Trial Outcomes & Findings for Budesonide in Patients With Immune Mediated Enteropathies (NCT NCT03866538)

NCT ID: NCT03866538

Last Updated: 2022-08-26

Results Overview

Investigators will determine change in small bowel villi after withdrawal of budesonide compared to continued therapy to assess small intestinal injury. This will be accomplished by esophagogastroduodenoscopy (upper scope) with biopsies from the small intestine.

Recruitment status

TERMINATED

Study phase

PHASE4

Target enrollment

1 participants

Primary outcome timeframe

12 weeks

Results posted on

2022-08-26

Participant Flow

Participant milestones

Participant milestones
Measure
Continued Budesonide
Patients in this arm continued budesonide at the dose they were taking at the time of enrollment in the trial
Withdrawal of Budesonide
Patients were weaned off of budesonide over 2 weeks and continued off of the medication for the duration of the trial Withdrawal of Oral Budesonide: The intervention arm tapered and stoped budesonide therapy (withdrawal).
Overall Study
STARTED
0
1
Overall Study
COMPLETED
0
1
Overall Study
NOT COMPLETED
0
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Budesonide in Patients With Immune Mediated Enteropathies

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Continued Budesonide
Patients in this arm continued budesonide at the dose they were taking at the time of enrollment in the trial
Withdrawal of Budesonide
n=1 Participants
Patients were weaned off of budesonide over 2 weeks and continued off of the medication for the duration of the trial Withdrawal of Oral Budesonide: The intervention arm tapered and stoped budesonide therapy (withdrawal).
Total
n=1 Participants
Total of all reporting groups
Age, Categorical
<=18 years
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
1 Participants
n=7 Participants
1 Participants
n=5 Participants
Age, Categorical
>=65 years
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Sex: Female, Male
Female
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Sex: Female, Male
Male
1 Participants
n=7 Participants
1 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
White
1 Participants
n=7 Participants
1 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Region of Enrollment
United States
1 participants
n=7 Participants
1 participants
n=5 Participants

PRIMARY outcome

Timeframe: 12 weeks

Population: Study was terminated due to recruitment being difficult and not achieved. Data was not collected nor analyzed.

Investigators will determine change in small bowel villi after withdrawal of budesonide compared to continued therapy to assess small intestinal injury. This will be accomplished by esophagogastroduodenoscopy (upper scope) with biopsies from the small intestine.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: 12 weeks

Population: Study was terminated due to recruitment being difficult and not achieved. Data was not collected nor analyzed.

Symptoms (monitored daily) will be compared between patients that withdraw from budesonide compared to those that continue budesonide therapy. Symptoms will be measured on the Celiac Disease Symptom Diary (CDSD) questionnaire. First question asks if subject has diarrhea and how many times. Second question asks if subject has spontaneous bowel movement and how many. Third question asks if subject had abdominal pain and to rate on a scale from 0 to 10 with higher numbers being worse pain. Fourth question asks if experiencing bloating and if it is very mild, mild, moderate, severe, or very severe. Fifth question asks if subject has nausea and if it is ranked very mild, mild, moderate, severe, or very severe. The sixth question asks if the subject has experienced tiredness and to rank very mild, mild, moderate, severe or very severe. Each question is evaluated for changes or trends over time, and a composite score including multiple questions can be calculated and compared.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: 12 weeks

Population: Study was terminated due to recruitment being difficult and not achieved. Data was not collected nor analyzed.

Quality of life will be assessed monthly comparing those that withdraw from budesonide compared to those that continue therapy. This will be assessed by the Celiac Disease Quality of Life Questionnaire (CD-QOL). This survey includes 20 questions with scores for each ranging from 1 to 5, with higher numbers indicating improved quality of life. Total scores will range from 20 to 100 with higher numbers indicating better quality of life.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: 12 weeks

Population: Study was terminated due to recruitment being difficult and not achieved. Data was not collected nor analyzed.

Weight in kilograms will be monitored throughout the study. Changes will be compare between those withdrawing from budesonide compared to those continuing therapy.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: 12 weeks

Population: Study was terminated due to recruitment being difficult and not achieved. Data was not collected nor analyzed.

Iron in the blood will be compared to those that withdraw from budesonide compared to those that continue therapy. This will be assessed at the initiation and completion of the trial.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: 12 weeks

Population: Study was terminated due to recruitment being difficult and not achieved. Data was not collected nor analyzed.

25-hydroxy vitamin D in the blood will be compared to those that withdraw from budesonide compared to those that continue therapy. This will be assessed at the initiation and completion of the trial.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: 12 weeks

Population: Study was terminated due to recruitment being difficult and not achieved. Data was not collected nor analyzed.

Vitamin B12 in the blood will be compared to those that withdraw from budesonide compared to those that continue therapy. This will be assessed at the initiation and completion of the trial.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: 12 weeks

Population: Study was terminated due to recruitment being difficult and not achieved. Data was not collected nor analyzed.

Folate in the blood will be compared to those that withdraw from budesonide compared to those that continue therapy. This will be assessed at the initiation and completion of the trial.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: 12 weeks

Population: Study was terminated due to recruitment being difficult and not achieved. Data was not collected nor analyzed.

Zinc in the blood will be compared to those that withdraw from budesonide compared to those that continue therapy. This will be assessed at the initiation and completion of the trial.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: 12 weeks

Population: Study was terminated due to recruitment being difficult and not achieved. Data was not collected nor analyzed.

Copper in the blood will be compared to those that withdraw from budesonide compared to those that continue therapy. This will be assessed at the initiation and completion of the trial.

Outcome measures

Outcome data not reported

Adverse Events

Continued Budesonide

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Withdrawal of Budesonide

Serious events: 0 serious events
Other events: 1 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Continued Budesonide
Patients in this arm continued budesonide at the dose they were taking at the time of enrollment in the trial
Withdrawal of Budesonide
n=1 participants at risk
Patients were weaned off of budesonide over 2 weeks and continued off of the medication for the duration of the trial Withdrawal of Oral Budesonide: The intervention arm tapered and stoped budesonide therapy (withdrawal).
Gastrointestinal disorders
Diarrhea
0/0 • Adverse Events were collected from baseline to end of study, approximately 2 weeks
Study was terminated due to recruitment being difficult and not achieved. There was no accrual in the Continued Budesonide arm
100.0%
1/1 • Adverse Events were collected from baseline to end of study, approximately 2 weeks
Study was terminated due to recruitment being difficult and not achieved. There was no accrual in the Continued Budesonide arm

Additional Information

Joseph A. Murray, M.D.

Mayo Clinic

Phone: 507-284-2631

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place