OPN-375 Efficacy and Safety in Adolescents With Bilateral Nasal Polyps

NCT ID: NCT03747458

Last Updated: 2025-12-11

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

72 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-12-31

Study Completion Date

2026-03-31

Brief Summary

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This is a 16-Week Randomized, Double-Blind, Placebo Controlled, Parallel-Group, Multicenter Study Evaluating the Efficacy and Safety of OPN-375 186 μg Twice a Day (BID) in Adolescents with Bilateral Nasal Polyps followed by a 12-Week Open-Label Treatment Phase. The total planned number of subjects is approximately 72 adolescents (12-17 years of age) who will be randomly assigned to receive 1 of 2 study treatments using a 2:1 ratio (OPN-375 186 μg: Placebo). For the PK sub-study, up to 14 subjects will be enrolled to obtain 10 completers.

Detailed Description

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The primary objective of this study is to evaluate the efficacy of intranasal administration of OPN-375 186 μg Twice a Day (BID) versus placebo in adolescents with bilateral nasal polyposis and nasal congestion by analyzing the reduction of nasal congestion/obstruction symptoms at the end of Week 4 measured by the 7-day average instantaneous morning diary symptom scores and the reduction in total polyp grade at Week 16 as determined by a nasal polyp grading scale score measured using a 0 to 6 point severity grading scale.

Conditions

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Bilateral Nasal Polyposis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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OPN-375 186 μg BID

Double-Blind Treatment Phase: OPN-375 186 μg BID x 16 weeks

Open-Label Extension Phase: OPN-375 186 μg BID x 12 weeks

Group Type ACTIVE_COMPARATOR

OPN-375

Intervention Type DRUG

OPN-375, BID

Placebo

Double-Blind Treatment Phase: Matching Placebo BID x 16 weeks

Group Type PLACEBO_COMPARATOR

OPN-375

Intervention Type DRUG

OPN-375, BID

Interventions

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OPN-375

OPN-375, BID

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Male or female subjects aged 12 to 17 years, inclusive, at time of Visit 1 (Screening).
2. Female subjects, if sexually active, must,

1. be practicing an effective method of birth control (e.g., prescription oral contraceptives, contraceptive injections, contraceptive patch, intrauterine device, double-barrier method \[e.g., condoms, diaphragm, or cervical cap with spermicidal foam, cream, or gel\], or male partner sterilization) before entry and throughout the study, or
2. be surgically sterile (have had a hysterectomy or bilateral oophorectomy, tubal ligation, or otherwise be incapable of pregnancy), or
3. be abstinent.
3. All female subjects not documented to be infertile (e.g., infertility due to congenital abnormality or surgical sterilization) must have a negative serum or urine beta-human chorionic gonadotropin (hCG) at Visit 1 (Screening) and a negative urine pregnancy test at the Visit 2 (Day 1/Randomization/Baseline).
4. Must have bilateral nasal polyposis with a grade of 1 to 3 in each of the nasal cavities as determined by a nasal polyp grading scale score measured by nasoendoscopy at Visit 1 (Screening).
5. Must report at least mild symptoms of nasal congestion/obstruction as demonstrated by an average morning nasal congestion/obstruction score of at least 1.0 over a 7 day period during the single-blind run-in period. (Subjects not meeting this inclusion criterion may be re-screened once after at least 4 weeks.)
6. Subjects with comorbid asthma must be stable, defined as no exacerbations (e.g., no emergency room visits, hospitalization, or oral or parenteral steroid use) within the 3 months before Visit 1 (Screening). Subjects who received inhaled corticosteroids are required to be on no more than a moderate dosage regimen as defined by 2015 Global Initiative for Asthma Guidelines (GINA) for 1 month before Visit 1 (Screening) and to be expected to remain on it throughout the study (GINA 2015). Subjects receiving inhaled fluticasone alone or in combination may not participate in the PK sub-study.
7. Must be able to cease treatment with intranasal medications including, but not limited to, intranasal oxymetazoline or any other decongestants, intranasal antihistamines, intranasal steroids, intranasal sodium cromolyn, nasal atropine, nasal ipratropium bromide, inhaled corticosteroids (except permitted doses listed above for asthma) at Visit 1 (Screening). \[Note: intranasal antibiotics and saline are permissible\]
8. If taking oral antihistamines, must be on a stable regimen for at least 2 weeks prior to Visit 1 (Screening), and agree to not change the dose of these medications until after Visit 3 (Week 4) of the study.
9. Subjects (with assistance from parent or legal guardian if needed) must demonstrate the ability to complete the daily diary during the run-in period to be eligible for randomization.
10. Must demonstrate correct use of the demo EDS.
11. Must be capable, in the opinion of the investigator, of providing assent and the appropriate parent(s) or guardian must provide an informed consent to participate in the study.

20. Have received mepolizumab (Nucala®), reslizumab (Cinquair®), dupilumab (Dupixent®), omalizumab (Xolair®), or benralizumab (Fasenra™) within 6 months of Visit 1
21. Have nasal or oral candidiasis
22. Have taken a potent CYP3A4-inhibitor within 14 days before Visit 1 (Screening)
23. Any serious or unstable concurrent disease, psychiatric disorder, or any significant concomitant medical condition that, in the opinion of the investigator could confound the results of the study or could interfere with the subject's participation or compliance in the study, or pose a specific risk to the subject due to study participation
24. History or current diagnosis of any form of glaucoma or ocular hypertension (i.e., \>21 mm Hg)
25. History of intraocular pressure elevation on any form of steroid therapy
26. Current diagnosis of the presence (in either eye) of a cataract of Grade 1 or greater as defined on the Eye Examination Worksheet OR, less than a Grade 1 cataract with associated visual impairment
27. A recent (within 1 year of Visit 1 \[Screening\]) history of drug or alcohol abuse or dependence
28. Positive urine drug screen at screening visit for stimulants, opioids, or cocaine
29. Have participated in an investigational drug clinical trial within 30 days of Visit 1 (Screening)
30. Parents, guardian or caregivers of the subject who are employees of the investigator or study center, with direct involvement in the proposed study or other studies under the direction of that investigator or study center, as well as family members of the employees or the investigator.

Exclusion Criteria

1. Pregnancy or lactation
2. Has a history of cystic fibrosis
3. Have used XHANCE (fluticasone propionate) nasal spray within the past 2 months
4. Inability to achieve bilateral nasal airflow for any reason, including nasal septum deviation
5. Inability to examine both nasal cavities for any reason, including severe nasal septum deviation
6. Have known history of nasal septum erosion, ulceration or perforation, or evidence of such lesion on Visit 1 (Screening) nasal examination/nasoendoscopy
7. Other significant nasal pathology or abnormal anatomy
8. Has had any episode of epistaxis with frank bleeding in the 3 months before Visit 1 (Screening)
9. History of more than 5 sinus or nasal surgeries for either nasal polyps or nasal/sinus inflammation (lifetime)
10. Have had any surgery on the nasal septum
11. History of sinus or nasal surgery within 6 months before Visit 1 (Screening)
12. History of any surgical procedure that prevents the ability to accurately diagnose or grade polyps
13. Current, ongoing rhinitis medicamentosa (rebound rhinitis)
14. Have significant oral structural abnormalities (e.g., a cleft palate)
15. History of Churg-Strauss syndrome or dyskinetic ciliary syndromes
16. Purulent nasal infection (recent fever or symptoms of lethargy), acute sinusitis, or upper respiratory tract infection within 2 weeks before Visit 1 (Screening). Potential subjects presenting with one of these infections may be rescreened after 4 weeks.
17. Have an allergy, hypersensitivity, or contraindication to corticosteroids or steroids
18. Have a hypersensitivity to any excipients in the study drug
Minimum Eligible Age

12 Years

Maximum Eligible Age

17 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Optinose US Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Amy Manley

Role: STUDY_CHAIR

Paratek Pharma

Locations

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Clinical Research Center of Alabama

Birmingham, Alabama, United States

Site Status WITHDRAWN

San Tan Allergy & Asthma

Gilbert, Arizona, United States

Site Status COMPLETED

Kern Research

Bakersfield, California, United States

Site Status COMPLETED

Central California Clinical Research

Fresno, California, United States

Site Status COMPLETED

Sensa Health

Los Angeles, California, United States

Site Status RECRUITING

Children's Hospital of Los Angeles

Los Angeles, California, United States

Site Status RECRUITING

Children's Hospital of Orange County

Orange, California, United States

Site Status RECRUITING

Allergy and Asthma Consultants

Redwood City, California, United States

Site Status RECRUITING

Sacramento ENT

Roseville, California, United States

Site Status RECRUITING

Rady Children's Hospital San Diego

San Diego, California, United States

Site Status RECRUITING

Children's Hospital Colorado

Aurora, Colorado, United States

Site Status RECRUITING

Yale School of Medicine, Section of Otolaryngology

New Haven, Connecticut, United States

Site Status WITHDRAWN

Nemours Children's Specialty Care

Jacksonville, Florida, United States

Site Status WITHDRAWN

Children's Healthcare of Atlanta

Atlanta, Georgia, United States

Site Status COMPLETED

Rush University Medical Center - Department of Otorhinolaryngology

Chicago, Illinois, United States

Site Status WITHDRAWN

Chicago ENT

Chicago, Illinois, United States

Site Status RECRUITING

Kentuckiana ENT

Louisville, Kentucky, United States

Site Status RECRUITING

Ochsner Medical Center, Otorhinolaryngology Department

New Orleans, Louisiana, United States

Site Status WITHDRAWN

Children's Minnesota

Minneapolis, Minnesota, United States

Site Status WITHDRAWN

University of Missouri Medical Center

Columbia, Missouri, United States

Site Status WITHDRAWN

University of Rochester

Rochester, New York, United States

Site Status RECRUITING

Allergy Asthma & Immunology Research Institute

Charlotte, North Carolina, United States

Site Status RECRUITING

Allergy, Asthma & Clinical Research Center

Oklahoma City, Oklahoma, United States

Site Status RECRUITING

Vital Prospects Clinical Research Institute, P.C.

Tulsa, Oklahoma, United States

Site Status RECRUITING

MUSC Department of Otolaryngology, Head and Neck Surgery

Charleston, South Carolina, United States

Site Status WITHDRAWN

Carolina ENT

Orangeburg, South Carolina, United States

Site Status RECRUITING

STAAMP Research

San Antonio, Texas, United States

Site Status RECRUITING

University of Utah

Salt Lake City, Utah, United States

Site Status COMPLETED

Eastern Virginia Medical School - Otolaryngology

Norfolk, Virginia, United States

Site Status RECRUITING

Spokane ENT

Spokane Valley, Washington, United States

Site Status COMPLETED

West Virginia University

Morgantown, West Virginia, United States

Site Status WITHDRAWN

Instituto Medico Rio Cuarto

Río Cuarto, Córdoba Province, Argentina

Site Status RECRUITING

Instituto Medico de la Fundacion de Estudios Clinicos - Consultorios Integrados Rosario

Rosario, Santa Fe Province, Argentina

Site Status RECRUITING

Centro de Investigaciones Clinicas - Instituto de la Salud Rosario

Rosario, Santa Fe Province, Argentina

Site Status RECRUITING

Clinica Mayo, UMCB

San Miguel de Tucumán, Tucumán Province, Argentina

Site Status RECRUITING

Sanatorio Guemes

Buenos Aires, , Argentina

Site Status RECRUITING

Fundacion CIDEA

Buenos Aires, , Argentina

Site Status RECRUITING

InAER - Investigaciones en Alergia y Enfermedades Respiratorias

Buenos Aires, , Argentina

Site Status RECRUITING

Instituto de Asma Alergia y Enfermedades Respiratoria (IAAER)

Corrientes, , Argentina

Site Status RECRUITING

Centro Medico INSARES

Mendoza, , Argentina

Site Status RECRUITING

Countries

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United States Argentina

Central Contacts

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Alissa Sirbu

Role: CONTACT

484-751-4926

Amy Manley

Role: CONTACT

Facility Contacts

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Jee Yang

Role: primary

213-528-4669

Beth Osterbauer

Role: primary

323-361-3539

Eric Rodriguez

Role: primary

714-509-3344

Sherry Lipson

Role: primary

650-216-6111

Rose Khalatyan

Role: primary

916-786-3399 ext. 1101

Sasha Shenk

Role: primary

858-966-1700

Kristi Engle Folchert

Role: primary

702-777-5841

Joseph Ninos

Role: primary

773-289-1823

Wendi Miller

Role: primary

502-583-9425

Paul Allen

Role: primary

585-275-1186

Caroline Clemons

Role: primary

704-910-1402 ext. 350

Nasir Ali, MD

Role: primary

405-286-9431

Thana Seenivasan

Role: primary

918-392-4550

Simone Ansley

Role: primary

803-536-5511

Cinthia Aguirre Vargas

Role: primary

210-451-9911

Laura Stone

Role: primary

757-388-6238

Maria Soledad Sebben

Role: primary

+54 358 464 1599

Rosario Nemi Caldentey

Role: primary

+54 341 238 4171

Lucas Ardusso

Role: primary

+54 341 440 7011

Helena Gandur

Role: primary

+549 381 419 0200

Vanina Silvestri

Role: primary

+54 11 4959 8200

Martin Maspero

Role: primary

+54 11 4961 5466

Vanina Brondo

Role: primary

+54 11 4829 1822

Nereida Silva

Role: primary

+54 379 446 9413

Walter Rosales

Role: primary

+549 261 470 3227

Other Identifiers

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OPN-FLU-NP-3103

Identifier Type: -

Identifier Source: org_study_id

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