Trial Outcomes & Findings for A Multicenter Study Evaluating AZR-MD-001 in Patients With Meibomian Gland Dysfunction and Evaporative Dry Eye Disease (DED) (NCT NCT03652051)

NCT ID: NCT03652051

Last Updated: 2024-02-28

Results Overview

Change from Baseline in MGYLS. The MGYLS can range from 0 (abnormal) to 15 (normal)

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

321 participants

Primary outcome timeframe

Value at month 3 minus value at baseline

Results posted on

2024-02-28

Participant Flow

Participant milestones

Participant milestones
Measure
AZR-MD-001 Low Dose
AZR-MD-001 Low Dose was dosed twice weekly. AZR-MD-001 Low Dose: AZR-MD-001 is an ophthalmic ointment
AZR-MD-001 Mid Dose
AZR-MD-001 Mid Dose was dosed twice weekly. AZR-MD-001 Mid Dose: AZR-MD-001 is an ophthalmic ointment
AZR-MD-001 High Dose
AZR-MD-001 High Dose was dosed twice weekly. AZR-MD-001 High Dose: AZR-MD-001 is an ophthalmic ointment
AZR-MD-001 Vehicle
AZR-MD-001 Vehicle was dosed twice weekly. AZR-MD-001 Vehicle: AZR-MD-001 is a vehicle ophthalmic ointment
Stage 1
STARTED
9
27
24
16
Stage 1
COMPLETED
9
22
16
15
Stage 1
NOT COMPLETED
0
5
8
1
Stage 2
STARTED
0
82
83
80
Stage 2
COMPLETED
0
66
67
74
Stage 2
NOT COMPLETED
0
16
16
6

Reasons for withdrawal

Reasons for withdrawal
Measure
AZR-MD-001 Low Dose
AZR-MD-001 Low Dose was dosed twice weekly. AZR-MD-001 Low Dose: AZR-MD-001 is an ophthalmic ointment
AZR-MD-001 Mid Dose
AZR-MD-001 Mid Dose was dosed twice weekly. AZR-MD-001 Mid Dose: AZR-MD-001 is an ophthalmic ointment
AZR-MD-001 High Dose
AZR-MD-001 High Dose was dosed twice weekly. AZR-MD-001 High Dose: AZR-MD-001 is an ophthalmic ointment
AZR-MD-001 Vehicle
AZR-MD-001 Vehicle was dosed twice weekly. AZR-MD-001 Vehicle: AZR-MD-001 is a vehicle ophthalmic ointment
Stage 1
Adverse Event
0
5
7
1
Stage 1
Withdrawal by Subject
0
0
1
0
Stage 2
Adverse Event
0
2
1
0
Stage 2
Protocol Violation
0
1
6
0
Stage 2
Lost to Follow-up
0
2
0
3
Stage 2
Withdrawal by Subject
0
11
9
3

Baseline Characteristics

A Multicenter Study Evaluating AZR-MD-001 in Patients With Meibomian Gland Dysfunction and Evaporative Dry Eye Disease (DED)

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Stage 1: AZR-MD-001 Low Dose
n=9 Participants
AZR-MD-001 Low Dose was dosed twice weekly. AZR-MD-001 Low Dose: AZR-MD-001 is an ophthalmic ointment
Stage 1: AZR-MD-001 Mid Dose
n=27 Participants
AZR-MD-001 Mid Dose was dosed twice weekly. AZR-MD-001 Mid Dose: AZR-MD-001 is an ophthalmic ointment
Stage 1: AZR-MD-001 High Dose
n=24 Participants
AZR-MD-001 High Dose was dosed twice weekly. AZR-MD-001 High Dose: AZR-MD-001 is an ophthalmic ointment
Stage 1: AZR-MD-001 Vehicle
n=16 Participants
AZR-MD-001 Vehicle was dosed twice weekly. AZR-MD-001 Vehicle: AZR-MD-001 is a vehicle ophthalmic ointment
Stage 2: AZR-MD-001 Mid Dose
n=82 Participants
AZR-MD-001 Mid Dose was dosed twice weekly. AZR-MD-001 Mid Dose: AZR-MD-001 is an ophthalmic ointment
Stage 2: AZR-MD-001 High Dose
n=83 Participants
AZR-MD-001 High Dose was dosed twice weekly. AZR-MD-001 High Dose: AZR-MD-001 is an ophthalmic ointment
Stage 2: AZR-MD-001 Vehicle
n=80 Participants
AZR-MD-001 Vehicle was dosed twice weekly. AZR-MD-001 Vehicle: AZR-MD-001 is a vehicle ophthalmic ointment
Total
n=321 Participants
Total of all reporting groups
Age, Continuous
51.2 years
STANDARD_DEVIATION 18.79 • n=5 Participants
42.1 years
STANDARD_DEVIATION 17.71 • n=7 Participants
45.6 years
STANDARD_DEVIATION 22.02 • n=5 Participants
43.6 years
STANDARD_DEVIATION 20.34 • n=4 Participants
52.1 years
STANDARD_DEVIATION 16.9 • n=21 Participants
55.6 years
STANDARD_DEVIATION 17.2 • n=10 Participants
51.9 years
STANDARD_DEVIATION 18.5 • n=115 Participants
53.2 years
STANDARD_DEVIATION 17.5 • n=24 Participants
Sex: Female, Male
Female
6 Participants
n=5 Participants
11 Participants
n=7 Participants
11 Participants
n=5 Participants
5 Participants
n=4 Participants
51 Participants
n=21 Participants
56 Participants
n=10 Participants
56 Participants
n=115 Participants
196 Participants
n=24 Participants
Sex: Female, Male
Male
3 Participants
n=5 Participants
16 Participants
n=7 Participants
13 Participants
n=5 Participants
11 Participants
n=4 Participants
31 Participants
n=21 Participants
27 Participants
n=10 Participants
24 Participants
n=115 Participants
125 Participants
n=24 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
5 Participants
n=21 Participants
3 Participants
n=10 Participants
2 Participants
n=115 Participants
10 Participants
n=24 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
9 Participants
n=5 Participants
25 Participants
n=7 Participants
22 Participants
n=5 Participants
14 Participants
n=4 Participants
77 Participants
n=21 Participants
80 Participants
n=10 Participants
78 Participants
n=115 Participants
305 Participants
n=24 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
2 Participants
n=7 Participants
2 Participants
n=5 Participants
2 Participants
n=4 Participants
0 Participants
n=21 Participants
0 Participants
n=10 Participants
0 Participants
n=115 Participants
6 Participants
n=24 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
0 Participants
n=21 Participants
0 Participants
n=10 Participants
0 Participants
n=115 Participants
0 Participants
n=24 Participants
Race (NIH/OMB)
Asian
4 Participants
n=5 Participants
10 Participants
n=7 Participants
8 Participants
n=5 Participants
8 Participants
n=4 Participants
16 Participants
n=21 Participants
10 Participants
n=10 Participants
21 Participants
n=115 Participants
77 Participants
n=24 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
0 Participants
n=21 Participants
1 Participants
n=10 Participants
0 Participants
n=115 Participants
1 Participants
n=24 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
3 Participants
n=21 Participants
3 Participants
n=10 Participants
1 Participants
n=115 Participants
7 Participants
n=24 Participants
Race (NIH/OMB)
White
5 Participants
n=5 Participants
15 Participants
n=7 Participants
14 Participants
n=5 Participants
6 Participants
n=4 Participants
57 Participants
n=21 Participants
64 Participants
n=10 Participants
56 Participants
n=115 Participants
217 Participants
n=24 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
0 Participants
n=21 Participants
0 Participants
n=10 Participants
0 Participants
n=115 Participants
0 Participants
n=24 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
2 Participants
n=7 Participants
2 Participants
n=5 Participants
2 Participants
n=4 Participants
6 Participants
n=21 Participants
5 Participants
n=10 Participants
2 Participants
n=115 Participants
19 Participants
n=24 Participants
Meibomian Glands Yielding Liquid Secretion (Primary Sign Endpoint)
2.5 Gland Count (0 to 15)
STANDARD_DEVIATION 0.58 • n=5 Participants
2.8 Gland Count (0 to 15)
STANDARD_DEVIATION 1.26 • n=7 Participants
2.9 Gland Count (0 to 15)
STANDARD_DEVIATION 1.49 • n=5 Participants
2.8 Gland Count (0 to 15)
STANDARD_DEVIATION 1.64 • n=4 Participants
1.7 Gland Count (0 to 15)
STANDARD_DEVIATION 1.4 • n=21 Participants
1.9 Gland Count (0 to 15)
STANDARD_DEVIATION 1.4 • n=10 Participants
1.8 Gland Count (0 to 15)
STANDARD_DEVIATION 1.3 • n=115 Participants
1.8 Gland Count (0 to 15)
STANDARD_DEVIATION 1.3 • n=24 Participants
OSDI Total Score (Primary Symptom Endpoint)
25 Total Score (0 to 100)
STANDARD_DEVIATION 7.42 • n=5 Participants
23.1 Total Score (0 to 100)
STANDARD_DEVIATION 6.10 • n=7 Participants
21.34 Total Score (0 to 100)
STANDARD_DEVIATION 4.86 • n=5 Participants
22.64 Total Score (0 to 100)
STANDARD_DEVIATION 7.57 • n=4 Participants
25.2 Total Score (0 to 100)
STANDARD_DEVIATION 7.5 • n=21 Participants
24.2 Total Score (0 to 100)
STANDARD_DEVIATION 6 • n=10 Participants
25 Total Score (0 to 100)
STANDARD_DEVIATION 6.7 • n=115 Participants
24.8 Total Score (0 to 100)
STANDARD_DEVIATION 6.7 • n=24 Participants

PRIMARY outcome

Timeframe: Value at month 3 minus value at baseline

Change from Baseline in MGYLS. The MGYLS can range from 0 (abnormal) to 15 (normal)

Outcome measures

Outcome measures
Measure
Stage 1: AZR-MD-001 Low Dose
n=9 Participants
AZR-MD-001 Low Dose was dosed twice weekly. AZR-MD-001 Low Dose: AZR-MD-001 is an ophthalmic ointment
Stage 1: AZR-MD-001 Mid Dose
n=27 Participants
AZR-MD-001 Mid Dose was dosed twice weekly. AZR-MD-001 Mid Dose: AZR-MD-001 is an ophthalmic ointment
Stage 1: AZR-MD-001 High Dose
n=24 Participants
AZR-MD-001 High Dose was dosed twice weekly. AZR-MD-001 High Dose: AZR-MD-001 is an ophthalmic ointment
Stage 1: AZR-MD-001 Vehicle
n=16 Participants
AZR-MD-001 Vehicle was dosed twice weekly. AZR-MD-001 Vehicle: AZR-MD-001 is a vehicle ophthalmic ointment
Stage 2: AZR-MD-001 Mid Dose
n=82 Participants
AZR-MD-001 Mid Dose was dosed twice weekly. AZR-MD-001 Mid Dose: AZR-MD-001 is an ophthalmic ointment
Stage 2: AZR-MD-001 High Dose
n=83 Participants
AZR-MD-001 High Dose was dosed twice weekly. AZR-MD-001 High Dose: AZR-MD-001 is an ophthalmic ointment
Stage 2: AZR-MD-001 Vehicle
n=80 Participants
AZR-MD-001 Vehicle was dosed twice weekly. AZR-MD-001 Vehicle: AZR-MD-001 is a vehicle ophthalmic ointment
Meibomian Glands Yielding Liquid Secretion (MGYLS)
-0.7 Number of Open Glands
Standard Deviation 1.56
3.41 Number of Open Glands
Standard Deviation 0.8
3.07 Number of Open Glands
Standard Deviation 0.81
1.88 Number of Open Glands
Standard Deviation 1.38
4.2 Number of Open Glands
Standard Deviation 0.36
3.2 Number of Open Glands
Standard Deviation 0.4
2.4 Number of Open Glands
Standard Deviation 0.34

PRIMARY outcome

Timeframe: Value at month 3 minus value at baseline

Change from Baseline in OSDI Total Score. The OSDI Total Score can range from 100 (highly abnormal) to 0 (Normal)

Outcome measures

Outcome measures
Measure
Stage 1: AZR-MD-001 Low Dose
n=9 Participants
AZR-MD-001 Low Dose was dosed twice weekly. AZR-MD-001 Low Dose: AZR-MD-001 is an ophthalmic ointment
Stage 1: AZR-MD-001 Mid Dose
n=27 Participants
AZR-MD-001 Mid Dose was dosed twice weekly. AZR-MD-001 Mid Dose: AZR-MD-001 is an ophthalmic ointment
Stage 1: AZR-MD-001 High Dose
n=24 Participants
AZR-MD-001 High Dose was dosed twice weekly. AZR-MD-001 High Dose: AZR-MD-001 is an ophthalmic ointment
Stage 1: AZR-MD-001 Vehicle
n=16 Participants
AZR-MD-001 Vehicle was dosed twice weekly. AZR-MD-001 Vehicle: AZR-MD-001 is a vehicle ophthalmic ointment
Stage 2: AZR-MD-001 Mid Dose
n=82 Participants
AZR-MD-001 Mid Dose was dosed twice weekly. AZR-MD-001 Mid Dose: AZR-MD-001 is an ophthalmic ointment
Stage 2: AZR-MD-001 High Dose
n=83 Participants
AZR-MD-001 High Dose was dosed twice weekly. AZR-MD-001 High Dose: AZR-MD-001 is an ophthalmic ointment
Stage 2: AZR-MD-001 Vehicle
n=80 Participants
AZR-MD-001 Vehicle was dosed twice weekly. AZR-MD-001 Vehicle: AZR-MD-001 is a vehicle ophthalmic ointment
Ocular Surface Disease Index (OSDI) Total Score
12.93 Scores on a Scale
Standard Deviation 4.62
-8.73 Scores on a Scale
Standard Deviation 2.37
-4.74 Scores on a Scale
Standard Deviation 2.41
-2.34 Scores on a Scale
Standard Deviation 4.09
-7.29 Scores on a Scale
Standard Deviation 1.3
-6.1 Scores on a Scale
Standard Deviation 1.3
-3.8 Scores on a Scale
Standard Deviation 1.2

Adverse Events

Stage 1: AZR-MD-001 Low Dose

Serious events: 0 serious events
Other events: 2 other events
Deaths: 0 deaths

Stage 1: AZR-MD-001 Mid Dose

Serious events: 0 serious events
Other events: 13 other events
Deaths: 0 deaths

Stage 1: AZR-MD-001 High Dose

Serious events: 2 serious events
Other events: 14 other events
Deaths: 0 deaths

Stage 1: AZR-MD-001 Vehicle

Serious events: 0 serious events
Other events: 4 other events
Deaths: 0 deaths

Stage 2: AZR-MD-001 Mid Dose

Serious events: 1 serious events
Other events: 54 other events
Deaths: 0 deaths

Stage 2: AZR-MD-001 High Dose

Serious events: 1 serious events
Other events: 60 other events
Deaths: 0 deaths

Stage 2: AZR-MD-001 Vehicle

Serious events: 2 serious events
Other events: 8 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Stage 1: AZR-MD-001 Low Dose
n=9 participants at risk
AZR-MD-001 Low Dose was dosed twice weekly. AZR-MD-001 Low Dose: AZR-MD-001 is an ophthalmic ointment
Stage 1: AZR-MD-001 Mid Dose
n=27 participants at risk
AZR-MD-001 Mid Dose was dosed twice weekly. AZR-MD-001 Mid Dose: AZR-MD-001 is an ophthalmic ointment
Stage 1: AZR-MD-001 High Dose
n=24 participants at risk
AZR-MD-001 High Dose was dosed twice weekly. AZR-MD-001 High Dose: AZR-MD-001 is an ophthalmic ointment
Stage 1: AZR-MD-001 Vehicle
n=16 participants at risk
AZR-MD-001 Vehicle was dosed twice weekly. AZR-MD-001 Vehicle: AZR-MD-001 is a vehicle ophthalmic ointment
Stage 2: AZR-MD-001 Mid Dose
n=82 participants at risk
AZR-MD-001 Mid Dose was dosed twice weekly. AZR-MD-001 Mid Dose: AZR-MD-001 is an ophthalmic ointment
Stage 2: AZR-MD-001 High Dose
n=83 participants at risk
AZR-MD-001 High Dose was dosed twice weekly. AZR-MD-001 High Dose: AZR-MD-001 is an ophthalmic ointment
Stage 2: AZR-MD-001 Vehicle
n=80 participants at risk
AZR-MD-001 Vehicle was dosed twice weekly. AZR-MD-001 Vehicle: AZR-MD-001 is a vehicle ophthalmic ointment
Infections and infestations
pneumonia
0.00%
0/9 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/27 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/24 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/16 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
1.2%
1/82 • Number of events 1 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/83 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/80 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
Cardiac disorders
Pericarditis
0.00%
0/9 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/27 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/24 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/16 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/82 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/83 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
1.2%
1/80 • Number of events 80 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
Endocrine disorders
Thyroid mass
0.00%
0/9 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/27 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/24 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/16 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/82 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/83 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
1.2%
1/80 • Number of events 80 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
Injury, poisoning and procedural complications
Post procedural haemorrhage
0.00%
0/9 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/27 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/24 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/16 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/82 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
1.2%
1/83 • Number of events 83 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/80 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
Musculoskeletal and connective tissue disorders
n intervertebral disc protrusion
0.00%
0/9 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/27 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
4.2%
1/24 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/16 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/82 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/83 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/80 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
Eye disorders
ocular toxicity
0.00%
0/9 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/27 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
4.2%
1/24 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/16 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/82 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/83 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/80 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.

Other adverse events

Other adverse events
Measure
Stage 1: AZR-MD-001 Low Dose
n=9 participants at risk
AZR-MD-001 Low Dose was dosed twice weekly. AZR-MD-001 Low Dose: AZR-MD-001 is an ophthalmic ointment
Stage 1: AZR-MD-001 Mid Dose
n=27 participants at risk
AZR-MD-001 Mid Dose was dosed twice weekly. AZR-MD-001 Mid Dose: AZR-MD-001 is an ophthalmic ointment
Stage 1: AZR-MD-001 High Dose
n=24 participants at risk
AZR-MD-001 High Dose was dosed twice weekly. AZR-MD-001 High Dose: AZR-MD-001 is an ophthalmic ointment
Stage 1: AZR-MD-001 Vehicle
n=16 participants at risk
AZR-MD-001 Vehicle was dosed twice weekly. AZR-MD-001 Vehicle: AZR-MD-001 is a vehicle ophthalmic ointment
Stage 2: AZR-MD-001 Mid Dose
n=82 participants at risk
AZR-MD-001 Mid Dose was dosed twice weekly. AZR-MD-001 Mid Dose: AZR-MD-001 is an ophthalmic ointment
Stage 2: AZR-MD-001 High Dose
n=83 participants at risk
AZR-MD-001 High Dose was dosed twice weekly. AZR-MD-001 High Dose: AZR-MD-001 is an ophthalmic ointment
Stage 2: AZR-MD-001 Vehicle
n=80 participants at risk
AZR-MD-001 Vehicle was dosed twice weekly. AZR-MD-001 Vehicle: AZR-MD-001 is a vehicle ophthalmic ointment
Eye disorders
Application site pain
11.1%
1/9 • Number of events 9 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
44.4%
12/27 • Number of events 32 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
37.5%
9/24 • Number of events 24 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
6.2%
1/16 • Number of events 11 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
17.1%
14/82 • Number of events 16 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
15.7%
13/83 • Number of events 15 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/80 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
Eye disorders
Lacrimation increased
0.00%
0/9 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
14.8%
4/27 • Number of events 32 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
12.5%
3/24 • Number of events 24 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/16 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
11.0%
9/82 • Number of events 9 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
1.2%
1/83 • Number of events 1 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/80 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
Eye disorders
Punctate keratitis
0.00%
0/9 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
3.7%
1/27 • Number of events 32 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/24 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/16 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
9.8%
8/82 • Number of events 8 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
8.4%
7/83 • Number of events 15 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
1.2%
1/80 • Number of events 2 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
Eye disorders
Vital dye staining cornea present
0.00%
0/9 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
3.7%
1/27 • Number of events 32 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
8.3%
2/24 • Number of events 24 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/16 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
6.1%
5/82 • Number of events 7 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
8.4%
7/83 • Number of events 11 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
1.2%
1/80 • Number of events 2 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
Eye disorders
Eye pain
0.00%
0/9 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
11.1%
3/27 • Number of events 32 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
16.7%
4/24 • Number of events 24 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/16 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
6.1%
5/82 • Number of events 5 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
7.2%
6/83 • Number of events 10 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
1.2%
1/80 • Number of events 1 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
Eye disorders
Eye irritation
0.00%
0/9 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
25.9%
7/27 • Number of events 32 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
8.3%
2/24 • Number of events 24 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/16 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
4.9%
4/82 • Number of events 5 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
6.0%
5/83 • Number of events 7 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
2.5%
2/80 • Number of events 3 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
Eye disorders
Application site reaction
0.00%
0/9 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
3.7%
1/27 • Number of events 32 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
4.2%
1/24 • Number of events 24 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/16 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
4.9%
4/82 • Number of events 5 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
4.8%
4/83 • Number of events 5 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/80 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
Eye disorders
Foreign body sensation
11.1%
1/9 • Number of events 9 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
7.4%
2/27 • Number of events 32 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
8.3%
2/24 • Number of events 24 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
12.5%
2/16 • Number of events 11 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
4.9%
4/82 • Number of events 4 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
2.4%
2/83 • Number of events 2 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
1.2%
1/80 • Number of events 1 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
Eye disorders
Administration site reaction
11.1%
1/9 • Number of events 9 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
7.4%
2/27 • Number of events 32 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
29.2%
7/24 • Number of events 24 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
12.5%
2/16 • Number of events 11 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
4.9%
4/82 • Number of events 4 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
1.2%
1/83 • Number of events 2 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/80 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
Eye disorders
Photophobia
0.00%
0/9 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
18.5%
5/27 • Number of events 32 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
12.5%
3/24 • Number of events 24 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/16 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
4.9%
4/82 • Number of events 4 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
1.2%
1/83 • Number of events 1 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
1.2%
1/80 • Number of events 1 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
Eye disorders
Eye inflammation
0.00%
0/9 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/27 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/24 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/16 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
3.7%
3/82 • Number of events 3 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
9.6%
8/83 • Number of events 9 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
1.2%
1/80 • Number of events 1 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
Eye disorders
Application site irritation
0.00%
0/9 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
7.4%
2/27 • Number of events 32 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/24 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/16 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
2.4%
2/82 • Number of events 2 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
6.0%
5/83 • Number of events 5 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.
0.00%
0/80 • 3 months
AEs were classified into system organ class (SOC) and preferred term (PT) using MedDRA version 23.0 or higher. Treatment-emergent adverse events (TEAEs) were defined as events beginning or worsening on or after the planned first dose of study medication.

Additional Information

Charles Bosworth

Azura Ophthalmics

Phone: 17145598435

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place