A Study of Nivolumab Combined With Ipilimumab and Nivolumab Alone in Patients With Advanced or Metastatic Solid Tumors of High Tumor Mutational Burden (TMB-H)

NCT ID: NCT03668119

Last Updated: 2024-08-28

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

212 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-10-31

Study Completion Date

2023-08-02

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

The purpose of this study is to demonstrate the clinical activity of nivolumab in combination with ipilimumab in multiple types of tumors based on their Tumor Mutational Burden status.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Pan Tumor

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Nivolumab + Ipilimumab Combination

Group Type EXPERIMENTAL

Nivolumab

Intervention Type BIOLOGICAL

Specified dose on specified days

Ipilimumab

Intervention Type BIOLOGICAL

Specified dose on specified days

Nivolumab Monotherapy

Group Type EXPERIMENTAL

Nivolumab

Intervention Type BIOLOGICAL

Specified dose on specified days

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Nivolumab

Specified dose on specified days

Intervention Type BIOLOGICAL

Ipilimumab

Specified dose on specified days

Intervention Type BIOLOGICAL

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

Opdivo BMS-936558 Yervoy BMS-734016

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Participants with a refractory, metastatic, or unresectable histologically or cytologically confirmed solid malignant tumor with high tumor mutational burden (TMB-H) who are refractory to standard local therapies, or for which no standard treatment is available.
* Must be able to provide tissue and blood TMB-H testing results
* Must have measurable disease for response assessment

Exclusion Criteria

* Participants with melanoma, non-small cell lung cancer (NSCLC), renal cell carcinoma (RCC) or hematological malignancy as primary site of disease
* Participants who received prior treatment with an anti-programmed death-1 (anti-PD-1), anti-programmed death ligand 1 (anti-PD-L1), anti-programmed death ligand 2 (anti-PD-L2), anti-CD137, or anti-cytotoxic T-lymphocyte-associated protein 4 (anti-CTLA-4) antibody, or any other antibody or drug specifically targeting T-cell co-stimulation or checkpoint pathways
* Treatment with any chemotherapy, radiation therapy, biologics for cancer, or investigational therapy within 28 days of first administration of study treatment
Minimum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Bristol-Myers Squibb

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Bristol-Myers Squibb

Role: STUDY_DIRECTOR

Bristol-Myers Squibb

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

John Wayne Cancer Center

Santa Monica, California, United States

Site Status

Rocky Mountain Cancer Centers

Denver, Colorado, United States

Site Status

Local Institution - 0093

Minneapolis, Minnesota, United States

Site Status

Broome Oncology

Johnson City, New York, United States

Site Status

Duke Cancer Institute

Durham, North Carolina, United States

Site Status

Local Institution - 0079

Portland, Oregon, United States

Site Status

Local Institution - 0095

Austin, Texas, United States

Site Status

Local Institution - 0094

Dallas, Texas, United States

Site Status

Local Institution - 0090

Houston, Texas, United States

Site Status

Texas Oncology - Northeast Texas

Tyler, Texas, United States

Site Status

Local Institution - 0016

Ciudad Autonoma Beunos Aires, Buenos Aires, Argentina

Site Status

Local Institution - 0087

Ciudad Autónoma de Buenos Aires, Buenos Aires, Argentina

Site Status

Local Institution - 0078

CABA, , Argentina

Site Status

Local Institution - 0015

CABA, , Argentina

Site Status

Local Institution - 0119

Córdoba, , Argentina

Site Status

Local Institution - 0118

St Leonards, New South Wales, Australia

Site Status

Local Institution - 0062

Sydney, New South Wales, Australia

Site Status

Local Institution - 0117

Woolloongabba, Queensland, Australia

Site Status

Local Institution - 0112

Brussels, , Belgium

Site Status

Local Institution - 0113

Brussels, , Belgium

Site Status

Local Institution - 0114

Leuven, , Belgium

Site Status

Local Institution - 0010

Edmonton, Alberta, Canada

Site Status

Local Institution - 0060

Hamilton, Ontario, Canada

Site Status

Local Institution - 0036

Montreal, Quebec, Canada

Site Status

Local Institution - 0088

Montreal, Quebec, Canada

Site Status

Local Institution - 0018

Santiago, Santiago Metropolitan, Chile

Site Status

Local Institution - 0082

Santiago, Santiago Metropolitan, Chile

Site Status

Local Institution - 0080

Copenhagen, , Denmark

Site Status

Local Institution - 0081

Herlev, , Denmark

Site Status

Local Institution - 0072

Lyon, , France

Site Status

Local Institution - 0075

Marseille, , France

Site Status

Local Institution - 0073

Paris, , France

Site Status

Local Institution - 0074

Toulouse, , France

Site Status

Local Institution - 0085

Villejuif, , France

Site Status

Local Institution - 0039

Berlin, , Germany

Site Status

Local Institution - 0001

Bonn, , Germany

Site Status

Local Institution - 0002

Dresden, , Germany

Site Status

Local Institution - 0086

Essen, , Germany

Site Status

Local Institution - 0043

Würzburg, , Germany

Site Status

Local Institution - 0032

Genova, , Italy

Site Status

IRCCS Istituto Nazionale Tumori Milano

Milan, , Italy

Site Status

Local Institution - 0029

Napoli, , Italy

Site Status

Local Institution - 0031

Siena, , Italy

Site Status

Local Institution - 0116

Rotterdam, South Holland, Netherlands

Site Status

Local Institution - 0115

Amsterdam, , Netherlands

Site Status

Local Institution - 0076

Warsaw, Masovian Voivodeship, Poland

Site Status

Local Institution - 0077

Gdansk, , Poland

Site Status

Fundacion De Investigacion

San Juan, , Puerto Rico

Site Status

Local Institution - 0068

Cluj-Napoca, Cluj, Romania

Site Status

Local Institution - 0069

Bucharest, , Romania

Site Status

Local Institution - 0067

Craiova, , Romania

Site Status

Local Institution - 0070

Floreşti, , Romania

Site Status

Local Institution - 0071

Timisoara, Timis, , Romania

Site Status

Local Institution - 0065

Singapore, Central Singapore, Singapore

Site Status

Local Institution - 0066

Singapore, , Singapore

Site Status

Local Institution - 0084

Barcelona, , Spain

Site Status

Local Institution - 0083

Madrid, , Spain

Site Status

Local Institution - 0110

Pamplona, , Spain

Site Status

Local Institution - 0106

London, Greater London, United Kingdom

Site Status

Local Institution - 0107

Preston, , United Kingdom

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Argentina Australia Belgium Canada Chile Denmark France Germany Italy Netherlands Poland Puerto Rico Romania Singapore Spain United Kingdom

References

Explore related publications, articles, or registry entries linked to this study.

Schenker M, Burotto M, Richardet M, Ciuleanu TE, Goncalves A, Steeghs N, Schoffski P, Ascierto PA, Maio M, Lugowska I, Lupinacci L, Leary A, Delord JP, Grasselli J, Tan DSP, Friedmann J, Vuky J, Tschaika M, Konduru S, Vemula SV, Slepetis R, Kollia G, Pacius M, Duong Q, Huang N, Doshi P, Baden J, Di Nicola M. Randomized, open-label, phase 2 study of nivolumab plus ipilimumab or nivolumab monotherapy in patients with advanced or metastatic solid tumors of high tumor mutational burden. J Immunother Cancer. 2024 Aug 6;12(8):e008872. doi: 10.1136/jitc-2024-008872.

Reference Type DERIVED
PMID: 39107131 (View on PubMed)

Provided Documents

Download supplemental materials such as informed consent forms, study protocols, or participant manuals.

Document Type: Study Protocol and Statistical Analysis Plan

View Document

Related Links

Access external resources that provide additional context or updates about the study.

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2016-002898-35

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CA209-848

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.

Pan Tumor Rollover Study
NCT03899155 RECRUITING PHASE2