Zandelisib (ME-401) in Subjects With Follicular Lymphoma or Marginal Zone Lymphoma After Failure of Two or More Prior Therapies (TIDAL)

NCT ID: NCT03768505

Last Updated: 2024-12-31

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

169 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-06-25

Study Completion Date

2023-03-24

Brief Summary

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This is the study of the PI3Kδ inhibitor Zandelisib (ME-401) in subjects with relapsed/refractory follicular lymphoma or marginal zone lymphoma after failure of at least 2 prior lines of systemic therapy

Detailed Description

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This is a global, multicenter open-label, single-arm, Phase 2 study of the PI3Kδ inhibitor Zandelisib (ME-401) in subjects with relapsed/refractory follicular lymphoma or marginal zone lymphoma after failure of at least 2 prior lines of systemic therapy which must have included an anti-CD20 antibody and chemotherapy with an alkylating agent or a purine analogue.

Approximately 180 subjects will be enrolled and treated with Zandelisib (ME-401) on the intermittent schedule.

Conditions

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Follicular Lymphoma (FL) Non Hodgkin Lymphoma Marginal Zone Lymphoma

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Treatment with Zandelisib (ME-401) (60 mg) given orally once a day on an intermittent schedule
Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Zandelisib (ME-401) open label

Subjects with relapsed/refractory FL or MZL will be administered 60 mg of ME-401 orally, once a day on an intermittent schedule (IS).

Group Type EXPERIMENTAL

Zandelisib (ME-401)

Intervention Type DRUG

Zandelisib (ME-401) 60 mg

Interventions

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Zandelisib (ME-401)

Zandelisib (ME-401) 60 mg

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Histologically confirmed diagnosis as defined in the World Health Organization (WHO) classification scheme

1. Follicular Lymphoma (FL) limited to Grade 1,2 or 3a or
2. Marginal Zone Lymphoma (MZL) including nodal, extranodal and splenic MZL
* Subjects that have had progression of disease or had no response to therapy after at least 2 prior systemic therapies for FL or MZL
* Age ≥ 18
* At least one bi-dimensionally measurable nodal lesion \> 1.5 cm in its longest diameter by computed tomography (CT) scan as defined by the Lugano Classification
* Adequate hematologic, renal and hepatic parameters at screening unless abnormal values are due to FL per Investigator assessment
* QT-interval corrected according to Fridericia's formula (QTcF) ≤ 450 milliseconds (msec);
* Left ventricular ejection fraction (LVEF) ≥ 45%

Exclusion Criteria

* Histologically confirmed FL Grade 3b transformation from FL to an aggressive lymphoma
* Known lymphomatous involvement of the central nervous system
* Uncontrolled clinically significant illness
* Ongoing or history of drug-induced pneumonitis
* History of clinically significant cardiovascular abnormalities
* History of clinically significant GI conditions
* Known history of, or active HIV infection
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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MEI Pharma, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Oncology Institute of Hope and Innovation

Tucson, Arizona, United States

Site Status

Pacific Cancer Medical Center, Inc.

Anaheim, California, United States

Site Status

Tower Hematology Oncology

Beverly Hills, California, United States

Site Status

The Oncology Institute of Hope and Innovation

Downey, California, United States

Site Status

Sharp Memorial Hospital

San Diego, California, United States

Site Status

H. Lee Moffit Cancer Center

Tampa, Florida, United States

Site Status

Cleveland Clinic-Florida

Weston, Florida, United States

Site Status

Rush University Medical Center

Chicago, Illinois, United States

Site Status

Advocate Health & Hospitals Corporation

Niles, Illinois, United States

Site Status

Investigative Clinical Research of Indiana LLC

Indianapolis, Indiana, United States

Site Status

Dana-Farber Cancer Institute

Boston, Massachusetts, United States

Site Status

University of Michigan Medical School

Ann Arbor, Michigan, United States

Site Status

St. Vincent Frontier Cancer Center

Billings, Montana, United States

Site Status

The Oncology Institute of Hope and Innovation

Henderson, Nevada, United States

Site Status

Memorial Sloan Kettering

Basking Ridge, New Jersey, United States

Site Status

Memorial Sloan Kettering

Middletown, New Jersey, United States

Site Status

Memorial Sloan Kettering

Montvale, New Jersey, United States

Site Status

San Juan Oncology

Farmington, New Mexico, United States

Site Status

Memorial Sloan Kettering

Commack, New York, United States

Site Status

Memorial Sloan Kettering

Harrison, New York, United States

Site Status

Clinical Research Alliance

Lake Success, New York, United States

Site Status

Memorial Sloan Kettering

New York, New York, United States

Site Status

Stony Brook University

Stony Brook, New York, United States

Site Status

Memorial Sloan Kettering

Uniondale, New York, United States

Site Status

Duke Cancer Center

Durham, North Carolina, United States

Site Status

Cleveland Clinic

Cleveland, Ohio, United States

Site Status

Oregon Health and Science University

Portland, Oregon, United States

Site Status

Vanderbilt University

Nashville, Tennessee, United States

Site Status

Renovatio Clinical

Houston, Texas, United States

Site Status

Swedish Cancer Institute

Edmonds, Washington, United States

Site Status

Swedish Cancer Institute

Seattle, Washington, United States

Site Status

Medical Oncology Associates PS

Spokane, Washington, United States

Site Status

University of Wisconsin Carbone Cancer Center

Madison, Wisconsin, United States

Site Status

Marshfield Medical Center

Marshfield, Wisconsin, United States

Site Status

Peninsula and South Eastern Haematology and Oncology Group

Frankston, Victoria, Australia

Site Status

The Perth Blood Institute

West Perth, Western Australia, Australia

Site Status

Liverpool Hospital

Sydney, , Australia

Site Status

Kepler Universitatsklinikum GmBH

Linz, , Austria

Site Status

Medical University of Vienna

Vienna, , Austria

Site Status

AZ Sint-Jan Brugge-Oostende

Bruges, , Belgium

Site Status

Institut Jules Bordet

Brussels, , Belgium

Site Status

Cliniques Universitaires Saint-Luc

Brussels, , Belgium

Site Status

Antwerp University Hospital

Edegem, , Belgium

Site Status

C H de la Cote Basque, Service d'Hematologie

Bayonne, , France

Site Status

CHD Vendee, Onco-hematologie

La Roche-sur-Yon, , France

Site Status

Centre Hospitalier du Mans

Le Mans, , France

Site Status

Centre Hospitalier de Mulhouse

Mulhouse, , France

Site Status

Centre Hospitalier Universitaire (CHU) de Poitiers - Hôpital de la Miletrie

Poitiers, , France

Site Status

Institut Gustave Roussy

Villejuif, , France

Site Status

Klinikum Mutterhaus Feldstr

Trier, Rhineland-Palatinate, Germany

Site Status

Hamatologisch-Onkolgische Praxis

Nordheim, Stolberg, Germany

Site Status

Universitatsklinikum Halle

Halle, , Germany

Site Status

Munich Municipal Hospital

Munich, , Germany

Site Status

Universitatsklinikum Munster

Münster, , Germany

Site Status

Universitatsklinikum Ulm

Ulm, , Germany

Site Status

Centro di Riferimento Oncologico di Aviano (CRO) IRCCS

Aviano, , Italy

Site Status

Policlinico Sant'Orsola Malpighi

Bologna, , Italy

Site Status

IRCCS AOU Policlinico San Martino

Genova, , Italy

Site Status

Istituto Scientifico Romagnolo per lo Studio e la Cura dei Tumori I.R.S.T.

Meldola, , Italy

Site Status

UOC Oncoematologia

Napoli, , Italy

Site Status

Ospedale Santa Maria delle Croci

Ravenna, , Italy

Site Status

Infermi Hospital Rimini

Rimini, , Italy

Site Status

Universita Cattolica del Sacro Cuore

Roma, , Italy

Site Status

IRCCS Regina Elena National Cancer Institute

Rome, , Italy

Site Status

Azienda Ospedaliera Santa Maria

Terni, , Italy

Site Status

Ospedale DellAngelo Di Mestre Umberto I

Venice, , Italy

Site Status

North Shore Hospital

Auckland, , New Zealand

Site Status

Southern District Hospital

Dunedin, , New Zealand

Site Status

Szpital Uniwersytecki nr 2 im.

Bydgoszcz, , Poland

Site Status

Pratia MCM Krakow

Krakow, , Poland

Site Status

ojewodzkie Wielospecjalistyczne Centrum

Lodz, , Poland

Site Status

Primary Specialty Oncology

Warsaw, , Poland

Site Status

Instytut Hematologii i Transfuzjologii

Warsaw, , Poland

Site Status

Dolnoslaskie Centrum Transplantacji Komorkowych z Krajowym Bankiem Dawcow Szpiku

Wroclaw, , Poland

Site Status

Dong-A University Hospital

Busan, , South Korea

Site Status

Pusan National University Hospital

Busan, , South Korea

Site Status

Korea University Anam Hospital

Seoul, , South Korea

Site Status

Seoul National University Hospital

Seoul, , South Korea

Site Status

Asan Medical Center

Seoul, , South Korea

Site Status

Samsung Medical Center

Seoul, , South Korea

Site Status

Ewha Womans University Mokdong Hospital

Seoul, , South Korea

Site Status

The Catholic University of Korea-Seoul St. Marys Hospital

Seoul, , South Korea

Site Status

Ulsan University Hospital

Ulsan, , South Korea

Site Status

Hospital Universitario de Canarias

San Cristóbal de La Laguna, Tenerife, Spain

Site Status

Hospital Universitari Vall d'Hebron

Barcelona, , Spain

Site Status

Hospital Universitari Mutua Terrasa

Barcelona, , Spain

Site Status

ICO-Hospital Duran i Reynals

Barcelona, , Spain

Site Status

MD Anderson Cancer Center

Madrid, , Spain

Site Status

Hospital Universitario Ramon y Cajal

Madrid, , Spain

Site Status

Fundacion Jimenez Diaz

Madrid, , Spain

Site Status

Hospital Universitario Quiron Salud Madrid

Madrid, , Spain

Site Status

Complejo Hospitalario de Navarra

Pamplona, , Spain

Site Status

Hospital Clinico de Salamanca

Salamanca, , Spain

Site Status

Hospital Universitario Virgen Macarena

Seville, , Spain

Site Status

Hospital Virgen del Rocio

Seville, , Spain

Site Status

Miguel Servet Hospital

Zaragoza, , Spain

Site Status

Ente Ospedaliero Cantonale (EOC)

Bellinzona, , Switzerland

Site Status

China Medical University Hospital

Taichung, , Taiwan

Site Status

National Cheng Kung University Hospital

Tainan City, , Taiwan

Site Status

Chi-Mei Medical Center, Liouying

Tainan City, , Taiwan

Site Status

National Taiwan University Hospital NTUH

Taipei, , Taiwan

Site Status

North Wales Cancer Treatment Centre, Glan Clwyd Hospital

Rhyl, Denbighire, United Kingdom

Site Status

Royal Marsden Hospital

London, Sutton, United Kingdom

Site Status

Nottingham University Hospital

Nottingham, UK, United Kingdom

Site Status

Belfast Health and Social Care Trust - Belfast City Hospital

Belfast, , United Kingdom

Site Status

Royal Cornwall Hospital

Cornwell, , United Kingdom

Site Status

e Clatterbridge Cancer Centre

Liverpool, , United Kingdom

Site Status

Royal Liverpool University Hospital

Liverpool, , United Kingdom

Site Status

Lewisham and Greenwich University Hospital Lewisham

London, , United Kingdom

Site Status

St George's Hospital

London, , United Kingdom

Site Status

Centre for Haematology, Imperial College London

London, , United Kingdom

Site Status

The Christie NHS Foundation Trust

Manchester, , United Kingdom

Site Status

Norfolk and Norwich University Hospital NHS Foundation Trust

Norwich, , United Kingdom

Site Status

Oxford University Hospitals

Oxford, , United Kingdom

Site Status

Royal Hallamshire Hospital

Sheffield, , United Kingdom

Site Status

Countries

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United States Australia Austria Belgium France Germany Italy New Zealand Poland South Korea Spain Switzerland Taiwan United Kingdom

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2018-002896-17

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

ME-401-003

Identifier Type: -

Identifier Source: org_study_id