Efficacy and Safety Study of Apremilast (CC-10004) in Pediatric Subjects From 6 Through 17 Years of Age With Moderate to Severe Plaque Psoriasis

NCT ID: NCT03701763

Last Updated: 2024-12-16

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

245 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-12-19

Study Completion Date

2023-03-27

Brief Summary

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This is a Phase 3, multicenter, randomized, placebo-controlled, double-blind study of the efficacy and safety of apremilast (CC-10004) in pediatric subjects with moderate to severe plaque psoriasis.

At least 230 pediatric subjects (ages 6 through 17 years) will be randomized 2:1 to receive either apremilast or placebo for the first 16 weeks and then all subjects will receive apremilast during the 36 week Extension Phase for a total of 52 weeks. Randomization to apremilast arm or placebo arm will be stratified by age group (6 to 11 years or 12 to 17 years). Subjects will receive apremilast treatment of either 20 mg twice daily (BID) or 30 mg BID, depending on weight. This Phase 3 study is being conducted to evaluate the safety and efficacy of apremilast in the treatment of pediatric subjects.

Detailed Description

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Treatment will be assigned by weight with subjects 20 kg to \< 50 kg receiving apremilast 20 mg BID or placebo BID and subjects ≥ 50 kg receiving apremilast 30 mg BID or placebo BID. Total study duration is up to 71 weeks. Subjects completing all 52 weeks of the treatment and extension phase will be able to enter the Long-term study. Subjects not entering the Long-term study will return for 3 observational follow-up visits, 4, 8 and 14 weeks after last dose of study drug.

Conditions

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Psoriasis

Keywords

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Pediatric 6 through 17 years Plaque Psoriasis Psoriasis CC-10004 Apremilast Otezla Children Adolescents SPROUT

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Administration of Apremilast (CC-10004) - 20mg

Apremilast 20mg Twice Daily (BID)

Group Type EXPERIMENTAL

Apremilast (CC-10004)

Intervention Type DRUG

Apremilast (CC-10004)

Administration of Apremilast (CC-10004) - 30mg

Apremilast 30mg Twice Daily (BID)

Group Type EXPERIMENTAL

Apremilast (CC-10004)

Intervention Type DRUG

Apremilast (CC-10004)

Administration of Placebo

Placebo tablet Twice Daily (BID)

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

Placebo

Interventions

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Apremilast (CC-10004)

Apremilast (CC-10004)

Intervention Type DRUG

Placebo

Placebo

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

1. Males or female subjects 6 to 17 years of age, inclusive, at the time the informed consent form is signed by the legal guardian
2. Subjects must have a weight of ≥ 20 kg
3. Diagnosis of chronic plaque psoriasis for at least 6 months prior to Screening.
4. Has moderate to severe plaque psoriasis at Screening and Baseline as defined by:

* PASI score ≥ 12; and
* Body surface area (BSA) ≥ 10%; and
* sPGA ≥ 3 (moderate to severe)
5. Disease inadequately controlled by or inappropriate for topical therapy for psoriasis
6. Candidate for systemic therapy or phototherapy

Exclusion Criteria

1. Guttate, erythrodermic, or pustular psoriasis at Screening and Baseline
2. Psoriasis flare or rebound within 4 weeks prior to Screening
3. Prior history of suicide attempt at any time in the subject's lifetime prior to Screening or randomization in the study, or major psychiatric illness requiring hospitalization within 3 years prior to signing the assent and informed consent
4. Answer "Yes" to any question on the Columbia-Suicide Severity Rating Scale during Screening or at Baseline
5. Current or planned concurrent use of the following therapies that may have a possible effect on psoriasis

a. Topical therapy within 2 weeks prior to randomization (including but not limited to topical corticosteroids, topical retinoid or vitamin D analog preparations, tacrolimus, pimecrolimus, or anthralin/dithranol)

Exceptions\*:

i. Low potency or weak corticosteroids (please refer to the Investigators' Manual) will be allowed as background therapy for treatment of the face, axillae and groin in accordance with manufacturer's suggested usage ii. Unmedicated skin moisturizer (eg, Eucerin®) will also be permitted for body lesions

\*Subjects should not use these topical treatments within 24 hours prior to the clinic visit.

b. Conventional systemic therapy for psoriasis within 4 weeks prior to randomization c. Phototherapy treatment (ie, ultraviolet B \[UVB\], PUVA) within 4 weeks prior to randomization d. Biologic therapy within 4 weeks prior to randomization or 5 PK/PD half-lives (whichever is longer).
Minimum Eligible Age

6 Years

Maximum Eligible Age

17 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Amgen

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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MD

Role: STUDY_DIRECTOR

Amgen

Locations

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University of Alabama Birmingham

Birmingham, Alabama, United States

Site Status

Phoenix Childrens Hospital

Phoenix, Arizona, United States

Site Status

Johnson Dermatology Clinic

Fort Smith, Arkansas, United States

Site Status

Zenith Research Inc.

Beverly Hills, California, United States

Site Status

First OC Dermatology

Fountain Valley, California, United States

Site Status

Avance Clinical Trials

Laguna Niguel, California, United States

Site Status

Stanford University

Palo Alto, California, United States

Site Status

Coastal Family Dermatology

San Luis Obispo, California, United States

Site Status

University of California Los Angeles

Santa Monica, California, United States

Site Status

California Dermatology Institute

Thousand Oaks, California, United States

Site Status

Solutions Through Advanced Research Inc

Jacksonville, Florida, United States

Site Status

Glick Skin Institute Clinical Research

Margate, Florida, United States

Site Status

University of Miami Hospital

Miami, Florida, United States

Site Status

Ciocca Dermatology

Miami, Florida, United States

Site Status

University of South Florida Health Morsani Center for Advanced Healthcare

Tampa, Florida, United States

Site Status

Skin Care Physicians of Georgia

Macon, Georgia, United States

Site Status

Treasure Valley Medical Research

Meridian, Idaho, United States

Site Status

DeNova Research

Chicago, Illinois, United States

Site Status

Dawes Fretzin Dermatology Group Inc

Indianapolis, Indiana, United States

Site Status

Epiphany Dermatology of Kansas, LLC

Overland Park, Kansas, United States

Site Status

ActivMed Practices and Research Inc

Beverly, Massachusetts, United States

Site Status

Mayo Clinic

Rochester, Minnesota, United States

Site Status

J Woodson Dermatology and Associates Ltd

Henderson, Nevada, United States

Site Status

Dartmouth-Hitchcock Medical Center

Lebanon, New Hampshire, United States

Site Status

Forest Hills Dermatology Group

Forest Hills, New York, United States

Site Status

SUNY Downstate Medical Center

Manhasset, New York, United States

Site Status

Montefiore Medical Center

The Bronx, New York, United States

Site Status

Cincinnati Childrens Hospital Medical Center

Cincinnati, Ohio, United States

Site Status

Wright State Physicians

Fairborn, Ohio, United States

Site Status

Essential Medical Research, LLC

Tulsa, Oklahoma, United States

Site Status

Medical University of South Carolina

Charleston, South Carolina, United States

Site Status

Arlington Research Center

Arlington, Texas, United States

Site Status

Driscoll Childrens Hospital

Corpus Christi, Texas, United States

Site Status

Modern Research Associates PLLC

Dallas, Texas, United States

Site Status

Mosaic Dermatology

Houston, Texas, United States

Site Status

Texas Dermatology and Laser Specialists

San Antonio, Texas, United States

Site Status

Jordan Valley Dermatology Center

West Jordan, Utah, United States

Site Status

University of Wisconsin Hospital and Clinics

Madison, Wisconsin, United States

Site Status

Childrens Hospital of Wisconsin

Milwaukee, Wisconsin, United States

Site Status

Centre Hospitalier Universitaire Saint Pierre

Brussels, , Belgium

Site Status

Cliniques Universitaires St Luc

Brussels, , Belgium

Site Status

Universitair Ziekenhuis Gent

Ghent, , Belgium

Site Status

Kirk Barber Research

Calgary, Alberta, Canada

Site Status

Stollery Children's Hospital

Edmonton, Alberta, Canada

Site Status

Enverus Medical Research

Surrey, British Columbia, Canada

Site Status

Winnipeg Clinic Dermatology Research

Winnipeg, Manitoba, Canada

Site Status

Karma Clinical Trials

St. John's, Newfoundland and Labrador, Canada

Site Status

AvantDerm

Toronto, Ontario, Canada

Site Status

CHU Saint-Justine

Montreal, Quebec, Canada

Site Status

Fakultni nemocnice Hradec Kralove

Hradec Králové, , Czechia

Site Status

Fakultni nemocnice Kralovske Vinohrady

Prague, , Czechia

Site Status

Synexus Czech sro

Prague, , Czechia

Site Status

Centre Hospitalier Victor Dupouy Argenteuil

Argenteuil, , France

Site Status

Centre Hospitalier Universitaire Lyon

Bron, , France

Site Status

Cabinet du Docteur Ruer-Mulard Mireille

Martigues, , France

Site Status

Hotel Dieu CHU Nantes

Nantes, , France

Site Status

Centre Hospitalier Universitaire de Nice

Nice, , France

Site Status

Hopital Necker

Paris, , France

Site Status

Centre Hospitalier de Cornouaille - Hopital Laennec

Quimper, , France

Site Status

CHU Saint Etienne Hopital Nord

Saint-Priest En Jarrez, , France

Site Status

Centre Hospitalier Universitaire de Toulouse - Hopital Larrey

Toulouse, , France

Site Status

Centre Hospitalier de Valence

Valence, , France

Site Status

Chaim Sheba Medical Center

Ramat Gan, , Israel

Site Status

Azienda Ospedaliero Universitaria Di Bologna Policlinico S Orsola Malpighi

Bologna, , Italy

Site Status

Azienda Ospedaliera Universitaria di Cagliari

Cagliari, , Italy

Site Status

Fondazione IRCCS Ca Granda Ospedale Maggiore Policlinico

Milan, , Italy

Site Status

Azienda Ospedaliera Universitaria Federico II

Napoli, , Italy

Site Status

Azienda Ospedaliera di Padova

Padua, , Italy

Site Status

Azienda Ospedaliera di Reggio Emilia Arcispedale Santa Maria Nuova

Reggio Emilia, , Italy

Site Status

Policlinico Tor Vergata

Roma, , Italy

Site Status

Istituto Dermatologico San Gallicano IRCCS Dermatologia Clinica

Roma, , Italy

Site Status

Radboud university medical center

Nijmegen, , Netherlands

Site Status

Altai State Medical University

Barnaul, , Russia

Site Status

Chelyabinsk Regional Clinical Skin and Venereal Dispensary

Chelyabinsk, , Russia

Site Status

Republican Clinical Dermatology and Venerology Dispensary

Kazan', , Russia

Site Status

Clinical Dispensary of Dermatology and Venereology of Krasnodar Territory of the Ministry of Health

Krasnodar, , Russia

Site Status

State Scientific Center for Dermatovenereology and Cosmetology

Moscow, , Russia

Site Status

Russian Children's Clinical Hospital

Moscow, , Russia

Site Status

Moscow Scientific Practical Center of Dermatology Venerology and Cosmetology

Moscow, , Russia

Site Status

National Medical Research Center for Children's Health

Moscow, , Russia

Site Status

LLC Medical Center Zdorovaya Semiya

Novosibirsk, , Russia

Site Status

Pierre Wolkenshtein Skin Diseases Clinic LLC

Saint Petersburg, , Russia

Site Status

LLC PiterKlinika

Saint Petersburg, , Russia

Site Status

Saint Petersburg State Pediatric Medical University

Saint Petesburg, , Russia

Site Status

Bashkiria State Medical University

Ufa, , Russia

Site Status

Yarosavl State Medical Academy

Yaroslavl, , Russia

Site Status

Ural Scientific Research Institute of Dermatovenereology and Immunopathology

Yekaterinburg, , Russia

Site Status

Hospital Marques de Valdecilla

Santander, Cantabria, Spain

Site Status

Hospital General Universitario de Alicante

Alicante, Valencia, Spain

Site Status

Hospital Universitari Germans Trias i Pujol Can Ruti

Badalona, , Spain

Site Status

Hospital Sant Joan de Deu

Barcelona, , Spain

Site Status

Hospital Puerta del Mar

Cadiz, , Spain

Site Status

Hospital Universitario Reina Sofia

Córdoba, , Spain

Site Status

Hospital General Universitario Gregorio Maranon

Madrid, , Spain

Site Status

Hospital Infantil Universitario Nino Jesus

Madrid, , Spain

Site Status

Hospital 12 de Octubre

Madrid, , Spain

Site Status

Hospital La Paz

Madrid, , Spain

Site Status

Complexo Hospitalario De Pontevedra

Pontevedra, , Spain

Site Status

Hospital Universitario Virgen del Rocio - PPDS

Seville, , Spain

Site Status

Countries

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Germany Hungary Mexico United States Belgium Canada Czechia France Israel Italy Netherlands Russia Spain

References

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Fiorillo L, Becker E, de Lucas R, Belloni-Fortina A, Armesto S, Elewski B, Maes P, Oberoi RK, Paris M, Zhang W, Zhang Z, Arkin L. Efficacy and safety of apremilast in pediatric patients with moderate-to-severe plaque psoriasis: 16-week results from SPROUT, a randomized controlled trial. J Am Acad Dermatol. 2024 Jun;90(6):1232-1239. doi: 10.1016/j.jaad.2023.11.068. Epub 2024 Jan 23.

Reference Type BACKGROUND
PMID: 38266683 (View on PubMed)

Paller AS, Fiorillo L, Becker E, Armesto S, Kontzias A, Oberoi RK, Zhang W, Amouzadeh H, Zhang Z, Arkin L. Efficacy and safety of apremilast in pediatric patients with moderate to severe plaque psoriasis: 52-week results from the SPROUT randomized controlled trial. Br J Dermatol. 2025 Jul 30:ljaf305. doi: 10.1093/bjd/ljaf305. Online ahead of print.

Reference Type DERIVED
PMID: 40737559 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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http://www.amgentrials.com

AmgenTrials clinical trials website

Other Identifiers

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U1111-1219-3112

Identifier Type: REGISTRY

Identifier Source: secondary_id

2018-002918-12

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CC-10004-PPSO-003

Identifier Type: -

Identifier Source: org_study_id