Study Results
The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.
Basic Information
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SUSPENDED
60 participants
OBSERVATIONAL
2020-08-06
2026-02-28
Brief Summary
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Detailed Description
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Conditions
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Study Design
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COHORT
PROSPECTIVE
Study Groups
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MNGIE Patients
Patients with mitochondrial neurogastrointestinal encephalomyopathy
Non-interventional
Non-interventional natural history study
Interventions
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Non-interventional
Non-interventional natural history study
Eligibility Criteria
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Inclusion Criteria
Exclusion Criteria
5 Years
ALL
No
Sponsors
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Entrada Therapeutics, Inc.
INDUSTRY
Responsible Party
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Principal Investigators
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Michio Hirano, MD
Role: STUDY_CHAIR
Columbia University
Locations
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Children's Hospital Colorado
Aurora, Colorado, United States
Columbia University
New York, New York, United States
Baylor St Luke's Medical Center and Texas Children's Hospital at Baylor College of Medicine
Houston, Texas, United States
Ege University Medical Faculty; Department of Pediatrics
Bornova, İzmir, Turkey (Türkiye)
Gazi Üniversitesi Tıp Fakültesi
Ankara, , Turkey (Türkiye)
Countries
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Other Identifiers
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ET-NHS-901
Identifier Type: -
Identifier Source: org_study_id
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