Study of BHV-4157 in Alzheimer's Disease

NCT ID: NCT03605667

Last Updated: 2023-12-06

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

350 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-07-31

Study Completion Date

2021-12-23

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

Preclinical models suggest that riluzole, the active metabolite of BHV-4157, may protect from AD-related pathology and cognitive dysfunction. Titrated dose of BHV-4157 to 280 mg, or placebo, were administered orally once daily. Duration of treatment is 48 weeks in double-blind phase. There is also a screening period of up to 42 days; and a 4-week post-treatment observation period. Eligible participants who completed the double-blind treatment phase had the opportunity to receive open-label troriluzole for up to 48 weeks in an open-label extension (OLE) phase.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Alzheimer Disease

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

BHV-4157

troriluzole, 280 mg (2 x 140 mg) capsules, QD

Group Type EXPERIMENTAL

troriluzole

Intervention Type DRUG

Oral BHV-4157 will be given daily for up to 48 weeks

Placebo

matching 280 mg (2 x 140 mg) placebo capsules, QD

Group Type PLACEBO_COMPARATOR

Placebo oral capsule

Intervention Type DRUG

Oral matching placebo will be given daily for up to 48 weeks

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

troriluzole

Oral BHV-4157 will be given daily for up to 48 weeks

Intervention Type DRUG

Placebo oral capsule

Oral matching placebo will be given daily for up to 48 weeks

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

BHV-4157

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Age 50 to 85 (inclusive) at screening
* Diagnosed with probable Alzheimer's disease dementia: Core clinical criteria in accordance with NIA/Alzheimer's Association Guidelines.
* Living in the community (includes assisted living facilities, but excludes long-term care nursing facilities).
* Ambulatory, or able to walk with an assistive device, such as a cane or walker.
* Participants must have a study partner who has frequent interaction with them (approximately \>3-4 times per week), will be present for all clinic visits, and can assist in compliance with study procedures.
* An Mini-Mental State Examination score of 14 to 24, inclusive, at screening.
* A brain MRI scan within 6 months of screening consistent with a diagnosis of Alzheimer's disease.
* Participants should be treated with a stable dosage regimen of FDA-approved AD medications (acetylcholinesterase inhibitors (AchEI) and/or memantine) for at least 3 months prior to screening. Participants should be expected to remain on a stable dosage regimen of these medications for the duration of the trial.
* Participants who are not being treated with FDA-approved AD medications at the time of screening, because they have contraindications to these medications, or because they have previously failed treatment with these medications, are also eligible for inclusion, if it is expected that they will not be treated with these medications for the duration of the trial.

Exclusion Criteria

* Hepatic impairment defined as Child-Pugh class of A or more severe liver impairment.
* Other neurodegenerative diseases and causes of dementias, including Parkinson's disease and Huntington's disease, vascular dementia, CJD (Creutzfeldt-Jakob disease), LBD (Lewy Body dementia), PSP (Progressive Supranuclear Palsy), AIDS (Acquired Immunodeficiency Syndrome), or NPH (normal pressure hydrocephalus).
* History of a major depressive episode within the past 6 months of screening.
* Insulin-dependent diabetes or uncontrolled diabetes with HbA1c value \>8.0 %.
* Cancer or a malignant tumor within the past 3 years, except patients who underwent potentially curative therapy with no evidence of recurrence for \>3 years. Patients with stable prostate cancer or non-melanoma skin cancers are not excluded.
* Participation in another clinical trial for an investigational agent and having taken at least one dose of study medication, unless confirmed as having been on placebo, within 12 weeks prior to screening. The end of a previous investigational trial is defined as the date of the last dose of an investigational agent.
Minimum Eligible Age

50 Years

Maximum Eligible Age

85 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Alzheimer's Disease Cooperative Study (ADCS)

OTHER

Sponsor Role collaborator

Biohaven Pharmaceuticals, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Xenoscience, Inc.

Phoenix, Arizona, United States

Site Status

Barrow Neurological Institute

Phoenix, Arizona, United States

Site Status

Banner Sun Health Research Institute

Sun City, Arizona, United States

Site Status

Neurology Center of North Orange County

Fullerton, California, United States

Site Status

University of California, San Diego

La Jolla, California, United States

Site Status

University of Southern California

Los Angeles, California, United States

Site Status

SC3 Research Group - Pasadena

Pasadena, California, United States

Site Status

Geriatric and Adult Psychiatry

Hamden, Connecticut, United States

Site Status

Yale University School of Medicine

New Haven, Connecticut, United States

Site Status

Ki Health PARTNERS LLC DBA NEW ENGLAND INSTITUTE FOR CLINICAL RESEARCH

Stamford, Connecticut, United States

Site Status

Brain Matters Research

Delray Beach, Florida, United States

Site Status

University of Miami

Miami, Florida, United States

Site Status

USF Health Byrd Alzheimer's Institute

Tampa, Florida, United States

Site Status

Northwestern University

Chicago, Illinois, United States

Site Status

Great Lakes Clinical Trials

Chicago, Illinois, United States

Site Status

Southern Illinois University

Springfield, Illinois, United States

Site Status

Indiana University

Indianapolis, Indiana, United States

Site Status

University of Iowa

Iowa City, Iowa, United States

Site Status

University of Kentucky

Lexington, Kentucky, United States

Site Status

Pennington Biomedical Research Center

Baton Rouge, Louisiana, United States

Site Status

Northern Light Acadia Hospital

Bangor, Maine, United States

Site Status

Johns Hopkins University

Baltimore, Maryland, United States

Site Status

University of Michigan, Ann Arbor

Ann Arbor, Michigan, United States

Site Status

Michigan State University

East Lansing, Michigan, United States

Site Status

Galen Research

Chesterfield, Missouri, United States

Site Status

Cleveland Clinic Lou Ruvo Center

Las Vegas, Nevada, United States

Site Status

Princeton Medical Institute

Princeton, New Jersey, United States

Site Status

Columbia University

New York, New York, United States

Site Status

University of Rochester Medical Center

Rochester, New York, United States

Site Status

SUNY Upstate Medical University Department of Geriatrics

Syracuse, New York, United States

Site Status

James J. Peters VAMC

The Bronx, New York, United States

Site Status

Case Western Reserve University

Beachwood, Ohio, United States

Site Status

Ohio State University

Columbus, Ohio, United States

Site Status

Tulsa Clinical Research

Tulsa, Oklahoma, United States

Site Status

Oregon Health and Science University

Portland, Oregon, United States

Site Status

Keystone Clinical Studies, LLC

Norristown, Pennsylvania, United States

Site Status

University of Pittsburgh

Pittsburgh, Pennsylvania, United States

Site Status

Geisinger Medical Clinic

Wilkes-Barre, Pennsylvania, United States

Site Status

Abington Neurological Associates

Willow Grove, Pennsylvania, United States

Site Status

Rhode Island Hospital

Providence, Rhode Island, United States

Site Status

CBRI, Roper Hospital

Charleston, South Carolina, United States

Site Status

Vanderbilt Memory & Alzheimer's Center

Nashville, Tennessee, United States

Site Status

The Glenn Biggs Institute for Alzheimer's and Neurodegenerative Diseases,University of Texas Health Science Center at San Antonio

San Antonio, Texas, United States

Site Status

University of Washington

Seattle, Washington, United States

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States

References

Explore related publications, articles, or registry entries linked to this study.

Qiu Y, Jacobs DM, Messer K, Salmon DP, Wellington CL, Stukas S, Revta C, Brewer JB, Leger GC, Askew B, Donahue L, Kaplita S, Coric V, Qureshi IA, Feldman HH; Alzheimer's Disease Cooperative Study T2 Protect AD Study Group. Prognostic value of plasma biomarkers for informing clinical trial design in mild-to-moderate Alzheimer's disease. Alzheimers Res Ther. 2025 May 2;17(1):97. doi: 10.1186/s13195-025-01745-3.

Reference Type DERIVED
PMID: 40317057 (View on PubMed)

Provided Documents

Download supplemental materials such as informed consent forms, study protocols, or participant manuals.

Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

BHV4157-203

Identifier Type: -

Identifier Source: org_study_id