Trial Outcomes & Findings for PRevention Using EPA Against coloREctal Cancer (NCT NCT04216251)

NCT ID: NCT04216251

Last Updated: 2024-05-03

Results Overview

Measured using the extraction of fatty acid with gas chromatography-mass spectrometry from the biopsy tissue.

Recruitment status

COMPLETED

Study phase

PHASE1/PHASE2

Target enrollment

81 participants

Primary outcome timeframe

8-12 weeks

Results posted on

2024-05-03

Participant Flow

Patients who meet the inclusion criteria will be identified through investigators during their routine clinical practice, supplemented by a periodic query of the MGH endoscopy and pathology databases. Potentially eligible participants are approached by letter from their treating physician. Two weeks after receiving the letter, study staff will contact eligible parties and screen for eligibility via phone interview. Enrollment began in December 2020 and ended in September 2022.

Participant milestones

Participant milestones
Measure
AMR101
The first dose of the study medication will be given to patients after the initial flexible sigmoidoscopy. Participants will be expected to take 4 0.5 gram capsules orally, twice daily (daily dose of 4 grams) for a minimum of 8 weeks and maximum of 12 weeks
Overall Study
STARTED
81
Overall Study
COMPLETED
73
Overall Study
NOT COMPLETED
8

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

PRevention Using EPA Against coloREctal Cancer

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
AMR101
n=81 Participants
The first dose of the study medication will be given to patients after the initial flexible sigmoidoscopy. Participants will be expected to take 4 0.5 gram capsules orally, twice daily (daily dose of 4 grams) for a minimum of 8 weeks and maximum of 12 weeks.
Age, Categorical
<=18 years
0 Participants
n=93 Participants
Age, Categorical
Between 18 and 65 years
49 Participants
n=93 Participants
Age, Categorical
>=65 years
32 Participants
n=93 Participants
Age, Continuous
61.95 years
STANDARD_DEVIATION 8.91 • n=93 Participants
Sex: Female, Male
Female
26 Participants
n=93 Participants
Sex: Female, Male
Male
55 Participants
n=93 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
5 Participants
n=93 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
75 Participants
n=93 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
1 Participants
n=93 Participants
Race (NIH/OMB)
American Indian or Alaska Native
1 Participants
n=93 Participants
Race (NIH/OMB)
Asian
4 Participants
n=93 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=93 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=93 Participants
Race (NIH/OMB)
White
76 Participants
n=93 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=93 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=93 Participants

PRIMARY outcome

Timeframe: 8-12 weeks

Measured using the extraction of fatty acid with gas chromatography-mass spectrometry from the biopsy tissue.

Outcome measures

Outcome measures
Measure
Pre-treatment
n=59 Participants
This is the baseline (e.g., pre-treatment) measurement.
Post-treatment
n=59 Participants
This is the post-treatment measurement.
Change in the Marine Omega-3 Polyunsaturated Fatty Acid (MO3PUFA) Composition in Colorectal Tissues as a Result of the AMR101 Treatment.
0.54 percentage of total fatty acids
Standard Deviation 0.33
2.95 percentage of total fatty acids
Standard Deviation 1.65

SECONDARY outcome

Timeframe: 8-12 weeks 8-12 weeks 8-12 weeks 8-12 weeks

Population: This is after quality control filtering and excluding participants who had missing pre- or post-treatment samples.

Measured using shotgun metagenomic sequencing of microbial DNA on pre- and post-treatment stool samples. The reported results represent the Shannon Diversity Index, which is a quantitative measure that reflects how many different bacterial species there are in a sample. The index's values range from 0 to 5, but usually range from 1.5 to 3.5. The greater the index, the more diverse the gut microbiota. A negative change indicates a decrease in diversity and a positive change indicates an increase in diversity. We used the vegan R package to conduct the analysis.

Outcome measures

Outcome measures
Measure
Pre-treatment
n=67 Participants
This is the baseline (e.g., pre-treatment) measurement.
Post-treatment
n=67 Participants
This is the post-treatment measurement.
Change in the Gut Microbiome Composition
3.082 Shannon diversity index
Interval 2.927 to 3.266
3.133 Shannon diversity index
Interval 2.968 to 3.281

SECONDARY outcome

Timeframe: 8-12 weeks

Population: This is after quality control filtering and excluding participants who had missing pre- or post-treatment samples.

Butyrate is the metabolite of our most interest for the current study, based on the prior data suggesting that marine omega-3 fatty acid may increase the production of butyrate by bacterial fermentation of dietary fiber. The metabolites were measured by the non-targeted global metabolomic panel. The measurement represents the abundance (assessed as weight percentage of density) of a metabolite after total-signal normalization to account for varying water weight across stool samples.

Outcome measures

Outcome measures
Measure
Pre-treatment
n=64 Participants
This is the baseline (e.g., pre-treatment) measurement.
Post-treatment
n=64 Participants
This is the post-treatment measurement.
Change in Fecal Metabolite Levels (Butyrate)
0.64 Weight percentage of butyrate density
Interval 0.42 to 0.81
0.63 Weight percentage of butyrate density
Interval 0.39 to 0.76

Adverse Events

AMR101

Serious events: 1 serious events
Other events: 20 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
AMR101
n=81 participants at risk
The first dose of the study medication will be given to patients after the initial flexible sigmoidoscopy. Participants will be expected to take 4 0.5 gram capsules orally, twice daily (daily dose of 4 grams) for a minimum of 8 weeks and maximum of 12 weeks
Vascular disorders
Ischemic right foot with thrombosis of right external iliac artery stent and common femoral artery
1.2%
1/81 • 3 months

Other adverse events

Other adverse events
Measure
AMR101
n=81 participants at risk
The first dose of the study medication will be given to patients after the initial flexible sigmoidoscopy. Participants will be expected to take 4 0.5 gram capsules orally, twice daily (daily dose of 4 grams) for a minimum of 8 weeks and maximum of 12 weeks
Gastrointestinal disorders
GI Upset (i.e. nausea/gas/diarrhea/constipation/stomach ache/loss of appetite)
14.8%
12/81 • 3 months
Infections and infestations
COVID and Flu-like symptoms (congestion, chills, fever, body ache, headache)
4.9%
4/81 • 3 months
Respiratory, thoracic and mediastinal disorders
Chest pain
2.5%
2/81 • 3 months
Skin and subcutaneous tissue disorders
Skin issues (acne, hyperpigmentation)
2.5%
2/81 • 3 months
Musculoskeletal and connective tissue disorders
Pain (joint pain, muscle aches)
3.7%
3/81 • 3 months
Gastrointestinal disorders
Esophagitis
1.2%
1/81 • 3 months

Additional Information

Andrew T. Chan, MD, MPH

Massachusetts General Hspital

Phone: 617-726-3212

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place