Topical Ruxolitinib Evaluation in Vitiligo Study 1 (TRuE-V1)

NCT ID: NCT04052425

Last Updated: 2025-08-22

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

330 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-09-20

Study Completion Date

2021-10-21

Brief Summary

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The purpose of this study is to evaluate the efficacy and safety of ruxolitinib cream in adolescent and adult participants with non-segmental vitiligo for whom total body involved vitiligo area (facial and nonfacial) does not exceed 10% body surface area (BSA).

Detailed Description

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Conditions

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Non-segmental Vitiligo

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

CROSSOVER

Participants will receive ruxolitinib cream or vehicle for 24 weeks, after which they will be offered the opportunity to continue in the treatment extension period. Participants initially randomized to vehicle will be crossed over to active drug, and participants treated with ruxolitinib cream will receive an additional 28 weeks of treatment with ruxolitinib cream.
Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors

Study Groups

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Double-Blind Period: Ruxolitinib cream 1.5% BID

Participants applied ruxolitinib 1.5% cream twice daily (BID) for 24 weeks.

Group Type EXPERIMENTAL

Ruxolitinib cream

Intervention Type DRUG

Ruxolitinib cream is a topical formulation applied as a thin film to affected areas.

Double-Blind Period: Vehicle cream BID

Participants applied matching vehicle cream BID for 24 weeks.

Group Type PLACEBO_COMPARATOR

Vehicle

Intervention Type DRUG

Vehicle cream is a topical formulation applied as a thin film to affected areas.

Treatment-Extension Period: Ruxolitinib cream 1.5% BID

Participants who completed the Week 24 assessments with no safety concerns could continue into the 28-week Treatment-Extension Period. Participants who applied ruxolitinib cream 1.5% BID during the Double-Blind Period continued to apply ruxolitinib cream 1.5% BID for an additional 28 weeks in the Treatment-Extension Period.

Group Type EXPERIMENTAL

Ruxolitinib cream

Intervention Type DRUG

Ruxolitinib cream is a topical formulation applied as a thin film to affected areas.

Treatment-Extension Period: Vehicle cream to Ruxolitinib cream 1.5% BID

Participants who completed the Week 24 assessments with no safety concerns could continue into the 28-week Treatment-Extension Period. Participants who applied vehicle cream BID during the Double-Blind Period applied ruxolitinib cream 1.5%m BID for 28 weeks in the Treatment-Extension Period.

Group Type EXPERIMENTAL

Ruxolitinib cream

Intervention Type DRUG

Ruxolitinib cream is a topical formulation applied as a thin film to affected areas.

Vehicle

Intervention Type DRUG

Vehicle cream is a topical formulation applied as a thin film to affected areas.

Interventions

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Ruxolitinib cream

Ruxolitinib cream is a topical formulation applied as a thin film to affected areas.

Intervention Type DRUG

Vehicle

Vehicle cream is a topical formulation applied as a thin film to affected areas.

Intervention Type DRUG

Other Intervention Names

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INCB018424 cream

Eligibility Criteria

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Inclusion Criteria

* Clinical diagnosis of non-segmental vitiligo with depigmented area including ≥ 0.5% BSA on the face, ≥ 0.5 F-VASI, ≥ 3% BSA on nonfacial areas, ≥ 3 T-VASI, and total body vitiligo area (facial and nonfacial) not exceeding 10% BSA.
* Agree to discontinue all agents used to treat vitiligo from screening through the final safety follow-up visit. Over-the-counter preparations deemed acceptable by the investigator and camouflage makeups are permitted.
* Must be willing to take appropriate contraceptive measures to avoid pregnancy or fathering a child for the duration of study participation.

Exclusion Criteria

* No pigmented hair within any of the vitiligo areas on the face.
* Other forms of vitiligo (eg, segmental) or other differential diagnosis of vitiligo or other skin depigmentation disorders (eg, piebaldism, pityriasis alba, leprosy, postinflammatory hypopigmentation, progressive macule hypomelanosis, nevus anemicus, chemical leukoderma, and tinea versicolor).
* Have used depigmentation treatments (eg, monobenzone) for past treatment of vitiligo or other pigmented areas.
* Use of protocol-defined treatments within the indicated washout period before baseline.
Minimum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Incyte Corporation

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Kathleen Butler, MD

Role: STUDY_DIRECTOR

Incyte Corporation

Locations

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Cahaba Dermatology

Hoover, Alabama, United States

Site Status

Cognitive Clinical Trials Scottsdale Btc Ppds

Scottsdale, Arizona, United States

Site Status

Burke Pharmaceutical Research

Hot Springs, Arkansas, United States

Site Status

First Oc Dermatology

Fountain Valley, California, United States

Site Status

Marvel Clinical Research Llc

Huntington Beach, California, United States

Site Status

Rady Children'S Hospital - San Diego

San Diego, California, United States

Site Status

University of California San Francisco Sub Location

San Francisco, California, United States

Site Status

Clinical Research Center of Ct

Danbury, Connecticut, United States

Site Status

Harmony Medical Research Institute

Hialeah, Florida, United States

Site Status

San Marcus Research Clinic Inc.

Miami Lakes, Florida, United States

Site Status

ForCare Medical Center

Tampa, Florida, United States

Site Status

Forcare Clinical Research Fcr Forward Clinical Trials, Inc

Tampa, Florida, United States

Site Status

Metabolic Research Institute Inc

West Palm Beach, Florida, United States

Site Status

Northwestern University

Chicago, Illinois, United States

Site Status

Clinical Trials Management Llc

Metairie, Louisiana, United States

Site Status

Great Lakes Research Group Inc

Bay City, Michigan, United States

Site Status

Dermatology Specialists of Brighton

Brighton, Michigan, United States

Site Status

Suny Downstate Medical Center

Brooklyn, New York, United States

Site Status

Forest Hills Dermatology Group

Forest Hills, New York, United States

Site Status

The Dermatology Specialists Greenwich

New York, New York, United States

Site Status

Wake Research Associates Llc

Raleigh, North Carolina, United States

Site Status

Wake Forest University

Winston-Salem, North Carolina, United States

Site Status

Kgl Skin Study Center

Broomall, Pennsylvania, United States

Site Status

Dermatology Associates of Plymouth Meeting

Plymouth Meeting, Pennsylvania, United States

Site Status

Palmetto Clinical Trial Services

Anderson, South Carolina, United States

Site Status

International Clinical Research Tennessee Llc

Murfreesboro, Tennessee, United States

Site Status

Progressive Clinical Research

San Antonio, Texas, United States

Site Status

Dermatology Clinical Research Center of San Antonio

San Antonio, Texas, United States

Site Status

Dermatology Specialists of Spokane

Spokane, Washington, United States

Site Status

Multiprofile Hospital For Active Treatement - Clinic of Dermatology and Venerology

Pleven, , Bulgaria

Site Status

DCC 28

Sofia, , Bulgaria

Site Status

Medical Center Eurohealth

Sofia, , Bulgaria

Site Status

Dermatology Research Institute

Calgary, Alberta, Canada

Site Status

Institute For Skin Advancement

Calgary, Alberta, Canada

Site Status

Skin Centre For Dermatology

Peterborough, Ontario, Canada

Site Status

Windsor Clinical Research Inc

Windsor, Ontario, Canada

Site Status

McGill University Health Centre / Carey/Wang Clinic

Montreal, Quebec, Canada

Site Status

Siena Medical Reserch Corporation

Westmount, Quebec, Canada

Site Status

Centre Hospitalier Universitaire de Nantes

Nantes, , France

Site Status

Chu de Nice - Hopital L'Archet 1

Nice, , France

Site Status

Hopital Charles Nicolle Chu Rouen - Hopital de Bois-Guillaume

Rouen, , France

Site Status

Chu de Toulouse Hopital Larrey Centre de Reference Des Maladies Rares de La Peau Service de Dermatol

Toulouse, , France

Site Status

University Clinic Carl Gustav Carus, Technical University Dresden

Dresden, , Germany

Site Status

Universitatsklinik Munster Dermatologie

Münster, , Germany

Site Status

Presidio Ospedaliero Piero Palagi

Florence, , Italy

Site Status

Istituto Dermatologico San Gallicano

Rome, , Italy

Site Status

Synexus - Polska Sp Z Oo Oddzial W Gdansk

Gdansk, , Poland

Site Status

Synexus Polska Sp. Z O.O. Oddzial W Gdyni

Gdynia, , Poland

Site Status

Synexus - Sp Z Oo Oddzial W Katowice

Katowice, , Poland

Site Status

Dermedic Dr. Zdybski

Ostrowiec, , Poland

Site Status

Synexus Polska Sp. Z O.O. Oddzial W Poznaniu

Poznan, , Poland

Site Status

Poradnia Dermatologiczno-Wenerologiczna Mediderm S.C. Nzoz

Torun, , Poland

Site Status

Synexus Polska Sp. Z O.O. Oddzial We Wroclawiu

Wroclaw, , Poland

Site Status

Hospital Cima Sanitas

Barcelona, , Spain

Site Status

Hospital Clinic de Barcelona

Barcelona, , Spain

Site Status

Hospital Universitario San Cecilio

Granada, , Spain

Site Status

Clinica Universidad de Navarra (Cun)

Pamplona, , Spain

Site Status

Countries

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United States Bulgaria Canada France Germany Italy Poland Spain

References

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Rosmarin D, Pandya AG, Passeron T, Forman SB, Zdybski J, Amster M, Feser C, Papp KA, Nuara A, Kornacki D, Wei S, Ren H, Harris JE, Ezzedine K. Long-Term Integrated Safety Summary of Ruxolitinib Cream in Phase 3 Clinical Trials of Patients with Vitiligo. Dermatol Ther (Heidelb). 2025 Oct 22. doi: 10.1007/s13555-025-01555-3. Online ahead of print.

Reference Type DERIVED
PMID: 41125994 (View on PubMed)

Seneschal J, Wolkerstorfer A, Desai SR, Grimes P, Ezzedine K, Pandya AG, Kornacki D, Wei S, Passeron T, Rosmarin D. Efficacy and Safety of Ruxolitinib Cream in Vitiligo by Patient Characteristic Subgroups: Descriptive Pooled Analysis From Two Phase 3 Studies. Dermatol Ther (Heidelb). 2025 May;15(5):1227-1238. doi: 10.1007/s13555-025-01381-7. Epub 2025 Mar 29.

Reference Type DERIVED
PMID: 40156697 (View on PubMed)

Rosmarin D, Passeron T, Pandya AG, Grimes P, Harris JE, Desai SR, Lebwohl M, Ruer-Mulard M, Seneschal J, Wolkerstorfer A, Kornacki D, Sun K, Butler K, Ezzedine K; TRuE-V Study Group. Two Phase 3, Randomized, Controlled Trials of Ruxolitinib Cream for Vitiligo. N Engl J Med. 2022 Oct 20;387(16):1445-1455. doi: 10.1056/NEJMoa2118828.

Reference Type DERIVED
PMID: 36260792 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

Other Identifiers

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2019-000846-37

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

INCB 18424-306

Identifier Type: -

Identifier Source: org_study_id

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