Study on the Effects of Mutations Under Inherited Retinal Disease in Korean

NCT ID: NCT03613948

Last Updated: 2021-10-25

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Total Enrollment

280 participants

Study Classification

OBSERVATIONAL

Study Start Date

2018-04-10

Study Completion Date

2021-01-20

Brief Summary

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To develop comprehensive genetic maps of inherited retinal diseases in Korean

* Establishment of comprehensive genetic database in Koreans with inherited retinal diseases including frequently mutated genes, genotype-phenotype correlations, and visual prognosis."

Detailed Description

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Group/ Cohort Label : Subject with age between 6 months and 65 years who have not receive molecular genetic testing Group / Cohort Description : Consecutive subjects with inherited retinal disease who are willing to do genetic testing using whole exome sequencing (n=265) and whole genome sequencing (n=15) and agree to informed consent of the study

Conditions

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Inherited Retinal Dystrophy Primarily Involving Sensory Retina Inherited Retinal Dystrophy Primarily Involving Retinal Pigment Epithelium

Study Design

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Observational Model Type

CASE_ONLY

Study Time Perspective

CROSS_SECTIONAL

Eligibility Criteria

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Inclusion Criteria

* Inherited retinal disease
* Age between 4 months and 75 years
* Subject who has clinically confirmed visual impairment including night blindness or photophobia. Subject should meet one of the following criteria
* pigmentary retinopathy in both eyes
* reduced response in photopic or scotopic electroretinogram in both eyes
* photoreceptor degeneration in optical coherence tomography in both eyes

Exclusion Criteria

* unilateral retinal disease
* Subject who had previously confirmed genetic testing
* Age less than 4 months or more than 75 years
* When congenital infection or trauma are suspicious for the cause of retinal disease
* When age-related macular degeneration, myopic degeneration, autoimmune origin are suspicious for the cause of retinal disease
* No visual impairment or normal electroretinogram (e.g., benign fleck)
* Illiterate subject who can not understand informed consent
* Foreigners
Minimum Eligible Age

4 Months

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Gangnam Severance Hospital

OTHER

Sponsor Role lead

Responsible Party

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Jinu Han

Associate Professor

Responsibility Role PRINCIPAL_INVESTIGATOR

Principal Investigators

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Jinu Han

Role: PRINCIPAL_INVESTIGATOR

Gangnam Severance Hospital

Locations

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Gangnam Severance Hospital

Seoul, , South Korea

Site Status

Countries

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South Korea

References

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Stone EM, Andorf JL, Whitmore SS, DeLuca AP, Giacalone JC, Streb LM, Braun TA, Mullins RF, Scheetz TE, Sheffield VC, Tucker BA. Clinically Focused Molecular Investigation of 1000 Consecutive Families with Inherited Retinal Disease. Ophthalmology. 2017 Sep;124(9):1314-1331. doi: 10.1016/j.ophtha.2017.04.008. Epub 2017 May 27.

Reference Type RESULT
PMID: 28559085 (View on PubMed)

Other Identifiers

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3-2018-0026

Identifier Type: -

Identifier Source: org_study_id