GEN1042 Safety Trial and Anti-tumor Activity in Participants With Malignant Solid Tumors

NCT ID: NCT04083599

Last Updated: 2026-01-30

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE1/PHASE2

Total Enrollment

350 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-09-17

Study Completion Date

2026-11-30

Brief Summary

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The goal of this trial is to learn about the antibody GEN1042 when it is used alone and when it is used together with another antibody cancer drug, pembrolizumab (with or without chemotherapy), for treatment of participants with certain types of cancer.

Detailed Description

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This is an open-label, multicenter phase 1/2 study designed to assess the safety, pharmacokinetics, pharmacodynamics and anti-tumor activity of GEN1042 administered as a monotherapy or in combination in participants with metastatic or locally advanced solid tumors.

Participants will receive either GEN1042 alone, GEN1042 with pembrolizumab, or GEN1042 with pembrolizumab and chemotherapy. All participants will receive active drug; no one will receive placebo.

This trial has 2 parts. The purpose of the first part is to find out if GEN1042 is safe and to find out the best doses of GEN1042 to use. The purpose of the second part is to give GEN1042 to more participants to see how well the dose(s) of GEN1042 selected in the first part work against cancer with GEN1042 when given alone or in combination with pembrolizumab or in combination with pembrolizumab and chemotherapy.

Trial details include:

* The average trial duration will be about 3 years.
* The treatment duration will be up to 2 years (when GEN1042 is combined with pembrolizumab).
* The visit frequency will be weekly at first and lessening over time until visits are only once every 3 weeks.

Conditions

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Malignant Solid Tumor Non-Small Cell Lung Cancer (NSCLC) Colorectal Cancer (CRC) Melanoma Head and Neck Squamous Cell Carcinoma (HNSCC) Pancreatic Ductal Adenocarcinoma (PDAC)

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SEQUENTIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Monotherapy - Dose Escalation and Dose Expansion Parts

Group Type EXPERIMENTAL

GEN1042

Intervention Type BIOLOGICAL

Intravenous

Combination Therapy - Safety Run-in and Expansion Parts

Group Type EXPERIMENTAL

GEN1042

Intervention Type BIOLOGICAL

Intravenous

Pembrolizumab

Intervention Type DRUG

Intravenous

Cisplatin

Intervention Type DRUG

Intravenous

Carboplatin

Intervention Type DRUG

Intravenous

5-FU

Intervention Type DRUG

Intravenous

Gemcitabine

Intervention Type DRUG

Intravenous

Nab paclitaxel

Intervention Type DRUG

Intravenous

Pemetrexed

Intervention Type DRUG

Intravenous

Paclitaxel

Intervention Type DRUG

Intravenous

Interventions

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GEN1042

Intravenous

Intervention Type BIOLOGICAL

Pembrolizumab

Intravenous

Intervention Type DRUG

Cisplatin

Intravenous

Intervention Type DRUG

Carboplatin

Intravenous

Intervention Type DRUG

5-FU

Intravenous

Intervention Type DRUG

Gemcitabine

Intravenous

Intervention Type DRUG

Nab paclitaxel

Intravenous

Intervention Type DRUG

Pemetrexed

Intravenous

Intervention Type DRUG

Paclitaxel

Intravenous

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

Monotherapy - Dose Escalation and Dose Expansion Parts

* Participants with non-CNS solid tumors that is metastatic or unresectable and for whom there is no available standard therapy.
* Participants with a confirmed diagnosis of relapsed or refractory, advanced and/or metastatic melanoma, NSCLC, or CRC and for whom there is no available standard therapy

Combination Therapy - Dose Expansion Part

* Participants with unresectable Stage III or Stage IV melanoma with no prior systemic anticancer therapy for unresectable or metastatic disease. Primary ocular or mucosal melanoma is excluded.
* Participants with Stage IV metastatic or recurrent NSCLC with no prior systemic anticancer therapy, no actionable mutation.
* Participants with recurrent or metastatic HNSCC with no prior systemic therapy administered in the recurrent or metastatic setting.
* Participants with confirmed metastatic PDAC with no previous radiotherapy, surgery, chemotherapy, or investigational therapy for the treatment of metastatic disease.

General (all phases):

* Must be age ≥ 18 years of age on the day of signing informed consent, or the legal age of consent in the jurisdiction in which the trial is taking place.
* Measurable disease according to RECIST 1.1
* Eastern Cooperative Oncology Group (ECOG) 0-1
* Normal or adequate liver, renal, cardiac and bone marrow function

Exclusion Criteria

Monotherapy - Dose Escalation and Dose Expansion Parts

* Treatment with an anti-cancer agent (within 21 days or after at least 5 half-lives of the drug, whichever is shorter), prior to GEN1042 administration
* Radiotherapy within 14 days prior to first GEN1042 administration
* Toxicities from previous anti-cancer therapies that have not resolved

Combination Therapy - Dose Expansion Part

* Has received prior systemic cytotoxic chemotherapy, biological therapy, OR major surgery within 3 weeks or at least 5 half-lives of the drug (whichever is shorter) of the first dose of trial treatment.
* Radiotherapy within 14 days of start of trial treatment or received lung radiation therapy of \> 30 Gy within 6 months of the first dose of trial treatment.

General (all phases)

* Participants has an active, known, or suspected autoimmune disease.
* History of non-infectious pneumonitis that required steroids or currently has pneumonitis.
* History of ≥ grade 3 allergic reactions to monoclonal antibody (mAb) therapy
* Participants with a condition requiring systemic treatment with either corticosteroids (\>10 mg daily prednisone equivalent) or other immunosuppressive medications within 14 days of first treatment.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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BioNTech SE

INDUSTRY

Sponsor Role collaborator

Genmab

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Study Official

Role: STUDY_DIRECTOR

Genmab

Locations

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Alaska Oncology and Hematology LLC

Anchorage, Alaska, United States

Site Status

Cancer & Blood Specialty Clinic

Los Alamitos, California, United States

Site Status

Moores Cancer Center at the UC San Diego Health

San Diego, California, United States

Site Status

Yale University Cancer Center

New Haven, Connecticut, United States

Site Status

ChristianaCare

Newark, Delaware, United States

Site Status

Mount Sinai Comprehensive Cancer Center

Miami Beach, Florida, United States

Site Status

Florida Cancer Affiliates

Ocala, Florida, United States

Site Status

Hope and Healing Cancer Services

Hinsdale, Illinois, United States

Site Status

University of Kentucky

Lexington, Kentucky, United States

Site Status

Norton Cancer Institute

Louisville, Kentucky, United States

Site Status

Maryland Oncology Hematology PA

Columbia, Maryland, United States

Site Status

Washington University School of Medicine

St Louis, Missouri, United States

Site Status

Levine Cancer Center

Charlotte, North Carolina, United States

Site Status

Novant Health Cancer Institute - Forsyth (Medical Oncology)

Winston-Salem, North Carolina, United States

Site Status

Kaiser Permanente (KP) Oncology/Hematology

Portland, Oregon, United States

Site Status

University of Pennsylvania

Philadelphia, Pennsylvania, United States

Site Status

Fox Chase Cancer Center

Philadelphia, Pennsylvania, United States

Site Status

Sarah Cannon Research Institute

Nashville, Tennessee, United States

Site Status

Lumi Research

Kingwood, Texas, United States

Site Status

Utah Cancer Specialists

Salt Lake City, Utah, United States

Site Status

Virgina Cancer Specialists

Fairfax, Virginia, United States

Site Status

Adventist Health System/Sunbelt,Inc

Seattle, Washington, United States

Site Status

Medical Oncology Associates, PS

Spokane, Washington, United States

Site Status

Rigshospitalet (Copenhagen University Hospital)

Copenhagen, , Denmark

Site Status

Herlev University Hospital

Herlev, , Denmark

Site Status

University Hospital of Southern Denmark, Vejle Hospital

Vejle, , Denmark

Site Status

Centre hospitalier Universitaire de Bordeaux

Bordeaux, , France

Site Status

Centre Antoine Lacassagne

Nice, , France

Site Status

Gustave Roussy

Villejuif, , France

Site Status

ARENSIA Research Clinic at the Research Institute of Clinical Medicine

Tbilisi, , Georgia

Site Status

Nationales Centrum fr Tumorerkrankungen NCT

Heidelberg, , Germany

Site Status

Klinikum der Stadt Ludwigshafen am Rhein gGmbH

Ludwigshafen, , Germany

Site Status

Department of Dermatology, University of Mainz

Mainz, , Germany

Site Status

Universitätsmedizin Mannheim Dermatologie

Mannheim, , Germany

Site Status

Universitaetsklinikum Wuerzburg

Würzburg, , Germany

Site Status

Rabin Medical Center

Petah Tikva, , Israel

Site Status

Tel Aviv Sourasky Medical Center

Tel Aviv, , Israel

Site Status

Azienda Ospedaliera Spedali Civili di Brescia

Brescia, , Italy

Site Status

Azienda Ospedaliera S.Croce e Carle Cuneo

Cuneo, , Italy

Site Status

Istituto Nazionale dei Tumori

Milan, , Italy

Site Status

Istituto Clinico Humanitas

Rozzano, , Italy

Site Status

ARENSIA Research Clinic at the Oncology Institute

Chisinau, , Moldova

Site Status

Chungbuk National University Hospital

Cheongju-si, , South Korea

Site Status

Jeonbuk National University Hospital

Jeonju, , South Korea

Site Status

Gachon University Gil Medical Center

Namdong, , South Korea

Site Status

Korea University Guro Hospital

Seoul, , South Korea

Site Status

Samsung Medical Center

Seoul, , South Korea

Site Status

Severance Hospital, Yonsei University Health System

Seoul, , South Korea

Site Status

Pusan National University Yangsan Hospital

Yangsan, , South Korea

Site Status

H. Vall d'Hebron

Barcelona, , Spain

Site Status

START Barcelona HM Nou Delfos

Barcelona, , Spain

Site Status

Hospital Duran i Reynals - ICO L Hospitalet

L'Hospitalet de Llobregat, , Spain

Site Status

Hospital Universitario Insular de Gran Canaria

Las Palmas de Gran Canaria, , Spain

Site Status

Hospital Universitario Lucus Augusti

Lugo, , Spain

Site Status

Clinica Universidad de Navarra

Madrid, , Spain

Site Status

HM CIOCC Hospital Universitario HM Sanchinarro

Madrid, , Spain

Site Status

Hospital Clinico San Carlos

Madrid, , Spain

Site Status

Hospital General Universitario Gregorio Maran

Madrid, , Spain

Site Status

Hospital Universitario 12 de Octubre

Madrid, , Spain

Site Status

Hospital Universitario La Paz

Madrid, , Spain

Site Status

Hospital Universitario Ramon y Cajal

Madrid, , Spain

Site Status

MD Anderson Cancer Center Madrid

Madrid, , Spain

Site Status

START Madrid - Hospital Universitario Fundacion Jimenez Diaz

Madrid, , Spain

Site Status

Hospital Universitario Virgen de la Victoria

Málaga, , Spain

Site Status

Clinica Universidad de Navarra

Pamplona, , Spain

Site Status

Complejo Hospitalario Universitario de Santiago (CHUS)

Santiago de Compostela, , Spain

Site Status

Hospital Virgen del Rocio

Seville, , Spain

Site Status

Hospital Clinico Universitario de Valencia

Valencia, , Spain

Site Status

Chang Gung Memorial Hospital (CGMH) - Kaohsiung Branch

Kaohsiung City, , Taiwan

Site Status

Kaohsiung Medical University Memorial Hospital

Kaohsiung City, , Taiwan

Site Status

China Medical University Hospital

Taichung, , Taiwan

Site Status

National Cheng Kung University Hospital

Tainan, , Taiwan

Site Status

Taipei Medical University Hospital

Taipei, , Taiwan

Site Status

Taipei Veterans General Hospital, VGHTPE

Taipei, , Taiwan

Site Status

Chang Gung Memorial Hospital Linkou Branch

Taoyuan District, , Taiwan

Site Status

Royal Marsden NHS Foundation Trust

Sutton, , United Kingdom

Site Status

Countries

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United States Denmark France Georgia Germany Israel Italy Moldova South Korea Spain Taiwan United Kingdom

References

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Muik A, Adams 3rd HC, Gieseke F, Altintas I, Schoedel KB, Blum JM, Sanger B, Burm SM, Stanganello E, Verzijl D, Spires VM, Vascotto F, Toker A, Quinkhardt J, Fereshteh M, Diken M, Satijn DPE, Kreiter S, Ahmadi T, Breij ECW, Tureci O, Sasser K, Sahin U, Jure-Kunkel M. DuoBody-CD40x4-1BB induces dendritic-cell maturation and enhances T-cell activation through conditional CD40 and 4-1BB agonist activity. J Immunother Cancer. 2022 Jun;10(6):e004322. doi: 10.1136/jitc-2021-004322.

Reference Type DERIVED
PMID: 35688554 (View on PubMed)

Other Identifiers

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2018-003716-47

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

IRAS ID: 263292

Identifier Type: REGISTRY

Identifier Source: secondary_id

MOH_2023-07-31_012855

Identifier Type: REGISTRY

Identifier Source: secondary_id

2023-508526-10

Identifier Type: OTHER

Identifier Source: secondary_id

RECF-005255

Identifier Type: OTHER

Identifier Source: secondary_id

Rg13-835_03.08.2023

Identifier Type: OTHER

Identifier Source: secondary_id

2023-508526-10-00

Identifier Type: CTIS

Identifier Source: secondary_id

GCT1042-01

Identifier Type: -

Identifier Source: org_study_id

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