Bio Equivalency 20 Mgm Orfadin and 20 Mgm of Nitisonine

NCT ID: NCT04113772

Last Updated: 2019-10-03

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

NA

Total Enrollment

4 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-11-01

Study Completion Date

2021-03-31

Brief Summary

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he purpose of this study is to determine whether Nitisinone 10 mg Tablets (Test Product are bioequivalent to the reference product Orfadin 10 mg

Detailed Description

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Detailed Description:

The specific aim is to conduct a randomized, single dose, three-period crossover bioequivalence study in at least 18 healthy male and female subjects at a single study center to evaluate the in vivo performance of two formulations of Nitisinone 10 mg and the reference product Orfadin under fasting.

A total of 4 healthy female and male volunteers (age 18 to 55 years old) will be entered into the study. Volunteers will be determined to be free of significant medical conditions as assessed by medical history, physical examination, and blood and urine tests. Volunteers will be randomly allocated to a treatment sequence, before administration of investigational nitinosine

Determination of succinylacetone (SA) in blood (serum/plasma) and/or urine will be performed. Results from samples analyzed at the central laboratory, including determination of nitisinone, will be used in the evaluation of pharmacokinetics, efficacy and safety during the two treatment periods.

Conditions

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Hereditary Tyrosinemia, Type I

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

CROSSOVER

Primary Study Purpose

TREATMENT

Blinding Strategy

SINGLE

Participants

Study Groups

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Orfandin .5 mgm/kg mgm bid

Two participant will receive .5 mgm/kg mgm of orfadin

Group Type ACTIVE_COMPARATOR

Orfadin

Intervention Type DRUG

Orfadin

Nitinosine .5 mgm/kg bid

Two participant will receive .5 mgm/kg of nitinosine

Group Type EXPERIMENTAL

Nitisinone

Intervention Type DRUG

Measure bio equivalency/efficacy of nitinosine and orfadin

Interventions

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Nitisinone

Measure bio equivalency/efficacy of nitinosine and orfadin

Intervention Type DRUG

Orfadin

Orfadin

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* All HT-1 patients receiving Orfadin treatment are eligible for entry.
* Male and female patients of all ages diagnosed with HT-1.
* Stable lab values, including liver values \<2 ULN (ALP, ALT, AST, bilirubin, INR).
* Women of childbearing potential willing to use adequate contraception
* Signed informed consent/assent.

Exclusion Criteria

* Any medical condition which in the opinion of the investigator makes the patient unsuitable for inclusion.
* Enrollment in another concurrent clinical interventional study within three months prior to inclusion in this study.
* Pregnant women.
* Lactating women. .Known hepatitis B, hepatitis C or HIV infection.
* Foreseeable inability to cooperate with given instructions or study procedures.
Minimum Eligible Age

18 Years

Maximum Eligible Age

50 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Sutphin Drugs

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Lifein Multi-Specialty Hospital

Navsari, Gujarat, India

Site Status

Countries

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India

Central Contacts

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Ajai Prakash

Role: CONTACT

7185260310

Other Identifiers

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Global CRO Orfadin

Identifier Type: -

Identifier Source: org_study_id

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