A Study of Atezolizumab Plus Carboplatin and Etoposide With or Without Tiragolumab in Patients With Untreated Extensive-Stage Small Cell Lung Cancer

NCT ID: NCT04256421

Last Updated: 2025-10-22

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

490 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-02-04

Study Completion Date

2025-07-31

Brief Summary

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This study will evaluate the efficacy of tiragolumab plus atezolizumab and carboplatin and etoposide (CE) compared with placebo plus atezolizumab and CE in participants with chemotherapy-naive extensive-stage small cell lung cancer (ES-SCLC). Eligible participants will be stratified by Eastern Cooperative Oncology Group (ECOG) Performance Status (0 vs. 1), LDH (\</= upper limit of normal \[ULN\] vs. \> ULN), and presence or history of brain metastasis (yes vs. no) and randomly assigned in a 1:1 ratio to receive one of the following treatment regimens during induction phase:

* Arm A: Tiragolumab plus atezolizumab plus CE
* Arm B: Placebo plus atezolizumab plus CE

Following the induction phase, participants will continue maintenance therapy with either atezolizumab plus tiragolumab (Arm A) or atezolizumab plus placebo (Arm B).

Detailed Description

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Conditions

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Small Cell Lung Cancer

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

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Placebo + Atezolizumab + CE

Participants will receive atezolizumab on Day 1 of each 21-day cycle followed by placebo on Day 1 of each 21-day cycle. Carboplatin will be administered followed by etoposide on Day 1 for 4 cycles. Participants will also receive etoposide on Days 2 and 3.

Group Type ACTIVE_COMPARATOR

Atezolizumab

Intervention Type DRUG

Atezolizumab 1200 mg administered by IV infusion on Day 1 of each 21-day cycle.

Carboplatin

Intervention Type DRUG

Carboplatin was administered by IV infusion on Day 1 of each 21-day cycle for 4 cycles.

Etoposide

Intervention Type DRUG

Etoposide 100 mg/m\^2 administered by IV infusion on Days 1, 2 and 3 of each 21-day cycle for 4 cycles.

Placebo

Intervention Type DRUG

Placebo administered by IV infusion on Day 1 of each 21-day cycle.

Tiragolumab + Atezolizumab + CE

Participants will receive atezolizumab on Day 1 of each 21-day cycle followed by tiragolumab on Day 1 of each 21-day cycle. Carboplatin will be administered followed by etoposide on Day 1 for 4 cycles. Participants will also receive etoposide on Days 2 and 3.

Group Type EXPERIMENTAL

Tiragolumab

Intervention Type DRUG

Tiragolumab 600 milligrams (mg) administered by IV infusion on Day 1 of each 21-day cycle.

Atezolizumab

Intervention Type DRUG

Atezolizumab 1200 mg administered by IV infusion on Day 1 of each 21-day cycle.

Carboplatin

Intervention Type DRUG

Carboplatin was administered by IV infusion on Day 1 of each 21-day cycle for 4 cycles.

Etoposide

Intervention Type DRUG

Etoposide 100 mg/m\^2 administered by IV infusion on Days 1, 2 and 3 of each 21-day cycle for 4 cycles.

Interventions

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Tiragolumab

Tiragolumab 600 milligrams (mg) administered by IV infusion on Day 1 of each 21-day cycle.

Intervention Type DRUG

Atezolizumab

Atezolizumab 1200 mg administered by IV infusion on Day 1 of each 21-day cycle.

Intervention Type DRUG

Carboplatin

Carboplatin was administered by IV infusion on Day 1 of each 21-day cycle for 4 cycles.

Intervention Type DRUG

Etoposide

Etoposide 100 mg/m\^2 administered by IV infusion on Days 1, 2 and 3 of each 21-day cycle for 4 cycles.

Intervention Type DRUG

Placebo

Placebo administered by IV infusion on Day 1 of each 21-day cycle.

Intervention Type DRUG

Other Intervention Names

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MTIG7192A Tecentriq

Eligibility Criteria

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Inclusion Criteria

* Histologically or cytologically confirmed extensive-stage small cell lung cancer (ES-SCLC)
* No prior systemic treatment for ES-SCLC
* Eastern Cooperative Oncology Group (ECOG) Performance Status of 0 or 1
* Measurable disease, as defined by Response Evaluation Criteria in Solid Tumors version 1.1 (RECIST v1.1)
* Adequate hematologic and end-organ function
* Treatment-free for at least 6 months since last chemo/radiotherapy, among those treated (with curative intent) with prior chemo/radiotherapy for limited-stage SCLC

Exclusion Criteria

* Symptomatic or actively progressing central nervous system (CNS) metastases
* Malignancies other than small cell lung cancer (SCLC) within 5 years prior to randomization, with the exception of those with a negligible risk of metastasis or death treated with expected curative outcome
* Active or history of autoimmune disease or immune deficiency
* History of idiopathic pulmonary fibrosis, organizing pneumonia, drug-induced pneumonitis, or idiopathic pneumonitis, or evidence of active pneumonitis on screening chest computed tomography (CT) scan
* Positive test result for human immunodeficiency virus (HIV)
* Active hepatitis B or hepatitis C
* Severe infection at the time of randomization
* Treatment with any other investigational agent within 28 days prior to initiation of study treatment
* Prior treatment with CD137 agonists or immune checkpoint blockade therapies, anti-cytotoxic T lymphocyte-associated protein 4 (anti-CTLA-4), anti-TIGIT, anti-PD-1, and anti-PD-L1 therapeutic antibodies
* Treatment with systemic immunostimulatory agents within 4 weeks or 5 drug elimination half-lives prior to randomization
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Hoffmann-La Roche

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Trials

Role: STUDY_DIRECTOR

Hoffmann-La Roche

Locations

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Rocky Mountain Cancer Centers - Lone Tree

Lone Tree, Colorado, United States

Site Status

MedStar Georgetown University Hospital (Lombardi Comprehensive Cancer Center)

Washington D.C., District of Columbia, United States

Site Status

Florida Cancer Specialists

Fort Myers, Florida, United States

Site Status

SCRI Florida Cancer Specialists North

Sarasota, Florida, United States

Site Status

Northwest Georgia Oncology Centers PC - Marietta

Marietta, Georgia, United States

Site Status

Illinois Cancer Care

Peoria, Illinois, United States

Site Status

New England Cancer Specialists

Scarborough, Maine, United States

Site Status

Weinberg Cancer Institution at Franklin Square

Baltimore, Maryland, United States

Site Status

Minnesota Oncology Hematology

Minneapolis, Minnesota, United States

Site Status

Comprehensive Cancer Centers of Nevada

Henderson, Nevada, United States

Site Status

Broome Oncology - Binghamton

Binghamton, New York, United States

Site Status

Memorial Sloan Kettering Cancer Center

New York, New York, United States

Site Status

Sarah Cannon Research Institute / Tennessee Oncology

Chattanooga, Tennessee, United States

Site Status

Sarah Cannon Research Inst.

Nashville, Tennessee, United States

Site Status

Texas Oncology Cancer Center

Austin, Texas, United States

Site Status

Virginia Cancer Specialists

Fairfax, Virginia, United States

Site Status

Blue Ridge Cancer Care

Roanoke, Virginia, United States

Site Status

University of Wisconsin School of Medicine and Public Health

Madison, Wisconsin, United States

Site Status

Chris O'Brien Lifehouse

Camperdown, New South Wales, Australia

Site Status

Nepean Hospital

Kingswood, New South Wales, Australia

Site Status

Sunshine Coast University Hospital

Birtinya, Queensland, Australia

Site Status

Lyell McEwin Hospital

Elizabeth Vale, South Australia, Australia

Site Status

Tiroler Landeskrankenanstalten Ges.M.B.H.

Innsbruck, , Austria

Site Status

Klinik Penzing

Vienna, , Austria

Site Status

Krankenhaus Nord - Klinik Floridsdorf

Vienna, , Austria

Site Status

AZ St Maarten Campus Leopoldstr

Mechelen, , Belgium

Site Status

Clinique Ste-Elisabeth

Namur, , Belgium

Site Status

AZ Delta (Campus Rumbeke)

Roeselare, , Belgium

Site Status

Vitaz

Sint-Niklaas, , Belgium

Site Status

Oncocentro Serviços Médicos e Hospitalares Ltda

Fortaleza, Ceará, Brazil

Site Status

Hospital Sao Rafael - HSR

Salvador, Estado de Bahia, Brazil

Site Status

Hospital de Clínicas de Passo Fundo

Passo Fundo, Rio Grande do Sul, Brazil

Site Status

Hospital Nossa Senhora da Conceicao

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

Clínica de Oncologia Reichow

Blumenau, Santa Catarina, Brazil

Site Status

Instituto do Cancer do Estado de Sao Paulo - ICESP

São Paulo, São Paulo, Brazil

Site Status

Fakultni nemocnice Olomouc

Olomouc, , Czechia

Site Status

Vitkovicka Nemocnice Bma, A.S.

Ostrava, , Czechia

Site Status

Thomayerova nemocnice

Praha 4 - Krc, , Czechia

Site Status

Helios Klinikum Emil von Behring GmbH

Berlin, , Germany

Site Status

LungenClinic Großhansdorf GmbH

Großhansdorf, , Germany

Site Status

Asklepios Klinik Harburg

Hamburg, , Germany

Site Status

Fachklinik für Lungenerkrankungen

Immenhausen, , Germany

Site Status

Universitätsklinikum Schleswig-Holstein

Lübeck, , Germany

Site Status

Asklepios Klinik Gauting

München-Gauting, , Germany

Site Status

General Hospital "G.Papanikolaou"

Asvestochóri, , Greece

Site Status

Uoa Sotiria Hospital

Athens, , Greece

Site Status

Metropolitan General Hospital

Cholargós, , Greece

Site Status

Univ General Hosp Heraklion

Heraklion, , Greece

Site Status

Orszagos Koranyi TBC es Pulmonologiai Intezet

Budapest, , Hungary

Site Status

Jasz-Nagykun-Szolnok Megyei Hetenyi Geza Korhaz-Rend.Int.

Szolnok, , Hungary

Site Status

Tudogyogyintezet Torokbalint

Törökbálint, , Hungary

Site Status

Irccs Ist. Tumori Giovanni Paolo Ii

Bari, Apulia, Italy

Site Status

AORN Ospedali dei Colli Ospedale Monaldi

Napoli, Campania, Italy

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AUSL della Romagna

Ravenna, Emilia-Romagna, Italy

Site Status

IRCCS Istituto Clinico Humanitas

Rozzano, Lombardy, Italy

Site Status

Azienda Sanitaria Ospedaliera S Luigi Gonzaga

Orbassano, Piedmont, Italy

Site Status

Azienda Ospedaliero-Universitaria ?PoliclinicoVittorio Emanuele?- P.O. G. Rodolico

Catania, Sicily, Italy

Site Status

IRCCS Istituto Oncologico Veneto (IOV)

Padua, Veneto, Italy

Site Status

National Cancer Center Hospital East

Chiba, , Japan

Site Status

Kyushu University Hospital

Fukuoka, , Japan

Site Status

Niigata Cancer Center Hospital

Niigata, , Japan

Site Status

Osaka International Cancer Institute

Osaka, , Japan

Site Status

Kindai University Hospital

Osaka, , Japan

Site Status

NHO Kinki-Chuo Chest Medical Center

Osaka, , Japan

Site Status

Saitama Cancer Center

Saitama, , Japan

Site Status

Shizuoka Cancer Center

Shizuoka, , Japan

Site Status

National Cancer Center Hospital

Tokyo, , Japan

Site Status

The Cancer Institute Hospital of JFCR

Tokyo, , Japan

Site Status

Wakayama Medical University Hospital

Wakayama, , Japan

Site Status

Maastricht University Medical Center

Maastricht, , Netherlands

Site Status

Erasmus MC

Rotterdam, , Netherlands

Site Status

Auckland City Hospital

Auckland, , New Zealand

Site Status

Szpital Specjalistyczny Podkarpacki O?rodek Onkologiczny

Brzozów, , Poland

Site Status

Uniwersyteckie Centrum Kliniczne, Klinika Onkologii i Radioterapii

Gdansk, , Poland

Site Status

Krakowski Szpital Specjalistyczny im sw.Jana Pawla II

Krakow, , Poland

Site Status

Warminsko-Mazurskie Centrum Chorób P?uc w Olsztynie

Olsztyn, , Poland

Site Status

Mazowieckie Centrum Leczenia Chorob Pluc I Gruzlicy

Otwock, , Poland

Site Status

Wielkopolskie Centrum Pulmonologii i Torakochirurgii w Poznaniu

Poznan, , Poland

Site Status

Narod.Inst.Onkol. im. M.Sklodowskiej - Curie-Panst.Inst.Bad

Warsaw, , Poland

Site Status

Principal Military Clinical Hospital n.a. N.N. Burdenko

Moscow, Moscow Oblast, Russia

Site Status

Blokhin Cancer Research Center

Moscow, Moscow Oblast, Russia

Site Status

Scientific Research Institute n.a. N.N. Petrov

Saint Petersburg, Sankt-Peterburg, Russia

Site Status

Clinical Center of Serbia

Belgrade, , Serbia

Site Status

Clinical Hospital Center ''Bezanijska Kosa''

Belgrade, , Serbia

Site Status

Institute for Pulmonary Diseases of Vojvodina

Kamenitz, , Serbia

Site Status

National University Hospital

Singapore, , Singapore

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National Cancer Centre

Singapore, , Singapore

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Chungbuk National University Hospital

Cheongju-si, , South Korea

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National Cancer Center

Gyeonggi-do, , South Korea

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Seoul National University Bundang Hospital

Gyeonggi-do, , South Korea

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Samsung Changwon Hospital

Gyeongsangnam-do, , South Korea

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Seoul National University Hospital

Seoul, , South Korea

Site Status

Severance Hospital, Yonsei University Health System

Seoul, , South Korea

Site Status

Asan Medical Center

Seoul, , South Korea

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Samsung Medical Center

Seoul, , South Korea

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Seoul St Mary's Hospital

Seoul, , South Korea

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Ulsan University Hosiptal

Ulsan, , South Korea

Site Status

Vall d?Hebron Institute of Oncology (VHIO), Barcelona

Barcelona, , Spain

Site Status

Hospital Clinic Barcelona

Barcelona, , Spain

Site Status

Fundacion Jimenez Diaz

Madrid, , Spain

Site Status

Hospital Universitario La Paz

Madrid, , Spain

Site Status

Hospital Clinico Universitario Virgen de la Victoria

Málaga, , Spain

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Hospital Universitario Virgen del Rocio

Seville, , Spain

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Hospital Clínico Universitario de Valencia

Valencia, , Spain

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Hospital Clinico Universitario Lozano Blesa

Zaragoza, , Spain

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CHUV

Lausanne, , Switzerland

Site Status

UniversitätsSpital Zürich

Zurich, , Switzerland

Site Status

National Cheng-Kung University Hospital

Tainan City, , Taiwan

Site Status

Taipei Veterans General Hospital

Taipei, , Taiwan

Site Status

Chang-Gung Medical Foundation, Linkou Branch

Taoyuan District, , Taiwan

Site Status

National Taiwan University Hospital

Zhongzheng Dist., , Taiwan

Site Status

Adana Baskent University Hospital

Adana, , Turkey (Türkiye)

Site Status

Ankara University Medical Faculty

Ankara, , Turkey (Türkiye)

Site Status

Gazi University Medical Faculty

Ankara, , Turkey (Türkiye)

Site Status

Istanbul University Cerrahpa?a-Cerrahpa?a Medical Faculty

Istanbul, , Turkey (Türkiye)

Site Status

Medipol University Medical Faculty

Istanbul, , Turkey (Türkiye)

Site Status

?zmir Medical Park

Izm?r, , Turkey (Türkiye)

Site Status

NHS Lothian - Western General Hospital

Edinburgh, , United Kingdom

Site Status

Guys and St Thomas Hospital

London, , United Kingdom

Site Status

Christie Foundation Trust

Manchester, , United Kingdom

Site Status

Royal Cornwall Hospital

Truro, , United Kingdom

Site Status

Countries

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United States Australia Austria Belgium Brazil Czechia Germany Greece Hungary Italy Japan Netherlands New Zealand Poland Russia Serbia Singapore South Korea Spain Switzerland Taiwan Turkey (Türkiye) United Kingdom

References

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Rudin CM, Liu SV, Soo RA, Lu S, Hong MH, Lee JS, Bryl M, Dumoulin DW, Rittmeyer A, Chiu CH, Ozyilkan O, Johnson M, Navarro A, Novello S, Ozawa Y, Tam SH, Patil NS, Wen X, Huang M, Hoang T, Meng R, Reck M. SKYSCRAPER-02: Tiragolumab in Combination With Atezolizumab Plus Chemotherapy in Untreated Extensive-Stage Small-Cell Lung Cancer. J Clin Oncol. 2024 Jan 20;42(3):324-335. doi: 10.1200/JCO.23.01363. Epub 2023 Nov 17.

Reference Type DERIVED
PMID: 37976444 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2019-003301-97

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

GO41767

Identifier Type: -

Identifier Source: org_study_id

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