Study to Evaluate the Safety and Efficacy of Oral CR845 (Difelikefalin) in Patients With Primary Biliary Cholangitis (PBC) and Moderate-to-Severe Pruritus

NCT ID: NCT03995212

Last Updated: 2023-07-03

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

14 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-06-25

Study Completion Date

2022-06-29

Brief Summary

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This is a multicenter, randomized, double-blind, placebo-controlled study to evaluate the safety and efficacy of twice-daily (BID) oral CR845 1.0 mg in patients with PBC with moderate-to-severe pruritus. The study includes a 16-week Treatment Period.

Detailed Description

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This study will consist of a Screening Visit, a 7-day Run-in Period, a 16-week Treatment Period, and a Follow-up Visit (approximately 7-10 days after the last dose of study drug). Informed consent will be obtained prior to performing any study-specific procedures.

The Screening Visit will occur within 7 to 28 days prior to randomization to assess eligibility.

Day 1 of the Treatment Period will be defined as the day of the administration of the first dose of study drug. If patients continue to meet all inclusion and no exclusion criteria at the end of the 7-day Run-in Period, they will be randomized in a 1:1 ratio to receive either placebo or CR845 tablets at a dose of 1.0 mg orally BID for 16 weeks.

Conditions

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Cholestatic Pruritus

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

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CR845 1.0 mg

Oral CR845 1.0 mg tablet administered twice daily

Group Type ACTIVE_COMPARATOR

CR845 1.0 mg

Intervention Type DRUG

Oral CR845 1.0 mg administered twice daily

Placebo

Oral placebo tablet administered twice daily

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Oral Placebo administered twice daily

Interventions

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CR845 1.0 mg

Oral CR845 1.0 mg administered twice daily

Intervention Type DRUG

Placebo

Oral Placebo administered twice daily

Intervention Type DRUG

Other Intervention Names

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CR845 Difelikefalin

Eligibility Criteria

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Inclusion Criteria

To be eligible for inclusion into the study, a patient must meet the following criteria:

* Confirmed diagnosis of PBC;
* If currently taking ursodeoxycholic acid (UDCA), should be on stable dose for \>12 weeks prior to screening and plan on continuing to take UDCA throughout the study;
* If previously taking UDCA, should have discontinued its use \>12 weeks prior to screening;
* Self-reports experiencing daily or near-daily pruritus during the month prior to screening;
* Prior to randomization has a mean baseline WI-NRS score indicative of moderate to severe pruritus.

Exclusion Criteria

A patient will be excluded from the study if any of the following criteria are met:

* Presence of Child-Pugh Class C decompensated cirrhosis at screening;
* Itching secondary to biliary obstruction;
* History or presence of hepatocellular carcinoma, hepatic abscess, or acute portal vein thrombosis;
* Current placement on liver transplantation list with anticipated liver transplant during the course of the study or current Model for End-stage Liver Disease (MELD) score ≥15;
* Alanine aminotransferase or aspartate aminotransferase \>5 × upper limit of normal at screening, or within 2 months prior to screening;
* Anticipates receiving an opioid antagonist (eg, naloxone, naltrexone) or opioid-mixed agonist-antagonist (eg, buprenorphine, nalbuphine) from the start of screening through the end of the Treatment Period;
* New or change of treatment with antihistamines and corticosteroids (oral, intravenous, or topical), opioids, gabapentin, pregabalin, cholestyramine, rifampicin or fibrates within 14 days prior to screening.
Minimum Eligible Age

18 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Cara Therapeutics, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Frédérique Menzaghi, PhD

Role: STUDY_DIRECTOR

Cara Therapeutics

Locations

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Cara Therapeutics Study Site

Coronado, California, United States

Site Status

Cara Therapeutics Study Site

Rialto, California, United States

Site Status

Cara Therapeutics Study Site

San Francisco, California, United States

Site Status

Cara Therapeutics Study Site

Colorado Springs, Colorado, United States

Site Status

Cara Therapeutics Study Site

Miami, Florida, United States

Site Status

Cara Therapeutics Study Site

Plantation, Florida, United States

Site Status

Cara Therapeutics Study Site

Indianapolis, Indiana, United States

Site Status

Cara Therapeutics Study Site 2

Boston, Massachusetts, United States

Site Status

Cara Therapeutics Study Site

Boston, Massachusetts, United States

Site Status

Cara Therapeutics Study Site

New York, New York, United States

Site Status

Cara Therapeutics Study Site

Nashville, Tennessee, United States

Site Status

Cara Therapeutics Study Site

Arlington, Texas, United States

Site Status

Cara Therapeutics Study Site

Newport News, Virginia, United States

Site Status

Cara Therapeutics Study Site

Morgantown, West Virginia, United States

Site Status

Countries

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United States

Other Identifiers

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CR845-210401

Identifier Type: -

Identifier Source: org_study_id

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