Trial Outcomes & Findings for Efficacy and Safety of Namilumab for Moderate-to-severe Axial Spondyloarthritis (NCT NCT03622658)

NCT ID: NCT03622658

Last Updated: 2022-03-08

Results Overview

The primary endpoint was the proportion of subjects who achieved an Assessment in Ankylosing Spondylitis with 20% improvement (ASAS20) clinical response at Week 12. An ASAS20 clinical response was defined as an improvement of at least 20% and an absolute improvement of at least 10 units on a 0 to 100 scale in at least three of the following four domains collected in the electronic case report form (eCRF) and no worsening in the fourth domain: Subject's Global Assessment of Disease Status, Subject's Assessment of Spinal Pain, function (Bath Ankylosing Spondylitis Functional Index \[BASFI\]) and inflammation (last two questions of the BASDAI). Lower values within the individual domains represent less severe symptoms.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

42 participants

Primary outcome timeframe

Weeks 12

Results posted on

2022-03-08

Participant Flow

Participant milestones

Participant milestones
Measure
Placebo
Placebo solution administered by subcutaneous injection on 4 occasions over 10 weeks Placebo: Placebo solution for subcutaneous injection.
Namilumab
Namilumab (150 mg) administered by subcutaneous injection on 4 occasions over 10 weeks Namilumab: Namilumab solution for subcutaneous injection
Overall Study
STARTED
6
36
Overall Study
COMPLETED
3
32
Overall Study
NOT COMPLETED
3
4

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Efficacy and Safety of Namilumab for Moderate-to-severe Axial Spondyloarthritis

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Placebo
n=6 Participants
Placebo solution administered by subcutaneous injection on 4 occasions over 10 weeks Placebo: Placebo solution for subcutaneous injection.
Namilumab
n=36 Participants
Namilumab (150 mg) administered by subcutaneous injection on 4 occasions over 10 weeks Namilumab: Namilumab solution for subcutaneous injection
Total
n=42 Participants
Total of all reporting groups
Age, Categorical
<=18 years
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
6 Participants
n=5 Participants
35 Participants
n=7 Participants
41 Participants
n=5 Participants
Age, Categorical
>=65 years
0 Participants
n=5 Participants
1 Participants
n=7 Participants
1 Participants
n=5 Participants
Sex: Female, Male
Female
2 Participants
n=5 Participants
15 Participants
n=7 Participants
17 Participants
n=5 Participants
Sex: Female, Male
Male
4 Participants
n=5 Participants
21 Participants
n=7 Participants
25 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
1 Participants
n=5 Participants
0 Participants
n=7 Participants
1 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
5 Participants
n=5 Participants
33 Participants
n=7 Participants
38 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
3 Participants
n=7 Participants
3 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
1 Participants
n=5 Participants
0 Participants
n=7 Participants
1 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
White
5 Participants
n=5 Participants
34 Participants
n=7 Participants
39 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
1 Participants
n=7 Participants
1 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
1 Participants
n=7 Participants
1 Participants
n=5 Participants
Region of Enrollment
United Kingdom
6 Participants
n=5 Participants
36 Participants
n=7 Participants
42 Participants
n=5 Participants
Height
175.5 cm
n=5 Participants
173.5 cm
n=7 Participants
174.5 cm
n=5 Participants
Weight
86.5 kg
n=5 Participants
80.5 kg
n=7 Participants
82.15 kg
n=5 Participants
BMI
27.85 kg/m^2
n=5 Participants
27.6 kg/m^2
n=7 Participants
27.65 kg/m^2
n=5 Participants
Prior use of anti-tumor necrosis factor (TNF) treatment
1 participants
n=5 Participants
6 participants
n=7 Participants
7 participants
n=5 Participants
Duration of disease <2years
4 participants
n=5 Participants
16 participants
n=7 Participants
20 participants
n=5 Participants

PRIMARY outcome

Timeframe: Weeks 12

Population: Full Analysis Set.

The primary endpoint was the proportion of subjects who achieved an Assessment in Ankylosing Spondylitis with 20% improvement (ASAS20) clinical response at Week 12. An ASAS20 clinical response was defined as an improvement of at least 20% and an absolute improvement of at least 10 units on a 0 to 100 scale in at least three of the following four domains collected in the electronic case report form (eCRF) and no worsening in the fourth domain: Subject's Global Assessment of Disease Status, Subject's Assessment of Spinal Pain, function (Bath Ankylosing Spondylitis Functional Index \[BASFI\]) and inflammation (last two questions of the BASDAI). Lower values within the individual domains represent less severe symptoms.

Outcome measures

Outcome measures
Measure
Placebo
n=6 Participants
Placebo solution administered by subcutaneous injection on 4 occasions over 10 weeks Placebo: Placebo solution for subcutaneous injection.
Namilumab
n=36 Participants
Namilumab (150 mg) administered by subcutaneous injection on 4 occasions over 10 weeks Namilumab: Namilumab solution for subcutaneous injection
The Proportion of Subjects Who Achieved ASAS20 Clinical Response
3 Participants
14 Participants

SECONDARY outcome

Timeframe: Week 12

Population: Full Analysis Set.

Proportion of subjects who achieved Assessment in Ankylosing Spondylitis with 40% improvement (ASAS40) response at Week 12

Outcome measures

Outcome measures
Measure
Placebo
n=6 Participants
Placebo solution administered by subcutaneous injection on 4 occasions over 10 weeks Placebo: Placebo solution for subcutaneous injection.
Namilumab
n=36 Participants
Namilumab (150 mg) administered by subcutaneous injection on 4 occasions over 10 weeks Namilumab: Namilumab solution for subcutaneous injection
Proportion of Subjects Who Achieved ASAS40 Clinical Response at Week 12
3 Participants
9 Participants

SECONDARY outcome

Timeframe: Week 6

Population: Full Analysis Set.

Proportion of subjects who achieved an ASAS20 clinical response at Week 6

Outcome measures

Outcome measures
Measure
Placebo
n=6 Participants
Placebo solution administered by subcutaneous injection on 4 occasions over 10 weeks Placebo: Placebo solution for subcutaneous injection.
Namilumab
n=36 Participants
Namilumab (150 mg) administered by subcutaneous injection on 4 occasions over 10 weeks Namilumab: Namilumab solution for subcutaneous injection
Proportion of Subjects Who Achieved an ASAS20 Clinical Response at Week 6
0 Participants
12 Participants

SECONDARY outcome

Timeframe: Week 6

Population: Full Analysis Set. Overall number of participants analyzed reflect those with available ASDAS-CRP Scores as reported in the final clinical study report.

Proportion (percentage) of subjects who achieved Ankylosing Spondylitis Disease Activity Score C-reactive Protein (ASDAS-CRP) response at Week 6, Clinically Important Improvement

Outcome measures

Outcome measures
Measure
Placebo
n=5 Participants
Placebo solution administered by subcutaneous injection on 4 occasions over 10 weeks Placebo: Placebo solution for subcutaneous injection.
Namilumab
n=33 Participants
Namilumab (150 mg) administered by subcutaneous injection on 4 occasions over 10 weeks Namilumab: Namilumab solution for subcutaneous injection
Proportion of Subjects Who Achieved Ankylosing Spondylitis Disease Activity Score C-reactive Protein (ASDAS-CRP) Response at Weeks 6
0 Participants
10 Participants

SECONDARY outcome

Timeframe: Week 12

Population: Full Analysis Set. Overall number of participants analyzed reflect those with available ASDAS-CRP Scores as reported in the final clinical study report.

Proportion of Subjects Who Achieved Clinically Important ASDAS-CRP Score at Week 12, Clinically Important Improvement

Outcome measures

Outcome measures
Measure
Placebo
n=5 Participants
Placebo solution administered by subcutaneous injection on 4 occasions over 10 weeks Placebo: Placebo solution for subcutaneous injection.
Namilumab
n=32 Participants
Namilumab (150 mg) administered by subcutaneous injection on 4 occasions over 10 weeks Namilumab: Namilumab solution for subcutaneous injection
Proportion of Subjects Who Achieved Clinically Important ASDAS-CRP Score at Week 12
1 Participants
10 Participants

Adverse Events

Placebo

Serious events: 0 serious events
Other events: 5 other events
Deaths: 0 deaths

Namilumab

Serious events: 1 serious events
Other events: 31 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Placebo
n=6 participants at risk
Placebo solution administered by subcutaneous injection on 4 occasions over 10 weeks Placebo: Placebo solution for subcutaneous injection.
Namilumab
n=36 participants at risk
Namilumab (150 mg) administered by subcutaneous injection on 4 occasions over 10 weeks Namilumab: Namilumab solution for subcutaneous injection
Gastrointestinal disorders
Duodenitis
0.00%
0/6 • 28 weeks
2.8%
1/36 • 28 weeks
Injury, poisoning and procedural complications
Road traffic accident
0.00%
0/6 • 28 weeks
2.8%
1/36 • 28 weeks

Other adverse events

Other adverse events
Measure
Placebo
n=6 participants at risk
Placebo solution administered by subcutaneous injection on 4 occasions over 10 weeks Placebo: Placebo solution for subcutaneous injection.
Namilumab
n=36 participants at risk
Namilumab (150 mg) administered by subcutaneous injection on 4 occasions over 10 weeks Namilumab: Namilumab solution for subcutaneous injection
Blood and lymphatic system disorders
Macrocytosis
16.7%
1/6 • 28 weeks
0.00%
0/36 • 28 weeks
Gastrointestinal disorders
Nausea
16.7%
1/6 • 28 weeks
19.4%
7/36 • 28 weeks
Gastrointestinal disorders
Frequent bowel movement
16.7%
1/6 • 28 weeks
0.00%
0/36 • 28 weeks
General disorders
Chest discomfort
16.7%
1/6 • 28 weeks
2.8%
1/36 • 28 weeks
Infections and infestations
Lower respiratory tract infection
16.7%
1/6 • 28 weeks
5.6%
2/36 • 28 weeks
Infections and infestations
Nasopharyngitis
0.00%
0/6 • 28 weeks
25.0%
9/36 • 28 weeks
Infections and infestations
Urinary tract infection
16.7%
1/6 • 28 weeks
5.6%
2/36 • 28 weeks
Infections and infestations
Upper respiratory tract infection
16.7%
1/6 • 28 weeks
2.8%
1/36 • 28 weeks
Infections and infestations
Otitis externa
16.7%
1/6 • 28 weeks
0.00%
0/36 • 28 weeks
Gastrointestinal disorders
Diarrhoea
0.00%
0/6 • 28 weeks
8.3%
3/36 • 28 weeks
Gastrointestinal disorders
Vomiting
0.00%
0/6 • 28 weeks
8.3%
3/36 • 28 weeks
Gastrointestinal disorders
Gastritis
0.00%
0/6 • 28 weeks
5.6%
2/36 • 28 weeks
Musculoskeletal and connective tissue disorders
Arthralgia
0.00%
0/6 • 28 weeks
5.6%
2/36 • 28 weeks
Musculoskeletal and connective tissue disorders
Pain in extremity
16.7%
1/6 • 28 weeks
2.8%
1/36 • 28 weeks
Musculoskeletal and connective tissue disorders
Neck pain
16.7%
1/6 • 28 weeks
0.00%
0/36 • 28 weeks
Musculoskeletal and connective tissue disorders
Osteopenia
16.7%
1/6 • 28 weeks
0.00%
0/36 • 28 weeks
Nervous system disorders
Hypoaethesia
0.00%
0/6 • 28 weeks
8.3%
3/36 • 28 weeks
Psychiatric disorders
Anxiety
0.00%
0/6 • 28 weeks
5.6%
2/36 • 28 weeks
Reproductive system and breast disorders
Polymenorrhoea
16.7%
1/6 • 28 weeks
0.00%
0/36 • 28 weeks
Respiratory, thoracic and mediastinal disorders
Cough
0.00%
0/6 • 28 weeks
8.3%
3/36 • 28 weeks
Respiratory, thoracic and mediastinal disorders
Dyspnoea
0.00%
0/6 • 28 weeks
8.3%
3/36 • 28 weeks
Respiratory, thoracic and mediastinal disorders
Pleuritic pain
16.7%
1/6 • 28 weeks
2.8%
1/36 • 28 weeks
Skin and subcutaneous tissue disorders
Urticaria
16.7%
1/6 • 28 weeks
0.00%
0/36 • 28 weeks
Vascular disorders
Hypertension
0.00%
0/6 • 28 weeks
5.6%
2/36 • 28 weeks
Infections and infestations
Infected cyst
16.7%
1/6 • 28 weeks
0.00%
0/36 • 28 weeks
Injury, poisoning and procedural complications
Limb injury
16.7%
1/6 • 28 weeks
0.00%
0/36 • 28 weeks
Investigations
Protein urine present
16.7%
1/6 • 28 weeks
0.00%
0/36 • 28 weeks

Additional Information

Dr. Simon Lowry, Chief Medical Officer

Kinevant Sciences Inc. on behalf of Kinevant Science GmbH

Phone: 646-495-5368

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place