A Long-Term Safety Extension Study of Mavacamten in Adults Who Have Completed MAVERICK-HCM or EXPLORER-HCM

NCT ID: NCT03723655

Last Updated: 2025-06-17

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE2/PHASE3

Total Enrollment

282 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-09-27

Study Completion Date

2026-01-16

Brief Summary

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Approximately 30 sites that enrolled participants in the MAVERICK-HCM (MYK-461-006) study in the United States (US) will initiate this study.

Approximately 90 sites that enrolled participants in the EXPLORER-HCM (MYK-461-005) study in the US, Europe, and Israel will initiate this study.

Note: Approximately 30 centers overlap between MAVERICK and EXPLORER.

Detailed Description

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Conditions

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Hypertrophic Cardiomyopathy Obstructive Hypertrophic Cardiomyopathy Non-obstructive Hypertrophic Cardiomyopathy

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators
Site, Care Provider and Patients are blinded to study dose. Sponsor is now unblinded to study dose.

Study Groups

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Group 1

Active Treatment for participants with base target trough concentration

Group Type EXPERIMENTAL

mavacamten

Intervention Type DRUG

mavacamten capsules

Group 2

Active Treatment for participants with higher target trough concentration

Group Type EXPERIMENTAL

mavacamten

Intervention Type DRUG

mavacamten capsules

Group 3

Active Treatment for participants dose titrated to clinical response

Group Type EXPERIMENTAL

mavacamten

Intervention Type DRUG

mavacamten capsules

Interventions

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mavacamten

mavacamten capsules

Intervention Type DRUG

Other Intervention Names

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MYK-461

Eligibility Criteria

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Inclusion Criteria

* Has completed the Parent Study through to the EOS Visit within 90 days of consent. (Participants who are beyond the 90-day window from EOS Visit may be included in this study pending MyoKardia Medical Monitoring approval) Participants who prematurely discontinued from the Parent Study or the MAVA-LTE study may be considered for inclusion.
* Has a body weight greater than 45 kg at the Screening Visit
* Has adequate acoustic windows to enable accurate TTEs.
* Has documented LVEF ≥ 50% by echocardiography core laboratory read of screening TTE at rest.
* Has safety laboratory parameters (chemistry, hematology, coagulation, and urinalysis) within normal limits (according to the central laboratory reference range).
* Female participants must not be pregnant or lactating and, if sexually active, must use one of the following highly effective birth control methods from the Screening Visit through 90 days after the last dose of investigational medicinal product (IMP).

In addition to the above contraceptive requirements for female participants, male partners must also use a contraceptive (eg. barrier, condom, or vasectomy).

Exclusion Criteria

* Has any ECG abnormality considered by the investigator to pose a risk to participant safety (eg. second degree atrioventricular block type II).
* Has a history of syncope or a history of sustained ventricular tachyarrhythmia with exercise between Parent Study EOS Visit and Screening Visit.
* Has a history of resuscitated sudden cardiac arrest or known history of appropriate implantable cardioverter-defibrillator (ICD) discharge for life-threatening ventricular arrhythmia between Parent Study EOS Visit and Screening Visit. (Note: history of anti-tachycardia pacing (ATP) is allowed).• Currently treated with disopyramide or ranolazine (within 14 days prior to Screening) or treatment with disopyramide or ranolazine is planned during the study.
* Has any acute or serious comorbid condition (eg. major infection or hematologic, renal, metabolic, gastrointestinal, or endocrine dysfunction) that, in the judgment of the Investigator, could lead to premature termination of study participation or interfere with the measurement or interpretation of the efficacy and safety assessments in the study.
* History of clinically significant malignant disease that developed since enrollment in the Parent Study.
* Is unable to comply with the study requirements, including the number of required visits to the clinical site.
* Has participated in a clinical trial in which the participant received any investigational drug (or is currently using an investigational device) within 30 days prior to Screening, or at least 5 times the respective elimination half-life (whichever is longer), except for participation in MAVERICK-HCM or EXPLORER-HCM. Prior participation in a non-interventional observational study is allowed.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Bristol-Myers Squibb

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Bristol-Myers Squibb

Role: STUDY_DIRECTOR

Bristol-Myers Squibb

Locations

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Local Institution - 0045

Scottsdale, Arizona, United States

Site Status

Local Institution - 0058

Los Angeles, California, United States

Site Status

Local Institution - 0066

San Francisco, California, United States

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Local Institution - 0063

Stanford, California, United States

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Local Institution - 0043

New Haven, Connecticut, United States

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Local Institution - 0067

Jacksonville, Florida, United States

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Local Institution - 0050

Chicago, Illinois, United States

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Local Institution - 0070

Indianapolis, Indiana, United States

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Local Institution - 0049

Iowa City, Iowa, United States

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Local Institution - 0054

Boston, Massachusetts, United States

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Local Institution - 0051

Ann Arbor, Michigan, United States

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Local Institution - 0074

Grand Rapids, Michigan, United States

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Local Institution - 0048

St Louis, Missouri, United States

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Local Institution - 0060

New York, New York, United States

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Local Institution - 0056

New York, New York, United States

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Local Institution - 0071

Charlotte, North Carolina, United States

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Local Institution - 0047

Durham, North Carolina, United States

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Local Institution - 0052

Cincinnati, Ohio, United States

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Local Institution - 0044

Portland, Oregon, United States

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Local Institution - 0068

Bethlehem, Pennsylvania, United States

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Local Institution - 0046

Philadelphia, Pennsylvania, United States

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Local Institution - 0064

Pittsburgh, Pennsylvania, United States

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Local Institution - 0073

Memphis, Tennessee, United States

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Local Institution - 0061

Dallas, Texas, United States

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Local Institution - 0055

Houston, Texas, United States

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Local Institution - 0057

Houston, Texas, United States

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Local Institution - 0072

Murray, Utah, United States

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Local Institution - 0062

Salt Lake City, Utah, United States

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Local Institution - 0053

Charlottesville, Virginia, United States

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Local Institution - 0059

Richmond, Virginia, United States

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Local Institution - 0065

Seattle, Washington, United States

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Local Institution - 0002

Aalst, , Belgium

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Local Institution - 0001

Brussels, , Belgium

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Local Institution - 0003

Edegem, , Belgium

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Local Institution - 0010

Prague, , Czechia

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Local Institution - 0009

Prague, , Czechia

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Local Institution - 0011

Aarhus, , Denmark

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Local Institution - 0012

Frederiksberg, , Denmark

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Local Institution - 0013

Odense, , Denmark

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Local Institution - 0014

Nantes, , France

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Local Institution - 0017

Paris, , France

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Local Institution - 0016

Paris, , France

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Local Institution - 0015

Toulouse, , France

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Local Institution - 0020

Bad Nauheim, , Germany

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Local Institution - 0018

Dresden, , Germany

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Local Institution - 0019

Göttingen, , Germany

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Local Institution - 0021

Heidelberg, , Germany

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Local Institution - 0027

Jerusalem, , Israel

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Local Institution - 0024

Petah Tikva, , Israel

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Local Institution - 0022

Ramat Gan, , Israel

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Local Institution - 0025

Rehovot, , Israel

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Local Institution - 0023

Safed, , Israel

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Local Institution - 0026

Tel Aviv, , Israel

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Local Institution - 0028

Florence, , Italy

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Local Institution - 0029

Maastricht, , Netherlands

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Local Institution - 0030

Rotterdam, , Netherlands

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Local Institution - 0033

Katowice, , Poland

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Local Institution - 0034

Krakow, , Poland

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Local Institution - 0031

Poznan, , Poland

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Local Institution - 0032

Warsaw, , Poland

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Local Institution - 0036

Almada, , Portugal

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Local Institution - 0035

Lisbon, , Portugal

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Local Institution - 0038

A Coruña, , Spain

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Local Institution - 0037

El Palmar, , Spain

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Local Institution - 0040

Madrid, , Spain

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Local Institution - 0039

Majadahonda, , Spain

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Local Institution - 0041

Seville, , Spain

Site Status

Local Institution - 0042

London, , United Kingdom

Site Status

Countries

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United States Belgium Czechia Denmark France Germany Israel Italy Netherlands Poland Portugal Spain United Kingdom

References

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Rader F, Oreziak A, Choudhury L, Saberi S, Fermin D, Wheeler MT, Abraham TP, Garcia-Pavia P, Zwas DR, Masri A, Owens A, Hegde SM, Seidler T, Fox S, Balaratnam G, Sehnert AJ, Olivotto I. Mavacamten Treatment for Symptomatic Obstructive Hypertrophic Cardiomyopathy: Interim Results From the MAVA-LTE Study, EXPLORER-LTE Cohort. JACC Heart Fail. 2024 Jan;12(1):164-177. doi: 10.1016/j.jchf.2023.09.028.

Reference Type DERIVED
PMID: 38176782 (View on PubMed)

Related Links

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Other Identifiers

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CV027-003

Identifier Type: -

Identifier Source: org_study_id

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