Pharmacokinetics, Pharmacodynamics, and Safety Profile of Understudied Drugs Administered to Children Per Standard of Care (POPS)

NCT ID: NCT04278404

Last Updated: 2025-03-12

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Total Enrollment

5000 participants

Study Classification

OBSERVATIONAL

Study Start Date

2020-03-05

Study Completion Date

2027-09-30

Brief Summary

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The study investigators are interested in learning more about how drugs, that are given to children by their health care provider, act in the bodies of children and young adults in hopes to find the most safe and effective dose for children. The primary objective of this study is to evaluate the PK of understudied drugs currently being administered to children per SOC as prescribed by their treating provider.

Detailed Description

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Conditions

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Coronavirus Infection (COVID-19) Pulmonary Arterial Hypertension Urinary Tract Infections in Children Hypertension Pain Hyperphosphatemia Primary Hyperaldosteronism Edema Hypokalemia Heart Failure Hemophilia Menorrhagia Insomnia Pneumonia Skin Infection Arrythmia Asthma in Children Bronchopulmonary Dysplasia Adrenal Insufficiency Fibrinolysis; Hemorrhage Attention Deficit Hyperactivity Disorder Multisystem Inflammatory Syndrome in Children (MIS-C) Kawasaki Disease Coagulation Disorder Down Syndrome

Study Design

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Observational Model Type

OTHER

Study Time Perspective

PROSPECTIVE

Study Groups

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Children and young adults who are prescribed drugs of interest

Children and young adults who are prescribed drugs of interest as part of their routine medical care OR are SARS-CoV-2 positive.

The POP02 study is collecting bodily fluid samples (i.e., whole blood, effluent samples) of children prescribed the following drugs of interest per standard of care:

Intervention Type DRUG

The prescribing of drugs to children is not part of this protocol. Participants will receive DOIs as prescribed by their treating provider.

Interventions

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The POP02 study is collecting bodily fluid samples (i.e., whole blood, effluent samples) of children prescribed the following drugs of interest per standard of care:

The prescribing of drugs to children is not part of this protocol. Participants will receive DOIs as prescribed by their treating provider.

Intervention Type DRUG

Other Intervention Names

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Aminocaproic acid Amiodarone Bosentan Budesonide Cefdinir Cefepime Ceftazidime Clindamycin Clobazam Dexamethasone Dexmedetomidine Dextroamphetamine/Amphetamine Fosfomycin Furosemide Gabapentin Guanfacine Hydrocortisone Labetalol Meropenem Metformin Milrinone Nalbuphine Nicardipine Nifedipine Oseltamivir Oxycodone Risperidone Sertraline Sevelamer Carbonate / Sevelamer Hydrochloride Spironolactone Terbutaline Tranexamic acid Voriconazole Zolpidem Azithromycin Lopinavir/Ritonavir Ribavirin Tocilizumab Anakinra Aspirin Canakinumab Colchicine Interferon Remdesivir Ruxolitinib Sarilumab Abatacept Infliximab

Eligibility Criteria

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Inclusion Criteria

1. Participant is \< 21 years of age
2. Parent/ Legal Guardian/ Adult Participant can understand the consent process and is willing to provide informed consent/HIPAA:
3. (a) Participant is receiving one or more of the study drugs of interest at the time of enrollment or (b) Participant is NOT receiving one or more of the study drugs of interest but is SARS-COV-2 positive within 60 days prior to enrollment

Exclusion Criteria

1. Participant has a known pregnancy


Participants receiving one or more of the study drugs of interest at the time of enrollment, DOI administration or PK sampling: (Refer to DOI specific appendices for details on enrollment cohort specifications and additional eligibility criteria)
2. Has had intermittent dialysis within previous 24 hours
3. Has had a kidney transplant within previous 30 days
4. Has had a liver transplant within previous 1 year
5. Has had a stem cell transplant within previous 1 year
6. Has had therapeutic hypothermia within previous 24 hours
7. Has had plasmapheresis within the previous 24 hours
8. Has a Ventricular Assist Device
9. Has any condition which would make the participant, in the opinion of the investigator, unsuitable for the study
Minimum Eligible Age

0 Years

Maximum Eligible Age

20 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

Yes

Sponsors

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The Emmes Company, LLC

INDUSTRY

Sponsor Role collaborator

Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)

NIH

Sponsor Role collaborator

Duke University

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Chi Hornik

Role: PRINCIPAL_INVESTIGATOR

Duke Clinical Research Institute

Locations

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Phoenix Children's Hospital

Phoenix, Arizona, United States

Site Status ACTIVE_NOT_RECRUITING

Arkansas Children's Hospital Research Institute

Little Rock, Arkansas, United States

Site Status RECRUITING

University of California, Los Angeles Medical Center

Los Angeles, California, United States

Site Status RECRUITING

Lucile Packard Children's Hospital

Palo Alto, California, United States

Site Status RECRUITING

Colorado University Denver

Aurora, Colorado, United States

Site Status RECRUITING

The Children's Hospital Colorado

Aurora, Colorado, United States

Site Status RECRUITING

Alfred I. DuPont Hospital for Children

Wilmington, Delaware, United States

Site Status COMPLETED

University of Florida Jacksonville Shands Medical Center

Jacksonville, Florida, United States

Site Status RECRUITING

Kapiolani Womens and Childrens Medical Center

Honolulu, Hawaii, United States

Site Status RECRUITING

Ann and Robert H. Lurie Childrens Hospital of Chicago

Chicago, Illinois, United States

Site Status RECRUITING

Ann and Robert H. Lurie Childrens Hospital of Chicago

Chicago, Illinois, United States

Site Status RECRUITING

Riley Hospital for Children at Indiana University

Indianapolis, Indiana, United States

Site Status RECRUITING

University of Iowa Stead Family Children's Hospital

Iowa City, Iowa, United States

Site Status RECRUITING

University of Kansas Medical Center-JG Kidney Institute

Kansas City, Kansas, United States

Site Status COMPLETED

University of Louisville Norton Childrens Hospital

Louisville, Kentucky, United States

Site Status RECRUITING

Tulane University Health Science Center

New Orleans, Louisiana, United States

Site Status COMPLETED

Ochsner Baptist Clinical Trials Unit

New Orleans, Louisiana, United States

Site Status RECRUITING

University of Maryland Medical Center

Baltimore, Maryland, United States

Site Status COMPLETED

Boston Children's Hospital

Boston, Massachusetts, United States

Site Status ENROLLING_BY_INVITATION

Massachusetts General Hospital

Lexington, Massachusetts, United States

Site Status RECRUITING

University of Minnesota

Minneapolis, Minnesota, United States

Site Status COMPLETED

University of Mississippi Medical Center

Jackson, Mississippi, United States

Site Status RECRUITING

Mississippi Center for Advanced Medicine

Madison, Mississippi, United States

Site Status COMPLETED

Children's Mercy Hospital

Kansas City, Missouri, United States

Site Status COMPLETED

University of Nebraska Medical Center

Omaha, Nebraska, United States

Site Status RECRUITING

Dartmouth-Hitchcock Medical Center

Lebanon, New Hampshire, United States

Site Status COMPLETED

University of New Mexico Health Science Center

Albuquerque, New Mexico, United States

Site Status COMPLETED

University of North Carolina at Chapel Hill

Chapel Hill, North Carolina, United States

Site Status RECRUITING

Duke University Health System

Durham, North Carolina, United States

Site Status RECRUITING

Cincinnati Childrens Hospital Medical Center

Cincinnati, Ohio, United States

Site Status RECRUITING

Cincinnati Childrens Hospital Medical Center

Cincinnati, Ohio, United States

Site Status RECRUITING

Board of Regents of the University of Oklahoma

Oklahoma City, Oklahoma, United States

Site Status RECRUITING

Oregon Health and Science University

Portland, Oregon, United States

Site Status RECRUITING

Pennsylvania State University--Hershey Children's Hospital

Hershey, Pennsylvania, United States

Site Status RECRUITING

Rhode Island Hospital

Providence, Rhode Island, United States

Site Status COMPLETED

Medical University of South Carolina Children's Hospital

Charleston, South Carolina, United States

Site Status RECRUITING

University of South Carolina

Columbia, South Carolina, United States

Site Status COMPLETED

Avera McKennan Hospital & University Medical Center

Sioux Falls, South Dakota, United States

Site Status COMPLETED

Monroe Carell Jr. Children's Hospital at Vanderbilt

Nashville, Tennessee, United States

Site Status RECRUITING

Dell Children's Medical Center of Central Texas

Austin, Texas, United States

Site Status RECRUITING

University of Texas-Southwestern Medical Center Dallas

Dallas, Texas, United States

Site Status ACTIVE_NOT_RECRUITING

University of Texas--Memorial Hermann Texas Medical Center

Houston, Texas, United States

Site Status RECRUITING

The Womens Hospital of Texas

Houston, Texas, United States

Site Status RECRUITING

University of Utah

Salt Lake City, Utah, United States

Site Status RECRUITING

Seattle Children's Hospital

Seattle, Washington, United States

Site Status RECRUITING

West Virginia University Hospital

Morgantown, West Virginia, United States

Site Status ACTIVE_NOT_RECRUITING

University of Wisconsin

Madison, Wisconsin, United States

Site Status RECRUITING

University Wisconsin Madison

Madison, Wisconsin, United States

Site Status ENROLLING_BY_INVITATION

Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Site Status RECRUITING

The Hospital for Sick Children

Toronto, Ontario, Canada

Site Status RECRUITING

CHU Sainte-Justine

Montreal, Quebec, Canada

Site Status RECRUITING

Countries

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United States Canada

Central Contacts

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Chi Hornik

Role: CONTACT

(919) 260-7626

Jerry Kirchner

Role: CONTACT

(919) 812-1798

Facility Contacts

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Justin Williamson

Role: backup

416-813-7654

Clothilde Gravel

Role: primary

514-345-4931

Vincent Lague

Role: backup

514-345-4931

Haley Spradin

Role: primary

501-364-5023

Lee Howard

Role: backup

501-364-6990

Michelle Carter

Role: primary

310-206-6369

Yun Yong Margarida Lei

Role: backup

310-206-2439

Yasaman Nourkhala

Role: primary

650-724-4548

Shelby Burk

Role: backup

650-704-2186

Lexi Petruccelli

Role: primary

720-777-9881

Aline Maddux

Role: backup

Rebecca Bernstein

Role: primary

720-777-2714

Kristine Wolter-Warmerd

Role: backup

507-319-9808

Amna Riaz

Role: primary

904-244-3059

Daisy Khalif

Role: backup

904-244-3849

Moara Santos

Role: primary

808-535-7829

Annette Amiotte

Role: backup

808-535-7291

Ally Byrd

Role: primary

312-227-0067

Prachi Patel

Role: backup

773-729-0397

Harrison Lee

Role: primary

312-227-4668

Rohit Kalra

Role: backup

312-227-6281

Jessica Mendoza

Role: primary

317-278-7858

Ashley Moore

Role: backup

317-278-7858

Maureen Austin

Role: primary

319-356-0378

Madison Jessie

Role: primary

502-588-3070

Tori Clements

Role: backup

502-629-5283

Nadrine Hayden

Role: primary

504-897-5811

Sarah Foster

Role: backup

504-703-7122

Heli Patel

Role: primary

781-860-1784

Alexander Cordova

Role: backup

1-781-860-1784

Emily Fratesi

Role: primary

601-815-4179

Taylor Fry

Role: backup

601-815-4180

Joann Von Bonn

Role: primary

402-836-9756

Rachel Wellman

Role: backup

402-253-9176

Sneha Makhijani

Role: primary

984-974-7865

Melissa Harward

Role: primary

919-668-3910

Bethany Kristler

Role: backup

919-681-2554

Aine Powell

Role: primary

513-636-0674

kellie Voth

Role: backup

513-636-0674

Luana Johnson

Role: primary

513-803-0854

Michaela Collins

Role: backup

513-803-7340

Tracy Jones

Role: primary

405-271-5211

Katherine Mitchell

Role: backup

405-271-8000

Kyle Patubo

Role: primary

503-494-2797

Courtney Byrnes

Role: primary

717-531-0003

Ellen Stoute

Role: backup

717-531-1260

Mary Freeman

Role: primary

843-792-5762

Al Sarraf Layla

Role: backup

843-876-5203

Harrison Moody

Role: primary

615-322-0558

Jennifer Jaimes

Role: primary

512-324-4000

Ila Sehgal

Role: backup

512-324-0165

Elizabeth Aguilera

Role: primary

713-500-5806

Gabriela Del Bianco

Role: backup

713-500-5806

Joanna Williams

Role: primary

281-743-2941

Amanda Sowden

Role: backup

601-543-3154

Fumiko Alger

Role: primary

801-213-7372

Ella Burkholz

Role: backup

801-819-3275

Megan Kelton

Role: primary

206-987-5539

Emily Pao

Role: backup

206-987-2524

Lensy Porior

Role: primary

608-228-4940

Cassandra Nelson

Role: backup

608-228-4940

Sadaf Shad

Role: primary

414-266-7426

Miranda Privatt

Role: backup

414-266-3973

Maggie Rumantir

Role: primary

416-813-7654

References

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Autmizguine J, Melloni C, Hornik CP, Dallefeld S, Harper B, Yogev R, Sullivan JE, Atz AM, Al-Uzri A, Mendley S, Poindexter B, Mitchell J, Lewandowski A, Delmore P, Cohen-Wolkowiez M, Gonzalez D; the Pediatric Trials Network Steering Committee. Population Pharmacokinetics of Trimethoprim-Sulfamethoxazole in Infants and Children. Antimicrob Agents Chemother. 2017 Dec 21;62(1):e01813-17. doi: 10.1128/AAC.01813-17. Print 2018 Jan.

Reference Type BACKGROUND
PMID: 29084742 (View on PubMed)

Dallefeld SH, Atz AM, Yogev R, Sullivan JE, Al-Uzri A, Mendley SR, Laughon M, Hornik CP, Melloni C, Harper B, Lewandowski A, Mitchell J, Wu H, Green TP, Cohen-Wolkowiez M. A pharmacokinetic model for amiodarone in infants developed from an opportunistic sampling trial and published literature data. J Pharmacokinet Pharmacodyn. 2018 Jun;45(3):419-430. doi: 10.1007/s10928-018-9576-y. Epub 2018 Feb 12.

Reference Type BACKGROUND
PMID: 29435949 (View on PubMed)

Hornik CP, Gonzalez D, van den Anker J, Atz AM, Yogev R, Poindexter BB, Ng KC, Delmore P, Harper BL, Melloni C, Lewandowski A, Gelber C, Cohen-Wolkowiez M, Lee JH; Pediatric Trial Network Steering Committee. Population Pharmacokinetics of Intramuscular and Intravenous Ketamine in Children. J Clin Pharmacol. 2018 Aug;58(8):1092-1104. doi: 10.1002/jcph.1116. Epub 2018 Apr 20.

Reference Type BACKGROUND
PMID: 29677389 (View on PubMed)

Drolet BA, Boakye-Agyeman F, Harper B, Holland K, Lewandowski A, Stefanko N, Melloni C; Pediatric Trials Network Steering Committee (See Acknowledgments for a listing of committee members.). Systemic timolol exposure following topical application to infantile hemangiomas. J Am Acad Dermatol. 2020 Mar;82(3):733-736. doi: 10.1016/j.jaad.2019.02.029. Epub 2019 Feb 18. No abstract available.

Reference Type BACKGROUND
PMID: 30790601 (View on PubMed)

Tremoulet A, Le J, Poindexter B, Sullivan JE, Laughon M, Delmore P, Salgado A, Ian-U Chong S, Melloni C, Gao J, Benjamin DK Jr, Capparelli EV, Cohen-Wolkowiez M; Administrative Core Committee of the Best Pharmaceuticals for Children Act-Pediatric Trials Network. Characterization of the population pharmacokinetics of ampicillin in neonates using an opportunistic study design. Antimicrob Agents Chemother. 2014 Jun;58(6):3013-20. doi: 10.1128/AAC.02374-13. Epub 2014 Mar 10.

Reference Type BACKGROUND
PMID: 24614374 (View on PubMed)

Hornik CP, Benjamin DK Jr, Smith PB, Pencina MJ, Tremoulet AH, Capparelli EV, Ericson JE, Clark RH, Cohen-Wolkowiez M; Best Pharmaceuticals for Children Act-Pediatric Trials Network. Electronic Health Records and Pharmacokinetic Modeling to Assess the Relationship between Ampicillin Exposure and Seizure Risk in Neonates. J Pediatr. 2016 Nov;178:125-129.e1. doi: 10.1016/j.jpeds.2016.07.011. Epub 2016 Aug 10.

Reference Type BACKGROUND
PMID: 27522443 (View on PubMed)

Le J, Poindexter B, Sullivan JE, Laughon M, Delmore P, Blackford M, Yogev R, James LP, Melloni C, Harper B, Mitchell J, Benjamin DK Jr, Boakye-Agyeman F, Cohen-Wolkowiez M. Comparative Analysis of Ampicillin Plasma and Dried Blood Spot Pharmacokinetics in Neonates. Ther Drug Monit. 2018 Feb;40(1):103-108. doi: 10.1097/FTD.0000000000000466.

Reference Type BACKGROUND
PMID: 29271816 (View on PubMed)

Gonzalez D, Melloni C, Yogev R, Poindexter BB, Mendley SR, Delmore P, Sullivan JE, Autmizguine J, Lewandowski A, Harper B, Watt KM, Lewis KC, Capparelli EV, Benjamin DK Jr, Cohen-Wolkowiez M; Best Pharmaceuticals for Children Act - Pediatric Trials Network Administrative Core Committee. Use of opportunistic clinical data and a population pharmacokinetic model to support dosing of clindamycin for premature infants to adolescents. Clin Pharmacol Ther. 2014 Oct;96(4):429-37. doi: 10.1038/clpt.2014.134. Epub 2014 Jun 20.

Reference Type BACKGROUND
PMID: 24949994 (View on PubMed)

Gonzalez D, Delmore P, Bloom BT, Cotten CM, Poindexter BB, McGowan E, Shattuck K, Bradford KK, Smith PB, Cohen-Wolkowiez M, Morris M, Yin W, Benjamin DK Jr, Laughon MM. Clindamycin Pharmacokinetics and Safety in Preterm and Term Infants. Antimicrob Agents Chemother. 2016 Apr 22;60(5):2888-94. doi: 10.1128/AAC.03086-15. Print 2016 May.

Reference Type BACKGROUND
PMID: 26926644 (View on PubMed)

Gonzalez D, Melloni C, Poindexter BB, Yogev R, Atz AM, Sullivan JE, Mendley SR, Delmore P, Delinsky A, Zimmerman K, Lewandowski A, Harper B, Lewis KC, Benjamin DK Jr, Cohen-Wolkowiez M; Best Pharmaceuticals for Children Act--Pediatric Trials Network Administrative Core Committee. Simultaneous determination of trimethoprim and sulfamethoxazole in dried plasma and urine spots. Bioanalysis. 2015;7(9):1137-49. doi: 10.4155/bio.15.38.

Reference Type BACKGROUND
PMID: 26039810 (View on PubMed)

Hornik CP, Yogev R, Mourani PM, Watt KM, Sullivan JE, Atz AM, Speicher D, Al-Uzri A, Adu-Darko M, Payne EH, Gelber CE, Lin S, Harper B, Melloni C, Cohen-Wolkowiez M, Gonzalez D; Best Pharmaceuticals for Children Act-Pediatric Trials Network Steering Committee. Population Pharmacokinetics of Milrinone in Infants, Children, and Adolescents. J Clin Pharmacol. 2019 Dec;59(12):1606-1619. doi: 10.1002/jcph.1499. Epub 2019 Jul 17.

Reference Type BACKGROUND
PMID: 31317556 (View on PubMed)

Related Links

Access external resources that provide additional context or updates about the study.

http://www.fda.gov/media/90358/download

Food and Drug Administration. General Clinical Pharmacology Considerations for Pediatric Studies for Drugs and Biological Products

https://www.elso.org/Registry/Statistics/InternationalSummary.aspx

Extracorporeal Life Support Organization (ELSO). ECLS Registry Report: International Summary Ann Arbor, MI: Extracorporeal Life Support Organization (ELSO); 2020

https://pdfs.semanticscholar.org/b0d9/11f1f38ad7a83694bbee99fd41ae3db5b07d.pdf

Wildschut E, editor. Drug therapies in neonates and children during extracorporeal membrane oxygenation (ECMO); Keep your eyes open. Rotterdam, The Netherlands: Erasmus MC; 2010.

Other Identifiers

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Pro00103838

Identifier Type: -

Identifier Source: org_study_id

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