Platinum-Based Chemotherapy With/Without INCMGA00012, an Anti-PD-1 Antibody, in Non-Small Cell Lung Cancer

NCT ID: NCT04205812

Last Updated: 2025-09-25

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

583 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-09-11

Study Completion Date

2026-08-28

Brief Summary

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The purpose of this study is to assess the efficacy and safety of platinum-based chemotherapy with or without INCMGA00012 in participants with metastatic squamous and nonsquamous non-small cell lung cancer (NSCLC).

Detailed Description

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Conditions

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Metastatic Squamous Non-Small Cell Lung Cancer Metastatic Nonsquamous Non-Small Cell Lung Cancer

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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INCMGA00012 + chemotherapy (nonsquamous NSCLC)

INCMGA00012 with pemetrexed + cisplatin OR carboplatin followed by INCMGA00012 plus pemetrexed until progression.

Group Type EXPERIMENTAL

Retifanlimab

Intervention Type DRUG

INCMGA00012 administered intravenously every 3 weeks on Day 1 of each cycle for up to 35 cycles.

Pemetrexed

Intervention Type DRUG

Pemetrexed administered intravenously every 3 weeks on Day 1 of each cycle.

Cisplatin

Intervention Type DRUG

Cisplatin administered intravenously every 3 weeks on Day 1 of each cycle for 4 cycles.

Carboplatin

Intervention Type DRUG

Carboplatin administered intravenously every 3 weeks on Day 1 of each cycle for 4 cycles.

Placebo + chemotherapy (nonsquamous NSCLC)

Placebo with pemetrexed + cisplatin OR carboplatin followed by placebo plus pemetrexed until progression. Participants assigned to placebo + chemotherapy will have the option of receiving open-label monotherapy INCMGA00012 in a crossover period after documentation of progressive disease.

Group Type ACTIVE_COMPARATOR

Placebo

Intervention Type DRUG

Placebo administered intravenously every 3 weeks on Day 1 of each cycle for up to 35 cycles.

Pemetrexed

Intervention Type DRUG

Pemetrexed administered intravenously every 3 weeks on Day 1 of each cycle.

Cisplatin

Intervention Type DRUG

Cisplatin administered intravenously every 3 weeks on Day 1 of each cycle for 4 cycles.

Carboplatin

Intervention Type DRUG

Carboplatin administered intravenously every 3 weeks on Day 1 of each cycle for 4 cycles.

INCMGA00012 + chemotherapy (squamous NSCLC)

INCMGA00012 with carboplatin + paclitaxel OR nab-paclitaxel followed by INCMGA00012 until progression.

Group Type EXPERIMENTAL

Retifanlimab

Intervention Type DRUG

INCMGA00012 administered intravenously every 3 weeks on Day 1 of each cycle for up to 35 cycles.

Carboplatin

Intervention Type DRUG

Carboplatin administered intravenously every 3 weeks on Day 1 of each cycle for 4 cycles.

Paclitaxel

Intervention Type DRUG

Paclitaxel administered intravenously every 3 weeks on Day 1 of each cycle for 4 cycles.

nab-Paclitaxel

Intervention Type DRUG

nab-Paclitaxel administered intravenously every 3 weeks on Days 1, 8, and 15 of each cycle for 4 cycles.

Placebo + chemotherapy (squamous NSCLC)

Placebo with carboplatin + paclitaxel OR nab-paclitaxel followed by placebo until progression. Participants assigned to placebo + chemotherapy will have the option of receiving open-label monotherapy INCMGA00012 in a crossover period after documentation of progressive disease.

Group Type ACTIVE_COMPARATOR

Placebo

Intervention Type DRUG

Placebo administered intravenously every 3 weeks on Day 1 of each cycle for up to 35 cycles.

Carboplatin

Intervention Type DRUG

Carboplatin administered intravenously every 3 weeks on Day 1 of each cycle for 4 cycles.

Paclitaxel

Intervention Type DRUG

Paclitaxel administered intravenously every 3 weeks on Day 1 of each cycle for 4 cycles.

nab-Paclitaxel

Intervention Type DRUG

nab-Paclitaxel administered intravenously every 3 weeks on Days 1, 8, and 15 of each cycle for 4 cycles.

Interventions

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Retifanlimab

INCMGA00012 administered intravenously every 3 weeks on Day 1 of each cycle for up to 35 cycles.

Intervention Type DRUG

Placebo

Placebo administered intravenously every 3 weeks on Day 1 of each cycle for up to 35 cycles.

Intervention Type DRUG

Pemetrexed

Pemetrexed administered intravenously every 3 weeks on Day 1 of each cycle.

Intervention Type DRUG

Cisplatin

Cisplatin administered intravenously every 3 weeks on Day 1 of each cycle for 4 cycles.

Intervention Type DRUG

Carboplatin

Carboplatin administered intravenously every 3 weeks on Day 1 of each cycle for 4 cycles.

Intervention Type DRUG

Paclitaxel

Paclitaxel administered intravenously every 3 weeks on Day 1 of each cycle for 4 cycles.

Intervention Type DRUG

nab-Paclitaxel

nab-Paclitaxel administered intravenously every 3 weeks on Days 1, 8, and 15 of each cycle for 4 cycles.

Intervention Type DRUG

Other Intervention Names

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INCMGA00012

Eligibility Criteria

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Inclusion Criteria

* Histologically or cytologically confirmed NSCLC (either nonsquamous or squamous) that is Stage IV (AJCC v8).
* No prior systemic treatment for the advanced/metastatic NSCLC
* Able to provide a formalin-fixed archival tumor tissue sample during screening, or a fresh tumor biopsy
* Measurable disease per RECIST v1.1.
* Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1.
* Life expectancy of at least 3 months.
* Willingness to avoid pregnancy or fathering children.
* Adequate organ function as indicated by protocol-specified laboratory values. - Has been fully vaccinated against SARS-CoV-2 or is willing and able to be fully vaccinated against SARS-CoV-2 during the study by starting the vaccination process during screening.

Exclusion Criteria

* Clinically significant cardiac disease within 6 months of start of study treatment.
* Any major surgery within 3 weeks of the first dose of study treatment.
* Thoracic radiation therapy of \> 30 Gy within 6 months of the first dose of study treatment.
* History of peripheral neuropathy ≥ Grade 2 CTCAE v5 for participants who may receive cisplatin, paclitaxel, or nab-paclitaxel.
* Untreated central nervous system metastases and/or carcinomatous meningitis.
* Evidence or history of interstitial lung disease or noninfectious pneumonitis that required systemic steroids.
* Active infection requiring systemic therapy or active tuberculosis. Note: If required by country or local regulations to be tested for COVID-19 during screening, a participant should be excluded if they have a positive test result for SARS CoV-2 infection until both the retesting result is negative and clinical recovery is obtained.
* Superficial bladder cancer, squamous cell carcinoma of the skin, in situ cervical cancer, or other in situ cancers.
* Has contraindications to chemotherapy agents used in the study.
* Has an active autoimmune disease that has required systemic treatment in past 2 years.
* Is receiving systemic antibiotics or steroid therapy ≤ 7 days prior to the first dose of study treatment.
* Has received a live vaccine within 30 days before the first dose of study treatment (and until 90 days after last dose of study drug).

Note: While based on approved SARS-CoV-2 vaccines available worldwide, many vaccines are not live (mRNA and adenovirus vaccines do not contain live virus), if a live vaccine against SARS-CoV-2 is the only available option, prior consultation with the medical monitor should be obtained.

• Has known active HBV or HCV (testing must be performed to determine eligibility)
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Incyte Corporation

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Incyte Medical Monitor

Role: STUDY_DIRECTOR

Incyte Corporation

Locations

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Pacific Cancer Medical Center

Anaheim, California, United States

Site Status

Innovative Clinical Research Institute

Whittier, California, United States

Site Status

Reading Hospital and Medical Center

Reading, Pennsylvania, United States

Site Status

Fundacao Pio Xii Hospital de Cancer de Barretos

Barretos, , Brazil

Site Status

Incan - Instituto Do Cancer - Hospital Pompeia

Caxias do Sul, , Brazil

Site Status

Centro Regional Integrado de Oncologia

Fortaleza, , Brazil

Site Status

Oncosite - Centro de Pesquisa Clinica E Oncologia

Ijuí, , Brazil

Site Status

Clinica de Neoplasias Litoral Ltda

Itajaí, , Brazil

Site Status

Hospital Do Cancer de Londrina

Londrina, , Brazil

Site Status

Instituto Mederi de Pesquisa E Saude

Passo Fundo, , Brazil

Site Status

Hgb - Hospital Giovanni Battista - Mae de Deus Center

Porto Alegre, , Brazil

Site Status

Inca - Instituto Nacional de Cancer

Rio de Janeiro, , Brazil

Site Status

Sao Camilo Oncologia

S?O Paulo, , Brazil

Site Status

Cepho - Centro de Estudos E Pesquisas de Hematologia E Oncologia

Santo André, , Brazil

Site Status

Fundacao Faculdade Regional de Medicina de Sao Jose Do Rio Preto

São José, , Brazil

Site Status

Mc Women'S Health-Nadezhda Eood

Sofia, , Bulgaria

Site Status

Acibadem Cityclinica Mhat Tokuda

Sofia, , Bulgaria

Site Status

Umhat Sv. Ivan Rilski Ead

Sofia, , Bulgaria

Site Status

Mhat Serdika Eood

Sofia, , Bulgaria

Site Status

Multiprofile Hospital For Active Treatment Central Onco Hospital Ood

Sofia, , Bulgaria

Site Status

Shatod Dr Marko Marko - Varna Ltd

Varna, , Bulgaria

Site Status

Hunan Cancer Hospital

Changsha, , China

Site Status

The First Affiliated Hospital Sun Yat-Sen University

Guangzhou, , China

Site Status

Sir Run Run Shaw Hospital Zhejiang University School of Medicine

Hangzhou, , China

Site Status

Hangzhou Cancer Hospital

Hangzhou, , China

Site Status

The First Affiliated Hospital of Zhejiang University

Hangzhou, , China

Site Status

Zhejiang Cancer Hospital

Hangzhou, , China

Site Status

Harbin Medical University Cancer Hospital

Harbin, , China

Site Status

University of Science and Technology of China-First Affiliated Hospital (Anhui Provincial Hospital)

Hefei, , China

Site Status

The Second Hospital of Anhui Medical University

Hefei, , China

Site Status

Jinan Central Hospital

Jinan, , China

Site Status

Linyi Cancer Hospital

Linyi, , China

Site Status

The Second Affiliated Hospital of Nanchang University

Nanchang, , China

Site Status

The First Affiliated Hospital of Guangxi Medical University

Nanning, , China

Site Status

Shanghai Chest Hospital

Shanghai, , China

Site Status

General Hospital of Tianjin

Tianjing, , China

Site Status

The Affiliated Cancer Hospital of Xinjiang Medical University

Ürümqi, , China

Site Status

Henan Cancer Hostipal

Zhengzhou, , China

Site Status

Henan Provincial Peoples Hospital

Zhengzhou, , China

Site Status

The First Affiliated Hospital of Zhengzhou University

Zhengzhou, , China

Site Status

University Hospital Hradec Kralove

Hradec Králové, , Czechia

Site Status

Fakultni Nemocnice Olomouc

Olomouc, , Czechia

Site Status

Nemocnice Agel Ostrava - Vitkovice A.S

Ostrava - Vitkovice, , Czechia

Site Status

Fakultni Nemocnice V Motole

Prague, , Czechia

Site Status

High Technology Hospital Medcenter

Batumi, , Georgia

Site Status

Jsc Evex Hospitals

Kutaisi, , Georgia

Site Status

Archangel St. Michael Multi Profile Clinical Hospital

Tbilisi, , Georgia

Site Status

Israel-Georgian Medical Research Clinic Helsicore

Tbilisi, , Georgia

Site Status

New Hospitals

Tbilisi, , Georgia

Site Status

Medulla Chemotherapy and Immunotherapy Clinic

Tbilisi, , Georgia

Site Status

Tbilisi State Medical University First University Clinic

Tbilisi, , Georgia

Site Status

High Technology Medical Center, University Clinic

Tbilisi, , Georgia

Site Status

Institute of Clinical Oncology Ltd

Tbilisi, , Georgia

Site Status

Cancer Research Center Ltd

Tbilisi, , Georgia

Site Status

Orszagos Koranyi Tbc Es Pulmonological Intezet

Budapest, , Hungary

Site Status

Bacs Kiskun Megyei Oktatokorhaz

Kecskemét, , Hungary

Site Status

Advanced Medical and Dental Institute Husm

Kepala Batas, , Malaysia

Site Status

University Malaya Medical Centre

Kuala Lumpur, , Malaysia

Site Status

Hospital Tengku Ampuan Afzan

Kuantan, , Malaysia

Site Status

Sarawak General Hospital

Kuching, , Malaysia

Site Status

Beacon Hospital Sdn Bhd

Petaling Jaya, , Malaysia

Site Status

Hospital Pulau Pinang

Pulau Pinang, , Malaysia

Site Status

Institut Kanser Negara - National Cancer Institute

Putrajaya, , Malaysia

Site Status

Cebu Doctors University Hospital

Cebu City, , Philippines

Site Status

Asian Hospital and Medical Center

City of Muntinlupa, , Philippines

Site Status

Davao Doctors Hospital

Davao City, , Philippines

Site Status

West Visayas State University Medical Center

Iloilo City, , Philippines

Site Status

Makati Medical Center

Makati, , Philippines

Site Status

Makati Medical Center

Makati City, , Philippines

Site Status

Philippine General Hospital

Manila, , Philippines

Site Status

The Medical City

Pasig, , Philippines

Site Status

St. Lukes Medical Center

Quezon City, , Philippines

Site Status

Ko-Med Centra Kliniczne Biala Podlaska

Biała Podlaska, , Poland

Site Status

Przychodnia Lekarska Komed

Konin, , Poland

Site Status

Centrum Medyczne Plejady

Krakow, , Poland

Site Status

Centrum Terapii Wspolczesnej J.M. Jasnorzewska Sp. Komandytowo-Akcyjna

Lodz, , Poland

Site Status

Przychodnia Med-Polonia Sp. Z O.O.

Poznan, , Poland

Site Status

S.C Oncopremium Team S.R.L

Baia Mare, , Romania

Site Status

Institutul Oncologic Prof. Dr. Ion Chiricuta Cluj-Napoca

Cluj-Napoca, , Romania

Site Status

Spitalul Clinic Militar de Urgenta Dr. Constantin Papilian Cluj-Napoca

Cluj-Napoca, , Romania

Site Status

Spitalul Clinic Judetean de Urgenta Constanta

Constanța, , Romania

Site Status

S C Oncocenter Oncologie Medicala S R L

Timișoara, , Romania

Site Status

Oncomed Srl

Timișoara, , Romania

Site Status

Sbih of Arkhangelsk Region Arkhangelsk Clinical Oncological Dispensary

Arkhangelsk, , Russia

Site Status

Rbih Kursk Regional Clinical Oncology Dispensary of Kursk Region Healthcare Committee

Kursk, , Russia

Site Status

Federal State Institution "Russian Cancer Research Center Named After N.N. Blokhin" Rams

Moscow, , Russia

Site Status

Llc Tonus

Nizniy Novgorod, , Russia

Site Status

Sbhi of Novosibirsk Region Novosibirsk Regional Oncological Dispensary

Novosibirsk, , Russia

Site Status

Bhi of Omsk Region Clinical Oncology Dispensary

Omsk, , Russia

Site Status

Pavlov First Saint Petersburg State Medical University

Saint Petersburg, , Russia

Site Status

N.N. Petrov Research Institute of Oncology

Saint Petersburg, , Russia

Site Status

Sbhi Volgograd Regional Onclogy Dispensary

Volgograd, , Russia

Site Status

Clinical Center of Serbia

Belgrade, , Serbia

Site Status

Clinical Center Bezanijska Kosa

Belgrade, , Serbia

Site Status

Clinical Center of Serbia

Belgrade, , Serbia

Site Status

Oncomed-System

Belgrade, , Serbia

Site Status

Institute For Pulmonary Diseases of Vojvodina

Kamenitz, , Serbia

Site Status

Clinical Center Kragujevac

Kragujevac, , Serbia

Site Status

Cape Town Oncology Trials (Pty) Ltd

Cape Town, , South Africa

Site Status

Cancercare Rondebosch Oncology Centre

Cape Town, , South Africa

Site Status

Wits Clinical Research

Johannesburg, , South Africa

Site Status

Sandton Oncology Centre

Johannesburg, , South Africa

Site Status

University of Pretoria Oncology Department

Pretoria, , South Africa

Site Status

Mary Potter Oncology Centre

Pretoria, , South Africa

Site Status

Acibadem Adana Hospital

Adana, , Turkey (Türkiye)

Site Status

Adana Sehir Hastanesi

Adana, , Turkey (Türkiye)

Site Status

Hacettepe Universitesi Tip Fakultesi Hastanesi

Ankara, , Turkey (Türkiye)

Site Status

Dr. Abdurrahman Yurtaslan Onkology Teaching and Research Hospital

Ankara, , Turkey (Türkiye)

Site Status

Memorial Ankara Hospital

Ankara, , Turkey (Türkiye)

Site Status

Yildirim Beyazit University Ankara Ataturk Training and Research Hospital

Ankara, , Turkey (Türkiye)

Site Status

Memorial Antalya Hastanesi

Antalya, , Turkey (Türkiye)

Site Status

Trakya Universitesi Tip Fakultesi

Edirne, , Turkey (Türkiye)

Site Status

Gaziantep University Gaziantep Oncology Hospital

Gaziantep, , Turkey (Türkiye)

Site Status

Istanbul University Cerrahpasa - Cerrahpasa Medical Faculty

Istanbul, , Turkey (Türkiye)

Site Status

Bakirkoy Dr Sadi Konuk Teaching and Research Hospital

Istanbul, , Turkey (Türkiye)

Site Status

Medipol University Medical Faculty

Istanbul, , Turkey (Türkiye)

Site Status

Izmir Medicalpark Hospital

Izmir, , Turkey (Türkiye)

Site Status

Necmettin Erbakan Universitesi Meram Tip Fakultesi Hastanesi

Konya, , Turkey (Türkiye)

Site Status

Inonu Universitesi Turgut Ozal Tip Merkezi

Malatya, , Turkey (Türkiye)

Site Status

Multifield Clinical Hospital No 4

Dnipro, , Ukraine

Site Status

Ci Carpathian Clinical Oncological Center

Ivano-Frankivsk, , Ukraine

Site Status

Communal Non-Profit Enterprise Regional Center of Oncology

Kharkiv, , Ukraine

Site Status

V.T.Zaycev Institute of General and Urgent Surgery of National Academy Medical Sciences of Ukraine

Kharkiv, , Ukraine

Site Status

Kherson Regional Oncologic Dispensary

Kherson, , Ukraine

Site Status

Pp Ppc Acinus Medical and Diagnostic Centre

Kropyvnytskyi, , Ukraine

Site Status

Mi Kryviy Rih Center of Dnipropetrovsk Regional Council

Kryvyi Rih, , Ukraine

Site Status

Kyiv City Clinical Oncological Center

Kyiv, , Ukraine

Site Status

Medical Center Asklepion Llc

Kyiv, , Ukraine

Site Status

Ci of Krc Kyiv Regional Oncologic Dispensary

Kyiv, , Ukraine

Site Status

Volyn Regional Oncological Dispensary

Lutsk, , Ukraine

Site Status

Rmi Sumy Regional Clinical Oncology Dispensary

Sumy, , Ukraine

Site Status

Cne Ccch of Uzh Cc Oncological Center

Uzhhorod, , Ukraine

Site Status

Medical Center Oncolife Llc

Zaporizhzhia, , Ukraine

Site Status

Can Tho Oncology Hospital

Can Tho, , Vietnam

Site Status

103 Military Hospital

Hanoi, , Vietnam

Site Status

Bach Mai Hospital

Hanoi, , Vietnam

Site Status

Hanoi Oncology Hospital

Hanoi, , Vietnam

Site Status

National Cancer Hospital

Hanoi, , Vietnam

Site Status

National Lung Hospital

Hanoi, , Vietnam

Site Status

Hcmc Oncology Hospital

Ho Chi Minh City, , Vietnam

Site Status

Countries

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United States Brazil Bulgaria China Czechia Georgia Hungary Malaysia Philippines Poland Romania Russia Serbia South Africa Turkey (Türkiye) Ukraine Vietnam

References

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Lu S, Vynnychenko O, Kulyaba Y, Kuchava V, Ibrahim A, Moiseenko F, Arslan C, Nguyen DT, Petrovic M, Cicin I, Bibichadze K, Cil T, Shi J, Olmez OF, Gogishvili M, Artac M, Nguyen HG, Cornfeld M, Tian C, Munteanu MC, Sette CVM, Bondarenko I; POD1UM-304 Study Team. Retifanlimab versus placebo in combination with platinum-based chemotherapy in patients with first-line non-squamous or squamous metastatic non-small-cell lung cancer (POD1UM-304): a phase 3, multiregional, placebo-controlled, double-blind, randomised study. Lancet Respir Med. 2025 Sep 19:S2213-2600(25)00209-7. doi: 10.1016/S2213-2600(25)00209-7. Online ahead of print.

Reference Type DERIVED
PMID: 40983066 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2019-003372-39

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

2022-501987-16-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

INCMGA 0012-304

Identifier Type: -

Identifier Source: org_study_id

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