Trial Outcomes & Findings for Omega -3 Fatty Acid in Combination With Tyrosine Kinase Inhibitors in Chronic Myeloid Leukemia (NCT NCT04006847)

NCT ID: NCT04006847

Last Updated: 2022-07-01

Results Overview

Recommended Phase II dose of EPA will be established by using a standard 3 + 3 statistical design to determine the MTD as assessed by DLTs when administered orally in combination with a TKI in subjects with CML in stable chronic phase. Toxicity will be evaluated using the NCI Common Toxicity Criteria (CTC) version 5.0.

Recruitment status

TERMINATED

Study phase

PHASE1/PHASE2

Target enrollment

1 participants

Primary outcome timeframe

the time of initiation of the study medication to 30 days after last dose of study medication

Results posted on

2022-07-01

Participant Flow

One subject was consented but withdrew from participation.

Participant milestones

Participant milestones
Measure
Eicosapentaenoic Acid (EPA)
Phase I: TKI with escalating/de-escalating doses of EPA to determine MTD. Phase I dose levels: Dose Level 1 = EPA 1500 mg orally once per day; Dose Level 2 = EPA 2000 mg orally once per day; Dose Level 3 = EPA 3000 mg orally once per day; Dose Level -1 = EPA 1000 mg orally once per day; Dose Level -2 = EPA 500 mg orally once per day. Phase II: TKI administered in combination with the recommended Phase II dose of EPA Eicosapentaenoic Acid: Eicosapentaenoic Acid once per day orally Tyrosine kinase inhibitor: Tyrosine kinase inhibitor to be administered at subjects' pre-study dose
Overall Study
STARTED
1
Overall Study
COMPLETED
0
Overall Study
NOT COMPLETED
1

Reasons for withdrawal

Reasons for withdrawal
Measure
Eicosapentaenoic Acid (EPA)
Phase I: TKI with escalating/de-escalating doses of EPA to determine MTD. Phase I dose levels: Dose Level 1 = EPA 1500 mg orally once per day; Dose Level 2 = EPA 2000 mg orally once per day; Dose Level 3 = EPA 3000 mg orally once per day; Dose Level -1 = EPA 1000 mg orally once per day; Dose Level -2 = EPA 500 mg orally once per day. Phase II: TKI administered in combination with the recommended Phase II dose of EPA Eicosapentaenoic Acid: Eicosapentaenoic Acid once per day orally Tyrosine kinase inhibitor: Tyrosine kinase inhibitor to be administered at subjects' pre-study dose
Overall Study
Product issue
1

Baseline Characteristics

Omega -3 Fatty Acid in Combination With Tyrosine Kinase Inhibitors in Chronic Myeloid Leukemia

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Eicosapentaenoic Acid (EPA)
n=1 Participants
Phase I: TKI with escalating/de-escalating doses of EPA to determine MTD. Phase I dose levels: Dose Level 1 = EPA 1500 mg orally once per day; Dose Level 2 = EPA 2000 mg orally once per day; Dose Level 3 = EPA 3000 mg orally once per day; Dose Level -1 = EPA 1000 mg orally once per day; Dose Level -2 = EPA 500 mg orally once per day. Phase II: TKI administered in combination with the recommended Phase II dose of EPA Eicosapentaenoic Acid: Eicosapentaenoic Acid once per day orally Tyrosine kinase inhibitor: Tyrosine kinase inhibitor to be administered at subjects' pre-study dose
Age, Continuous
55 years
STANDARD_DEVIATION 0 • n=5 Participants
Sex: Female, Male
Female
0 Participants
n=5 Participants
Sex: Female, Male
Male
1 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
0 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
1 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
0 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=5 Participants
Race (NIH/OMB)
White
1 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
Region of Enrollment
United States
1 participants
n=5 Participants

PRIMARY outcome

Timeframe: the time of initiation of the study medication to 30 days after last dose of study medication

Population: data were not collected

Recommended Phase II dose of EPA will be established by using a standard 3 + 3 statistical design to determine the MTD as assessed by DLTs when administered orally in combination with a TKI in subjects with CML in stable chronic phase. Toxicity will be evaluated using the NCI Common Toxicity Criteria (CTC) version 5.0.

Outcome measures

Outcome data not reported

PRIMARY outcome

Timeframe: 1 year

Population: data were not collected

BCR-ABL transcript levels will be assessed every 3 months post initiation of Eicosapentaenoic Acid to assess Anti-CML response.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: 1 year

Population: data were not collected

Log reduction from stable molecular response with bcr-abl PCR at MR 3 or more to bcr-abl to major molecular response (MR 4.5) or complete molecular response

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: 2 years

Population: data were not collected

Apoptosis will be analyzed by in vitro correlative studies using subject's plasma with effect on known leukemia cell line with CML leukemic stem cells. EPA metabolite will be examined by flow cytometry using Annexin V staining and adding serum from treated study subject to murine CML cells grown in vitro culture. The evaluation will be done at baseline, Month 1, and every 3 months up to year 2

Outcome measures

Outcome data not reported

Adverse Events

Eicosapentaenoic Acid (EPA)

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Adverse event data not reported

Additional Information

Seema Naik, MD

Penn State Health

Phone: 7175318678

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place