Phase 1/2 Study of UCART22 in Patients With Relapsed or Refractory CD22+ B-cell Acute Lymphoblastic Leukemia (BALLI-01)

NCT ID: NCT04150497

Last Updated: 2025-09-09

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE1/PHASE2

Total Enrollment

52 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-10-14

Study Completion Date

2026-06-30

Brief Summary

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This is a first-in-human, open-label, dose escalation and expansion study of UCART22 administered intravenously to patients with relapsed or refractory B-cell acute Lymphoblastic Leukemia (B-ALL). The purpose of this study is to evaluate the safety and clinical activity of UCART22 and determine the Maximum Tolerated Dose (MTD) and Recommended Phase 2 Dose (RP2D)

Detailed Description

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Conditions

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B-cell Acute Lymphoblastic Leukemia

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Dose Escalation

Several tested doses of UCART22 until the Maximum Tolerated Dose (MTD) is identified and establish Recommended Phase 2 Dose (RP2D)

Dose Expansion: UCART22 administered at the RP2D

Group Type EXPERIMENTAL

UCART22

Intervention Type BIOLOGICAL

Allogeneic engineered T-cells expressing anti-CD22 Chimeric Antigen Receptor given following a lymphodepleting regimen

CLLS52

Intervention Type BIOLOGICAL

A monoclonal antibody that recognizes a CD52 antigen

Interventions

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UCART22

Allogeneic engineered T-cells expressing anti-CD22 Chimeric Antigen Receptor given following a lymphodepleting regimen

Intervention Type BIOLOGICAL

CLLS52

A monoclonal antibody that recognizes a CD52 antigen

Intervention Type BIOLOGICAL

Other Intervention Names

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Alemtuzumab

Eligibility Criteria

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Inclusion Criteria

* B-ALL blast cells expressing CD22
* Diagnosed with R/R B-ALL
* Prior therapy must include at least one standard chemotherapy regimen and at least one salvage regimen

Exclusion Criteria

-Prior cellular therapy or investigational cellular or gene therapy within 90 days prior to enrollment
Minimum Eligible Age

15 Years

Maximum Eligible Age

50 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Cellectis S.A.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Nitin Jain, MD

Role: PRINCIPAL_INVESTIGATOR

M.D. Anderson Cancer Center

Locations

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University of California, Los Angeles (UCLA) - Medical Center

Los Angeles, California, United States

Site Status RECRUITING

University of Colorado - Aurora Cancer Center

Aurora, Colorado, United States

Site Status RECRUITING

Sarah Cannon - Colorado Blood Cancer Institute

Denver, Colorado, United States

Site Status RECRUITING

University of Chicago

Chicago, Illinois, United States

Site Status RECRUITING

Dana Farber Cancer Institute

Boston, Massachusetts, United States

Site Status RECRUITING

Roswell Park Comprehensive Cancer Center

Buffalo, New York, United States

Site Status RECRUITING

Memorial Sloan Kettering Cancer Center (MSKCC) David H. Koch Center for Cancer Care at Memorial Sloan Kettering Cancer Center

New York, New York, United States

Site Status RECRUITING

Weill Medical College of Cornell University

New York, New York, United States

Site Status WITHDRAWN

Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, United States

Site Status RECRUITING

Sarah Cannon - HCA Research Institute

Nashville, Tennessee, United States

Site Status RECRUITING

Sarah Cannon - St. David's South Austin Medical Center

Austin, Texas, United States

Site Status RECRUITING

MD Anderson Cancer Center

Houston, Texas, United States

Site Status RECRUITING

Sarah Cannon - Texas Transplant Institute at Methodist Hospital

San Antonio, Texas, United States

Site Status RECRUITING

University of Wisconsin Carbone Cancer Center

Madison, Wisconsin, United States

Site Status RECRUITING

CHU de Nantes - Hôtel-Dieu

Nantes, , France

Site Status RECRUITING

Hôpital Saint Louis, Unité d'Hématologie Adolescents et Jeunes Adultes Département d'Hématologie

Paris, , France

Site Status RECRUITING

Hôpital Robert Debré - Service d'hémato-immunologie

Paris, , France

Site Status RECRUITING

Hôpital Lyon Sud

Pierre-Bénite, , France

Site Status RECRUITING

CHU Rennes - Hopital Pontchaillou

Rennes, , France

Site Status RECRUITING

Countries

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United States France

Central Contacts

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Cellectis Central Contact

Role: CONTACT

+1 (347) 752-4044

Other Identifiers

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UCART22_01

Identifier Type: -

Identifier Source: org_study_id

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