Trial Outcomes & Findings for Safety and Effectiveness of Acthar Gel for Inflammation of the Eye's Uvea (Middle Layer) (NCT NCT03656692)

NCT ID: NCT03656692

Last Updated: 2021-08-03

Results Overview

The Nussenblatt grading scale uses photographic measurement of cloudy, declining vision (vitreous haze). The scale goes from 0 to 4, and lower scores are better.

Recruitment status

TERMINATED

Study phase

PHASE4

Target enrollment

5 participants

Primary outcome timeframe

Week 36

Results posted on

2021-08-03

Participant Flow

Approximately 30 participants were planned, but only 5 enrolled before the study was terminated

Participant milestones

Participant milestones
Measure
Acthar Gel
Participants receive Acthar Gel
Overall Study
STARTED
5
Overall Study
COMPLETED
2
Overall Study
NOT COMPLETED
3

Reasons for withdrawal

Reasons for withdrawal
Measure
Acthar Gel
Participants receive Acthar Gel
Overall Study
Worsening of disease activity
2
Overall Study
Physician Decision
1

Baseline Characteristics

Safety and Effectiveness of Acthar Gel for Inflammation of the Eye's Uvea (Middle Layer)

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Acthar Gel
n=5 Participants
Participants receive Acthar Gel
Age, Continuous
58.0 years
n=5 Participants
Sex: Female, Male
Female
4 Participants
n=5 Participants
Sex: Female, Male
Male
1 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
2 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
3 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
0 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=5 Participants
Race (NIH/OMB)
White
5 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
Region of Enrollment
United States
5 participants
n=5 Participants

PRIMARY outcome

Timeframe: Week 36

Population: Data were not collected.

The Nussenblatt grading scale uses photographic measurement of cloudy, declining vision (vitreous haze). The scale goes from 0 to 4, and lower scores are better.

Outcome measures

Outcome data not reported

PRIMARY outcome

Timeframe: Week 36

Population: Data were not collected.

Protein that escapes from blood vessels inside the eye make a sudden burst of scattered light (flare) when a laser shines on them. This is called a laser flare. It is used to measure the amount and size of proteins in the clear fluid in the front of the eyeball (aqueous humour). The larger the flare, the more inflammation is inside the eye (intraocular inflammation) in patients with uveitis. Laser flare is scored on a scale from 0 (no visible flare when compared with the normal eye) to 3 (severe - very dense flare). Lower scores are better.

Outcome measures

Outcome data not reported

PRIMARY outcome

Timeframe: Week 36

Population: Data were not collected.

The number of cells (like white blood cells) floating in the aqueous humour (aqueous cells) are measured on a scale from 0 (none) to 4 (more than 30 cells), and lower scores are better.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Week 36

Population: Data were not collected.

Eye pressure is measured in millimeters of mercury (mmHg). Normal eye pressure ranges from 12-22 mmHg, and eye pressure greater than 22 mmHg is considered higher than normal. During a 24-hour period, IOP normally varies by 2 to 6 mmHg because of different amounts of secretion and drainage at different times of the day. The word diurnal means "around the day," and IOP means "pressure inside the eye", so diurnal IOP is the measure of pressure inside the eye during a 24-hour period. Diurnal IOP is measured in millimeters of mercury (mmHg) using Goldmann Applanation Tonometry (GAT). Lower scores are better.

Outcome measures

Outcome data not reported

Adverse Events

Acthar Gel

Serious events: 0 serious events
Other events: 5 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Acthar Gel
n=5 participants at risk
Participants receive Acthar Gel
Eye disorders
Iris adhesions
20.0%
1/5 • Up to 44 weeks
Treatment Emergent non-serious adverse events and all serious adverse events are reported. Treatment emergent adverse events are those that started or got worse after the first dose of study drug. Clinically significant change in vital signs, laboratory values and/or physical examinations are recorded as adverse events.
Gastrointestinal disorders
Nausea
20.0%
1/5 • Up to 44 weeks
Treatment Emergent non-serious adverse events and all serious adverse events are reported. Treatment emergent adverse events are those that started or got worse after the first dose of study drug. Clinically significant change in vital signs, laboratory values and/or physical examinations are recorded as adverse events.
Immune system disorders
Drug hypersensitivity
20.0%
1/5 • Up to 44 weeks
Treatment Emergent non-serious adverse events and all serious adverse events are reported. Treatment emergent adverse events are those that started or got worse after the first dose of study drug. Clinically significant change in vital signs, laboratory values and/or physical examinations are recorded as adverse events.
Investigations
Intraocular pressure increased
40.0%
2/5 • Up to 44 weeks
Treatment Emergent non-serious adverse events and all serious adverse events are reported. Treatment emergent adverse events are those that started or got worse after the first dose of study drug. Clinically significant change in vital signs, laboratory values and/or physical examinations are recorded as adverse events.
Psychiatric disorders
Insomnia
40.0%
2/5 • Up to 44 weeks
Treatment Emergent non-serious adverse events and all serious adverse events are reported. Treatment emergent adverse events are those that started or got worse after the first dose of study drug. Clinically significant change in vital signs, laboratory values and/or physical examinations are recorded as adverse events.
Eye disorders
Uveitis
60.0%
3/5 • Up to 44 weeks
Treatment Emergent non-serious adverse events and all serious adverse events are reported. Treatment emergent adverse events are those that started or got worse after the first dose of study drug. Clinically significant change in vital signs, laboratory values and/or physical examinations are recorded as adverse events.

Additional Information

Medical Information Call Center

Mallinckrodt

Phone: 800-844-2830

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place