Study of Aldafermin (NGM282) in Subjects With Compensated Cirrhosis (ALPINE 4)

NCT ID: NCT04210245

Last Updated: 2025-03-26

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

160 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-03-23

Study Completion Date

2023-02-23

Brief Summary

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A multi-center evaluation of aldafermin in a randomized, double-blind, placebo-controlled study in subjects with compensated cirrhosis.

Detailed Description

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The study will compare multiple doses of aldafermin against placebo in a compensated NASH cirrhosis population for 48 weeks of treatment.

Conditions

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Compensated Cirrhosis Nonalcoholic Steatohepatitis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Daily 0.3 mg dose

Administered by subcutaneous injection

Group Type EXPERIMENTAL

aldafermin

Intervention Type BIOLOGICAL

aldafermin

Daily 1 mg dose

Administered by subcutaneous injection

Group Type EXPERIMENTAL

aldafermin

Intervention Type BIOLOGICAL

aldafermin

Daily 3 mg dose

Administered by subcutaneous injection

Group Type EXPERIMENTAL

aldafermin

Intervention Type BIOLOGICAL

aldafermin

Placebo

Administered by subcutaneous injection

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

Placebo for aldafermin

Interventions

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aldafermin

aldafermin

Intervention Type BIOLOGICAL

Placebo

Placebo for aldafermin

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

1. Liver biopsy consistent with NASH cirrhosis.
2. Compensated cirrhosis due to NASH.

Exclusion Criteria

1. Other causes of liver disease including but not limited to alcoholic liver disease, hepatitis B, hepatitis C, autoimmune disorders, primary biliary cirrhosis, drug-induced hepatotoxicity, Wilson's disease, hemochromatosis, and alpha-1-anti-trypsin definition based on medical history and/or centralized read of liver histology.
2. Evidence of drug induced steatohepatitis secondary to amiodarone, corticosteroids, estrogens, methotrexate, tetracycline, or other medications known to cause hepatic steatosis.
3. History of hepatic decompensation including variceal bleeding, ascites, or hepatic encephalopathy.
4. Model of end stage liver disease (MELD) score \>12.
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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NGM Biopharmaceuticals, Inc

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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NGM Study Director

Role: STUDY_DIRECTOR

NGM Biopharmaceuticals

Locations

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NGM Clinical Study Site

Glendale, Arizona, United States

Site Status

NGM Clinical Study Site 413

Tucson, Arizona, United States

Site Status

NGM Clinical Study Site 415

Tucson, Arizona, United States

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NGM Clinical Study Site

North Little Rock, Arkansas, United States

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NGM Clinical Study Site

Fresno, California, United States

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NGM Clinical Study Site

La Jolla, California, United States

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NGM Clinical Study Site

Los Angeles, California, United States

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NGM Clinical Study Site

Panorama City, California, United States

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NGM Clinical Study Site

Rialto, California, United States

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NGM Clinical Study Site

Boca Raton, Florida, United States

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NGM Clinical Study Site

Miami, Florida, United States

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NGM Clinical Study Site

Marietta, Georgia, United States

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NGM Clinical Study Site

Chicago, Illinois, United States

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NGM Clinical Study Site

Chicago, Illinois, United States

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NGM Clinical Study Site

Baltimore, Maryland, United States

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NGM Clinical Study Site

Boston, Massachusetts, United States

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NGM Clinical Study Site

Boston, Massachusetts, United States

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NGM Clinical Study Site

Flowood, Mississippi, United States

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NGM Clinical Study Site 488

Jackson, Mississippi, United States

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NGM Clinical Study Site

Kansas City, Missouri, United States

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NGM Clinical Study Site

Durham, North Carolina, United States

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NGM Clinical Study Site

Germantown, Tennessee, United States

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NGM Clinical Study Site

Austin, Texas, United States

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NGM Clinical Study Site

Edinburg, Texas, United States

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NGM Clinical Study Site

Edinburg, Texas, United States

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NGM Clinical Study Site 481

Houston, Texas, United States

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NGM Clinical Study Site

San Antonio, Texas, United States

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NGM Clinical Study Site

San Antonio, Texas, United States

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NGM Clinical Study Site

Richmond, Virginia, United States

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NGM Clinical Study Site

Richmond, Virginia, United States

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NGM Clinical Study Site 482

Seattle, Washington, United States

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NGM Clinical Study Site

Camperdown, New South Wales, Australia

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NGM Clinical Study Site

Westmead, New South Wales, Australia

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NGM Clinical Study Site

Adelaide, South Australia, Australia

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NGM Clinical Study Site

Bedford Park, South Australia, Australia

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NGM Clinical Study Site

Clayton, Victoria, Australia

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NGM Clinical Study Site

Fitzroy, Victoria, Australia

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NGM Clinical Study Site

Heidelberg, Victoria, Australia

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NGM Clinical Study Site

Melbourne, Victoria, Australia

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NGM Clinical Study Site

Brussels, , Belgium

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NGM Clinical Study Site

Paris, , France

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NGM Clinical Study Site

Pessac, , France

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NGM Clinical Study Site

Leipzig, , Germany

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NGM Clinical Study Site

Leipzig, , Germany

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NGM Clinical Study Site

Shatin, , Hong Kong

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NGM Clinical Study Site 444

Wroclaw, , Poland

Site Status

NGM Clinical Study Site 446

Wroclaw, , Poland

Site Status

NGM Clinical Study Site

San Juan, , Puerto Rico

Site Status

NGM Clinical Study Site 466

London, , United Kingdom

Site Status

Countries

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United States Australia Belgium France Germany Hong Kong Poland Puerto Rico United Kingdom

References

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Rinella ME, Lieu HD, Kowdley KV, Goodman ZD, Alkhouri N, Lawitz E, Ratziu V, Abdelmalek MF, Wong VW, Younes ZH, Sheikh AM, Brannan D, Freilich B, Membreno F, Sinclair M, Melchor-Khan L, Sanyal AJ, Ling L, Harrison SA. A randomized, double-blind, placebo-controlled trial of aldafermin in patients with NASH and compensated cirrhosis. Hepatology. 2024 Mar 1;79(3):674-689. doi: 10.1097/HEP.0000000000000607. Epub 2023 Sep 21.

Reference Type DERIVED
PMID: 37732990 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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282-CC-207

Identifier Type: -

Identifier Source: org_study_id

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