A 12-week Study Treating Participants Who Have alpha1-antitrypsin-related COPD With Alvelestat (MPH966) or Placebo.

NCT ID: NCT03636347

Last Updated: 2022-04-14

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

99 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-10-29

Study Completion Date

2022-03-30

Brief Summary

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The purpose of this study is to investigate the effect of alvelestat (an oral neutrophil elastase inhibitor) on blood and sputum biomarkers in patients with PiZZ, null or rare variant phenotype/genotype alpha-1 anti-trypsin deficient lung disease. Change in a number of different blood and sputum biomarkers related to lung damage, inflammation and elastase activity will be measured over a 12 week period. The effect on lung function and respiratory symptoms will also be measured.

Detailed Description

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Conditions

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Alpha 1-Antitrypsin Deficiency Emphysema COPD

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

placebo-controlled, dose ascending, sequential group
Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors
Double-blind

Study Groups

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Placebo oral tablet

Group Type PLACEBO_COMPARATOR

Placebo Oral Tablet

Intervention Type DRUG

twice daily administration

Alvelestat oral tablet - dose 1

MPH966

Group Type ACTIVE_COMPARATOR

Alvelestat oral tablet - dose 1

Intervention Type DRUG

twice daily administration

Alvelestat oral tablet - dose 2

MPH966

Group Type ACTIVE_COMPARATOR

Alvelestat oral tablet - dose 2

Intervention Type DRUG

twice daily administration

Interventions

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Placebo Oral Tablet

twice daily administration

Intervention Type DRUG

Alvelestat oral tablet - dose 1

twice daily administration

Intervention Type DRUG

Alvelestat oral tablet - dose 2

twice daily administration

Intervention Type DRUG

Other Intervention Names

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MPH966 MPH966

Eligibility Criteria

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Inclusion Criteria

* Patients with a confirmed diagnosis of alpha-1-anti-trypsin deficiency and a PiZZ, null or other rare geno/phenotype and serum anti-alpha1 antitrypsin levels of less than 11uM
* FEV1 ≥20% predicted
* Computerised tomography (CT) scan evidence of emphysema
* Non-smokers

Exclusion Criteria

* Primary diagnosis of bronchiectasis
* An ongoing acute exacerbation of the underlying lung disease
* Underlying liver disease or abnormal liver function tests
* Previous augmentation therapy within 6 months of dosing
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Syneos Health

OTHER

Sponsor Role collaborator

Mereo BioPharma

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Robert Stockley, Prof.

Role: PRINCIPAL_INVESTIGATOR

University of Birmingham

Locations

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University of Alabama, Birmingham (UAB)

Birmingham, Alabama, United States

Site Status

UCLA Medical Center

Los Angeles, California, United States

Site Status

UC Davis Medical Centre

Sacramento, California, United States

Site Status

PMG Research of Wilmington

Wilmington, North Carolina, United States

Site Status

UZ Gent

Ghent, , Belgium

Site Status

UZ Leuven

Leuven, , Belgium

Site Status

The University Lung Clinic

Edmonton, Alberta, Canada

Site Status

Centre for Heart Lung Innovation, St Pauls Hospital

Vancouver, British Columbia, Canada

Site Status

Inspiration Research Ltd

Toronto, Ontario, Canada

Site Status

University of Saskatchewan Royal University Hospital

Saskatoon, Saskatchewan, Canada

Site Status

Aarhus Universitetshospital

Aarhus, , Denmark

Site Status

Gentofte Hospital

Hellerup, , Denmark

Site Status

Synddansk Universitet (SDU) - Odense University

Odense, , Denmark

Site Status

Instytut Gruzilicy Chorob Pluc

Warsaw, , Poland

Site Status

Hospital Univ Clinico San Carlos

Madrid, , Spain

Site Status

Hospital Sierrallana

Torrelavega, , Spain

Site Status

CTC Gothia Forum Sahlgrenska University Hospital

Gothenburg, , Sweden

Site Status

Lund University Hospital

Lund, , Sweden

Site Status

University Hospitals Birmingham NHS Foundation Trust

Birmingham, , United Kingdom

Site Status

Cambridge University Hospitals Foundation NHS Trust

Cambridge, , United Kingdom

Site Status

University Hospital Coventry and Warwickshire

Coventry, , United Kingdom

Site Status

Royal Infirmary of Edinburgh

Edinburgh, , United Kingdom

Site Status

Royal Devon and Exeter NHS Trust

Exeter, , United Kingdom

Site Status

University Hospitals of Leicester NHS Trust

Leicester, , United Kingdom

Site Status

Royal Brompton Hospital

London, , United Kingdom

Site Status

Southampton General Hospital

Southampton, , United Kingdom

Site Status

Countries

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United States Belgium Canada Denmark Poland Spain Sweden United Kingdom

Other Identifiers

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2018-001309-95

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

MPH966-2-01

Identifier Type: -

Identifier Source: org_study_id

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