Trial Outcomes & Findings for Repeated-dose Safety, Efficacy, Pharmacokinetic and Pharmacodynamic of CTAP101, Immediate-release Calcifediol, High-dose Cholecalciferol, and Paricalcitol Plus Low-dose Cholecalciferol in Patients With Secondary Hyperparathyroidism, Chronic Kidney Disease 3-4 and Vitamin D Insufficiency (NCT NCT03588884)

NCT ID: NCT03588884

Last Updated: 2022-12-09

Results Overview

This study is descriptive and no primary or secondary efficacy endpoints are defined.

Recruitment status

COMPLETED

Study phase

PHASE4

Target enrollment

69 participants

Primary outcome timeframe

5 months

Results posted on

2022-12-09

Participant Flow

Participant milestones

Participant milestones
Measure
CTAP101
CTAP101/Calcifediol Capsules 60 micrograms (mcg) once daily at bedtime, except on Days 1 and 29 when dosing will occur in the morning before breakfast Calcifediol Oral Capsule: Capsule, daily
Immediate-release (IR) Calcifediol
Immediate-release (IR) calcifediol/266 micrograms (mcg) capsule before breakfast on the mornings of Day 1 and Day 29 Calcifediol Oral Product: Capsule, once a month
Cholecalciferol
Cholecalciferol/Capsules 300,000 International Units (IU) (high-dose) before breakfast on the mornings of Day 1 and Day 29 Cholecalciferol: Capsule, once a month
Paricalcitol
Paricalcitol/Capsules 1 mcg plus cholecalciferol capsules 800 IU (low-dose) once daily in the morning before breakfast, except on Days 1 and29 when dosing will occur before breakfast Cholecalciferol: Capsule, once a month Paricalcitol Oral Capsule: Capsule, daily
Overall Study
STARTED
18
18
18
15
Overall Study
COMPLETED
18
15
15
14
Overall Study
NOT COMPLETED
0
3
3
1

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Repeated-dose Safety, Efficacy, Pharmacokinetic and Pharmacodynamic of CTAP101, Immediate-release Calcifediol, High-dose Cholecalciferol, and Paricalcitol Plus Low-dose Cholecalciferol in Patients With Secondary Hyperparathyroidism, Chronic Kidney Disease 3-4 and Vitamin D Insufficiency

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
CTAP101
n=18 Participants
CTAP101/Calcifediol Capsules 60 micrograms (mcg) once daily at bedtime, except on Days 1 and 29 when dosing will occur in the morning before breakfast Calcifediol Oral Capsule: Capsule, daily
Immediate-release (IR) Calcifediol
n=18 Participants
Immediate-release (IR) calcifediol/266 micrograms (mcg) capsule before breakfast on the mornings of Day 1 and Day 29 Calcifediol Oral Product: Capsule, once a month
Cholecalciferol
n=18 Participants
Cholecalciferol/Capsules 300,000 International Units (IU) (high-dose) before breakfast on the mornings of Day 1 and Day 29 Cholecalciferol: Capsule, once a month
Paricalcitol
n=15 Participants
Paricalcitol/Capsules 1 mcg plus cholecalciferol capsules 800 IU (low-dose) once daily in the morning before breakfast, except on Days 1 and29 when dosing will occur before breakfast Cholecalciferol: Capsule, once a month Paricalcitol Oral Capsule: Capsule, daily
Total
n=69 Participants
Total of all reporting groups
Age, Continuous
67.1 Year
STANDARD_DEVIATION 10.7 • n=5 Participants
70.1 Year
STANDARD_DEVIATION 14.4 • n=7 Participants
67.9 Year
STANDARD_DEVIATION 9.8 • n=5 Participants
63.4 Year
STANDARD_DEVIATION 12.0 • n=4 Participants
67.3 Year
STANDARD_DEVIATION 11.8 • n=21 Participants
Sex: Female, Male
Female
11 Participants
n=5 Participants
6 Participants
n=7 Participants
5 Participants
n=5 Participants
10 Participants
n=4 Participants
32 Participants
n=21 Participants
Sex: Female, Male
Male
7 Participants
n=5 Participants
12 Participants
n=7 Participants
13 Participants
n=5 Participants
5 Participants
n=4 Participants
37 Participants
n=21 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
1 Participants
n=5 Participants
1 Participants
n=7 Participants
1 Participants
n=5 Participants
1 Participants
n=4 Participants
4 Participants
n=21 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
17 Participants
n=5 Participants
17 Participants
n=7 Participants
17 Participants
n=5 Participants
14 Participants
n=4 Participants
65 Participants
n=21 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
0 Participants
n=21 Participants

PRIMARY outcome

Timeframe: 5 months

This study is descriptive and no primary or secondary efficacy endpoints are defined.

Outcome measures

Outcome measures
Measure
CTAP101
n=18 Participants
CTAP101/Calcifediol Capsules 60 micrograms (mcg) once daily at bedtime, except on Days 1 and 29 when dosing will occur in the morning before breakfast Calcifediol Oral Capsule: Capsule, daily
Immediate-release (IR) Calcifediol
n=18 Participants
Immediate-release (IR) calcifediol/266 micrograms (mcg) capsule before breakfast on the mornings of Day 1 and Day 29 Calcifediol Oral Product: Capsule, once a month
Cholecalciferol
n=18 Participants
Cholecalciferol/Capsules 300,000 International Units (IU) (high-dose) before breakfast on the mornings of Day 1 and Day 29 Cholecalciferol: Capsule, once a month
Paricalcitol
n=15 Participants
Paricalcitol/Capsules 1 mcg plus cholecalciferol capsules 800 IU (low-dose) once daily in the morning before breakfast, except on Days 1 and29 when dosing will occur before breakfast Cholecalciferol: Capsule, once a month Paricalcitol Oral Capsule: Capsule, daily
Incidence and Severity of Treatment-Emergent Adverse Events (TEAE) as Assessed by Common Terminology Criteria for Adverse Events (CTCAE) Version 5.0.
Grade 2 Moderate
1 number of TEAE count
3 number of TEAE count
8 number of TEAE count
5 number of TEAE count
Incidence and Severity of Treatment-Emergent Adverse Events (TEAE) as Assessed by Common Terminology Criteria for Adverse Events (CTCAE) Version 5.0.
Grade 1 Mild
39 number of TEAE count
12 number of TEAE count
13 number of TEAE count
10 number of TEAE count
Incidence and Severity of Treatment-Emergent Adverse Events (TEAE) as Assessed by Common Terminology Criteria for Adverse Events (CTCAE) Version 5.0.
Grade 3 Severe
2 number of TEAE count
3 number of TEAE count
0 number of TEAE count
1 number of TEAE count
Incidence and Severity of Treatment-Emergent Adverse Events (TEAE) as Assessed by Common Terminology Criteria for Adverse Events (CTCAE) Version 5.0.
Grade Potentially Life Threatening
0 number of TEAE count
0 number of TEAE count
0 number of TEAE count
0 number of TEAE count
Incidence and Severity of Treatment-Emergent Adverse Events (TEAE) as Assessed by Common Terminology Criteria for Adverse Events (CTCAE) Version 5.0.
Grade 5 Fatal
0 number of TEAE count
0 number of TEAE count
0 number of TEAE count
0 number of TEAE count

Adverse Events

CTAP101

Serious events: 1 serious events
Other events: 7 other events
Deaths: 0 deaths

Immediate-release (IR) Calcifediol

Serious events: 2 serious events
Other events: 7 other events
Deaths: 0 deaths

Cholecalciferol

Serious events: 4 serious events
Other events: 8 other events
Deaths: 0 deaths

Paricalcitol

Serious events: 1 serious events
Other events: 8 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
CTAP101
n=18 participants at risk
CTAP101/Calcifediol Capsules 60 micrograms (mcg) once daily at bedtime, except on Days 1 and 29 when dosing will occur in the morning before breakfast Calcifediol Oral Capsule: Capsule, daily
Immediate-release (IR) Calcifediol
n=18 participants at risk
Immediate-release (IR) calcifediol/266 micrograms (mcg) capsule before breakfast on the mornings of Day 1 and Day 29 Calcifediol Oral Product: Capsule, once a month
Cholecalciferol
n=18 participants at risk
Cholecalciferol/Capsules 300,000 International Units (IU) (high-dose) before breakfast on the mornings of Day 1 and Day 29 Cholecalciferol: Capsule, once a month
Paricalcitol
n=15 participants at risk
Paricalcitol/Capsules 1 mcg plus cholecalciferol capsules 800 IU (low-dose) once daily in the morning before breakfast, except on Days 1 and29 when dosing will occur before breakfast Cholecalciferol: Capsule, once a month Paricalcitol Oral Capsule: Capsule, daily
Gastrointestinal disorders
Melaena
0.00%
0/18 • 5 months
5.6%
1/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/15 • 5 months
Gastrointestinal disorders
Rectal haemorrhage
5.6%
1/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/15 • 5 months
Nervous system disorders
Hypertensive encephalopathy
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
5.6%
1/18 • 5 months
0.00%
0/15 • 5 months
Nervous system disorders
Lumbar radiculopathy
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
6.7%
1/15 • 5 months
Nervous system disorders
Quadrantanopia
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
5.6%
1/18 • 5 months
0.00%
0/15 • 5 months
Respiratory, thoracic and mediastinal disorders
Acute respiratory distress syndrome
0.00%
0/18 • 5 months
5.6%
1/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/15 • 5 months
Respiratory, thoracic and mediastinal disorders
Pulmonary oedema
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
5.6%
1/18 • 5 months
0.00%
0/15 • 5 months
Hepatobiliary disorders
Cholecystitis
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
5.6%
1/18 • 5 months
0.00%
0/15 • 5 months
Metabolism and nutrition disorders
Diabetic ketoacidosis
0.00%
0/18 • 5 months
5.6%
1/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/15 • 5 months
Musculoskeletal and connective tissue disorders
Intervertebral disc protrusion
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
6.7%
1/15 • 5 months
Musculoskeletal and connective tissue disorders
Lumbar spinal stenosis
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
6.7%
1/15 • 5 months
Renal and urinary disorders
Acute kidney injury
0.00%
0/18 • 5 months
5.6%
1/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/15 • 5 months
Respiratory, thoracic and mediastinal disorders
Blister
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
5.6%
1/18 • 5 months
0.00%
0/15 • 5 months

Other adverse events

Other adverse events
Measure
CTAP101
n=18 participants at risk
CTAP101/Calcifediol Capsules 60 micrograms (mcg) once daily at bedtime, except on Days 1 and 29 when dosing will occur in the morning before breakfast Calcifediol Oral Capsule: Capsule, daily
Immediate-release (IR) Calcifediol
n=18 participants at risk
Immediate-release (IR) calcifediol/266 micrograms (mcg) capsule before breakfast on the mornings of Day 1 and Day 29 Calcifediol Oral Product: Capsule, once a month
Cholecalciferol
n=18 participants at risk
Cholecalciferol/Capsules 300,000 International Units (IU) (high-dose) before breakfast on the mornings of Day 1 and Day 29 Cholecalciferol: Capsule, once a month
Paricalcitol
n=15 participants at risk
Paricalcitol/Capsules 1 mcg plus cholecalciferol capsules 800 IU (low-dose) once daily in the morning before breakfast, except on Days 1 and29 when dosing will occur before breakfast Cholecalciferol: Capsule, once a month Paricalcitol Oral Capsule: Capsule, daily
Gastrointestinal disorders
Diarrhoea
11.1%
2/18 • 5 months
5.6%
1/18 • 5 months
5.6%
1/18 • 5 months
6.7%
1/15 • 5 months
Gastrointestinal disorders
Nausea
5.6%
1/18 • 5 months
0.00%
0/18 • 5 months
5.6%
1/18 • 5 months
6.7%
1/15 • 5 months
Gastrointestinal disorders
Abdominal pain upper
5.6%
1/18 • 5 months
5.6%
1/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/15 • 5 months
Gastrointestinal disorders
Vomiting
5.6%
1/18 • 5 months
5.6%
1/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/15 • 5 months
Gastrointestinal disorders
Constipation
5.6%
1/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/15 • 5 months
Gastrointestinal disorders
Dyspepsia
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
6.7%
1/15 • 5 months
Gastrointestinal disorders
Flatulence
5.6%
1/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/15 • 5 months
Gastrointestinal disorders
Melaena
0.00%
0/18 • 5 months
5.6%
1/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/15 • 5 months
Gastrointestinal disorders
Rectal haemorrhage
5.6%
1/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/15 • 5 months
Nervous system disorders
Headache
11.1%
2/18 • 5 months
11.1%
2/18 • 5 months
0.00%
0/18 • 5 months
13.3%
2/15 • 5 months
Nervous system disorders
Dizziness
5.6%
1/18 • 5 months
0.00%
0/18 • 5 months
5.6%
1/18 • 5 months
0.00%
0/15 • 5 months
Nervous system disorders
Cervical radiculopathy
0.00%
0/18 • 5 months
5.6%
1/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/15 • 5 months
Nervous system disorders
Hypertensive encephalopathy
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
5.6%
1/18 • 5 months
0.00%
0/15 • 5 months
Nervous system disorders
Lumbar radiculopathy
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
6.7%
1/15 • 5 months
Nervous system disorders
Presyncope
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
5.6%
1/18 • 5 months
0.00%
0/15 • 5 months
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Quadrantanopia
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
5.6%
1/18 • 5 months
0.00%
0/15 • 5 months
Respiratory, thoracic and mediastinal disorders
Acute respiratory distress syndrome
0.00%
0/18 • 5 months
5.6%
1/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/15 • 5 months
Respiratory, thoracic and mediastinal disorders
Cough
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
5.6%
1/18 • 5 months
0.00%
0/15 • 5 months
Respiratory, thoracic and mediastinal disorders
Epistaxis
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
6.7%
1/15 • 5 months
Respiratory, thoracic and mediastinal disorders
Hiccups
5.6%
1/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/15 • 5 months
Respiratory, thoracic and mediastinal disorders
Nasal congestion
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
5.6%
1/18 • 5 months
0.00%
0/15 • 5 months
Respiratory, thoracic and mediastinal disorders
Pulmonary oedema
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
5.6%
1/18 • 5 months
0.00%
0/15 • 5 months
Respiratory, thoracic and mediastinal disorders
Throat irritation
5.6%
1/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/15 • 5 months
Metabolism and nutrition disorders
Decreased appetite
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
5.6%
1/18 • 5 months
0.00%
0/15 • 5 months
Metabolism and nutrition disorders
Diabetes mellitus
0.00%
0/18 • 5 months
5.6%
1/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/15 • 5 months
Metabolism and nutrition disorders
Diabetic ketoacidosis
0.00%
0/18 • 5 months
5.6%
1/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/15 • 5 months
Metabolism and nutrition disorders
Hyperkalaemia
0.00%
0/18 • 5 months
5.6%
1/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/15 • 5 months
Metabolism and nutrition disorders
Hypernatraemia
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
5.6%
1/18 • 5 months
0.00%
0/15 • 5 months
Musculoskeletal and connective tissue disorders
Arthralgia
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
5.6%
1/18 • 5 months
6.7%
1/15 • 5 months
Musculoskeletal and connective tissue disorders
Joint swelling
5.6%
1/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
6.7%
1/15 • 5 months
Musculoskeletal and connective tissue disorders
Back pain
5.6%
1/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/15 • 5 months
Musculoskeletal and connective tissue disorders
Intervertebral disc protrusion
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
6.7%
1/15 • 5 months
Musculoskeletal and connective tissue disorders
Lumbar spinal stenosis
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
6.7%
1/15 • 5 months
Musculoskeletal and connective tissue disorders
Myalgia
5.6%
1/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/15 • 5 months
Musculoskeletal and connective tissue disorders
Pain in extremity
5.6%
1/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/15 • 5 months
General disorders
Asthenia
0.00%
0/18 • 5 months
5.6%
1/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/15 • 5 months
General disorders
Chills
5.6%
1/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/15 • 5 months
General disorders
Fatigue
5.6%
1/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/15 • 5 months
General disorders
Influenza like illness
0.00%
0/18 • 5 months
5.6%
1/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/15 • 5 months
General disorders
Peripheral swelling
5.6%
1/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/15 • 5 months
General disorders
Tenderness
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
6.7%
1/15 • 5 months
Injury, poisoning and procedural complications
Laceration
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
11.1%
2/18 • 5 months
0.00%
0/15 • 5 months
Injury, poisoning and procedural complications
Road traffic accident
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
6.7%
1/15 • 5 months
Injury, poisoning and procedural complications
Skin abrasion
0.00%
0/18 • 5 months
5.6%
1/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/15 • 5 months
Blood and lymphatic system disorders
Anaemia
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
5.6%
1/18 • 5 months
6.7%
1/15 • 5 months
Infections and infestations
Bronchitis
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
6.7%
1/15 • 5 months
Infections and infestations
Cystitis
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
5.6%
1/18 • 5 months
0.00%
0/15 • 5 months
Renal and urinary disorders
Acute kidney injury
0.00%
0/18 • 5 months
5.6%
1/18 • 5 months
5.6%
1/18 • 5 months
0.00%
0/15 • 5 months
Skin and subcutaneous tissue disorders
Blister
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
5.6%
1/18 • 5 months
0.00%
0/15 • 5 months
Skin and subcutaneous tissue disorders
Rash
5.6%
1/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/15 • 5 months
Eye disorders
Eye pain
0.00%
0/18 • 5 months
5.6%
1/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/15 • 5 months
Hepatobiliary disorders
Cholecystitis
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
5.6%
1/18 • 5 months
0.00%
0/15 • 5 months
Investigations
Blood creatinine increased
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
5.6%
1/18 • 5 months
0.00%
0/15 • 5 months
Reproductive system and breast disorders
Breast pain
5.6%
1/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/15 • 5 months
Vascular disorders
Hypertension
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
5.6%
1/18 • 5 months
0.00%
0/15 • 5 months
Musculoskeletal and connective tissue disorders
Muscle spasms
5.6%
1/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/15 • 5 months
Musculoskeletal and connective tissue disorders
Musculoskeletal stiffness
5.6%
1/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/18 • 5 months
0.00%
0/15 • 5 months

Additional Information

OPKO Health Inc

OPKO Health Inc

Phone: 3055754100

Results disclosure agreements

  • Principal investigator is a sponsor employee Some institution and PI have the right to publish info 12 months after the study ended. For one PI that all Confidential Information must be held secret for a period of 5 years after end of the relevant Work Order.
  • Publication restrictions are in place

Restriction type: OTHER