Efficacy and Safety of Pirfenidone in Patient With Dermatomyositis Interstitial Lung Disease (Dm-ILD)

NCT ID: NCT03857854

Last Updated: 2019-02-28

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

PHASE3

Total Enrollment

152 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-06-05

Study Completion Date

2021-05-31

Brief Summary

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The purpose of this study is to evaluate the efficacy and safety of pirfenidone in subjects with dermatomyositis interstitial lung disease

Detailed Description

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Conditions

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Dermatomyositis Interstitial Lung Disease (Dm-ILD)

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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treatment group

pirfenidone group

Group Type EXPERIMENTAL

Pirfenidone

Intervention Type DRUG

treatment group

placebo group

control group

Group Type PLACEBO_COMPARATOR

Placebos

Intervention Type DRUG

placebo group

Interventions

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Pirfenidone

treatment group

Intervention Type DRUG

Placebos

placebo group

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Female or male subjects aged between 18 and 65 years of age
2. According to the 1975 Borhan and Peter inflammatory myopathy diagnosed as dermatomyositis classification criteria (dermatomyositis, DM); or according to the revised clinical criteria for diagnosis of Sontheimer disease dermatomyositis (CADM).
3. The diagnosis of pulmonary related Interstitial Lung Disease confirmed by HRCT
4. Forced vital capacity (FVC) 40% to 80% predicted(include 40% and80% )
5. Carbon monoxide diffusing capacity (DLco) 30% to 89% of predicted normal(include 30% and89% )
6. Has received Glucocorticoid (hereinafter referred to as the "hormone") and at least one immunosuppressive therapy for more than 3 months, the hormone dosage (prednisone equivalent dose calculation) should be less than 15mg/d for at least 1 months, should be immunosuppressant cyclophosphamide, mycophenolate mofetil, cyclosporine, tacrolimus, azathioprine and at least one of methotrexate in, and the type and dose of immunosuppressive agents should be at least stable more than 3 months. The hormone and immunosuppressant therapy scheme allows a reduction in the study period, but is not allowed to increase the volume.
7. Women of childbearing age must agree and promise to use the form of medical care for at least 3 months after the trial, during the entire study period (including follow-up), and at the end of the trial.
8. Patients volunteered to participate in the trial, with good compliance and ability to understand and sign informed consent before the study.

2. Combined with other rheumatic diseases such as systemic sclerosis, systemic lupus erythematosus, Sjogren's syndrome, mixed connective tissue disease, undifferentiated connective tissue disease, and systemic vasculitis, such as ANCA associated vasculitis.
3. Combined with other muscle diseases and may cause symptoms of myasthenia gravis disease, including neurological diseases (such as muscular dystrophy, myasthenia gravis, amyotrophic lateral sclerosis, Guillain Barre syndrome), cancer, drugs (such as statins), infection, genetic diseases, endocrine disorders, electrolyte disorder rhabdomyolysis.
4. The clinical history, signs, serological examination, HRCT and bronchoalveolar lavage results suggest that in addition to inflammatory myopathy and other diseases caused by ILD, such as CTD, systemic vasculitis, infection, tumor, allergic pneumonia caused by sarcoidosis or environmental factors.
5. Combined viscera function significantly abnormal patient:

1. Liver:AST, ALT \>1.3ULN;Bilirubin \>1.5 ULN; Cirrhosis of the liver class for Child Pugh C;
2. Kidney:Creatinine clearance \<30 mL/min;
3. Lung:Airway obstruction (pre-bronchodilator FEV1/FVC \<0.7);Other clinically significant pulmonary abnormalities;
4. Cardiovascular:i.Six weeks in severe hypertension, and out of control after treatment(≥160/100mmHg);ii.Myocardial infarction within six months;iii.A period of 6 Months in unstable angina;iv.pulmonary artery hypertension and right heart failure were significant;
5. Gastrointestinal tract: with active peptic ulcer;
6. Nervous system: Patients with psychiatric disorders;
7. The blood coagulation function: History of thrombotic event within last year(Including stroke and transient ischemic attack).
6. Researchers, for other diseases (not inflammatory myopathy, such as malignant tumor) and make the life expectancy of \< 1 year of patients
7. Allergic to test drugs or components (e.g. lactose)
8. Patients with actinic dermatitis
9. Previous treatment with nintedanib or pirfenidone
10. Within 3 months to participate in other clinical trials;
11. Combined medication: hormone \> 15mg/d, were less than 1 months before a stable dose of patients; the use of other immunosuppressive agents (except cyclophosphamide, mycophenolate mofetil, cyclosporine, tacrolimus, azathioprine, methotrexate and) patients; immunosuppression stable \< 3 months; during the study of hormones and immunosuppressive agents are likely to increase patients.
12. Major surgery is planned during the treatment period.
13. Pregnancy or lactation or make a schedule during the trials.
14. Give the drug 28 days before or after administration of the 3 month period, women of childbearing age \* are unwilling or unable to use contraceptive methods highly effective (according to ICH M3 (R2)), a highly effective means in the correct and consistent application of a barrier method when the failure rate of less than 1% per year. \* women of childbearing age is defined has undergone menarche and in line with "infertile women" standard "\[female infertile women" is defined as: postmenopausal period (12 months without menstruation, no other medical reasons) or permanent sterilization (e.g., tubal occlusion, hysterectomy, bilateral ovarian resection or bilateral tubal resection women)\].
15. According to the researchers,exhibited evidence of alcohol or drug abuse.
16. Patients who were unable to understand or comply with the study procedures, including the completion of a self-administered questionnaire in the absence of help, were less likely to complete the trial.
17. Severe limb weakness or joint disease that affects the stability and endurance of a patient who is unable to perform a 6 minute walking test.
18. Clinical signs of malabsorption or needing parenteral nutrition.
19. Patients who were unable to cope with pulmonary function tests.
20. With mental illness .
21. Researchers determined that they did not participate in the trial.
Minimum Eligible Age

18 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Beijing Continent Pharmaceutical Co, Ltd.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Zhang, Ling

Beijing, Beijing Municipality, China

Site Status RECRUITING

Countries

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China

Facility Contacts

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Ling Zhang

Role: primary

Other Identifiers

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GNI-F647-1702

Identifier Type: -

Identifier Source: org_study_id