Trial Outcomes & Findings for Tolperisone in Acute Muscle Spasm of the Back (NCT NCT03802565)

NCT ID: NCT03802565

Last Updated: 2022-02-01

Results Overview

Mean effect size between Tolperisone and Placebo of subject-rated pain due to acute back spasm using a Numerical Rating Scale (NRS; 0-10 scale, from no pain to worst possible pain) on Day 14 "right now."

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

415 participants

Primary outcome timeframe

Day 1 to Day 14

Results posted on

2022-02-01

Participant Flow

Participant milestones

Participant milestones
Measure
Tolperisone 50 mg
TID (150 mg/day) Tolperisone: TID
Tolperisone 100 mg
TID (300 mg/day) Tolperisone: TID
Tolperisone 150 mg
TID (450 mg/day) Tolperisone: TID
Tolperisone 200 mg
TID (600 mg/day) Tolperisone: TID
Placebo
TID Placebo: Placebo
Overall Study
STARTED
82
87
83
85
78
Overall Study
COMPLETED
77
83
74
77
72
Overall Study
NOT COMPLETED
5
4
9
8
6

Reasons for withdrawal

Reasons for withdrawal
Measure
Tolperisone 50 mg
TID (150 mg/day) Tolperisone: TID
Tolperisone 100 mg
TID (300 mg/day) Tolperisone: TID
Tolperisone 150 mg
TID (450 mg/day) Tolperisone: TID
Tolperisone 200 mg
TID (600 mg/day) Tolperisone: TID
Placebo
TID Placebo: Placebo
Overall Study
Adverse Event
0
1
2
1
1
Overall Study
Withdrawal by Subject
2
2
2
0
1
Overall Study
Protocol Violation
2
1
4
5
1
Overall Study
Lost to Follow-up
0
0
1
0
0
Overall Study
Subjects Related to Each Other
1
0
0
2
1
Overall Study
Elevated Enzymes
0
0
0
0
2

Baseline Characteristics

Tolperisone in Acute Muscle Spasm of the Back

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Tolperisone 50 mg
n=82 Participants
TID (150 mg/day) Tolperisone: TID
Tolperisone 100 mg
n=87 Participants
TID (300 mg/day) Tolperisone: TID
Tolperisone 150 mg
n=83 Participants
TID (450 mg/day) Tolperisone: TID
Tolperisone 200 mg
n=85 Participants
TID (600 mg/day) Tolperisone: TID
Placebo
n=78 Participants
TID Placebo: Placebo
Total
n=415 Participants
Total of all reporting groups
Age, Customized
43.5 years
n=5 Participants
44.4 years
n=7 Participants
44.3 years
n=5 Participants
42.0 years
n=4 Participants
41.6 years
n=21 Participants
43.6 years
n=10 Participants
Sex: Female, Male
Female
45 Participants
n=5 Participants
57 Participants
n=7 Participants
41 Participants
n=5 Participants
41 Participants
n=4 Participants
49 Participants
n=21 Participants
233 Participants
n=10 Participants
Sex: Female, Male
Male
37 Participants
n=5 Participants
30 Participants
n=7 Participants
42 Participants
n=5 Participants
44 Participants
n=4 Participants
29 Participants
n=21 Participants
182 Participants
n=10 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
13 Participants
n=5 Participants
18 Participants
n=7 Participants
22 Participants
n=5 Participants
20 Participants
n=4 Participants
16 Participants
n=21 Participants
89 Participants
n=10 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
69 Participants
n=5 Participants
69 Participants
n=7 Participants
61 Participants
n=5 Participants
65 Participants
n=4 Participants
62 Participants
n=21 Participants
326 Participants
n=10 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
0 Participants
n=21 Participants
0 Participants
n=10 Participants
Race (NIH/OMB)
American Indian or Alaska Native
1 Participants
n=5 Participants
0 Participants
n=7 Participants
1 Participants
n=5 Participants
0 Participants
n=4 Participants
1 Participants
n=21 Participants
3 Participants
n=10 Participants
Race (NIH/OMB)
Asian
1 Participants
n=5 Participants
4 Participants
n=7 Participants
2 Participants
n=5 Participants
4 Participants
n=4 Participants
3 Participants
n=21 Participants
14 Participants
n=10 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
1 Participants
n=5 Participants
1 Participants
n=7 Participants
1 Participants
n=5 Participants
0 Participants
n=4 Participants
0 Participants
n=21 Participants
3 Participants
n=10 Participants
Race (NIH/OMB)
Black or African American
29 Participants
n=5 Participants
32 Participants
n=7 Participants
29 Participants
n=5 Participants
35 Participants
n=4 Participants
29 Participants
n=21 Participants
154 Participants
n=10 Participants
Race (NIH/OMB)
White
50 Participants
n=5 Participants
50 Participants
n=7 Participants
49 Participants
n=5 Participants
45 Participants
n=4 Participants
42 Participants
n=21 Participants
236 Participants
n=10 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
0 Participants
n=7 Participants
1 Participants
n=5 Participants
0 Participants
n=4 Participants
3 Participants
n=21 Participants
4 Participants
n=10 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
1 Participants
n=4 Participants
0 Participants
n=21 Participants
1 Participants
n=10 Participants
Body Mass Index
28.23 kilogram/meter^2
n=5 Participants
28.48 kilogram/meter^2
n=7 Participants
28.34 kilogram/meter^2
n=5 Participants
28.45 kilogram/meter^2
n=4 Participants
28.53 kilogram/meter^2
n=21 Participants
28.38 kilogram/meter^2
n=10 Participants

PRIMARY outcome

Timeframe: Day 1 to Day 14

Mean effect size between Tolperisone and Placebo of subject-rated pain due to acute back spasm using a Numerical Rating Scale (NRS; 0-10 scale, from no pain to worst possible pain) on Day 14 "right now."

Outcome measures

Outcome measures
Measure
Tolperisone 50 mg
n=82 Participants
TID (150 mg/day) Tolperisone: TID
Tolperisone 100 mg
n=87 Participants
TID (300 mg/day) Tolperisone: TID
Tolperisone 150 mg
n=83 Participants
TID (450 mg/day) Tolperisone: TID
Tolperisone 200 mg
n=85 Participants
TID (600 mg/day) Tolperisone: TID
Placebo
n=78 Participants
TID Placebo: Placebo
Mean Effect Size in Subjected-Rated Pain
-4.2 score on a scale
Interval -9.0 to 1.0
-4.0 score on a scale
Interval -10.0 to 2.0
-3.7 score on a scale
Interval -8.0 to 1.0
-4.4 score on a scale
Interval -10.0 to 1.0
-3.5 score on a scale
Interval -8.0 to 1.0

Adverse Events

Tolperisone 50 mg

Serious events: 0 serious events
Other events: 7 other events
Deaths: 0 deaths

Tolperisone 100 mg

Serious events: 0 serious events
Other events: 13 other events
Deaths: 0 deaths

Tolperisone 150 mg

Serious events: 0 serious events
Other events: 12 other events
Deaths: 0 deaths

Tolperisone 200 mg

Serious events: 0 serious events
Other events: 14 other events
Deaths: 0 deaths

Placebo

Serious events: 0 serious events
Other events: 5 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Tolperisone 50 mg
n=82 participants at risk
TID (150 mg/day) Tolperisone: TID
Tolperisone 100 mg
n=87 participants at risk
TID (300 mg/day) Tolperisone: TID
Tolperisone 150 mg
n=83 participants at risk
TID (450 mg/day) Tolperisone: TID
Tolperisone 200 mg
n=85 participants at risk
TID (600 mg/day) Tolperisone: TID
Placebo
n=78 participants at risk
TID Placebo: Placebo
Nervous system disorders
Headache
3.7%
3/82 • First Dose, Day 1 to Follow-up, Day 28
5.7%
5/87 • First Dose, Day 1 to Follow-up, Day 28
9.6%
8/83 • First Dose, Day 1 to Follow-up, Day 28
9.4%
8/85 • First Dose, Day 1 to Follow-up, Day 28
3.8%
3/78 • First Dose, Day 1 to Follow-up, Day 28
Nervous system disorders
Dizziness
1.2%
1/82 • First Dose, Day 1 to Follow-up, Day 28
2.3%
2/87 • First Dose, Day 1 to Follow-up, Day 28
0.00%
0/83 • First Dose, Day 1 to Follow-up, Day 28
2.4%
2/85 • First Dose, Day 1 to Follow-up, Day 28
0.00%
0/78 • First Dose, Day 1 to Follow-up, Day 28
Nervous system disorders
Somnolence
0.00%
0/82 • First Dose, Day 1 to Follow-up, Day 28
3.4%
3/87 • First Dose, Day 1 to Follow-up, Day 28
0.00%
0/83 • First Dose, Day 1 to Follow-up, Day 28
1.2%
1/85 • First Dose, Day 1 to Follow-up, Day 28
2.6%
2/78 • First Dose, Day 1 to Follow-up, Day 28
Gastrointestinal disorders
Diarrhoea
2.4%
2/82 • First Dose, Day 1 to Follow-up, Day 28
2.3%
2/87 • First Dose, Day 1 to Follow-up, Day 28
3.6%
3/83 • First Dose, Day 1 to Follow-up, Day 28
1.2%
1/85 • First Dose, Day 1 to Follow-up, Day 28
0.00%
0/78 • First Dose, Day 1 to Follow-up, Day 28
Gastrointestinal disorders
Nausea
1.2%
1/82 • First Dose, Day 1 to Follow-up, Day 28
1.1%
1/87 • First Dose, Day 1 to Follow-up, Day 28
1.2%
1/83 • First Dose, Day 1 to Follow-up, Day 28
2.4%
2/85 • First Dose, Day 1 to Follow-up, Day 28
0.00%
0/78 • First Dose, Day 1 to Follow-up, Day 28

Additional Information

Randall Kaye, MD - Chief Medical Officer

Neurana Pharmaceuticals, Inc.

Phone: 858-732-0708

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place