Trial Outcomes & Findings for Minimally Invasive Fetoscopic Regenerative Repair of Spina Bifida - A Pilot Study (NCT NCT03936322)

NCT ID: NCT03936322

Last Updated: 2025-02-24

Results Overview

Total number of maternal adverse events

Recruitment status

COMPLETED

Study phase

NA

Target enrollment

3 participants

Primary outcome timeframe

From time of surgery until delivery (up to 21 weeks)

Results posted on

2025-02-24

Participant Flow

Participant milestones

Participant milestones
Measure
Pregnant Women Diagnosed With Fetal Myelomeningocele
Women subjects who are pregnant and diagnosed with myelomeningocele (MMC), also known as fetal spina bifida or neural tube defect, will undergo a minimally invasive fetoscopic repair of MMC. Minimally invasive fetoscopic repair of MMC: Uses a technique to open your belly (skin, muscles and abdomen) without opening the uterus, except for a small puncture, to repair the fetal spina bifida defect during the second trimester of pregnancy.
Overall Study
STARTED
3
Overall Study
COMPLETED
1
Overall Study
NOT COMPLETED
2

Reasons for withdrawal

Reasons for withdrawal
Measure
Pregnant Women Diagnosed With Fetal Myelomeningocele
Women subjects who are pregnant and diagnosed with myelomeningocele (MMC), also known as fetal spina bifida or neural tube defect, will undergo a minimally invasive fetoscopic repair of MMC. Minimally invasive fetoscopic repair of MMC: Uses a technique to open your belly (skin, muscles and abdomen) without opening the uterus, except for a small puncture, to repair the fetal spina bifida defect during the second trimester of pregnancy.
Overall Study
Lost to Follow-up
1
Overall Study
Infant Death after delivery; therefore, no further follow up occurred
1

Baseline Characteristics

Minimally Invasive Fetoscopic Regenerative Repair of Spina Bifida - A Pilot Study

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Pregnant Women Diagnosed With Fetal Myelomeningocele
n=3 Participants
Women subjects who are pregnant and diagnosed with myelomeningocele (MMC), also known as fetal spina bifida or neural tube defect, will undergo a minimally invasive fetoscopic repair of MMC. Minimally invasive fetoscopic repair of MMC: Uses a technique to open your belly (skin, muscles and abdomen) without opening the uterus, except for a small puncture, to repair the fetal spina bifida defect during the second trimester of pregnancy.
Age, Categorical
<=18 years
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
3 Participants
n=5 Participants
Age, Categorical
>=65 years
0 Participants
n=5 Participants
Sex: Female, Male
Female
3 Participants
n=5 Participants
Sex: Female, Male
Male
0 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
1 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
2 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants

PRIMARY outcome

Timeframe: From time of surgery until delivery (up to 21 weeks)

Total number of maternal adverse events

Outcome measures

Outcome measures
Measure
Pregnant Women Diagnosed With Fetal Myelomeningocele
n=3 Participants
Women subjects who are pregnant and diagnosed with myelomeningocele (MMC), also known as fetal spina bifida or neural tube defect, will undergo a minimally invasive fetoscopic repair of MMC. Minimally invasive fetoscopic repair of MMC: Uses a technique to open your belly (skin, muscles and abdomen) without opening the uterus, except for a small puncture, to repair the fetal spina bifida defect during the second trimester of pregnancy.
Maternal Adverse Events
2 participants

PRIMARY outcome

Timeframe: From the time of surgery until 28 days of life (up 25 weeks)

Total number of neonatal adverse events

Outcome measures

Outcome measures
Measure
Pregnant Women Diagnosed With Fetal Myelomeningocele
n=3 Participants
Women subjects who are pregnant and diagnosed with myelomeningocele (MMC), also known as fetal spina bifida or neural tube defect, will undergo a minimally invasive fetoscopic repair of MMC. Minimally invasive fetoscopic repair of MMC: Uses a technique to open your belly (skin, muscles and abdomen) without opening the uterus, except for a small puncture, to repair the fetal spina bifida defect during the second trimester of pregnancy.
Neonatal Adverse Events
1 participants

Adverse Events

Pregnant Women Diagnosed With Fetal Myelomeningocele

Serious events: 1 serious events
Other events: 1 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Pregnant Women Diagnosed With Fetal Myelomeningocele
n=3 participants at risk
Women subjects who are pregnant and diagnosed with myelomeningocele (MMC), also known as fetal spina bifida or neural tube defect, will undergo a minimally invasive fetoscopic repair of MMC. Minimally invasive fetoscopic repair of MMC: Uses a technique to open your belly (skin, muscles and abdomen) without opening the uterus, except for a small puncture, to repair the fetal spina bifida defect during the second trimester of pregnancy.
Pregnancy, puerperium and perinatal conditions
Placenta abruption/neonatal demise
33.3%
1/3 • Number of events 1 • 1 year

Other adverse events

Other adverse events
Measure
Pregnant Women Diagnosed With Fetal Myelomeningocele
n=3 participants at risk
Women subjects who are pregnant and diagnosed with myelomeningocele (MMC), also known as fetal spina bifida or neural tube defect, will undergo a minimally invasive fetoscopic repair of MMC. Minimally invasive fetoscopic repair of MMC: Uses a technique to open your belly (skin, muscles and abdomen) without opening the uterus, except for a small puncture, to repair the fetal spina bifida defect during the second trimester of pregnancy.
Pregnancy, puerperium and perinatal conditions
premature rupture of the membranes
33.3%
1/3 • Number of events 1 • 1 year

Additional Information

Rodrigo Ruano MD PhD

UNIVERSITY OF MIAMI

Phone: (305) 585-5610

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place