Efficacy and Safety of Pemigatinib in Previously Treated Locally Advanced/Metastatic or Surgically Unresectable Solid Tumor Malignancies Harboring Activating FGFR Mutations or Translocations (FIGHT-207)

NCT ID: NCT03822117

Last Updated: 2025-11-04

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

111 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-10-17

Study Completion Date

2022-03-29

Brief Summary

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The purpose of this study is to evaluate the efficacy and safety of pemigatinib in participants with previously treated locally advanced/metastatic or surgically unresectable solid tumor malignancies harboring activating FGFR mutations or translocations.

Detailed Description

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Conditions

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Solid Tumor Malignancy

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

This study consists of 3 cohorts that will have study drug administered in parallel, Cohort A, Cohort B, and Cohort C. There is no difference in the treatment regimen between the cohorts.
Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Pemigatinib

Cohort A (Solid tumor malignancies with FGFR1-3 in frame fusions; any FGFR2 rearrangement; FGFR1/3 rearrangement with known partner\*). Cohort B (Solid tumor malignancies with known or likely activating mutations (excluding kinase domain) in FGFR1-3) Cohort C (Solid tumor malignancies with FGFR1-3 known activating mutations in kinase domain; FGFR1-3 putatively activating mutations; other FGFR1/3 rearrangements\* (not eligible for Cohort A)).

\*Only FGFR fusions or rearrangements with an intact kinase domain are eligible

Group Type EXPERIMENTAL

Pemigatinib

Intervention Type DRUG

Pemigatinib administered orally once daily (QD).

Interventions

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Pemigatinib

Pemigatinib administered orally once daily (QD).

Intervention Type DRUG

Other Intervention Names

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INCB054828

Eligibility Criteria

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Inclusion Criteria

* Histologically or cytologically confirmed solid tumor malignancy that is advanced or metastatic or is surgically unresectable.
* Radiographically measurable disease (per RECIST v1.1 or RANO for primary brain tumors). Tumor lesions located in a previously irradiated area or in an area subjected to other loco-regional therapy are considered measureable if progression has been clearly demonstrated in the lesion.
* Documentation of an FGFR1-3 gene mutation or translocation.
* Objective progression after at least 1 prior therapy and no therapy available that is likely to provide clinical benefit. Participants who are intolerant to or decline the approved therapy are eligible only if they have no therapy available that is likely to provide clinical benefit.
* Eastern Cooperative Oncology Group performance status 0 to 2.
* Baseline archival tumor specimen (if less than 24 months from date of screening) or willingness to undergo a pretreatment tumor biopsy to obtain the specimen. Must be a tumor block or approximately 15 unstained slides from biopsy or resection of primary tumor or metastasis.
* Willingness to avoid pregnancy or fathering children.

Exclusion Criteria

* Prior receipt of a selective FGFR inhibitor in the past 6 months.
* Receipt of anticancer medications or investigational drugs for any indication or reason within 28 days before first dose of pemigatinib.
* Cannot be a candidate for potentially curative surgery.
* Current evidence of clinically significant corneal or retinal disorder as confirmed by ophthalmologic examination.
* Radiation therapy administered within 2 weeks of enrollment/first dose of study treatment.
* Untreated brain or central nervous system (CNS) metastases or brain or CNS metastases that have progressed (eg, evidence of new or enlarging brain metastasis or new neurological symptoms attributable to brain or CNS metastases).
* Known additional malignancy that is progressing or requires active treatment.
* History of calcium and phosphate hemostasis disorder or systemic mineral imbalance with ectopic calcification of soft tissues.
* Clinically significant or uncontrolled cardiac disease.
* Active chronic or current infectious disease requiring systemic antibiotic, antifungal, or antiviral treatment within 2 weeks before enrollment (participants with asymptomatic chronic infections on prophylactic treatment are allowed).
* Evidence of active hepatitis B virus (HBV) or hepatitis C virus (HCV) infection (defined as elevated transaminases or cirrhosis; chronic HBV/HCV infection with no cirrhosis and no elevated transaminases is allowed).
* Known HIV infection.
* Use of any potent CYP3A4 inhibitors or inducers or moderate CYP3A4 inducers within 14 days or five half-lives (whichever is longer) before the first dose of study drug/treatment.
* Women who are pregnant or breastfeeding.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Incyte Corporation

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Peter Langmuir, MD

Role: STUDY_DIRECTOR

Incyte Corporation

Locations

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Samsung Medical Center

Seoul, , South Korea

Site Status

Cancer Treatment Centers of America

Goodyear, Arizona, United States

Site Status

Mayo Clinic Hospital

Phoenix, Arizona, United States

Site Status

The University of Arizona Cancer Center

Tucson, Arizona, United States

Site Status

Chao Family Comprehensive Cancer Center University of California, Irvine

Orange, California, United States

Site Status

Stanford Cancer Center

Palo Alto, California, United States

Site Status

John Wayne Cancer Institute

Santa Monica, California, United States

Site Status

St. Joseph Heritage Healthcare

Santa Rosa, California, United States

Site Status

Florida Cancer Specialists & Research Institute

Fort Myers, Florida, United States

Site Status

Mayo Clinic Jacksonville

Jacksonville, Florida, United States

Site Status

Florida Cancer Specialists

St. Petersburg, Florida, United States

Site Status

Florida Cancer Specialists

Tallahassee, Florida, United States

Site Status

Florida Cancer Specialists

West Palm Beach, Florida, United States

Site Status

Illinois Cancer Specialists

Arlington Heights, Illinois, United States

Site Status

Edward H Kaplan & Associates

Skokie, Illinois, United States

Site Status

Carle Cancer Center

Urbana, Illinois, United States

Site Status

Cancer Treatment Centers of America

Zion, Illinois, United States

Site Status

Indiana University Health - Arnett Cancer Care

Lafayette, Indiana, United States

Site Status

University of Iowa

Iowa City, Iowa, United States

Site Status

University of Kansas Cancer Center

Westwood, Kansas, United States

Site Status

Ochsner Clinic

New Orleans, Louisiana, United States

Site Status

Central Maine Medical Center

Lewiston, Maine, United States

Site Status

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

Umass Memorial Medical Center, Inc.

Worcester, Massachusetts, United States

Site Status

Mayo Clinic Rochester

Rochester, Minnesota, United States

Site Status

Comprehensive Cancer Centers of Nevada

Las Vegas, Nevada, United States

Site Status

Dartmouth Hitchcock Medical Center

Lebanon, New Hampshire, United States

Site Status

Summit Medical Group

Florham Park, New Jersey, United States

Site Status

Winthrop University Hospital

Mineola, New York, United States

Site Status

Oncology Specialists of Charlotte

Charlotte, North Carolina, United States

Site Status

Duke Cancer Center

Durham, North Carolina, United States

Site Status

Wake Forest Baptist Medical Center

Winston-Salem, North Carolina, United States

Site Status

Stephenson Cancer Center

Oklahoma City, Oklahoma, United States

Site Status

Southwestern Regional Medical Center

Tulsa, Oklahoma, United States

Site Status

Cancer Institute of Greenville Health System

Greenville, South Carolina, United States

Site Status

The West Clinic Pc

Germantown, Tennessee, United States

Site Status

University of Texas Southwestern Medical Center

Dallas, Texas, United States

Site Status

Houston Methodist Hospital

Houston, Texas, United States

Site Status

Joe Arrington Cancer Center

Lubbock, Texas, United States

Site Status

Virginia Cancer Specialists, Pc

Fairfax, Virginia, United States

Site Status

Virginia Oncology Associates-Lake Wright

Norfolk, Virginia, United States

Site Status

Seattle Cancer Care Alliance

Seattle, Washington, United States

Site Status

Multicare Institute For Research & Innovation

Tacoma, Washington, United States

Site Status

West Virginia University Hospitals Inc

Morgantown, West Virginia, United States

Site Status

University of Wisconsin Carbone Cancer Center

Madison, Wisconsin, United States

Site Status

The Finsen Centre National Hospital

Copenhagen, , Denmark

Site Status

Institut Bergonie

Bordeaux, , France

Site Status

CENTRE GEORGES FRAN�OIS LECLERC

Dijon, , France

Site Status

Centre Antoine Lacassagne

Nice, , France

Site Status

Hospital Saint Louis

Paris, , France

Site Status

A.P.H. Paris Hopital Cochin

Paris, , France

Site Status

Institut Universitaire Du Cancer de Toulouse Oncopole

Toulouse, , France

Site Status

Universitatsklinikum Koln

Cologne, , Germany

Site Status

University Medical Center Freiburg

Freiburg im Breisgau, , Germany

Site Status

University Medical Centre Hamburg-Eppendorf, Centre of Oncology

Hamburg, , Germany

Site Status

University Hospital Grosshadern Munich

Munich, , Germany

Site Status

Universitaetsklinikum in Tubingen

Tübingen, , Germany

Site Status

Ha Emek Medical Center

Afula, , Israel

Site Status

Rambam Health Care Campus

Haifa, , Israel

Site Status

Hadassah Hebrew University Medical Center Ein Karem Hadassah

Jerusalem, , Israel

Site Status

Rabin Medical Center - Beilinson Hospital

Petah Tikva, , Israel

Site Status

Assaf Harofeh Medical Center

Ẕerifin, , Israel

Site Status

L AZIENDA OSPEDALIERO-UNIVERSITARIA DI BOLOGNA POLICLINICO S. ORSOLA � MALPIGHI

Bologna, , Italy

Site Status

Fondazione Del Piemonte Per L Oncologia Ircc Candiolo

Candiolo, , Italy

Site Status

Fondazione Irccs Istituto Nazionale Dei Tumori

Milan, , Italy

Site Status

Istituto Nazionale Tumori Irccs Fondazione Pascale

Napoli, , Italy

Site Status

Istituto Nazionale Tumori Regina Elena Irccs

Roma, , Italy

Site Status

Centro Ricerche Cliniche Di Verona (Crc)

Verona, , Italy

Site Status

National Hospital Organization Kyushu Cancer Center

Fukuoka, , Japan

Site Status

Kanazawa University Hospital

Ishikawa, , Japan

Site Status

Kobe University Hospital

Kobe, , Japan

Site Status

Tohoku University Hospital

Sendai, , Japan

Site Status

Keio University Hospital

Shinjuku-ku, , Japan

Site Status

Shizuoka Cancer Center

Shizuoka, , Japan

Site Status

Kanagawa Cancer Center

Yokohama, , Japan

Site Status

National Cancer Center

Goyang-si, , South Korea

Site Status

Seoul National University Bundang Hospital

Seongnam-si, , South Korea

Site Status

Severance Hospital Yonsei University Health System

Seoul, , South Korea

Site Status

Hospital General Universitario Vall D Hebron

Barcelona, , Spain

Site Status

Hospital Clinic I Provincial

Barcelona, , Spain

Site Status

Centro Integral Oncologico Clara Campal (Ciocc)

Madrid, , Spain

Site Status

Hospital Regional Universitario de Malaga

Málaga, , Spain

Site Status

Clinica Universidad de Navarra (Cun)

Pamplona, , Spain

Site Status

Hospital Universitario Marques de Valdecilla

Santander, , Spain

Site Status

Hospital Universitario Y Politcnico de La Fe

Valencia, , Spain

Site Status

Inselspital - Universitaetsspital Bern

Bern, , Switzerland

Site Status

Universitatsspital Zurich

Zurich, , Switzerland

Site Status

University College London Hospitals (Uclh)

London, , United Kingdom

Site Status

Imperial College Healthcare Nhs Trust - Hammersmith Hospital

London, , United Kingdom

Site Status

Sarah Cannon Research Institute

London, , United Kingdom

Site Status

Countries

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United States Denmark France Germany Israel Italy Japan South Korea Spain Switzerland United Kingdom

References

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Rodon J, Damian S, Furqan M, Garcia-Donas J, Imai H, Italiano A, Spanggaard I, Ueno M, Yokota T, Veronese ML, Oliveira N, Li X, Gilmartin A, Schaffer M, Goyal L. Pemigatinib in previously treated solid tumors with activating FGFR1-FGFR3 alterations: phase 2 FIGHT-207 basket trial. Nat Med. 2024 Jun;30(6):1645-1654. doi: 10.1038/s41591-024-02934-7. Epub 2024 May 6.

Reference Type DERIVED
PMID: 38710951 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2018-004768-69

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

INCB 54828-207

Identifier Type: -

Identifier Source: org_study_id

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