A Study of the Efficacy and Safety of PXL770 Versus Placebo After 12 Weeks of Treatment in Patients With NAFLD

NCT ID: NCT03763877

Last Updated: 2021-10-28

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

121 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-03-29

Study Completion Date

2020-08-10

Brief Summary

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This study will assess the efficacy and safety of 3 doses of PXL770 versus placebo after 12 weeks of treatment.

Detailed Description

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The study will be performed in patients with Nonalcoholic Fatty Liver Disease. The primary endpoint will be the assessment of the change in the percentage of liver fat mass (assessed by MRI-PDFF).

Conditions

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Nonalcoholic Fatty Liver

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Group 1

PXL770 Dose 1

Group Type EXPERIMENTAL

PXL770

Intervention Type DRUG

Oral capsule

Group 2

PXL770 Dose 2

Group Type EXPERIMENTAL

PXL770

Intervention Type DRUG

Oral capsule

Group 3

PXL770 Dose 3

Group Type EXPERIMENTAL

PXL770

Intervention Type DRUG

Oral capsule

Group 4

Placebo oral capsule

Group Type PLACEBO_COMPARATOR

Placebo Oral Capsule

Intervention Type DRUG

Oral capsule

Interventions

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PXL770

Oral capsule

Intervention Type DRUG

Placebo Oral Capsule

Oral capsule

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Patients have given written informed consent
* Body mass index (BMI) ≥ 25 to ≤ 50 kg/m²
* For patients with type 2 diabetes mellitus: either naive of glucose lowering drug or under stable oral glucose lowering drug
* Estimated glomerular filtration rate (eGFR) ≥ 60 mL/\[min\*1.73m²\]
* Alanine amino transferase (ALT) \> 20 IU/L in females and \> 30 IU/L in males
* Hepatic steatosis (MRI-PDFF ≥ 10%)
* Effective contraception for women of child bearing potential

Exclusion Criteria

* Evidence of another form of liver disease
* Evidence of liver cirrhosis
* Evidence of hepatic impairment
* Positive serologic evidence of current infectious liver disease
* History of excessive alcohol intake
* Acute cardiovascular disease with 24 weeks prior to screening
* Uncontrolled high blood pressure
* Any disease which in the Investigator's opinion which in the Investigator's opinion would exclude the patient from the study
* Use of non-permitted concomitant medication
* Pregnancy or lactation
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Poxel SA

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Study Site 02

Los Angeles, California, United States

Site Status

Study Site 01

Gainesville, Florida, United States

Site Status

Study Site 11

Ocoee, Florida, United States

Site Status

Study Site 15

Orlando, Florida, United States

Site Status

Study Site 10

Athens, Georgia, United States

Site Status

Study Site 03

Indianapolis, Indiana, United States

Site Status

Study Site 07

Marrero, Louisiana, United States

Site Status

Study Site 05

West Monroe, Louisiana, United States

Site Status

Study Site 08

Berlin, New Jersey, United States

Site Status

Study Site 09

Durham, North Carolina, United States

Site Status

Study Site 13

Rapid City, South Dakota, United States

Site Status

Study Site 06

Arlington, Texas, United States

Site Status

Study Site 04

San Antonio, Texas, United States

Site Status

Study Site 12

San Antonio, Texas, United States

Site Status

Study Site 14

Richmond, Virginia, United States

Site Status

Countries

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United States

References

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Cusi K, Alkhouri N, Harrison SA, Fouqueray P, Moller DE, Hallakou-Bozec S, Bolze S, Grouin JM, Jeannin Megnien S, Dubourg J, Ratziu V. Efficacy and safety of PXL770, a direct AMP kinase activator, for the treatment of non-alcoholic fatty liver disease (STAMP-NAFLD): a randomised, double-blind, placebo-controlled, phase 2a study. Lancet Gastroenterol Hepatol. 2021 Nov;6(11):889-902. doi: 10.1016/S2468-1253(21)00300-9. Epub 2021 Sep 22.

Reference Type DERIVED
PMID: 34560015 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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Other Identifiers

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PXL770-004

Identifier Type: -

Identifier Source: org_study_id