ALXN1830 in Patients With Warm Autoimmune Hemolytic Anemia

NCT ID: NCT04256148

Last Updated: 2020-07-13

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

WITHDRAWN

Clinical Phase

PHASE2

Study Classification

INTERVENTIONAL

Study Start Date

2021-07-31

Study Completion Date

2023-04-30

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

The main objective of the study is to evaluate the safety and efficacy of ALXN1830 compared to placebo in adult participants with warm autoimmune hemolytic anemia (WAIHA).

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

This study will consist of a 4-week Screening period, 13-week Primary Treatment period, and optional Extended Treatment period (up to 2 years).

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Warm Autoimmune Hemolytic Anemia

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Participants randomized in 1:1:1:1 ratio to 1 of 4 study arms.
Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators
Double-blind

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

ALXN1830 Dosing Regimen 1

Group Type EXPERIMENTAL

ALXN1830

Intervention Type BIOLOGICAL

Administered via intravenous (IV) infusion

ALXN1830 Dosing Regimen 2

Group Type EXPERIMENTAL

ALXN1830

Intervention Type BIOLOGICAL

Administered via intravenous (IV) infusion

ALXN1830 Dosing Regimen 3

Group Type EXPERIMENTAL

ALXN1830

Intervention Type BIOLOGICAL

Administered via intravenous (IV) infusion

Placebo

Group Type ACTIVE_COMPARATOR

Placebo

Intervention Type OTHER

Matching placebo (sterile liquid diluent) administered via IV infusion

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

ALXN1830

Administered via intravenous (IV) infusion

Intervention Type BIOLOGICAL

Placebo

Matching placebo (sterile liquid diluent) administered via IV infusion

Intervention Type OTHER

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

SYNT001

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Primary or secondary WAIHA, diagnosed at least 6 weeks prior to Screening
* Failed or not tolerated at least 1 prior WAIHA treatment regimen, for example, corticosteroids, rituximab, azathioprine, cyclophosphamide, cyclosporine, mycophenolate mofetil, danazol, or vincristine
* Hemoglobin \< 10 g/dL and ≥ 6 g/dL
* Positive direct antiglobulin test (Coombs) (IgG positive, complement C3 \[C3\] positive or negative)
* Evidence of active hemolysis including any of the following: a) Lactate dehydrogenase (LDH) \> upper limit of normal (ULN), b) Haptoglobin \< lower limit of normal (LLN), c) Indirect bilirubin \> ULN
* Total IgG \> 500 mg/dL

Exclusion Criteria

* Human immunodeficiency virus (HIV) infection (positive HIV-1 or HIV-2 antibody test)
* Positive hepatitis B surface antigen (HBsAg) or hepatitis C antibody test
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Alexion Pharmaceuticals, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Alexion Study Site

Whittier, California, United States

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

ALXN1830-WAI-201

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.

Safety and Efficacy of Ruxolitinib for COVID-19
NCT04348071 WITHDRAWN PHASE2/PHASE3