Efficacy, Safety, and PK of Ascending Dosages of Moxidectin Versus Ivermectin Against Strongyloides Stercoralis

NCT ID: NCT04056325

Last Updated: 2024-12-09

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE2/PHASE3

Total Enrollment

617 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-11-27

Study Completion Date

2021-04-30

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

This study is a phase 2, blinded and randomized clinical trial. The phase 2a trial is single blinded and conducted in Lao, while the phase 2b trial is double-blinded and conducted in Lao and Cambodia. The study aims at providing evidence on effective doses and safety of moxidectin in adults against infection with S. stercoralis in Laos (trial 2a) and efficacy and safety of moxidectin compared to ivermectin in adults against infection with S. stercoralis in Laos and Cambodia (trial 2b). The efficacy of the treatment will be assessed by collecting three stool samples once pre-treatment and once 21 days post-treatment. The stool samples will be analyzed by a quantitative Baermann assay.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

This is a phase 2a single-blinded and a phase 2b double-blinded randomized clinical trial, which aims to determine efficacy and safety of (2a) seven ascending oral moxidectin dosages in 210 adults infected with S. stercoralis, namely placebo, 2 mg, 4 mg, 6 mg, 8 mg, 10 mg, 12 mg in Lao and (2b) the recommended dose moxidectin (i.e. the most promising dosage identified in trial A; between 2-12 mg) in comparison to the standard treatment dose of ivermectin (200 µg/kg) in 350 adults infected with S. stercoralis in Lao and Cambodia. Embedded in the trial is a pharmacokinetic/-dynamic study with the goal to measure moxidectin disposition in adults and to determine population pharmacokinetic (PK) parameters of the optimal dose of moxidectin in the treatment of S. stercoralis.

The primary objective is to determine the dose-response of moxidectin based on cure rates (CR) against S. stercoralis and to quantify the efficacy of the recommended dose to the standard treatment (ivermectin) in adults.

The secondary objectives of the trial are: Evaluation of the safety and tolerability of the dose-dependent treatment regimes, evaluation of the safety and tolerability of moxidectin compared to ivermectin, comparison of the larvae reduction rate (LRR) of the different treatment regimens against S. stercoralis (trial 2a,b), determination of an exposure- (including Cmax, area under curve (AUC) and tmax) -response correlation of moxidectin in adults, comparison of the exposure-response of moxidectin using venous and capillary blood, evaluation of the cure rate of the different moxidectin treatment regimens against co-infection and the determination of the population PK parameters of the optimal dose of moxidectin in the treatment of S. stercoralis.

After obtaining informed consent from each individual, the medical history of the participants will be assessed with a standardized questionnaire, in addition to a clinical examination carried out by the study physician before treatment. Enrollment will be based on collection and analysis by a quantitative Baermann method (in duplicates) of three stool samples. Randomization of participants into the different treatment arms will be stratified according to intensity of infection. The adults will also be interviewed before treatment, 3 and 24 hours as well as 21 days after treatment about the occurrence of adverse events (AE). The efficacy of the treatment will be determined 21 days post-treatment by collecting another three stool samples. All stool samples will be examined with duplicate Baermann assays recorded quantitatively. Co-infection with T. trichiura, A. lumbricoides and hookworm infection will be identified using duplicate Kato-Katz thick smears on stool samples.

A subsample of adults will further be sampled using finger pricking for micro sampling at 0, 2, 4, 8, 24, and 72 hours, 7 and 21 days post treatment to evaluate pharmacokinetic parameters (trial phase 2a) and at defined time windows, that are based on the PK model earned from trial 2a (trial phase 2b). For validation of the analytical method the subsample of one study arm (8 mg, trial phase 2a) will undergo venous blood sampling in addition to finger pricking.

An available case analysis (full analysis set according to the intention to treat principle) will be performed, including all subjects with primary end point data. Supplementary, a per-protocol analysis will be conducted. CRs will be calculated as the percentage of larvae-positive subjects at baseline who become larvae-negative after treatment. Larvae per gram (LPG) stool sample will be assessed by calculating the mean of the larvae counts from the three duplicate Baermann assays and divided by the mean weighted amount of these stool samples. The LRR will be calculated following: (LRR = (1-(mean at follow-up/mean at baseline))\*100) Geometric and arithmetic mean larvae counts will be calculated for the different treatment arms before and after treatment to assess the corresponding LRRs. Bootstrap resampling method with 2,000 replicates will be used to calculate 95% confidence intervals (CIs) for LRRs. Emax models using the dose finding package of the statistical software environment R will be implemented to predict the dose-response curves in terms of CRs and LRRs.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Strongyloides Stercoralis Infection

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Phase 2a: Parallel study with 7 treatment arms (including a placebo arm) Phase 2b: Parallel study with 2 treatment arms
Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Outcome Assessors
Phase 2a: single-blinded (participant and lab technician) Phase 2b: double-blinded (participant, Care Provider) PK sub-studies are single-blinded (participant)

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Phase 2a - Arm A

2 mg Moxidectin at day 0 administered orally

Group Type EXPERIMENTAL

Moxidectin

Intervention Type DRUG

Monotherapy, oral administration, single dose, fixed dose

Phase 2a - Arm B

4 mg Moxidectin at day 0 administered orally

Group Type EXPERIMENTAL

Moxidectin

Intervention Type DRUG

Monotherapy, oral administration, single dose, fixed dose

Phase 2a - Arm C

6 mg Moxidectin at day 0 administered orally

Group Type EXPERIMENTAL

Moxidectin

Intervention Type DRUG

Monotherapy, oral administration, single dose, fixed dose

Phase 2a - Arm D

8 mg Moxidectin at day 0 administered orally

Group Type EXPERIMENTAL

Moxidectin

Intervention Type DRUG

Monotherapy, oral administration, single dose, fixed dose

Phase 2a - Arm E

10 mg Moxidectin at day 0 administered orally

Group Type EXPERIMENTAL

Moxidectin

Intervention Type DRUG

Monotherapy, oral administration, single dose, fixed dose

Phase 2a - Arm F

12 mg Moxidectin at day 0 administered orally

Group Type EXPERIMENTAL

Moxidectin

Intervention Type DRUG

Monotherapy, oral administration, single dose, fixed dose

Phase 2a - Arm G

matching Placebo tablet(s) at day 0 administered orally

Group Type PLACEBO_COMPARATOR

Placebo oral tablet

Intervention Type DRUG

Monotherapy, oral administration, single dose, matching number of tablets

Phase 2b - Arm A

the recommended dose moxidectin (i.e. the most promising dosage identified in phase 2a; between 2-12 mg) at day 0 administered orally

\+ Ivermectin placebo, corresponding to Phase 2b - Arm B

Group Type EXPERIMENTAL

Moxidectin

Intervention Type DRUG

Monotherapy, oral administration, single dose, fixed dose

Phase 2b - Arm B

200 µg/kg ivermectin at day 0 administered orally

\+ Moxidectin placebo, corresponding to Phase 2b - Arm A

Group Type ACTIVE_COMPARATOR

Ivermectin

Intervention Type DRUG

Monotherapy, oral administration, single dose, weight dependent

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Moxidectin

Monotherapy, oral administration, single dose, fixed dose

Intervention Type DRUG

Ivermectin

Monotherapy, oral administration, single dose, weight dependent

Intervention Type DRUG

Placebo oral tablet

Monotherapy, oral administration, single dose, matching number of tablets

Intervention Type DRUG

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Adults (≥ 18 years) infected with S. stercoralis
* Absence of major systemic illnesses
* Written informed consent signed by individual

Exclusion Criteria

* Any abnormal medical conditions or chronic disease
* Negative diagnostic result for S. stercoralis
* No written informed consent by individual.
* Pregnant and lactating women.
* Recent use of anthelmintic drug (within past 4 weeks), attending other clinical trials during the study
* Known allergy to study medications (i.e. moxidectin, ivermectin)
* Currently taking medications with known interaction (i.e. for warfarin)
Minimum Eligible Age

18 Years

Maximum Eligible Age

60 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

National Institute of Public Health, Vientiane, Laos

OTHER

Sponsor Role collaborator

Jennifer Keiser

OTHER

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Jennifer Keiser

Prof. Jennifer Keiser, PhD

Responsibility Role SPONSOR_INVESTIGATOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Jennifer Keiser, Prof. Dr.

Role: PRINCIPAL_INVESTIGATOR

Swiss TPH

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

National Institute of Public Health

Vientiane, , Laos

Site Status

Countries

Review the countries where the study has at least one active or historical site.

Cambodia Laos

References

Explore related publications, articles, or registry entries linked to this study.

Sprecher VP, Hofmann D, Savathdy V, Xayavong P, Norkhankhame C, Huy R, Khieu V, Sayasone S, Hattendorf J, Keiser J. Efficacy and safety of moxidectin compared with ivermectin against Strongyloides stercoralis infection in adults in Laos and Cambodia: a randomised, double-blind, non-inferiority, phase 2b/3 trial. Lancet Infect Dis. 2024 Feb;24(2):196-205. doi: 10.1016/S1473-3099(23)00507-8. Epub 2023 Nov 7.

Reference Type DERIVED
PMID: 37949090 (View on PubMed)

Smit C, Hofmann D, Sayasone S, Keiser J, Pfister M. Characterization of the Population Pharmacokinetics of Moxidectin in Adults Infected with Strongyloides Stercoralis: Support for a Fixed-Dose Treatment Regimen. Clin Pharmacokinet. 2022 Jan;61(1):123-132. doi: 10.1007/s40262-021-01048-4. Epub 2021 Jul 23.

Reference Type DERIVED
PMID: 34296417 (View on PubMed)

Hofmann D, Sayasone S, Sengngam K, Chongvilay B, Hattendorf J, Keiser J. Efficacy and safety of ascending doses of moxidectin against Strongyloides stercoralis infections in adults: a randomised, parallel-group, single-blinded, placebo-controlled, dose-ranging, phase 2a trial. Lancet Infect Dis. 2021 Aug;21(8):1151-1160. doi: 10.1016/S1473-3099(20)30691-5. Epub 2021 Mar 30.

Reference Type DERIVED
PMID: 33798487 (View on PubMed)

Provided Documents

Download supplemental materials such as informed consent forms, study protocols, or participant manuals.

Document Type: Study Protocol and Statistical Analysis Plan

View Document

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

3

Identifier Type: -

Identifier Source: org_study_id