Trial Outcomes & Findings for Ketamine Treatment Effects on Synaptic Plasticity in Depression (NCT NCT04091971)

NCT ID: NCT04091971

Last Updated: 2023-11-13

Results Overview

PET imaging measure of synaptic density (\[11C\]UCB-J binding potential, BPND) before and after ketamine treatment. This type of brain scan takes pictures to measure the density of synapses, or connections between brain cells (neurons), in the brain. \[11C\]UCB-J is a radiotracer specific for SV2A, a protein present in presynaptic vesicles. \[11C\]UCB-J BPND was quantified in a brain region called the medial prefrontal cortex; previous studies have found lower levels of \[11C\]UCB-J binding in patients with more severe depression. BPND is the ratio at equilibrium of specifically bound radioligand to that of nondisplaceable radioligand in tissue. Time frame of assessment: Time frame 1 = baseline. This pre-treatment PET scan was acquired as close as possible prior to the first ketamine infusion, up to 7 days prior to first ketamine infusion. Time frame 2 = post-treatment. This post-treatment PET scan was acquired 24-48 hours following the final (4th) ketamine infusion.

Recruitment status

COMPLETED

Study phase

PHASE4

Target enrollment

9 participants

Primary outcome timeframe

Measured at two time frames: Time frame 1 = Baseline. Time frame 2 = post-treatment

Results posted on

2023-11-13

Participant Flow

Participant milestones

Participant milestones
Measure
Depressed Adults With Current MDD
Subjects will undergo 4 sequential intravenous infusions of ketamine administered over a two week period. Ketamine is administered at a dose of 0.5mg/kg intravenously as a slow continuous infusion over approximately 40 minutes, with 4 sequential infusions over an approximately two week period (two infusions per week for two weeks).
Overall Study
STARTED
9
Overall Study
COMPLETED
5
Overall Study
NOT COMPLETED
4

Reasons for withdrawal

Reasons for withdrawal
Measure
Depressed Adults With Current MDD
Subjects will undergo 4 sequential intravenous infusions of ketamine administered over a two week period. Ketamine is administered at a dose of 0.5mg/kg intravenously as a slow continuous infusion over approximately 40 minutes, with 4 sequential infusions over an approximately two week period (two infusions per week for two weeks).
Overall Study
Withdrawal by Subject
1
Overall Study
No longer met eligibility criteria after enrollment.
2
Overall Study
Panic attack during MRI; no MRI or PET but completed ketamine and other procedures
1

Baseline Characteristics

Ketamine Treatment Effects on Synaptic Plasticity in Depression

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Depressed Adults With Current MDD
n=6 Participants
Subjects will undergo 4 sequential intravenous infusions of ketamine administered over a two week period. Ketamine: See arm description.
Age, Continuous
37.33 years
STANDARD_DEVIATION 3.83 • n=5 Participants
Sex: Female, Male
Female
6 Participants
n=5 Participants
Sex: Female, Male
Male
0 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
2 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
4 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
0 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
3 Participants
n=5 Participants
Race (NIH/OMB)
White
2 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
1 Participants
n=5 Participants
Region of Enrollment
United States
6 participants
n=5 Participants

PRIMARY outcome

Timeframe: Measured at two time frames: Time frame 1 = Baseline. Time frame 2 = post-treatment

Population: Participants with MDD who completed PET imaging pre-post a course of ketamine infusions for depression

PET imaging measure of synaptic density (\[11C\]UCB-J binding potential, BPND) before and after ketamine treatment. This type of brain scan takes pictures to measure the density of synapses, or connections between brain cells (neurons), in the brain. \[11C\]UCB-J is a radiotracer specific for SV2A, a protein present in presynaptic vesicles. \[11C\]UCB-J BPND was quantified in a brain region called the medial prefrontal cortex; previous studies have found lower levels of \[11C\]UCB-J binding in patients with more severe depression. BPND is the ratio at equilibrium of specifically bound radioligand to that of nondisplaceable radioligand in tissue. Time frame of assessment: Time frame 1 = baseline. This pre-treatment PET scan was acquired as close as possible prior to the first ketamine infusion, up to 7 days prior to first ketamine infusion. Time frame 2 = post-treatment. This post-treatment PET scan was acquired 24-48 hours following the final (4th) ketamine infusion.

Outcome measures

Outcome measures
Measure
Depressed Adults With Current MDD
n=5 Participants
Subjects will undergo 4 sequential intravenous infusions of ketamine administered over a two week period. Ketamine: See arm description.
Synaptic Density
Pre-treatment [11C]UCB-J binding potential (BPnd) in medial prefrontal cortex
2.40 Ratio
Standard Deviation 0.81
Synaptic Density
Post-treatment [11C]UCB-J binding potential (BPnd) in medial prefrontal cortex
2.32 Ratio
Standard Deviation 0.67

SECONDARY outcome

Timeframe: Measured at 3 time frames. Time frame one = Baseline: 24 hours prior to infusion one ("PRE"). Time frame two = 24 hours following ketamine infusion 4 ("POST1"). Time frame three = one week following ketamine infusion 4 ("POST2").

Population: Including all participants with HDRS data, n=6. 1 of the 6 does not have PET data. Including data from the 3 time points relevant for analysis: 24 hours prior to first ketamine infusion ("PRE"), 24 hours following ketamine infusion 4 ("POST1") and 1 week following ketamine infusion 4 ("POST2").

The 17-item Hamilton Depression Rating Scale (HDRS) is a clinician-administered scale that quantifies depression severity, and includes items assessing mood, suicidal thinking, insomnia, feelings of guilt, work and activities, somatic symptoms, and insight. It is a well-characterized scale with excellent psychometric properties. The version of the scale used in this study has a range from 0 to 51. Interpretation of score values is as follows: None: 0-7 Mild: 8-13 Moderate: 14-19 Severe: 20-25 Very Severe: 26-51

Outcome measures

Outcome measures
Measure
Depressed Adults With Current MDD
n=6 Participants
Subjects will undergo 4 sequential intravenous infusions of ketamine administered over a two week period. Ketamine: See arm description.
17-item Hamilton Depression Rating Scale
HAM-17 24 hours prior to first ketamine infusion ("PRE")
19.5 score on a scale
Standard Deviation 3.0
17-item Hamilton Depression Rating Scale
HAM-17 24 hours following ketamine infusion 4 ("POST1")
6.5 score on a scale
Standard Deviation 2.4
17-item Hamilton Depression Rating Scale
HAM-17 1 week following ketamine infusion 4 ("POST2")
7.8 score on a scale
Standard Deviation 4.4

Adverse Events

Depressed Adults With Current MDD

Serious events: 0 serious events
Other events: 5 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Depressed Adults With Current MDD
n=9 participants at risk
Subjects will undergo 4 sequential intravenous infusions of ketamine administered over a two week period. Ketamine: Ketamine is administered at a dose of 0.5mg/kg intravenously as a slow continuous infusion over approximately 40 minutes, with 4 sequential infusions over an approximately two week period (two infusions per week for two weeks).
Nervous system disorders
Insomnia
22.2%
2/9 • Number of events 2 • 4 weeks
No differences
Nervous system disorders
Nightmares
11.1%
1/9 • Number of events 1 • 4 weeks
No differences
Nervous system disorders
Drowsiness
22.2%
2/9 • Number of events 4 • 4 weeks
No differences
Nervous system disorders
Feeling nervous or hyper
11.1%
1/9 • Number of events 1 • 4 weeks
No differences
Nervous system disorders
Irritability
22.2%
2/9 • Number of events 2 • 4 weeks
No differences
Nervous system disorders
Memory difficulties
22.2%
2/9 • Number of events 7 • 4 weeks
No differences
Nervous system disorders
Trouble concentrating
11.1%
1/9 • Number of events 1 • 4 weeks
No differences
Nervous system disorders
Headache
22.2%
2/9 • Number of events 3 • 4 weeks
No differences
Ear and labyrinth disorders
Ringing in Ears or Trouble Hearing
22.2%
2/9 • Number of events 2 • 4 weeks
No differences
General disorders
Drooling or Increased Salivation
11.1%
1/9 • Number of events 1 • 4 weeks
No differences
Cardiac disorders
Heartbeat rapid or pounding
11.1%
1/9 • Number of events 1 • 4 weeks
No differences
Respiratory, thoracic and mediastinal disorders
Trouble catching breath or hyperventilation
11.1%
1/9 • Number of events 1 • 4 weeks
No differences
Cardiac disorders
Chest pain
11.1%
1/9 • Number of events 1 • 4 weeks
No differences
Gastrointestinal disorders
Nausea or vomiting
11.1%
1/9 • Number of events 1 • 4 weeks
No differences
Renal and urinary disorders
Frequent need to urinate
22.2%
2/9 • Number of events 4 • 4 weeks
No differences
Reproductive system and breast disorders
Loss of Sexual Interest
11.1%
1/9 • Number of events 1 • 4 weeks
No differences
Reproductive system and breast disorders
Delayed or absent orgasm
11.1%
1/9 • Number of events 5 • 4 weeks
No differences
General disorders
Excessive Sweating
33.3%
3/9 • Number of events 6 • 4 weeks
No differences
Gastrointestinal disorders
Decreased appetite
33.3%
3/9 • Number of events 4 • 4 weeks
No differences
Gastrointestinal disorders
Increased appetite
11.1%
1/9 • Number of events 4 • 4 weeks
No differences
General disorders
Weight loss
11.1%
1/9 • Number of events 2 • 4 weeks
No differences
Skin and subcutaneous tissue disorders
Skin rash or allergy
11.1%
1/9 • Number of events 1 • 4 weeks
No differences
Nervous system disorders
Word finding difficulties
11.1%
1/9 • Number of events 1 • 4 weeks
No differences
Nervous system disorders
Apathy/emotional indifference
11.1%
1/9 • Number of events 1 • 4 weeks
No differences
General disorders
Hair thinning/loss
22.2%
2/9 • Number of events 2 • 4 weeks
No differences

Additional Information

Jeffrey Miller, M.D.

NYSPI

Phone: 646-774-7613

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place