Trial Outcomes & Findings for Collection of Blood Samples From Patients With Relapsing MS Who Developed ITP After Receiving Lemtrada (NCT NCT03784898)

NCT ID: NCT03784898

Last Updated: 2022-03-28

Results Overview

Each participant provided a maximum total of 69 milliliter of whole blood sample. Samples were collected in the following order: 1. Deoxyribonucleic acid (DNA) Paired box (PAX)gene tubes (2 tubes), 2. Ribonucleic acid (RNA) PAXgene tubes (2 tubes), 3. Ethylenediaminetetraacetic acid (EDTA) tubes for peripheral blood mononuclear cells (PBMCs) (5 tubes), 4. Serum Separator tube (SST) (1 tube), and 5. Dipotassium Ethylenediaminetetraacetic acid (K2EDTA) tube (1 tube); where DNA PAXgene tubes were used for DNA preparation, RNA PAXgene tubes for RNA preparation, EDTA for PBMC isolation, SST tubes for serum preparation and K2EDTA for plasma preparation. DNA was extracted from peripheral blood for future analysis.

Recruitment status

COMPLETED

Study phase

PHASE4

Target enrollment

13 participants

Primary outcome timeframe

Baseline (Day 1)

Results posted on

2022-03-28

Participant Flow

The study was conducted at a single site in the United States. A total of 14 participants were screened between 8 February 2019 to 11 December 2019, of which,1 participant was screen failure. Screen failures was mainly due to inclusion criteria not met.

A total of 13 participants were enrolled in the study.

Participant milestones

Participant milestones
Measure
Participants Diagnosed With ITP
Participants with Relapsing Forms of Multiple Sclerosis (RMS) who developed Immune thrombocytopenic purpura (ITP) after Lemtrada treatment were included in this study and provided blood samples for future genetic testing and biomarker analysis.
Overall Study
STARTED
13
Overall Study
COMPLETED
13
Overall Study
NOT COMPLETED
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Collection of Blood Samples From Patients With Relapsing MS Who Developed ITP After Receiving Lemtrada

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Participants Diagnosed With ITP
n=13 Participants
Participants with RMS who developed ITP after Lemtrada treatment were included in this study and provided blood samples for future genetic testing and biomarker analysis.
Age, Continuous
48.2 years
STANDARD_DEVIATION 7.8 • n=5 Participants
Sex: Female, Male
Female
10 Participants
n=5 Participants
Sex: Female, Male
Male
3 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
0 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=5 Participants
Race (NIH/OMB)
White
13 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants

PRIMARY outcome

Timeframe: Baseline (Day 1)

Population: Analysis was performed on all enrolled population.

Each participant provided a maximum total of 69 milliliter of whole blood sample. Samples were collected in the following order: 1. Deoxyribonucleic acid (DNA) Paired box (PAX)gene tubes (2 tubes), 2. Ribonucleic acid (RNA) PAXgene tubes (2 tubes), 3. Ethylenediaminetetraacetic acid (EDTA) tubes for peripheral blood mononuclear cells (PBMCs) (5 tubes), 4. Serum Separator tube (SST) (1 tube), and 5. Dipotassium Ethylenediaminetetraacetic acid (K2EDTA) tube (1 tube); where DNA PAXgene tubes were used for DNA preparation, RNA PAXgene tubes for RNA preparation, EDTA for PBMC isolation, SST tubes for serum preparation and K2EDTA for plasma preparation. DNA was extracted from peripheral blood for future analysis.

Outcome measures

Outcome measures
Measure
Participants Diagnosed With ITP
n=13 Participants
Participants with RMS who developed ITP after Lemtrada treatment were included in this study and provided blood samples for future genetic testing and biomarker analysis.
Number of Participants Who Provided Whole Blood Samples for DNA Extraction and Analysis
DNA PAXgene (tube 2)
12 Participants
Number of Participants Who Provided Whole Blood Samples for DNA Extraction and Analysis
EDTA for PBMCs (tube 3)
13 Participants
Number of Participants Who Provided Whole Blood Samples for DNA Extraction and Analysis
EDTA for PBMCs (tube 5)
5 Participants
Number of Participants Who Provided Whole Blood Samples for DNA Extraction and Analysis
DNA PAXgene (tube 1)
12 Participants
Number of Participants Who Provided Whole Blood Samples for DNA Extraction and Analysis
RNA PAXgene (tube 1)
12 Participants
Number of Participants Who Provided Whole Blood Samples for DNA Extraction and Analysis
RNA PAXgene (tube 2)
12 Participants
Number of Participants Who Provided Whole Blood Samples for DNA Extraction and Analysis
EDTA for PBMCs (tube 1)
13 Participants
Number of Participants Who Provided Whole Blood Samples for DNA Extraction and Analysis
EDTA for PBMCs (tube 2)
13 Participants
Number of Participants Who Provided Whole Blood Samples for DNA Extraction and Analysis
EDTA for PBMCs (tube 4)
13 Participants
Number of Participants Who Provided Whole Blood Samples for DNA Extraction and Analysis
SST tube
12 Participants
Number of Participants Who Provided Whole Blood Samples for DNA Extraction and Analysis
K2EDTA tube
12 Participants

Adverse Events

Participants Diagnosed With ITP

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Adverse event data not reported

Additional Information

Trial Transparency Team

Sanofi

Phone: 800-633-1610

Results disclosure agreements

  • Principal investigator is a sponsor employee The Sponsor supports publication of clinical trial results but may request that investigators temporarily delay or alter publications in order to protect proprietary information. The Sponsor may also require that the results of multicenter studies be published only in their entirety and not as individual site data.
  • Publication restrictions are in place

Restriction type: OTHER