KEYMAKER-U01 Substudy 01A: Efficacy and Safety Study of Pembrolizumab (MK-3475) With or Without Chemotherapy When Used With Investigational Agents in Treatment-naïve Participants With Stage IV Non-small Cell Lung Cancer (NSCLC) (MK-3475-01A/KEYMAKER-U01A)

NCT ID: NCT04165070

Last Updated: 2025-11-10

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE1/PHASE2

Total Enrollment

450 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-12-19

Study Completion Date

2032-02-13

Brief Summary

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The purpose of this study is to assess the efficacy and safety of pembrolizumab (MK-3475) with or without chemotherapy in combination with vibostolimab (MK-7684), boserolimab (MK-5890), MK-4830, MK-0482, I-DXd, or HER3-DXd in treatment-naïve participants with advanced squamous or non-squamous NSCLC.

This study is one of the pembrolizumab substudies being conducted under one pembrolizumab umbrella master protocol (MK-3475-U01/KEYMAKER-U01).

Detailed Description

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The master screening protocol is MK-3475-U01 (KEYMAKER-U01) - NCT04165798

Conditions

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Carcinoma, Non-Small-Cell Lung

Keywords

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Programmed Cell Death-1 (PD1, PD-1) Programmed Death-Ligand 1 (PDL1, PD-L1)

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Only participants in Part A will be randomized.
Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Part A: Pembrolizumab+Vibostolimab+Carboplatin + Paclitaxel

On Day 1 of each 3-week cycle, participants with squamous NSCLC receive pembrolizumab 200 mg intravenously (IV) PLUS vibostolimab IV PLUS carboplatin Area Under the Concentration-Time Curve (AUC) 6 IV PLUS paclitaxel 200 mg/m\^2 IV in Cycles 1-4, followed by maintenance treatment of pembrolizumab 200 mg IV PLUS vibostolimab IV in Cycles 5-35 (total treatment duration: up to approximately 2 years).

Group Type EXPERIMENTAL

Pembrolizumab

Intervention Type BIOLOGICAL

IV infusion

Carboplatin

Intervention Type DRUG

IV infusion

Paclitaxel

Intervention Type DRUG

IV infusion

Vibostolimab

Intervention Type BIOLOGICAL

IV infusion

Part A: Pembrolizumab+Vibostolimab+Carboplatin + Pemetrexed

On Day 1 of each 3-week cycle, participants with nonsquamous NSCLC receive pembrolizumab 200 mg IV PLUS vibostolimab IV PLUS carboplatin AUC 5 IV PLUS pemetrexed 500 mg/m\^2 IV in Cycles 1-4, followed by maintenance treatment of pembrolizumab 200 mg IV PLUS vibostolimab IV PLUS pemetrexed 500 mg/m\^2 IV in Cycles 5-35 (total treatment duration: up to approximately 2 years).

Group Type EXPERIMENTAL

Pembrolizumab

Intervention Type BIOLOGICAL

IV infusion

Carboplatin

Intervention Type DRUG

IV infusion

Pemetrexed

Intervention Type DRUG

IV infusion

Vibostolimab

Intervention Type BIOLOGICAL

IV infusion

Part A: Pembrolizumab+Boserolimab+Carboplatin+Paclitaxel

On Day 1 of each 3-week cycle, participants with squamous NSCLC receive pembrolizumab 200 mg IV PLUS carboplatin AUC 6 IV PLUS paclitaxel 200 mg/m\^2 IV PLUS boserolimab IV on Day 1 every 6 weeks (every other 3-week cycle) (Q6W) in Cycles 1-4, followed by maintenance treatment of pembrolizumab 200 mg IV Q3W PLUS boserolimab IV Q6W from Cycles 5 up to Cycle 35 (total treatment duration: up to approximately 2 years).

Group Type EXPERIMENTAL

Pembrolizumab

Intervention Type BIOLOGICAL

IV infusion

Carboplatin

Intervention Type DRUG

IV infusion

Paclitaxel

Intervention Type DRUG

IV infusion

Boserolimab

Intervention Type BIOLOGICAL

IV infusion

Part A: Pembrolizumab+Boserolimab+Carboplatin+Pemetrexed

On Day 1 of each 3-week cycle, participants with nonsquamous NSCLC receive pembrolizumab 200 mg IV PLUS carboplatin AUC 5 IV PLUS pemetrexed 500 mg/m\^2 IV PLUS boserolimab IV on Day 1 every 6 weeks (every other 3-week cycle) (Q6W) in Cycles 1-4, followed by maintenance treatment of pembrolizumab 200 mg IV Q3W PLUS pemetrexed 500 mg/m\^2 IV Q3W PLUS boserolimab IV Q6W from Cycles 5 up to Cycle 35 (total treatment duration: up to approximately 2 years).

Group Type EXPERIMENTAL

Pembrolizumab

Intervention Type BIOLOGICAL

IV infusion

Carboplatin

Intervention Type DRUG

IV infusion

Pemetrexed

Intervention Type DRUG

IV infusion

Boserolimab

Intervention Type BIOLOGICAL

IV infusion

Part A: Pembrolizumab+MK-4830+Carboplatin+Paclitaxel

On Day 1 of each 3-week cycle, participants with squamous NSCLC receive pembrolizumab 200 mg IV PLUS MK-4830 IV PLUS carboplatin AUC 6 IV PLUS paclitaxel 200 mg/m\^2 IV in Cycles 1-4, followed by maintenance treatment of pembrolizumab 200 mg IV PLUS MK-4830 IV in Cycles 5-35 (total treatment duration: up to approximately 2 years).

Group Type EXPERIMENTAL

Pembrolizumab

Intervention Type BIOLOGICAL

IV infusion

Carboplatin

Intervention Type DRUG

IV infusion

Paclitaxel

Intervention Type DRUG

IV infusion

MK-4830

Intervention Type BIOLOGICAL

IV infusion

Part A: Pembrolizumab+MK-4830+Carboplatin+Pemetrexed

On Day 1 of each 3-week cycle, participants with nonsquamous NSCLC receive pembrolizumab 200 mg IV PLUS MK-4830 IV PLUS carboplatin AUC 5 IV PLUS pemetrexed 500 mg/m\^2 IV in Cycles 1-4, followed by maintenance treatment of pembrolizumab 200 mg IV PLUS MK-4830 IV PLUS pemetrexed 500 mg/m\^2 IV in Cycles 5-35 (total treatment duration: up to approximately 2 years).

Group Type EXPERIMENTAL

Pembrolizumab

Intervention Type BIOLOGICAL

IV infusion

Carboplatin

Intervention Type DRUG

IV infusion

Pemetrexed

Intervention Type DRUG

IV infusion

MK-4830

Intervention Type BIOLOGICAL

IV infusion

Part A: Pembrolizumab+MK-0482+Carboplatin+Paclitaxel

On Day 1 of each 3-week cycle, participants with squamous NSCLC receive pembrolizumab 200 mg IV PLUS MK-0482 IV PLUS carboplatin AUC 6 IV PLUS paclitaxel 200 mg/m\^2 IV in Cycles 1-4, followed by maintenance treatment of pembrolizumab 200 mg IV PLUS MK-0482 IV in Cycles 5-35 (total treatment duration: up to approximately 2 years).

Group Type EXPERIMENTAL

Pembrolizumab

Intervention Type BIOLOGICAL

IV infusion

Carboplatin

Intervention Type DRUG

IV infusion

MK-0482

Intervention Type BIOLOGICAL

IV Infusion

Part A: Pembrolizumab+MK-0482+Carboplatin+Pemetrexed

On Day 1 of each 3-week cycle, participants with nonsquamous NSCLC receive pembrolizumab 200 mg IV PLUS MK-0482 IV PLUS carboplatin AUC 5 IV PLUS pemetrexed 500 mg/m\^2 IV in Cycles 1-4, followed by maintenance treatment of pembrolizumab 200 mg IV PLUS MK-0482 IV PLUS pemetrexed 500 mg/m\^2 IV in Cycles 5-35 (total treatment duration: up to approximately 2 years).

Group Type EXPERIMENTAL

Pembrolizumab

Intervention Type BIOLOGICAL

IV infusion

Carboplatin

Intervention Type DRUG

IV infusion

MK-0482

Intervention Type BIOLOGICAL

IV Infusion

Part B: Pembrolizumab + I-DXd

On Day 1 of each 3-week cycle, participants with squamous and nonsquamous NSCLC will receive pembrolizumab 200 mg IV for up to 2 years, PLUS I-DXd in escalating doses until progressive disease or toxicity.

Group Type EXPERIMENTAL

Pembrolizumab

Intervention Type BIOLOGICAL

IV infusion

Ifinatamab Deruxtecan (I-DXd)

Intervention Type BIOLOGICAL

IV infusion

Part B: Pembrolizumab + Carboplatin + I-DXd

On Day 1 of each 3-week cycle, participants will receive pembrolizumab 200 mg IV for up to 2 years, PLUS carboplatin AUC 5-6 up to 4 cycles PLUS I-DXd IV in escalating doses until PD or toxicity.

Group Type EXPERIMENTAL

Pembrolizumab

Intervention Type BIOLOGICAL

IV infusion

Carboplatin

Intervention Type DRUG

IV infusion

Ifinatamab Deruxtecan (I-DXd)

Intervention Type BIOLOGICAL

IV infusion

Part B: Pembrolizumab + Carboplatin + HER3-DXd

On Day 1 of each 3-week cycle, participants will receive pembrolizumab 200 mg IV for up to 2 years, PLUS carboplatin AUC 5-6 up to 4 cycles PLUS HER3-DXd IV in escalating doses until PD or toxicity.

Group Type EXPERIMENTAL

Pembrolizumab

Intervention Type BIOLOGICAL

IV infusion

Carboplatin

Intervention Type DRUG

IV infusion

HER3-DXd

Intervention Type BIOLOGICAL

IV Infusion

Interventions

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Pembrolizumab

IV infusion

Intervention Type BIOLOGICAL

Carboplatin

IV infusion

Intervention Type DRUG

Paclitaxel

IV infusion

Intervention Type DRUG

Pemetrexed

IV infusion

Intervention Type DRUG

Vibostolimab

IV infusion

Intervention Type BIOLOGICAL

Boserolimab

IV infusion

Intervention Type BIOLOGICAL

MK-4830

IV infusion

Intervention Type BIOLOGICAL

MK-0482

IV Infusion

Intervention Type BIOLOGICAL

Ifinatamab Deruxtecan (I-DXd)

IV infusion

Intervention Type BIOLOGICAL

HER3-DXd

IV Infusion

Intervention Type BIOLOGICAL

Other Intervention Names

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MK-3475 SCH 900475 KEYTRUDA® PARAPLATIN® ABRAXANE® ALIMTA® MK-7684 MK-5890 DS-7300a MK-2400 U3-1402 MK-1022

Eligibility Criteria

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Inclusion Criteria

* Has histologically- or cytologically-confirmed diagnosis of Stage IV squamous or nonsquamous NSCLC
* Participants with nonsquamous NSCLC who are not eligible for an approved targeted therapy
* Is able to provide archival tumor tissue sample collected either within 5 years or within the interval from completion of last treatment but before entering the screening period or newly obtained core or excisional biopsy of a tumor lesion not previously irradiated obtained within 90 days of treatment initiation
* Has not received prior systemic treatment for their metastatic NSCLC
* Is able to complete all screening procedures within the 35-day screening window for Part A and 28-day screening window for Part B

Exclusion Criteria

* Has a diagnosis of small cell lung cancer
* Has a diagnosis of immunodeficiency or is receiving chronic systemic steroid therapy (in dosing exceeding 10 mg daily of prednisone equivalent) or any other form of immunosuppressive therapy within 7 days before the first dose of study treatment
* Has a known additional malignancy that is progressing or has required active treatment within the past 2 years
* Has known active central nervous system (CNS) metastases and/or carcinomatous meningitis
* Has an active autoimmune disease that has required systemic treatment in the past 2 years
* Has a history of (noninfectious) pneumonitis that required steroids or has current pneumonitis
* Has an active infection requiring systemic therapy
* Has clinically significant cardiac disease, including unstable angina, acute myocardial infarction within 6 months from Day 1 of study treatment administration, or New York Heart Association Class III or IV congestive heart failure
* Has a known history of human immunodeficiency virus (HIV) infection. Well-controlled HIV with anti-retroviral therapy (ART) is not excluded
* Has a known history of Hepatitis B (HPV) or known active Hepatitis C virus infection. Hepatitis B surface antigen (HBsAg) positive is eligible if on HBV antiviral therapy for at least 4 weeks and HBV viral load is undetectable prior to randomization
* Has had major surgery \<3 weeks before the first dose of study treatment
* Is expected to require any other form of antineoplastic therapy while on study
* Has a history or current evidence of a gastrointestinal (GI) condition (e.g. inflammatory bowel disease, Crohn's disease, ulcerative colitis) or impaired liver function or diseases that in the opinion of the investigator may significantly alter the absorption or metabolism of oral medications
* Is getting chemotherapy and has clinically active diverticulitis, intra-abdominal abscess, GI obstruction, or peritoneal carcinomatosis
* Has preexisting neuropathy that is moderate in intensity
* Has received prior systemic cytotoxic chemotherapy or other targeted or biological antineoplastic therapy for metastatic disease
* Is unable or unwilling to take folic acid or vitamin B12 supplementation, for participants who will receive pemetrexed
* Has a known sensitivity to any component of carboplatin, paclitaxel, pemetrexed or any of their excipients
* Has received prior radiation therapy to the lung that is \>30 Gray (Gy) within 6 months of the first dose of study treatment
* Has received a live vaccine within 30 days before the first dose of study treatment. Any licensed COVID-19 vaccine (including for Emergency Use) in a particular country is allowed as long as they are messenger ribonucleic acid (mRNA) vaccines, adenoviral vaccines, or inactivated vaccines. Investigational vaccines (ie, those not licensed or approved for Emergency Use) are not allowed
* Has received any prior immunotherapy and was discontinued from that treatment due to a severe or worse immune-related adverse event (irAE)
* Has had chemotherapy or biological cancer therapy within 4 weeks before the first dose of study treatment or has not recovered to Common Terminology Criteria for Adverse Events (CTCAE) Grade 1 or better from the AEs due to cancer therapeutics administered more than 4 weeks before the first dose of study treatment (including participants who had previous immunomodulatory therapy with residual irAEs)
* Is currently participating in or has participated in a study of an investigational agent or has used an investigational device within 4 weeks before the first dose of study treatment
* Previously had a severe hypersensitivity reaction to treatment with monoclonal antibodies (including pembrolizumab) and/or any of their excipients
* Has had an allogenic tissue/solid organ transplant
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Daiichi Sankyo

INDUSTRY

Sponsor Role collaborator

Merck Sharp & Dohme LLC

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Medical Director

Role: STUDY_DIRECTOR

Merck Sharp & Dohme LLC

Locations

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Banner MD Anderson Cancer Center ( Site 0001)

Gilbert, Arizona, United States

Site Status RECRUITING

City of Hope ( Site 0014)

Duarte, California, United States

Site Status COMPLETED

UCSF Medical Center at Mission Bay ( Site 0007)

San Francisco, California, United States

Site Status COMPLETED

Georgetown University ( Site 0036)

Washington D.C., District of Columbia, United States

Site Status COMPLETED

University of Kentucky Markey Cancer Center ( Site 0019)

Lexington, Kentucky, United States

Site Status RECRUITING

MedStar Franklin Square Medical Center ( Site 0033)

Baltimore, Maryland, United States

Site Status COMPLETED

Massachusetts General Hospital ( Site 0003)

Boston, Massachusetts, United States

Site Status ACTIVE_NOT_RECRUITING

Dana Farber Cancer Institute ( Site 0002)

Boston, Massachusetts, United States

Site Status ACTIVE_NOT_RECRUITING

Oncology Hematology West, PC DBA Nebraska Cancer Specialists ( Site 0031)

Omaha, Nebraska, United States

Site Status COMPLETED

Dartmouth Hitchcock Medical Center ( Site 0016)

Lebanon, New Hampshire, United States

Site Status RECRUITING

John Theurer Cancer Center at Hackensack University Medical Center ( Site 0037)

Hackensack, New Jersey, United States

Site Status COMPLETED

Laura and Isaac Perlmutter Cancer Center ( Site 0034)

New York, New York, United States

Site Status ACTIVE_NOT_RECRUITING

Sanford Fargo Medical Center ( Site 0039)

Fargo, North Dakota, United States

Site Status RECRUITING

Cleveland Clinic Main ( Site 0006)

Cleveland, Ohio, United States

Site Status COMPLETED

Abramson Cancer Center of the University of Pennsylvania ( Site 0010)

Philadelphia, Pennsylvania, United States

Site Status RECRUITING

Sanford Cancer Center ( Site 0038)

Sioux Falls, South Dakota, United States

Site Status RECRUITING

The University of Texas MD Anderson Cancer Center ( Site 0009)

Houston, Texas, United States

Site Status RECRUITING

Petz Aladar Megyei Oktato Korhaz ( Site 0062)

Győr, Győr-Moson-Sopron, Hungary

Site Status RECRUITING

Jász-Nagykun-Szolnok Vármegyei Hetényi Géza Kórház ( Site 0061)

Szolnok, Jász-Nagykun-Szolnok, Hungary

Site Status RECRUITING

Orszagos Koranyi Pulmonologiai Intezet ( Site 0060)

Budapest, , Hungary

Site Status RECRUITING

Soroka Medical Center ( Site 0072)

Beersheba, , Israel

Site Status COMPLETED

Rambam Health Care Campus-Oncology ( Site 0076)

Haifa, , Israel

Site Status RECRUITING

Shaare Zedek Medical Center ( Site 0075)

Jerusalem, , Israel

Site Status RECRUITING

Meir Medical Center ( Site 0071)

Kfar Saba, , Israel

Site Status RECRUITING

Rabin Medical Center ( Site 0074)

Petah Tikva, , Israel

Site Status RECRUITING

Chaim Sheba Medical Center ( Site 0070)

Ramat Gan, , Israel

Site Status RECRUITING

Sourasky Medical Center ( Site 0077)

Tel Aviv, , Israel

Site Status RECRUITING

Azienda Ospedaliera Universitaria Careggi ( Site 0173)

Florence, Firenze, Italy

Site Status COMPLETED

IRCCS Ospedale San Raffaele ( Site 0171)

Milan, , Italy

Site Status COMPLETED

Policlinico Gemelli di Roma ( Site 0174)

Roma, , Italy

Site Status COMPLETED

Narodowy Instytut Onkologii im. Marii Sklodowskiej-Curie - P-Klinika Nowotworow Pluca i Klatki Pier ( Site 0151)

Warsaw, Masovian Voivodeship, Poland

Site Status COMPLETED

Uniwersyteckie Centrum Kliniczne-Early Clinical Trials Unit ( Site 0150)

Gdansk, Pomeranian Voivodeship, Poland

Site Status RECRUITING

Szpital Wojewódzki im. Mikoaja Kopernika w Koszalinie-Oddzial Dzienny Chemioterapii ( Site 0152)

Koszalin, West Pomeranian Voivodeship, Poland

Site Status ACTIVE_NOT_RECRUITING

Seoul National University Bundang Hospital ( Site 0081)

Seongnam-si, Kyonggi-do, South Korea

Site Status ACTIVE_NOT_RECRUITING

Severance Hospital ( Site 0080)

Seoul, , South Korea

Site Status ACTIVE_NOT_RECRUITING

Samsung Medical Center ( Site 0082)

Seoul, , South Korea

Site Status ACTIVE_NOT_RECRUITING

ICO L Hospitalet ( Site 0090)

L'Hospitalet de Llobregat, Barcelona, Spain

Site Status RECRUITING

Hospital Universitario Quiron Madrid ( Site 0091)

Madrid, , Spain

Site Status RECRUITING

Countries

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United States Hungary Israel Italy Poland South Korea Spain

Central Contacts

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Toll Free Number

Role: CONTACT

Phone: 1-888-577-8839

Email: [email protected]

Facility Contacts

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Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

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Study Coordinator

Role: primary

Study Coordinator

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Study Coordinator

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Study Coordinator

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Study Coordinator

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Study Coordinator

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Study Coordinator

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Study Coordinator

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Study Coordinator

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Study Coordinator

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Study Coordinator

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Study Coordinator

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Study Coordinator

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Study Coordinator

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Study Coordinator

Role: primary

Related Links

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Other Identifiers

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MK-3475-01A

Identifier Type: OTHER

Identifier Source: secondary_id

KEYMAKER-U01A

Identifier Type: OTHER

Identifier Source: secondary_id

2023-506932-33-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

U1111-1294-6474

Identifier Type: REGISTRY

Identifier Source: secondary_id

2020-001626-56

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

3475-01A

Identifier Type: -

Identifier Source: org_study_id