Trial Outcomes & Findings for Efficacy and Safety of Oral BT-11 in Ulcerative Colitis (NCT NCT03861143)

NCT ID: NCT03861143

Last Updated: 2023-06-29

Results Overview

Clinical remission rate at Week 12, defined using the 3-component modified Mayo Score as a rectal bleeding subscore of 0, a stool frequency subscore of 0 or 1, and an endoscopic subscore of 0 or 1.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

198 participants

Primary outcome timeframe

Week 12

Results posted on

2023-06-29

Participant Flow

Participant milestones

Participant milestones
Measure
BT-11 Low-dose (440 mg)
Oral, once daily tablet
BT-11 High-dose (880 mg)
Oral, once daily tablet
Placebo
Oral, once daily tablet
Overall Study
STARTED
66
66
66
Overall Study
COMPLETED
62
59
58
Overall Study
NOT COMPLETED
4
7
8

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Efficacy and Safety of Oral BT-11 in Ulcerative Colitis

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
BT-11 Low-dose (440 mg)
n=66 Participants
Oral, once daily tablet
BT-11 High-dose (880 mg)
n=66 Participants
Oral, once daily tablet
Placebo
n=66 Participants
Oral, once daily tablet
Total
n=198 Participants
Total of all reporting groups
Age, Continuous
43.1 years
STANDARD_DEVIATION 14.9 • n=93 Participants
43.3 years
STANDARD_DEVIATION 14.9 • n=4 Participants
43.3 years
STANDARD_DEVIATION 14.5 • n=27 Participants
43.2 years
STANDARD_DEVIATION 14.7 • n=483 Participants
Sex: Female, Male
Female
40 Participants
n=93 Participants
22 Participants
n=4 Participants
31 Participants
n=27 Participants
93 Participants
n=483 Participants
Sex: Female, Male
Male
26 Participants
n=93 Participants
44 Participants
n=4 Participants
35 Participants
n=27 Participants
105 Participants
n=483 Participants
Race (NIH/OMB)
American Indian or Alaska Native
1 Participants
n=93 Participants
0 Participants
n=4 Participants
0 Participants
n=27 Participants
1 Participants
n=483 Participants
Race (NIH/OMB)
Asian
0 Participants
n=93 Participants
0 Participants
n=4 Participants
0 Participants
n=27 Participants
0 Participants
n=483 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=93 Participants
0 Participants
n=4 Participants
0 Participants
n=27 Participants
0 Participants
n=483 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=93 Participants
1 Participants
n=4 Participants
2 Participants
n=27 Participants
3 Participants
n=483 Participants
Race (NIH/OMB)
White
65 Participants
n=93 Participants
65 Participants
n=4 Participants
64 Participants
n=27 Participants
194 Participants
n=483 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=93 Participants
0 Participants
n=4 Participants
0 Participants
n=27 Participants
0 Participants
n=483 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=93 Participants
0 Participants
n=4 Participants
0 Participants
n=27 Participants
0 Participants
n=483 Participants

PRIMARY outcome

Timeframe: Week 12

Population: ITT

Clinical remission rate at Week 12, defined using the 3-component modified Mayo Score as a rectal bleeding subscore of 0, a stool frequency subscore of 0 or 1, and an endoscopic subscore of 0 or 1.

Outcome measures

Outcome measures
Measure
BT-11 Low-dose (440 mg)
n=66 Participants
Oral, once daily tablet
BT-11 High-dose (880 mg)
n=66 Participants
Oral, once daily tablet
Placebo
n=66 Participants
Oral, once daily tablet
Clinical Remission
30.3 percentage of participants
31.8 percentage of participants
22.7 percentage of participants

Adverse Events

BT-11 Low-dose (440 mg)

Serious events: 2 serious events
Other events: 23 other events
Deaths: 0 deaths

BT-11 High-dose (880 mg)

Serious events: 3 serious events
Other events: 29 other events
Deaths: 0 deaths

Placebo

Serious events: 3 serious events
Other events: 27 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
BT-11 Low-dose (440 mg)
n=66 participants at risk
Oral, once daily tablet
BT-11 High-dose (880 mg)
n=66 participants at risk
Oral, once daily tablet
Placebo
n=66 participants at risk
Oral, once daily tablet
Gastrointestinal disorders
Colitis Ulcerative
0.00%
0/66 • 15 months
1.5%
1/66 • 15 months
1.5%
1/66 • 15 months
Gastrointestinal disorders
Proctitis
1.5%
1/66 • 15 months
0.00%
0/66 • 15 months
0.00%
0/66 • 15 months
Infections and infestations
Amoebiasis
0.00%
0/66 • 15 months
1.5%
1/66 • 15 months
0.00%
0/66 • 15 months
Infections and infestations
Pneumonia
0.00%
0/66 • 15 months
0.00%
0/66 • 15 months
1.5%
1/66 • 15 months
Infections and infestations
Pneumonia Viral
0.00%
0/66 • 15 months
0.00%
0/66 • 15 months
1.5%
1/66 • 15 months
Injury, poisoning and procedural complications
Foot Fracture
1.5%
1/66 • 15 months
0.00%
0/66 • 15 months
0.00%
0/66 • 15 months
Investigations
Coronavirus Test Positive
0.00%
0/66 • 15 months
1.5%
1/66 • 15 months
0.00%
0/66 • 15 months

Other adverse events

Other adverse events
Measure
BT-11 Low-dose (440 mg)
n=66 participants at risk
Oral, once daily tablet
BT-11 High-dose (880 mg)
n=66 participants at risk
Oral, once daily tablet
Placebo
n=66 participants at risk
Oral, once daily tablet
Blood and lymphatic system disorders
Anemia
3.0%
2/66 • 15 months
7.6%
5/66 • 15 months
0.00%
0/66 • 15 months
Gastrointestinal disorders
Colitis Ulcerative
15.2%
10/66 • 15 months
12.1%
8/66 • 15 months
9.1%
6/66 • 15 months
Gastrointestinal disorders
Diarrhea
4.5%
3/66 • 15 months
0.00%
0/66 • 15 months
1.5%
1/66 • 15 months
Gastrointestinal disorders
Nausea
0.00%
0/66 • 15 months
4.5%
3/66 • 15 months
0.00%
0/66 • 15 months
Infections and infestations
Corona Virus Infection
1.5%
1/66 • 15 months
1.5%
1/66 • 15 months
6.1%
4/66 • 15 months
Investigations
Blood Creatine Phosphokinase Increased
1.5%
1/66 • 15 months
4.5%
3/66 • 15 months
0.00%
0/66 • 15 months
Nervous system disorders
Headache
0.00%
0/66 • 15 months
1.5%
1/66 • 15 months
4.5%
3/66 • 15 months
General disorders
Other
9.1%
6/66 • 15 months
12.1%
8/66 • 15 months
19.7%
13/66 • 15 months

Additional Information

Clinical Development

NImmune Biopharma, Inc.

Phone: (540) 218-2262

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place