LUMINA Phase III Study Assessing the Efficacy and Safety of Intravitreal Injections of 440 ug DE-109 Sirolimus for the Treatment of Active, Non-Infectious Uveitis of the Posterior Segment of the Eye

NCT ID: NCT03711929

Last Updated: 2023-12-04

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

145 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-11-19

Study Completion Date

2022-06-14

Brief Summary

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This is a Phase III study to assess the efficacy and safety of DE-109 440 µg every 2 months in subjects with active, non-infectious uveitis of the posterior segment of the eye (NIU-PS).

There is a 6-month, single-arm, open-label period after completion of the 6-month double- masked, controlled period allows the evaluation of the efficacy and safety of intravitreal injection of DE-109 440 µg every 2 months for longer duration than appropriate for a placebo or sham control.

Detailed Description

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Conditions

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Non Infectious Uveitis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Test Arm: DE-109 Injectable Solution

Intravitreal injection of DE-109 440 µg in the study eye(s) every 2 months (Day 1, Month 2, and Month 4).

Group Type EXPERIMENTAL

DE-109 Intravitreal Injections

Intervention Type DRUG

440 ug of DE-109 Injectable Solution

Control Arm: Sham Procedure

Sham procedure administered to the study eye(s) every 2 months (Day 1, Month 2, and Month 4). The sham procedure mimics an intravitreal injection without penetrating the eye.

Group Type SHAM_COMPARATOR

Sham Procedure

Intervention Type OTHER

The sham procedure mimics an intravitreal injection without penetrating the eye.

Dummy Arm: DE-109 Injectable Solution

Dummy Arm: Intravitreal injection of DE-109 at an undisclosed, fixed dose (within the range of 44 µg to 880 µg) in the study eye(s) every 2 months (Day 1, Month 2, and Month 4).

Group Type OTHER

DE-109 Intravitreal Injections

Intervention Type DRUG

Undisclosed Fixed Dose of DE-109 Injectable Solution (range of 44 ug to 880 ug)

Open-label:DE-109 Injectable Solution

Subjects completing the Month 6 pre-dose evaluations (the final evaluations in the double-masked period) began the open-label period of the study, in which all subjects received intravitreal injection of DE-109 440 μg in the study eye(s) every 2 months for an additional 6 months of dosing.

Group Type EXPERIMENTAL

DE-109 Intravitreal Injections (Open Label)

Intervention Type DRUG

After double-masked treatment period (injections every 2 months), eligible subjects would enter the open-labeled period and had DE-109 440 ug injections every 2 months (Month 6, Month 8, and Month 10)

Interventions

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DE-109 Intravitreal Injections

440 ug of DE-109 Injectable Solution

Intervention Type DRUG

Sham Procedure

The sham procedure mimics an intravitreal injection without penetrating the eye.

Intervention Type OTHER

DE-109 Intravitreal Injections

Undisclosed Fixed Dose of DE-109 Injectable Solution (range of 44 ug to 880 ug)

Intervention Type DRUG

DE-109 Intravitreal Injections (Open Label)

After double-masked treatment period (injections every 2 months), eligible subjects would enter the open-labeled period and had DE-109 440 ug injections every 2 months (Month 6, Month 8, and Month 10)

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

Non-Infectious Active Uveitis of the Posterior Segment

Exclusion Criteria

Females who are pregnant, nursing, or planning a pregnancy Confirmed or suspected infectious uveitis
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Santen Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Arizona Retina & Vitreous Consultants

Phoenix, Arizona, United States

Site Status

Retina-Vitreous Associates Medical Group

Beverly Hills, California, United States

Site Status

Kaiser Permanente Medical Center

Los Angeles, California, United States

Site Status

USC Roski Eye Institute

Los Angeles, California, United States

Site Status

Byers Eye Institute at Stanford

Palo Alto, California, United States

Site Status

California Eye Specialist Medical Group, Inc.

Pasadena, California, United States

Site Status

Colorado Retina Associates

Golden, Colorado, United States

Site Status

Retina Vitreous Associates of Florida

St. Petersburg, Florida, United States

Site Status

University of South Florida Eye Institute

Tampa, Florida, United States

Site Status

Emory Eye Center

Atlanta, Georgia, United States

Site Status

Marietta Eye Clinic

Marietta, Georgia, United States

Site Status

Cook County Health & Hospitals System

Chicago, Illinois, United States

Site Status

Illinois Retina Associate

Oak Park, Illinois, United States

Site Status

Raj K.Maturi, MD

Indianapolis, Indiana, United States

Site Status

University of Kansas School of Medicine

Prairie Village, Kansas, United States

Site Status

Cumberland Valley Retina Consultants

Hagerstown, Maryland, United States

Site Status

Ophthalmic Consultants of Boston

Boston, Massachusetts, United States

Site Status

Kresge Eye Institute

Detroit, Michigan, United States

Site Status

Associated Retina Consultants-Royal Oak

Royal Oak, Michigan, United States

Site Status

Discover Vision Center

Independence, Missouri, United States

Site Status

Eye Associates of New Mexico

Albuquerque, New Mexico, United States

Site Status

New York Eye & Ear Infirmary of Mt. Sinai

New York, New York, United States

Site Status

Wake Forest Baptist Medical Center/Surgery

Winston-Salem, North Carolina, United States

Site Status

Cleveland Clinic Cole Eye Institute

Cleveland, Ohio, United States

Site Status

Cascade Medical Research Institute, LLC

Eugene, Oregon, United States

Site Status

Retina Vitreous Consultants

Monroeville, Pennsylvania, United States

Site Status

Mid Atlantic Retina

Philadelphia, Pennsylvania, United States

Site Status

UPMC Eye Center

Pittsburgh, Pennsylvania, United States

Site Status

Vanderbilt Eye Institute

Nashville, Tennessee, United States

Site Status

Austin Retina Associate

Austin, Texas, United States

Site Status

Texas Retina Associates-Dallas-Main

Dallas, Texas, United States

Site Status

Houston Eye Associates

Houston, Texas, United States

Site Status

Retina Consultants of Houston

Houston, Texas, United States

Site Status

Valley Retina Institute

McAllen, Texas, United States

Site Status

Foresight Studies, San Antonio

San Antonio, Texas, United States

Site Status

Medical Center Ophthalmology Associate

San Antonio, Texas, United States

Site Status

Retina Group of Washington

Fairfax, Virginia, United States

Site Status

West Virginia University Eye Institute

Morgantown, West Virginia, United States

Site Status

Centro De Ojos Loria SRL

Lomas de Zamora, Buenos Aires, Argentina

Site Status

Clinica Privada de Ojos

Mar del Plata, Buenos Aires, Argentina

Site Status

Primer Hospital Privado De Ojos

Buenos Aires, Buenos Aires F.D., Argentina

Site Status

Hospital Universitario Austral

Buenos Aires, Buenos Aires F.D., Argentina

Site Status

Gustavo Ariel Budmann Private Office

Buenos Aires, Odisha, Argentina

Site Status

Oftalmologia Global

Rosario, Santa Fe Province, Argentina

Site Status

Organización Médica de Investigación (OMI)

Caba, , Argentina

Site Status

Centro Privado de Ojos Romagosa Fundacion VER

Córdoba, , Argentina

Site Status

Sri Sankaradeva Nethralaya

Guwahati, Assam, India

Site Status

Banker's Retina Clinic & Laser Centre

Ahmedabad, Gujarat, India

Site Status

Narayana Nethralaya

Bangalore, Karnataka, India

Site Status

Disha Eye Hospitals Pvt Ltd

Pune, Maharashtra, India

Site Status

PBMA'S H. V. Desai Eye Hospital

Pune, Maharashtra, India

Site Status

LV Prasad Eye Institute

Bhubaneswar, Odisha, India

Site Status

SMS Hospital

Jaipur, Rajasthan, India

Site Status

Sankara Nethralaya

Chennai, Tamil Nadu, India

Site Status

Aravind Eye Hospital (Coimbatore)

Coimbatore, Tamil Nadu, India

Site Status

Aravind Eye Hospitals

Madurai, Tamil Nadu, India

Site Status

L V Prasad Eye Institute

Hyderabad, Telangana, India

Site Status

Dr. J.L. Rohatgi Memorial Eye Hospital

Kanpur, Uttar Pradesh, India

Site Status

BB Eye Foundation

Kolkata, West Bengal, India

Site Status

Advanced Eye Center

Chandigarh, , India

Site Status

Polo Universita degli Studi di Milano Ospedale Luigi Sacco Clinca Oculistica (Eye Clinic)

Milan, Lombardy, Italy

Site Status

Universita degli Studi di Padova - Azienda Ospedaliera di Padova - Clinica Oculistica

Padua, Veneto, Italy

Site Status

A.O.U. Policlinico SantOrsola-Malpigi

Bologna, , Italy

Site Status

San Raffaele Scientific Institute

Milan, , Italy

Site Status

Azienda USL IRCCS Reggio Emilia

Reggio Emilia, , Italy

Site Status

Countries

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United States Argentina India Italy

References

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Hashida N, Nishida K. Recent advances and future prospects: Current status and challenges of the intraocular injection of drugs for vitreoretinal diseases. Adv Drug Deliv Rev. 2023 Jul;198:114870. doi: 10.1016/j.addr.2023.114870. Epub 2023 May 10.

Reference Type DERIVED
PMID: 37172783 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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010906IN

Identifier Type: -

Identifier Source: org_study_id