Trial Outcomes & Findings for GLAD-AML - Glasdegib (Pf-04449913) With Two Standard Decitabine Regimens for Older Patients With Poor-risk Acute Myeloid Leukemia (NCT NCT04051996)

NCT ID: NCT04051996

Last Updated: 2021-10-15

Results Overview

The complete remission (CR) and complete remission with incomplete count recovery (CRi) combined rate will be defined by the 2017 European LeukemiaNet (ELN) AML response criteria.

Recruitment status

TERMINATED

Study phase

PHASE2

Target enrollment

1 participants

Primary outcome timeframe

Up to 2 years

Results posted on

2021-10-15

Participant Flow

Participant milestones

Participant milestones
Measure
DAC5
Glasdegib will be administered at the starting dose of 100 mg orally once daily and continuously in combination with either DAC5 (decitabine 20 mg/m2 IV on a 5-day schedule) or DAC10 (decitabine 20 mg/m2 IV on a 10-day schedule) as per randomization. Treatment will be administered in 28-day cycles. Glasdegib: Glasdegib will be administered at the starting dose of 100 mg orally once daily. Decitabine: Decitabine will be administered per local label and will be administered by IV infusion at a dose of 20 mg/m2/day for either 5 days or 10 days as determined by randomization. Each cycle will be every 28 days.
DAC10
Glasdegib will be administered at the starting dose of 100 mg orally once daily and continuously in combination with either DAC5 (decitabine 20 mg/m2 IV on a 5-day schedule) or DAC10 (decitabine 20 mg/m2 IV on a 10-day schedule) as per randomization. Treatment will be administered in 28-day cycles. Glasdegib: Glasdegib will be administered at the starting dose of 100 mg orally once daily. Decitabine: Decitabine will be administered per local label and will be administered by IV infusion at a dose of 20 mg/m2/day for either 5 days or 10 days as determined by randomization. Each cycle will be every 28 days.
Overall Study
STARTED
1
0
Overall Study
COMPLETED
1
0
Overall Study
NOT COMPLETED
0
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

GLAD-AML - Glasdegib (Pf-04449913) With Two Standard Decitabine Regimens for Older Patients With Poor-risk Acute Myeloid Leukemia

Baseline characteristics by cohort

Baseline data not reported

PRIMARY outcome

Timeframe: Up to 2 years

Population: Only 1 patient was enrolled in the study prior to termination and therefore would be identified through presenting these characteristics.

The complete remission (CR) and complete remission with incomplete count recovery (CRi) combined rate will be defined by the 2017 European LeukemiaNet (ELN) AML response criteria.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Up to 2 years

Population: Only 1 patient was enrolled in the study prior to termination and therefore would be identified through presenting these characteristics.

Overall survival (OS) is defined as the time from date of first study treatment to date of death due to any cause.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Up to 2 years

Population: Only 1 patient was enrolled in the study prior to termination and therefore would be identified through presenting these characteristics.

Event-free survival (EFS) will be monitored up to 2 years.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Up to 2 years

Population: Only 1 patient was enrolled in the study prior to termination and therefore would be identified through presenting these characteristics.

Relapse-free survival (RFS) will be monitored up to 2 years.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Up to 2 years

Population: Only 1 patient was enrolled in the study prior to termination and therefore would be identified through presenting these characteristics.

The time to complete remission (CR) and complete remission with incomplete count recovery (CRi) will be collected as a secondary outcome.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Up to 2 years

Population: Only 1 patient was enrolled in the study prior to termination and therefore would be identified through presenting these characteristics.

The duration of complete remission (CR) and complete remission with incomplete count recovery (CRi) will be collected as a secondary outcome.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Up to 2 years

Population: Only 1 patient was enrolled in the study prior to termination and therefore would be identified through presenting these characteristics.

Bone marrow mutational clearance of frequently-mutated genes in AML (e.g. NPM1, CEBPA, DNMT3A, RUNX1, TET2, IDH1/2) via next-generation DNA sequencing will be monitored up to 2 years.

Outcome measures

Outcome data not reported

Adverse Events

DAC5

Serious events: 1 serious events
Other events: 0 other events
Deaths: 1 deaths

DAC10

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
DAC5
n=1 participants at risk
Glasdegib will be administered at the starting dose of 100 mg orally once daily and continuously in combination with either DAC5 (decitabine 20 mg/m2 IV on a 5-day schedule) or DAC10 (decitabine 20 mg/m2 IV on a 10-day schedule) as per randomization. Treatment will be administered in 28-day cycles. Glasdegib: Glasdegib will be administered at the starting dose of 100 mg orally once daily. Decitabine: Decitabine will be administered per local label and will be administered by IV infusion at a dose of 20 mg/m2/day for either 5 days or 10 days as determined by randomization. Each cycle will be every 28 days.
DAC10
Glasdegib will be administered at the starting dose of 100 mg orally once daily and continuously in combination with either DAC5 (decitabine 20 mg/m2 IV on a 5-day schedule) or DAC10 (decitabine 20 mg/m2 IV on a 10-day schedule) as per randomization. Treatment will be administered in 28-day cycles. Glasdegib: Glasdegib will be administered at the starting dose of 100 mg orally once daily. Decitabine: Decitabine will be administered per local label and will be administered by IV infusion at a dose of 20 mg/m2/day for either 5 days or 10 days as determined by randomization. Each cycle will be every 28 days.
Respiratory, thoracic and mediastinal disorders
Dyspnea
100.0%
1/1 • Number of events 1 • Up to 2 years
There was only 1 patient enrolled in the study before termination and therefore there was only 1 treatment arm utilized.
0/0 • Up to 2 years
There was only 1 patient enrolled in the study before termination and therefore there was only 1 treatment arm utilized.
Injury, poisoning and procedural complications
Acute Kidney Injury
100.0%
1/1 • Number of events 1 • Up to 2 years
There was only 1 patient enrolled in the study before termination and therefore there was only 1 treatment arm utilized.
0/0 • Up to 2 years
There was only 1 patient enrolled in the study before termination and therefore there was only 1 treatment arm utilized.

Other adverse events

Adverse event data not reported

Additional Information

Dr. Amer Zeidan

Yale University

Phone: (203) 200-4363

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place