory or relapsed to anti-PD-1, anti-PD-L1 or anti-CTLA4 checkpoint inhibitors for all tumor types, For Part 1 and Part 2 of Phase 1a (BJ-001 single agent treatment) both checkpoint inhibitor naïve or refractory/relapsed patients will be considered.
* Patient who have diagnosis for which treatment with pembrolizumab to be enrolled. Patients previously treated with pembrolizumab and who have progressed are eligible. to be enrolled.

* Adequate hematologic function,
* Adequate hepatic function, defined by all of the following:
* Adequate renal function defined by estimated creatinine clearance ≥ 45 mL/min (Cockcroft and Gault formula
* ECOG Performance Status (PS) of 0-2.
* No history of any hematopoietic malignancy.
* No active or history of clinically significant autoimmune disease (as defined by previously requiring immunosuppressive therapy).

Exclusion Criteria

* Pregnant or nursing females.
* Receipt of any investigational product or any approved anticancer drug(s) or biological product(s) within 4 weeks prior to the first dose of study drug. Exceptions: Hormone replacement therapy, testosterone, or oral contraceptives (LHRH antagonists are allowed).
* Patients previously treated with an anti PD-1/PD-L1 targeting agent who have had any prior history of immune-mediated pneumonitis, any immune-mediated toxicity of ≥ Grade 3,
* Patients with a history of severe allergic or anaphylactic reactions to human mAb therapy or known hypersensitivity.
* Patients with a history of pneumonitis, myocarditis, history of Stevens-Johnson syndrome or toxic epidermal necrolysis.
* Patients who have undergone a bone marrow transplantation, solid organ transplantation, or stem cell transplant.
* Patients with unresolved AEs \> Grade 1 from prior anticancer therapy.
* Patients who have received prior interferon or IL-2 therapy less than 4 weeks prior to enrollment.
* Uncontrolled primary central nervous system (CNS) tumors or CNS metastases; based on screening.
* Patients with active autoimmune disease or a documented medical history of autoimmune disease managed by replacement therapy.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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PPD Development, LP

INDUSTRY

Sponsor Role collaborator

Merck Sharp & Dohme LLC

INDUSTRY

Sponsor Role collaborator

BJ Bioscience, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Joe Zhang, PhD

Role: STUDY_DIRECTOR

BJ Bioscience

Locations

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Washington University School of Medicine

St Louis, Missouri, United States

Site Status

Mount Sinai

New York, New York, United States

Site Status

Greenville Hospital System University Medical Center (ITOR)

Greenville, South Carolina, United States

Site Status

NEXT Oncology

San Antonio, Texas, United States

Site Status

Northwest Medical Specialities

Tacoma, Washington, United States

Site Status

Countries

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United States

References

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Related Links

Access external resources that provide additional context or updates about the study.

https://www.accessdata.fda.gov/drugsatfda_docs/label/2018/125514s037lbl.pdf

KEYTRUDA (pembrolizumab), \[package insert\]. Merck Sharp \& Dohme Corp. Whitehouse Station, NJ.2014. Accessed at Drugs@FDA: FDA Approved Drug Products on December 28, 2018.

https://www.accessdata.fda.gov/drugsatfda_docs/label/2018/125554s069lbl.pdf

OPDIVO (nivolumab), \[package insert\]. Bristol-Myers Squibb Company, Princeton, NJ. 2014. Accessed at Drugs@FDA: FDA Approved Drug Products on November 15, 2018.

https://www.accessdata.fda.gov/drugsatfda_docs/label/2018/761034s009lbl.pdf

TECENTRIQ (atezolizumab), \[package insert\]. Genentech, Inc. San Francisco, CA. 2016. Accessed at Drugs@FDA: FDA Approved Drug Products on December 6, 2018.

https://www.accessdata.fda.gov/drugsatfda_docs/label/2018/125377s096lbl.pdf

YERVOY (ipilimumab), \[package insert\]. Bristol-Myers Squibb Company, Princeton, NJ. 2011. Accessed at Drugs@FDA: FDA Approved Drug Products on July 10, 2018.

Other Identifiers

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KEYNOTE-F13

Identifier Type: OTHER

Identifier Source: secondary_id

BJ-001-01-001US

Identifier Type: -

Identifier Source: org_study_id

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