Trial Outcomes & Findings for A Study to Determine the Bioavailability of Lanadelumab (SHP643) Administered Subcutaneously With the Prefilled Syringe and the Autoinjector in Healthy Adult Volunteer Participants. (NCT NCT03918239)

NCT ID: NCT03918239

Last Updated: 2020-12-08

Results Overview

AUC(0-last) of SHP643 in plasma was reported. Geometric mean and geometric coefficient of variation percent (CV%) was reported.

Recruitment status

COMPLETED

Study phase

PHASE1

Target enrollment

190 participants

Primary outcome timeframe

Pre-dose, 8, 24, 48, 72, 96, 168, 336, 504, 672, 1008, 1344, 2016, 2664 hours post dose

Results posted on

2020-12-08

Participant Flow

This study was conducted at a single site in United States of America from 14 May 2019 (first participant first visit) to 13 November 2019 (last participant last visit).

A total of 190 participants were enrolled and received the treatment. Out of which, 173 participants completed this study.

Participant milestones

Participant milestones
Measure
SHP643 Prefilled Syringe (PFS)
Participants received 300 milligram (mg) of SHP643 PFS Subcutaneous (SC) injection into the abdomen on Day 1 during the in-house treatment period (Day 1 to Day 5).
SHP643 Autoinjector (AI)
Participants received 300 mg of SHP643 AI SC injection into the abdomen on Day 1 during the in-house treatment period (Day 1 to Day 5).
Overall Study
STARTED
94
96
Overall Study
COMPLETED
84
89
Overall Study
NOT COMPLETED
10
7

Reasons for withdrawal

Reasons for withdrawal
Measure
SHP643 Prefilled Syringe (PFS)
Participants received 300 milligram (mg) of SHP643 PFS Subcutaneous (SC) injection into the abdomen on Day 1 during the in-house treatment period (Day 1 to Day 5).
SHP643 Autoinjector (AI)
Participants received 300 mg of SHP643 AI SC injection into the abdomen on Day 1 during the in-house treatment period (Day 1 to Day 5).
Overall Study
Lost to Follow-up
3
1
Overall Study
Pregnancy
0
2
Overall Study
Withdrawal by Subject
3
3
Overall Study
positive urine drug screening results
4
1

Baseline Characteristics

A Study to Determine the Bioavailability of Lanadelumab (SHP643) Administered Subcutaneously With the Prefilled Syringe and the Autoinjector in Healthy Adult Volunteer Participants.

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
SHP643 Prefilled Syringe (PFS)
n=94 Participants
Participants received 300 milligram (mg) of SHP643 PFS Subcutaneous (SC) injection into the abdomen on Day 1 during the in-house treatment period (Day 1 to Day 5).
SHP643 Autoinjector (AI)
n=96 Participants
Participants received 300 mg of SHP643 AI SC injection into the abdomen on Day 1 during the in-house treatment period (Day 1 to Day 5).
Total
n=190 Participants
Total of all reporting groups
Age, Continuous
39.6 Years
STANDARD_DEVIATION 10.04 • n=5 Participants
42.1 Years
STANDARD_DEVIATION 9.67 • n=7 Participants
40.8 Years
STANDARD_DEVIATION 9.91 • n=5 Participants
Sex: Female, Male
Female
41 Participants
n=5 Participants
55 Participants
n=7 Participants
96 Participants
n=5 Participants
Sex: Female, Male
Male
53 Participants
n=5 Participants
41 Participants
n=7 Participants
94 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
91 Participants
n=5 Participants
92 Participants
n=7 Participants
183 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
3 Participants
n=5 Participants
4 Participants
n=7 Participants
7 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
13 Participants
n=5 Participants
19 Participants
n=7 Participants
32 Participants
n=5 Participants
Race (NIH/OMB)
White
81 Participants
n=5 Participants
77 Participants
n=7 Participants
158 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants

PRIMARY outcome

Timeframe: Pre-dose, 8, 24, 48, 72, 96, 168, 336, 504, 672, 1008, 1344, 2016, 2664 hours post dose

Population: Pharmacokinetic (PK) set was defined as all randomized participants who received the complete dose of SHP643 and had sufficient data to calculate at least one primary PK endpoint. Here, the number of participants analyzed signifies participants who were evaluable for this outcome measure.

AUC(0-last) of SHP643 in plasma was reported. Geometric mean and geometric coefficient of variation percent (CV%) was reported.

Outcome measures

Outcome measures
Measure
SHP643 Autoinjector (AI)
n=89 Participants
Participants received 300 mg of SHP643 AI SC injection into the abdomen on Day 1 during the in-house treatment period (Day 1 to Day 5).
SHP643 Prefilled Syringe (PFS)
n=89 Participants
Participants received 300 milligram (mg) of SHP643 PFS Subcutaneous (SC) injection into the abdomen on Day 1 during the in-house treatment period (Day 1 to Day 5).
Area Under the Concentration Versus Time Curve From Time Zero to the Last Quantifiable Concentration (AUC0-last) of SHP643 in Plasma
376.5 day*microgram per milliliter (day*ug/mL)
Geometric Coefficient of Variation 41.3
348.9 day*microgram per milliliter (day*ug/mL)
Geometric Coefficient of Variation 33.4

PRIMARY outcome

Timeframe: Pre-dose, 8, 24, 48, 72, 96, 168, 336, 504, 672, 1008, 1344, 2016, 2664 hours post-dose

Population: PK set was defined as all randomized participants who received the complete dose of SHP643 and had sufficient data to calculate at least one primary PK endpoint. Here, the number of participants analyzed signifies participants who were evaluable for this outcome measure.

AUC(0-infinity) of SHP643 in plasma was reported. Geometric mean and geometric coefficient of variation percent (CV%) was reported.

Outcome measures

Outcome measures
Measure
SHP643 Autoinjector (AI)
n=89 Participants
Participants received 300 mg of SHP643 AI SC injection into the abdomen on Day 1 during the in-house treatment period (Day 1 to Day 5).
SHP643 Prefilled Syringe (PFS)
n=89 Participants
Participants received 300 milligram (mg) of SHP643 PFS Subcutaneous (SC) injection into the abdomen on Day 1 during the in-house treatment period (Day 1 to Day 5).
Area Under the Concentration-Time Curve From Time Zero Extrapolated to Infinity (AUC0-Inf) of SHP643 in Plasma
380.3 day*μg/mL
Geometric Coefficient of Variation 40.8
352.5 day*μg/mL
Geometric Coefficient of Variation 32.9

PRIMARY outcome

Timeframe: Pre-dose, 8, 24, 48, 72, 96, 168, 336, 504, 672, 1008, 1344, 2016, 2664 hours post-dose

Population: PK set was defined as all randomized participants who received the complete dose of SHP643 and had sufficient data to calculate at least one primary PK endpoint. Here, the number of participants analyzed signifies participants who were evaluable for this outcome measure.

Cmax is the maximum observed plasma concentration of SHP643 in Plasma was reported. Geometric mean and geometric coefficient of variation percent (CV%) was reported.

Outcome measures

Outcome measures
Measure
SHP643 Autoinjector (AI)
n=94 Participants
Participants received 300 mg of SHP643 AI SC injection into the abdomen on Day 1 during the in-house treatment period (Day 1 to Day 5).
SHP643 Prefilled Syringe (PFS)
n=94 Participants
Participants received 300 milligram (mg) of SHP643 PFS Subcutaneous (SC) injection into the abdomen on Day 1 during the in-house treatment period (Day 1 to Day 5).
Maximum Observed Plasma Drug Concentration (Cmax) of SHP643 in Plasma
18.35 microgram per milliliter (ug/mL)
Geometric Coefficient of Variation 48.0
15.86 microgram per milliliter (ug/mL)
Geometric Coefficient of Variation 40.6

PRIMARY outcome

Timeframe: Pre-dose, 8, 24, 48, 72, 96, 168, 336, 504, 672, 1008, 1344, 2016, 2664 hours post-dose

Population: PPK set was defined as all randomized participants who received the complete dose of SHP643 and had sufficient data to calculate at least one primary PK endpoint. Here, the number of participants analyzed signifies participants who were evaluable for this outcome measure.

Tmax of of SHP643 in plasma was reported.

Outcome measures

Outcome measures
Measure
SHP643 Autoinjector (AI)
n=94 Participants
Participants received 300 mg of SHP643 AI SC injection into the abdomen on Day 1 during the in-house treatment period (Day 1 to Day 5).
SHP643 Prefilled Syringe (PFS)
n=94 Participants
Participants received 300 milligram (mg) of SHP643 PFS Subcutaneous (SC) injection into the abdomen on Day 1 during the in-house treatment period (Day 1 to Day 5).
Minimum Time to Reach (Tmax) in Maximum Observed Plasma Drug Concentration of SHP643 in Plasma
4.00 day
Interval 2.0 to 6.92
4.00 day
Interval 3.0 to 19.97

PRIMARY outcome

Timeframe: Pre-dose, 8, 24, 48, 72, 96, 168, 336, 504, 672, 1008, 1344, 2016, 2664 hours post-dose

Population: PK set was defined as all randomized participants who received the complete dose of SHP643 and had sufficient data to calculate at least one primary PK endpoint. Here, the number of participants analyzed signifies participants who were evaluable for this outcome measure.

t1/2 of of SHP643 in plasma was reported.

Outcome measures

Outcome measures
Measure
SHP643 Autoinjector (AI)
n=89 Participants
Participants received 300 mg of SHP643 AI SC injection into the abdomen on Day 1 during the in-house treatment period (Day 1 to Day 5).
SHP643 Prefilled Syringe (PFS)
n=89 Participants
Participants received 300 milligram (mg) of SHP643 PFS Subcutaneous (SC) injection into the abdomen on Day 1 during the in-house treatment period (Day 1 to Day 5).
Terminal Half-Life (T1/2) of SHP643 in Plasma
13.20 day
Interval 8.21 to 40.1
13.76 day
Interval 9.7 to 20.5

PRIMARY outcome

Timeframe: Pre-dose, 8, 24, 48, 72, 96, 168, 336, 504, 672, 1008, 1344, 2016, 2664 hours post-dose

Population: PK set was defined as all randomized participants who received the complete dose of SHP643 and had sufficient data to calculate at least one primary PK endpoint. Here, the number of participants analyzed signifies participants who were evaluable for this outcome measure.

CL/F of of SHP643 in plasma was reported. Geometric mean and geometric coefficient of variation percent (CV%) was reported.

Outcome measures

Outcome measures
Measure
SHP643 Autoinjector (AI)
n=89 Participants
Participants received 300 mg of SHP643 AI SC injection into the abdomen on Day 1 during the in-house treatment period (Day 1 to Day 5).
SHP643 Prefilled Syringe (PFS)
n=89 Participants
Participants received 300 milligram (mg) of SHP643 PFS Subcutaneous (SC) injection into the abdomen on Day 1 during the in-house treatment period (Day 1 to Day 5).
Apparent Total Body Clearance for Extravascular Administration Divided by the Fraction of Dose Absorbed (CL/F) of SHP643 in Plasma
0.7888 liter per day (L/day)
Geometric Coefficient of Variation 40.8
0.8511 liter per day (L/day)
Geometric Coefficient of Variation 32.9

PRIMARY outcome

Timeframe: Pre-dose, 8, 24, 48, 72, 96, 168, 336, 504, 672, 1008, 1344, 2016, 2664 hours post-dose

Population: PK set was defined as all randomized participants who received the complete dose of SHP643 and had sufficient data to calculate at least one primary PK endpoint. Here, the number of participants analyzed signifies participants who were evaluable for this outcome measure.

Vdz/F of SHP643 in plasma was reported. Geometric mean and geometric coefficient of variation percent (CV%) was reported.

Outcome measures

Outcome measures
Measure
SHP643 Autoinjector (AI)
n=89 Participants
Participants received 300 mg of SHP643 AI SC injection into the abdomen on Day 1 during the in-house treatment period (Day 1 to Day 5).
SHP643 Prefilled Syringe (PFS)
n=89 Participants
Participants received 300 milligram (mg) of SHP643 PFS Subcutaneous (SC) injection into the abdomen on Day 1 during the in-house treatment period (Day 1 to Day 5).
Apparent Volume of Distribution Associated With the Terminal Slope Following Extravascular Administration Divided by the Fraction of Dose Absorbed (Vdz/F) of SHP643 in Plasma
15.37 Liters (L)
Geometric Coefficient of Variation 42.7
16.79 Liters (L)
Geometric Coefficient of Variation 31.6

PRIMARY outcome

Timeframe: Pre-dose, 8, 24, 48, 72, 96, 168, 336, 504, 672, 1008, 1344, 2016, 2664 hours post-dose

Population: PK set was defined as all randomized participants who received the complete dose of SHP643 and had sufficient data to calculate at least one primary PK endpoint. Here, the number of participants analyzed signifies participants who were evaluable for this outcome measure.

Lambda z of SHP643 in Plasma was reported. Geometric mean and geometric coefficient of variation percent (CV%) was reported.

Outcome measures

Outcome measures
Measure
SHP643 Autoinjector (AI)
n=89 Participants
Participants received 300 mg of SHP643 AI SC injection into the abdomen on Day 1 during the in-house treatment period (Day 1 to Day 5).
SHP643 Prefilled Syringe (PFS)
n=89 Participants
Participants received 300 milligram (mg) of SHP643 PFS Subcutaneous (SC) injection into the abdomen on Day 1 during the in-house treatment period (Day 1 to Day 5).
Terminal Elimination Rate Constant (Lambda z) of SHP643 in Plasma
0.05132 one per day (1/day)
Geometric Coefficient of Variation 22.1
0.05070 one per day (1/day)
Geometric Coefficient of Variation 15.1

SECONDARY outcome

Timeframe: From start of study drug administration up to Day 112 (End of Study/Early Termination [EOS/ET])

Population: Safety analysis set consisted of all randomized participants who received the dose of SHP643.

An adverse event (AE) was any untoward medical occurrence in a clinical investigation participant administered a pharmaceutical product that did not necessarily have a causal relationship with the investigational product (IP) or medicinal product. A treatment-emergent AE (TEAE) was defined as any event emerging or manifesting at or after the initiation of treatment with an IP or medicinal product or any existing event that worsened in either intensity or frequency following exposure to the IP or medicinal product.

Outcome measures

Outcome measures
Measure
SHP643 Autoinjector (AI)
n=96 Participants
Participants received 300 mg of SHP643 AI SC injection into the abdomen on Day 1 during the in-house treatment period (Day 1 to Day 5).
SHP643 Prefilled Syringe (PFS)
n=94 Participants
Participants received 300 milligram (mg) of SHP643 PFS Subcutaneous (SC) injection into the abdomen on Day 1 during the in-house treatment period (Day 1 to Day 5).
Number of Participants With Treatment-Emergent Adverse Events (TEAEs)
30 Participants
19 Participants

SECONDARY outcome

Timeframe: Day 1, 14, 28, 56 and 112 (End of Study/Early Termination [EOS/ET])

Population: Safety analysis set consisted of all randomized participants who received the dose of SHP643.

Plasma samples were analyzed for presence of antidrug antibodies to SHP643. Participants who developed positive results for SHP643 antibodies were reported.

Outcome measures

Outcome measures
Measure
SHP643 Autoinjector (AI)
n=96 Participants
Participants received 300 mg of SHP643 AI SC injection into the abdomen on Day 1 during the in-house treatment period (Day 1 to Day 5).
SHP643 Prefilled Syringe (PFS)
n=94 Participants
Participants received 300 milligram (mg) of SHP643 PFS Subcutaneous (SC) injection into the abdomen on Day 1 during the in-house treatment period (Day 1 to Day 5).
Number of Participants Who Developed Positive Antidrug Antibodies to SHP643 at Specified Time Points
Participants with positive ADA: Day 1
0 Participants
1 Participants
Number of Participants Who Developed Positive Antidrug Antibodies to SHP643 at Specified Time Points
Participants with positive ADA: Day 14
0 Participants
0 Participants
Number of Participants Who Developed Positive Antidrug Antibodies to SHP643 at Specified Time Points
Participants with positive ADA: Day 28
0 Participants
1 Participants
Number of Participants Who Developed Positive Antidrug Antibodies to SHP643 at Specified Time Points
Participants with positive ADA: Day 56
1 Participants
0 Participants
Number of Participants Who Developed Positive Antidrug Antibodies to SHP643 at Specified Time Points
Participants with positive ADA: Day 112 (EOS/ET)
1 Participants
0 Participants

Adverse Events

SHP643 Prefilled Syringe (PFS)

Serious events: 2 serious events
Other events: 0 other events
Deaths: 0 deaths

SHP643 Autoinjector (AI)

Serious events: 2 serious events
Other events: 9 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
SHP643 Prefilled Syringe (PFS)
n=94 participants at risk
Participants received 300 milligram (mg) of SHP643 PFS Subcutaneous (SC) injection into the abdomen on Day 1 during the in-house treatment period (Day 1 to Day 5).
SHP643 Autoinjector (AI)
n=96 participants at risk
Participants received 300 mg of SHP643 AI SC injection into the abdomen on Day 1 during the in-house treatment period (Day 1 to Day 5).
Blood and lymphatic system disorders
Anaemia
0.00%
0/94 • From start of study drug administration up to Day 112 (End of Study/Early Termination [EOS/ET])
1.0%
1/96 • Number of events 1 • From start of study drug administration up to Day 112 (End of Study/Early Termination [EOS/ET])
Infections and infestations
Appendicitis
1.1%
1/94 • Number of events 1 • From start of study drug administration up to Day 112 (End of Study/Early Termination [EOS/ET])
0.00%
0/96 • From start of study drug administration up to Day 112 (End of Study/Early Termination [EOS/ET])
Pregnancy, puerperium and perinatal conditions
Abortion spontaneous
0.00%
0/94 • From start of study drug administration up to Day 112 (End of Study/Early Termination [EOS/ET])
1.0%
1/96 • Number of events 1 • From start of study drug administration up to Day 112 (End of Study/Early Termination [EOS/ET])
Renal and urinary disorders
Nephrolithiasis
0.00%
0/94 • From start of study drug administration up to Day 112 (End of Study/Early Termination [EOS/ET])
1.0%
1/96 • Number of events 1 • From start of study drug administration up to Day 112 (End of Study/Early Termination [EOS/ET])
Surgical and medical procedures
Abortion induced
1.1%
1/94 • Number of events 1 • From start of study drug administration up to Day 112 (End of Study/Early Termination [EOS/ET])
0.00%
0/96 • From start of study drug administration up to Day 112 (End of Study/Early Termination [EOS/ET])

Other adverse events

Other adverse events
Measure
SHP643 Prefilled Syringe (PFS)
n=94 participants at risk
Participants received 300 milligram (mg) of SHP643 PFS Subcutaneous (SC) injection into the abdomen on Day 1 during the in-house treatment period (Day 1 to Day 5).
SHP643 Autoinjector (AI)
n=96 participants at risk
Participants received 300 mg of SHP643 AI SC injection into the abdomen on Day 1 during the in-house treatment period (Day 1 to Day 5).
General disorders
Injection site haemorrhage
0.00%
0/94 • From start of study drug administration up to Day 112 (End of Study/Early Termination [EOS/ET])
9.4%
9/96 • Number of events 9 • From start of study drug administration up to Day 112 (End of Study/Early Termination [EOS/ET])

Additional Information

Study Director

Shire

Phone: +1 866-842-5335

Results disclosure agreements

  • Principal investigator is a sponsor employee If a multicenter publication is not submitted within twelve (12) months after conclusion, abandonment or termination of the Study at all sites, or after Sponsor confirms there shall be no multicenter Study publication, the Institution and/or such Principal Investigator may publish the results from the Institution site individually.
  • Publication restrictions are in place

Restriction type: OTHER