Trial Outcomes & Findings for Study to Evaluate the Efficacy and Safety of JTE-451 in Subjects With Moderate to Severe Plaque Psoriasis (NCT NCT03832738)

NCT ID: NCT03832738

Last Updated: 2021-08-20

Results Overview

The psoriasis area and severity index (PASI) combines the assessment of the severity of lesions (scaling, redness and plaque thickness) and the area affected into a single score in the range of 0.0 (no disease) to 72.0 (maximal disease). The body is divided into four sections: (1) Head and neck; (2) Upper limbs; (3) Trunk (including axillae and groin); and (4) Lower limbs (including buttocks). The PASI score can vary in increments of 0.1 and range from 0.0 to 72.0, with higher scores representing greater severity of psoriasis. The PASI-75 response rate is defined as at least 75 percent (%) reduction in PASI score at EOT (up to 16 weeks) relative to Baseline.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

152 participants

Primary outcome timeframe

End of Treatment (Up to 16 Weeks)

Results posted on

2021-08-20

Participant Flow

Written informed consent was obtained prior to performing any study-related procedures. A copy of the informed consent was provided to each subject enrolled in this study. To qualify for the study, subjects were required to satisfy defined criteria.

Following informed consent signing, screening procedures to confirm eligibility were performed. 1. Intent-to-Treat (ITT) Population - 152 subjects 2. Safety Population - 151 subjects 3. Pharmacokinetic (PK) Population - 101 subjects

Participant milestones

Participant milestones
Measure
JTE-451 200 mg Twice Daily
JTE-451 200 mg orally twice daily for 16 weeks (total daily dose - 400 mg)
JTE-451 400 mg Twice Daily
JTE-451 400 mg orally twice daily for 16 weeks (total daily dose - 800 mg)
Placebo Twice Daily
Placebo Tablets orally twice daily for 16 weeks
Overall Study
STARTED
51
50
51
Overall Study
COMPLETED
43
38
32
Overall Study
NOT COMPLETED
8
12
19

Reasons for withdrawal

Reasons for withdrawal
Measure
JTE-451 200 mg Twice Daily
JTE-451 200 mg orally twice daily for 16 weeks (total daily dose - 400 mg)
JTE-451 400 mg Twice Daily
JTE-451 400 mg orally twice daily for 16 weeks (total daily dose - 800 mg)
Placebo Twice Daily
Placebo Tablets orally twice daily for 16 weeks
Overall Study
Withdrawal by Subject
6
7
16
Overall Study
Physician Decision
0
1
2
Overall Study
Adverse Event
2
3
1
Overall Study
Pregnancy
0
1
0

Baseline Characteristics

Study to Evaluate the Efficacy and Safety of JTE-451 in Subjects With Moderate to Severe Plaque Psoriasis

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
JTE-451 200 mg Twice Daily
n=51 Participants
JTE-451 200 mg orally twice daily for 16 weeks (total daily dose - 400 mg)
JTE-451 400 mg Twice Daily
n=50 Participants
JTE-451 400 mg orally twice daily for 16 weeks (total daily dose - 800 mg)
Placebo Twice Daily
n=51 Participants
Placebo Tablets orally twice daily for 16 weeks
Total
n=152 Participants
Total of all reporting groups
Age, Categorical
<=18 years
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
Age, Categorical
Between 18 and 65 years
47 Participants
n=5 Participants
46 Participants
n=7 Participants
46 Participants
n=5 Participants
139 Participants
n=4 Participants
Age, Categorical
>=65 years
4 Participants
n=5 Participants
4 Participants
n=7 Participants
5 Participants
n=5 Participants
13 Participants
n=4 Participants
Sex: Female, Male
Female
13 Participants
n=5 Participants
21 Participants
n=7 Participants
16 Participants
n=5 Participants
50 Participants
n=4 Participants
Sex: Female, Male
Male
38 Participants
n=5 Participants
29 Participants
n=7 Participants
35 Participants
n=5 Participants
102 Participants
n=4 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
0 Participants
n=5 Participants
1 Participants
n=7 Participants
1 Participants
n=5 Participants
2 Participants
n=4 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
51 Participants
n=5 Participants
49 Participants
n=7 Participants
50 Participants
n=5 Participants
150 Participants
n=4 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
Race (NIH/OMB)
Asian
0 Participants
n=5 Participants
2 Participants
n=7 Participants
2 Participants
n=5 Participants
4 Participants
n=4 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
1 Participants
n=7 Participants
0 Participants
n=5 Participants
1 Participants
n=4 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
Race (NIH/OMB)
White
51 Participants
n=5 Participants
47 Participants
n=7 Participants
49 Participants
n=5 Participants
147 Participants
n=4 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
Region of Enrollment
Canada
5 participants
n=5 Participants
5 participants
n=7 Participants
3 participants
n=5 Participants
13 participants
n=4 Participants
Region of Enrollment
United States
2 participants
n=5 Participants
7 participants
n=7 Participants
6 participants
n=5 Participants
15 participants
n=4 Participants
Region of Enrollment
Poland
44 participants
n=5 Participants
38 participants
n=7 Participants
42 participants
n=5 Participants
124 participants
n=4 Participants
Prior exposure to biologics therapy
Had prior biologics therapy
11 Participants
n=5 Participants
15 Participants
n=7 Participants
13 Participants
n=5 Participants
39 Participants
n=4 Participants
Prior exposure to biologics therapy
No prior biologics therapy
40 Participants
n=5 Participants
35 Participants
n=7 Participants
38 Participants
n=5 Participants
113 Participants
n=4 Participants
Body weight
Below 90 kg
25 Participants
n=5 Participants
24 Participants
n=7 Participants
25 Participants
n=5 Participants
74 Participants
n=4 Participants
Body weight
90 kg or above
26 Participants
n=5 Participants
26 Participants
n=7 Participants
26 Participants
n=5 Participants
78 Participants
n=4 Participants

PRIMARY outcome

Timeframe: End of Treatment (Up to 16 Weeks)

Population: Subjects in the ITT Population at the EOT. The EOT value is defined as the last assessment during the treatment period (from the first dose of study drug to the last dose of study drug).

The psoriasis area and severity index (PASI) combines the assessment of the severity of lesions (scaling, redness and plaque thickness) and the area affected into a single score in the range of 0.0 (no disease) to 72.0 (maximal disease). The body is divided into four sections: (1) Head and neck; (2) Upper limbs; (3) Trunk (including axillae and groin); and (4) Lower limbs (including buttocks). The PASI score can vary in increments of 0.1 and range from 0.0 to 72.0, with higher scores representing greater severity of psoriasis. The PASI-75 response rate is defined as at least 75 percent (%) reduction in PASI score at EOT (up to 16 weeks) relative to Baseline.

Outcome measures

Outcome measures
Measure
JTE-451 200 mg Twice Daily
n=51 Participants
JTE-451 200 mg orally twice daily for 16 weeks (total daily dose - 400 mg)
JTE-451 400 mg Twice Daily
n=50 Participants
JTE-451 400 mg orally twice daily for 16 weeks (total daily dose - 800 mg)
Placebo Twice Daily
n=51 Participants
Placebo Tablets orally twice daily for 16 weeks
Percentage of Subjects Achieving a Minimum 75% Improvement From Baseline in the Psoriasis Area and Severity Index (PASI-75) at End-of-treatment (EOT)
11.8 % of subjects achieving PASI-75
22.0 % of subjects achieving PASI-75
7.8 % of subjects achieving PASI-75

SECONDARY outcome

Timeframe: End of Treatment (Up to 16 Weeks)

Population: Subjects in the ITT Population at the EOT. The EOT value is defined as the last assessment during the treatment period (from the first dose of study drug to the last dose of study drug).

The PASI combines the assessment of the severity of lesions (scaling, redness and plaque thickness) and the area affected into a single score in the range of 0.0 (no disease) to 72.0 (maximal disease). The body is divided into four sections: (1) Head and neck; (2) Upper limbs; (3) Trunk (including axillae and groin); and (4) Lower limbs (including buttocks). The PASI score can vary in increments of 0.1 and range from 0.0 to 72.0, with higher scores representing greater severity of psoriasis. The PASI-50 response rate is defined as at least 50 percent (%) reduction in PASI score at EOT (up to 16 weeks) relative to Baseline.

Outcome measures

Outcome measures
Measure
JTE-451 200 mg Twice Daily
n=51 Participants
JTE-451 200 mg orally twice daily for 16 weeks (total daily dose - 400 mg)
JTE-451 400 mg Twice Daily
n=50 Participants
JTE-451 400 mg orally twice daily for 16 weeks (total daily dose - 800 mg)
Placebo Twice Daily
n=51 Participants
Placebo Tablets orally twice daily for 16 weeks
Percentage of Subjects Achieving a Minimum 50% Improvement From Baseline in the Psoriasis Area and Severity Index (PASI-50) at EOT
33.3 % of subjects achieving PASI-50
42.0 % of subjects achieving PASI-50
17.6 % of subjects achieving PASI-50

SECONDARY outcome

Timeframe: End of Treatment (Up to 16 Weeks)

Population: Subjects in the ITT Population at the EOT. The EOT value is defined as the last assessment during the treatment period (from the first dose of study drug to the last dose of study drug).

The PASI combines the assessment of the severity of lesions (scaling, redness and plaque thickness) and the area affected into a single score in the range of 0.0 (no disease) to 72.0 (maximal disease). The body is divided into four sections: (1) Head and neck; (2) Upper limbs; (3) Trunk (including axillae and groin); and (4) Lower limbs (including buttocks). The PASI score can vary in increments of 0.1 and range from 0.0 to 72.0, with higher scores representing greater severity of psoriasis. The PASI-90 response rate is defined as at least 90 percent (%) reduction in PASI score at EOT (up to 16 weeks) relative to Baseline.

Outcome measures

Outcome measures
Measure
JTE-451 200 mg Twice Daily
n=51 Participants
JTE-451 200 mg orally twice daily for 16 weeks (total daily dose - 400 mg)
JTE-451 400 mg Twice Daily
n=50 Participants
JTE-451 400 mg orally twice daily for 16 weeks (total daily dose - 800 mg)
Placebo Twice Daily
n=51 Participants
Placebo Tablets orally twice daily for 16 weeks
Percentage of Subjects Achieving a Minimum 90% Improvement From Baseline in the Psoriasis Area and Severity Index (PASI-90) at EOT
2.0 % of subjects achieving PASI-90
6.0 % of subjects achieving PASI-90
2.0 % of subjects achieving PASI-90

SECONDARY outcome

Timeframe: End of Treatment (Up to 16 Weeks)

Population: Subjects in the ITT Population at the EOT. The EOT value is defined as the last assessment during the treatment period (from the first dose of study drug to the last dose of study drug).

The PASI combines the assessment of the severity of lesions (scaling, redness and plaque thickness) and the area affected into a single score in the range of 0.0 (no disease) to 72.0 (maximal disease). The body is divided into four sections: (1) Head and neck; (2) Upper limbs; (3) Trunk (including axillae and groin); and (4) Lower limbs (including buttocks). The PASI score can vary in increments of 0.1 and range from 0.0 to 72.0, with higher scores representing greater severity of psoriasis. Percent change from baseline to EOT (up to 16 weeks) in PASI score was calculated by taking the PASI score at EOT and subtracting the baseline PASI score, then dividing by the baseline PASI score and multiplying by 100.

Outcome measures

Outcome measures
Measure
JTE-451 200 mg Twice Daily
n=51 Participants
JTE-451 200 mg orally twice daily for 16 weeks (total daily dose - 400 mg)
JTE-451 400 mg Twice Daily
n=50 Participants
JTE-451 400 mg orally twice daily for 16 weeks (total daily dose - 800 mg)
Placebo Twice Daily
n=48 Participants
Placebo Tablets orally twice daily for 16 weeks
Percent Change From Baseline in Psoriasis Area and Severity Index (PASI) Score at EOT
-30.33 % change in PASI Score
Standard Deviation 40.971
-37.89 % change in PASI Score
Standard Deviation 37.896
-17.53 % change in PASI Score
Standard Deviation 34.701

SECONDARY outcome

Timeframe: End of Treatment (Up to 16 Weeks)

Population: Subjects in the ITT Population at the EOT. The EOT value is defined as the last assessment during the treatment period (from the first dose of study drug to the last dose of study drug).

The sPGA of psoriasis is scored on a 5-point scale, reflecting a global consideration of the redness, thickness and scaling across all psoriatic lesions. Average redness, thickness and scaling are scored separately over the whole body according to a 5-point severity scale (0 \[no symptoms\] to 4 \[severe symptoms\]). The total score is calculated as average of the 3 severity (redness, thickness and scaling) scores and rounded to the nearest whole number score to determine the sPGA score (0=cleared; 1=minimal; 2=mild; 3=moderate; and 4=severe). For this outcome measure, at EOT (up to 16 weeks), a score of 0 means no symptoms of psoriasis and a score of 1 means minimal symptoms of psoriasis.

Outcome measures

Outcome measures
Measure
JTE-451 200 mg Twice Daily
n=51 Participants
JTE-451 200 mg orally twice daily for 16 weeks (total daily dose - 400 mg)
JTE-451 400 mg Twice Daily
n=50 Participants
JTE-451 400 mg orally twice daily for 16 weeks (total daily dose - 800 mg)
Placebo Twice Daily
n=51 Participants
Placebo Tablets orally twice daily for 16 weeks
Percentage of Subjects Who Achieved Static Physician's Global Assessment (sPGA) Score of 0 or 1 at EOT
25.5 % of subjects achieving sPGA 0 or 1
28.0 % of subjects achieving sPGA 0 or 1
5.9 % of subjects achieving sPGA 0 or 1

SECONDARY outcome

Timeframe: End of Treatment (Up to 16 Weeks)

Population: Subjects in the ITT Population at the EOT. The EOT value is defined as the last assessment during the treatment period (from the first dose of study drug to the last dose of study drug).

The sPGA of psoriasis is scored on a 5-point scale, reflecting a global consideration of the redness, thickness and scaling across all psoriatic lesions. Average redness, thickness and scaling are scored separately over the whole body according to a 5-point severity scale (0 \[no symptoms\] to 4 \[severe symptoms\]). The total score is calculated as average of the 3 severity (redness, thickness and scaling) scores and rounded to the nearest whole number score to determine the sPGA score (0=cleared; 1=minimal; 2=mild; 3=moderate; and 4=severe). Change from baseline to EOT (up to 16 weeks) in sPGA score was calculated by taking the sPGA score at EOT and subtracting the baseline sPGA score.

Outcome measures

Outcome measures
Measure
JTE-451 200 mg Twice Daily
n=51 Participants
JTE-451 200 mg orally twice daily for 16 weeks (total daily dose - 400 mg)
JTE-451 400 mg Twice Daily
n=50 Participants
JTE-451 400 mg orally twice daily for 16 weeks (total daily dose - 800 mg)
Placebo Twice Daily
n=48 Participants
Placebo Tablets orally twice daily for 16 weeks
Change From Baseline in Static Physician's Global Assessment (sPGA) Score at EOT
-0.96 score on a scale
Standard Deviation 0.848
-1.02 score on a scale
Standard Deviation 0.869
-0.54 score on a scale
Standard Deviation 0.713

SECONDARY outcome

Timeframe: End of Treatment (Up to 16 Weeks)

Population: Subjects in the ITT Population at the EOT. The EOT value is defined as the last assessment during the treatment period (from the first dose of study drug to the last dose of study drug).

The total body surface area (BSA) affected by plaque-type psoriasis was obtained from the percentages of areas affected, including head, trunk, upper limbs and lower limbs. Each reported percentage was multiplied by its respective body region corresponding factor (head=0.1, upper limbs=0.2, trunk=0.3, lower limbs=0.4) and the resulting 4 values were added up to obtain the total psoriasis BSA (Range: 0 to 100). BSA (%)=0.1Sh+0.2Su+0.3St+0.4Sl, where S=body region surface area with psoriasis: h=head; u=upper limbs; t=trunk; l=lower limbs. Percent change from baseline to EOT (up to 16 weeks) in BSA was calculated by taking the EOT BSA and subtracting the baseline BSA, then dividing by the baseline BSA and multiplying by 100. A negative change from baseline at EOT indicates a reduction in the Psoriasis BSA compared to the baseline.

Outcome measures

Outcome measures
Measure
JTE-451 200 mg Twice Daily
n=51 Participants
JTE-451 200 mg orally twice daily for 16 weeks (total daily dose - 400 mg)
JTE-451 400 mg Twice Daily
n=50 Participants
JTE-451 400 mg orally twice daily for 16 weeks (total daily dose - 800 mg)
Placebo Twice Daily
n=48 Participants
Placebo Tablets orally twice daily for 16 weeks
Percent Change From Baseline in Psoriasis Body Surface Area (BSA) at EOT
-18.67 % Change in Psoriasis BSA
Standard Deviation 39.582
-19.03 % Change in Psoriasis BSA
Standard Deviation 48.696
-5.74 % Change in Psoriasis BSA
Standard Deviation 38.707

SECONDARY outcome

Timeframe: End of Treatment (Up to 16 Weeks)

Population: Subjects in the ITT Population at the EOT. The EOT value is defined as the last assessment during the treatment period (from the first dose of study drug to the last dose of study drug).

Skindex-16 questionnaire contains 16 questions related to quality of life in subjects with skin disease. It consists of a short 16-item assessment completed by the subject, with each item rated on a 7-point Likert scale (0=never bothered to 6=always bothered). Each raw score is multiplied by 16.667 to transform all responses to a linear scale from 0 (no effect) to 100 (effect experienced all the time). Responses to the Skindex-16 are categorized into 3 subscales: symptom, emotional \& functional; their respective scores are expressed in a linear scale from 0 to 100. Overall scale score is an average of 16 items expressed in a linear scale from 0 to 100. Change from baseline to EOT (up to 16 weeks) in the Skindex-16 Overall Score was calculated by taking the EOT Skindex-16 Overall Score and subtracting the baseline Skindex-16 Overall Score. A negative change from baseline at EOT indicates an improvement in the subject's condition compared to the baseline.

Outcome measures

Outcome measures
Measure
JTE-451 200 mg Twice Daily
n=51 Participants
JTE-451 200 mg orally twice daily for 16 weeks (total daily dose - 400 mg)
JTE-451 400 mg Twice Daily
n=50 Participants
JTE-451 400 mg orally twice daily for 16 weeks (total daily dose - 800 mg)
Placebo Twice Daily
n=48 Participants
Placebo Tablets orally twice daily for 16 weeks
Change From Baseline in the Skindex-16 Overall Score at EOT
-10.029 score on a scale
Standard Deviation 23.2635
-10.896 score on a scale
Standard Deviation 26.7910
-3.386 score on a scale
Standard Deviation 20.8617

SECONDARY outcome

Timeframe: End of Treatment (Up to 16 Weeks)

Population: Subjects in the ITT Population at the EOT. The EOT value is defined as the last assessment during the treatment period (from the first dose of study drug to the last dose of study drug).

Skindex-16 questionnaire contains 16 questions related to quality of life in subjects with skin disease. It consists of a short 16-item assessment completed by the subject, with each item rated on a 7-point Likert scale (0=never bothered to 6=always bothered). Each raw score is multiplied by 16.667 to transform all responses to a linear scale from 0 (no effect) to 100 (effect experienced all the time). Responses to the Skindex-16 are categorized into 3 subscales: symptom, emotional \& functional; their respective scores are expressed in a linear scale from 0 to 100. Symptoms scale score is an average of items 1 to 4 expressed in a linear scale from 0 to 100. Change from baseline to EOT (up to 16 weeks) in the Skindex-16 Symptoms Scale Score was calculated by taking the EOT Skindex-16 Symptoms Scale Score and subtracting the baseline Skindex-16 Symptoms Scale Score. A negative change from baseline at EOT indicates an improvement in the subject's condition compared to the baseline.

Outcome measures

Outcome measures
Measure
JTE-451 200 mg Twice Daily
n=51 Participants
JTE-451 200 mg orally twice daily for 16 weeks (total daily dose - 400 mg)
JTE-451 400 mg Twice Daily
n=50 Participants
JTE-451 400 mg orally twice daily for 16 weeks (total daily dose - 800 mg)
Placebo Twice Daily
n=48 Participants
Placebo Tablets orally twice daily for 16 weeks
Change From Baseline in the Skindex-16 Symptom Scale Scores at EOT
-8.905 score on a scale
Standard Deviation 34.2989
-11.500 score on a scale
Standard Deviation 31.5148
-2.170 score on a scale
Standard Deviation 26.0563

SECONDARY outcome

Timeframe: End of Treatment (Up to 16 Weeks)

Population: Subjects in the ITT Population at the EOT. The EOT value is defined as the last assessment during the treatment period (from the first dose of study drug to the last dose of study drug).

Skindex-16 questionnaire contains 16 questions related to quality of life in subjects with skin disease. It consists of a short 16-item assessment completed by the subject, with each item rated on a 7-point Likert scale (0=never bothered to 6=always bothered). Each raw score is multiplied by 16.667 to transform all responses to a linear scale from 0 (no effect) to 100 (effect experienced all the time). Responses to the Skindex-16 are categorized into 3 subscales: symptom, emotional \& functional; their respective scores are expressed in a linear scale from 0 to 100. Emotions scale score is an average of items 5 to 11 expressed in a linear scale from 0 to 100. Change from baseline to EOT (up to 16 weeks) in the Skindex-16 Emotions Scale Score was calculated by taking the EOT Skindex-16 Emotions Scale Score and subtracting the baseline Skindex-16 Emotions Scale Score. A negative change from baseline at EOT indicates an improvement in the subject's condition compared to the baseline.

Outcome measures

Outcome measures
Measure
JTE-451 200 mg Twice Daily
n=51 Participants
JTE-451 200 mg orally twice daily for 16 weeks (total daily dose - 400 mg)
JTE-451 400 mg Twice Daily
n=50 Participants
JTE-451 400 mg orally twice daily for 16 weeks (total daily dose - 800 mg)
Placebo Twice Daily
n=48 Participants
Placebo Tablets orally twice daily for 16 weeks
Change From Baseline in the Skindex-16 Emotions Scale Scores at EOT
-10.411 score on a scale
Standard Deviation 21.8268
-13.143 score on a scale
Standard Deviation 28.4467
-5.953 score on a scale
Standard Deviation 22.6358

SECONDARY outcome

Timeframe: End of Treatment (Up to 16 Weeks)

Population: Subjects in the ITT Population at the EOT. The EOT value is defined as the last assessment during the treatment period (from the first dose of study drug to the last dose of study drug).

Skindex-16 questionnaire contains 16 questions related to quality of life in subjects with skin disease. It consists of a short 16-item assessment completed by the subject, with each item rated on a 7-point Likert scale (0=never bothered to 6=always bothered). Each raw score is multiplied by 16.667 to transform all responses to a linear scale from 0 (no effect) to 100 (effect experienced all the time). Responses are categorized into 3 subscales: symptom, emotional \& functional; their respective scores are expressed in a linear scale from 0 to 100. Functioning scale score is an average of items 12 to 16 expressed in a linear scale from 0 to 100. Change from baseline to EOT (up to 16 weeks) in the Skindex-16 Functioning Scale Score was calculated by taking the EOT Skindex-16 Functioning Scale Score and subtracting the baseline Skindex-16 Functioning Scale Score. A negative change from baseline at EOT indicates an improvement in the subject's condition compared to the baseline.

Outcome measures

Outcome measures
Measure
JTE-451 200 mg Twice Daily
n=51 Participants
JTE-451 200 mg orally twice daily for 16 weeks (total daily dose - 400 mg)
JTE-451 400 mg Twice Daily
n=50 Participants
JTE-451 400 mg orally twice daily for 16 weeks (total daily dose - 800 mg)
Placebo Twice Daily
n=48 Participants
Placebo Tablets orally twice daily for 16 weeks
Change From Baseline in the Skindex-16 Functioning Scale Scores at EOT
-10.392 score on a scale
Standard Deviation 23.5294
-7.267 score on a scale
Standard Deviation 27.6823
-0.764 score on a scale
Standard Deviation 20.1090

SECONDARY outcome

Timeframe: End of Treatment (Up to 16 Weeks)

Population: Subjects in the ITT Population at the EOT. The EOT value is defined as the last assessment during the treatment period (from the first dose of study drug to the last dose of study drug).

The Itch NRS is a validated, self-reported, instrument for measurement of itch intensity and subjects were asked to rate the intensity of their itch on an 11-point scale ranging from 0 (no itch) to 10 (worst itch imaginable); higher scores indicated greater itch intensity. The Itch NRS scores were recorded by the subject using the e-diary once daily from screening through the last visit. Change from baseline to EOT (up to 16 weeks) in the Itch NRS Score was calculated by taking the Itch NRS Score (weekly average) at EOT and subtracting the baseline Itch NRS Score (weekly average).

Outcome measures

Outcome measures
Measure
JTE-451 200 mg Twice Daily
n=51 Participants
JTE-451 200 mg orally twice daily for 16 weeks (total daily dose - 400 mg)
JTE-451 400 mg Twice Daily
n=50 Participants
JTE-451 400 mg orally twice daily for 16 weeks (total daily dose - 800 mg)
Placebo Twice Daily
n=48 Participants
Placebo Tablets orally twice daily for 16 weeks
Change From Baseline in Itch Numeric Rating Scale (NRS) at EOT
-1.302 score on a scale
Standard Deviation 2.8165
-1.537 score on a scale
Standard Deviation 3.2634
-0.547 score on a scale
Standard Deviation 2.4239

SECONDARY outcome

Timeframe: Follow-up (Up to 20 Weeks)

Population: Safety Population (151, randomized subjects who received at least one dose of study drug).

Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug). The treatment-emergent adverse event (TEAE) is defined as one of the following: 1. An adverse event (AE) that occurred during the treatment period or the follow-up period. In the process of collecting the onset dates of AEs, an AE that occurs after the initiation of trial medication on Day 1 (the first day of the treatment period) should be treated as a TEAE. All AEs occurring on the day of first dose will be considered as TEAE if the time of AE occurrence relative to the dosing is unknown. 2. An AE present prior to the treatment period that worsened in severity during the treatment period or the follow-up period. 3. Any events that are present prior to the treatment period and have recovered, but recurred during the treatment period or the follow-up period should be considered as new TEAEs.

Outcome measures

Outcome measures
Measure
JTE-451 200 mg Twice Daily
n=51 Participants
JTE-451 200 mg orally twice daily for 16 weeks (total daily dose - 400 mg)
JTE-451 400 mg Twice Daily
n=50 Participants
JTE-451 400 mg orally twice daily for 16 weeks (total daily dose - 800 mg)
Placebo Twice Daily
n=50 Participants
Placebo Tablets orally twice daily for 16 weeks
Number of Subjects With Treatment-emergent Adverse Events
Number of subjects with TEAEs
27 Participants
28 Participants
25 Participants
Number of Subjects With Treatment-emergent Adverse Events
Number of subjects with no TEAEs
24 Participants
22 Participants
25 Participants

SECONDARY outcome

Timeframe: Week 16

Population: Subjects (75 subjects) in the PK population at Week 16 with available trough plasma concentrations of JTE-451 (subjects who received at least one dose of JTE-451 and have at least one usable JTE-451 plasma concentration measurement at Week 16).

Trough plasma concentration is the measured concentration at the end of a dosing interval at steady state (taken directly before next administration). Blood samples were collected at specific timepoints to measure trough plasma concentration of JTE-451 in the pharmacokinetic (PK) population.

Outcome measures

Outcome measures
Measure
JTE-451 200 mg Twice Daily
n=42 Participants
JTE-451 200 mg orally twice daily for 16 weeks (total daily dose - 400 mg)
JTE-451 400 mg Twice Daily
n=33 Participants
JTE-451 400 mg orally twice daily for 16 weeks (total daily dose - 800 mg)
Placebo Twice Daily
Placebo Tablets orally twice daily for 16 weeks
JTE-451 Trough Plasma Concentrations at Week 16
575 ng/mL
Standard Deviation 704
1210 ng/mL
Standard Deviation 1660

Adverse Events

JTE-451 200 mg Twice Daily

Serious events: 1 serious events
Other events: 20 other events
Deaths: 0 deaths

JTE-451 400 mg Twice Daily

Serious events: 2 serious events
Other events: 22 other events
Deaths: 0 deaths

Placebo Twice Daily

Serious events: 1 serious events
Other events: 17 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
JTE-451 200 mg Twice Daily
n=51 participants at risk
JTE-451 200 mg orally twice daily for 16 weeks (total daily dose - 400 mg)
JTE-451 400 mg Twice Daily
n=50 participants at risk
JTE-451 400 mg orally twice daily for 16 weeks (total daily dose - 800 mg)
Placebo Twice Daily
n=50 participants at risk
Placebo Tablets orally twice daily for 16 weeks
Cardiac disorders
Atrial fibrillation
0.00%
0/51 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
2.0%
1/50 • Number of events 1 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
0.00%
0/50 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
Infections and infestations
Breast Abscess
2.0%
1/51 • Number of events 1 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
0.00%
0/50 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
0.00%
0/50 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
Infections and infestations
Gastroenteritis
0.00%
0/51 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
2.0%
1/50 • Number of events 1 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
0.00%
0/50 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
Skin and subcutaneous tissue disorders
Psoriasis
0.00%
0/51 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
0.00%
0/50 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
2.0%
1/50 • Number of events 1 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).

Other adverse events

Other adverse events
Measure
JTE-451 200 mg Twice Daily
n=51 participants at risk
JTE-451 200 mg orally twice daily for 16 weeks (total daily dose - 400 mg)
JTE-451 400 mg Twice Daily
n=50 participants at risk
JTE-451 400 mg orally twice daily for 16 weeks (total daily dose - 800 mg)
Placebo Twice Daily
n=50 participants at risk
Placebo Tablets orally twice daily for 16 weeks
Vascular disorders
Hypertension
3.9%
2/51 • Number of events 3 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
0.00%
0/50 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
2.0%
1/50 • Number of events 1 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
Investigations
Alanine Aminotransferase Increased
2.0%
1/51 • Number of events 1 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
6.0%
3/50 • Number of events 3 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
2.0%
1/50 • Number of events 1 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
Investigations
Blood Glucose Increased
3.9%
2/51 • Number of events 2 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
2.0%
1/50 • Number of events 1 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
4.0%
2/50 • Number of events 2 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
Investigations
Gamma-Glutamyltransferase Increased
3.9%
2/51 • Number of events 2 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
4.0%
2/50 • Number of events 2 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
0.00%
0/50 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
Respiratory, thoracic and mediastinal disorders
Rhinorrhoea
0.00%
0/51 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
0.00%
0/50 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
4.0%
2/50 • Number of events 2 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
Nervous system disorders
Headache
7.8%
4/51 • Number of events 8 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
2.0%
1/50 • Number of events 1 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
4.0%
2/50 • Number of events 2 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
Gastrointestinal disorders
Abdominal Pain
3.9%
2/51 • Number of events 2 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
4.0%
2/50 • Number of events 2 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
2.0%
1/50 • Number of events 1 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
Gastrointestinal disorders
Abdominal Pain Upper
7.8%
4/51 • Number of events 4 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
4.0%
2/50 • Number of events 3 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
0.00%
0/50 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
Gastrointestinal disorders
Diarrhoea
13.7%
7/51 • Number of events 13 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
38.0%
19/50 • Number of events 30 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
6.0%
3/50 • Number of events 3 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
Skin and subcutaneous tissue disorders
Pruritus
2.0%
1/51 • Number of events 1 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
4.0%
2/50 • Number of events 4 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
2.0%
1/50 • Number of events 1 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
Infections and infestations
Nasopharyngitis
5.9%
3/51 • Number of events 4 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
4.0%
2/50 • Number of events 2 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
10.0%
5/50 • Number of events 5 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
Infections and infestations
Pharyngitis
2.0%
1/51 • Number of events 1 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
0.00%
0/50 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
4.0%
2/50 • Number of events 2 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
Infections and infestations
Sinusitis
0.00%
0/51 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
0.00%
0/50 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
4.0%
2/50 • Number of events 2 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
Infections and infestations
Upper Respiratory Tract Infection
3.9%
2/51 • Number of events 2 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
6.0%
3/50 • Number of events 3 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
8.0%
4/50 • Number of events 4 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
Infections and infestations
Urinary Tract Infection
5.9%
3/51 • Number of events 4 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
6.0%
3/50 • Number of events 3 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).
0.00%
0/50 • Up to 20 Weeks
Subjects in the Safety Population (151, randomized subjects who received at least one dose of study drug).

Additional Information

Kazuhiro Okamiya

Akros Pharma Inc.

Phone: 609-919-6123

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place

Restriction type: LTE60