Evaluate F901318 (Olorofim) Treatment of Invasive Fungal Infections in Participants Lacking Treatment Options

NCT ID: NCT03583164

Last Updated: 2024-07-10

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

203 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-06-06

Study Completion Date

2023-02-10

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

A study to evaluate olorofim (F901318) for the treatment of invasive fungal infections in participants lacking suitable alternative treatment options.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

An open label, single arm Phase IIb study of olorofim (F901318) in participants with invasive fungal infections with limited treatment options. Participants received study treatment for up to 12 weeks in the main phase of the study. At the Investigator's request and after discussion with the medical monitor, open-label treatment with F901318 could be continued in patients judged by the Investigator to need therapy beyond 84 days and considered likely to continue to benefit from extended treatment.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Invasive Fungal Infections

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Olorofim (F901318)

Olorofim (F901318) was given orally for up to 90 days in the Main Study Phase and could be continued for those participants entering the Extended Treatment Phase.

Patients received fixed doses comprising of a 1-day loading dose of 150 mg of olorofim twice a day followed by a maintenance dose of 90 mg of olorofim twice a day.

Up until Protocol Amendment 06, 58 patients received a weight-based olorofim dosing consisting of a 1-day loading dose of 4 mg/kg/day on Day 1, then a maintenance dose of 2.5 mg/kg/day (divided into 2 or 3 doses). The dose was then adjusted based on plasma levels of olorofim with the maximum total daily dose of 300 mg.

Group Type EXPERIMENTAL

Olorofim

Intervention Type DRUG

30mg oral tablets

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Olorofim

30mg oral tablets

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

F901318

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Male and female aged at least 18 years, or male and female aged 16 years or 17 years and who weigh at least 40 kg whom have given informed consent
* Ability and willingness to comply with the protocol.
* Able to take oral medication
* Females must be non-lactating and at no risk of pregnancy
* Male with female partners of childbearing potential must either abstain from sexual intercourse or use a highly effective means of contraception
* Participants with invasive fungal disease
* Participants who have limited alternative treatment options

Exclusion Criteria

* Women who are pregnant or breastfeeding.
* Known history of allergy, hypersensitivity, or any serious reaction to any component of the study drug.
* Participants with chronic aspergillosis, aspergilloma or allergic bronchopulmonary aspergillosis.
* Human Immunodeficiency Virus (HIV) infection but not currently receiving antiretroviral therapy.
* Participants with a medical condition that may jeopardize adherence to the protocol or may cause unacceptable additional risk to the participant
* Previously enrolled participants or participants enrolled in any clinical trial within the last 30 days
* Participants receiving treatment limited to supportive care due to predicted short survival time.
* Prohibited concomitant medications.
Minimum Eligible Age

16 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Iqvia Pty Ltd

INDUSTRY

Sponsor Role collaborator

F2G Biotech GmbH

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Sharon Chen

Role: PRINCIPAL_INVESTIGATOR

Westmead Hospital

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Valley Fever Institute at Kern Medical Center

Bakersfield, California, United States

Site Status

UC Davis Medical Center

Sacramento, California, United States

Site Status

University of California San Diego Medical Center

San Diego, California, United States

Site Status

Emory University

Atlanta, Georgia, United States

Site Status

University of Chicago

Chicago, Illinois, United States

Site Status

Johns Hopkins Hospital

Baltimore, Maryland, United States

Site Status

Brigham and Women's Hospital

Boston, Massachusetts, United States

Site Status

Washington University School of Medicine

St Louis, Missouri, United States

Site Status

Weill Cornell Medical College

New York, New York, United States

Site Status

Stony Brook University Medical Center

Stony Brook, New York, United States

Site Status

Duke University Health System

Durham, North Carolina, United States

Site Status

UPMC

Pittsburgh, Pennsylvania, United States

Site Status

University of Texas MD Anderson Cancer Center

Houston, Texas, United States

Site Status

The University of Texas Health Science Center at San Antonio

San Antonio, Texas, United States

Site Status

Westmead Hospital

Westmead, New South Wales, Australia

Site Status

Royal Brisbane and Women's Hospital

Herston, Queensland, Australia

Site Status

Peter MacCallum Centre-East Melbourne

Melbourne, Victoria, Australia

Site Status

Royal Melbourne Hospital

Melbourne, Victoria, Australia

Site Status

The Alfred Hospital

Melbourne, Victoria, Australia

Site Status

Fiona Stanley Hospital

Murdoch, Western Australia, Australia

Site Status

UZ Leuven

Leuven, Waals-Brabant, Belgium

Site Status

Institut Jules Bordet

Brussels, , Belgium

Site Status

Hôpital Erasme

Brussels, , Belgium

Site Status

Hospital Felício Rocho

Belo Horizonte, Minas Gerais, Brazil

Site Status

Santa Casa de Misericórdia de Belo Horizonte

Belo Horizonte, Minas Gerais, Brazil

Site Status

HC - UFPR - Hospital de Clínicas da Universidade Federal do Paraná

Curitiba, Paraná, Brazil

Site Status

Santa Casa de Misericórdia de Porto Alegre

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

Hospital de Clínicas de Porto Alegre

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

Hospital São Lucas da PUCRS

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

Hospital da Universidade Federal de Santa Maria CEP/UFSM

Santa Maria, Rio Grande do Sul, Brazil

Site Status

Hospital Erasto Gaertner - Liga Paranaense de Combate ao Câncer

Curitiba, , Brazil

Site Status

Santa Casa de Misericórdia de Passos

Passos, , Brazil

Site Status

Oncology Center, Mansoura University

Al Mansurah, , Egypt

Site Status

Alexandria University Hospital

Alexandria, , Egypt

Site Status

Cairo University Hospitals

Cairo, , Egypt

Site Status

Ain Shams University Hospital

Cairo, , Egypt

Site Status

Air Force Specialized Hospital

Cairo, , Egypt

Site Status

National Cancer Institute

Cairo, , Egypt

Site Status

Nasser Institute

Cairo, , Egypt

Site Status

CHU Strasbourg - Hôpital Hautepierre

Strasbourg, Bas Rhin, France

Site Status

CHU de Grenoble - Hôpital Albert Michallon

Grenoble, Isere, France

Site Status

Hôpital Necker - Enfants Malades

Paris, Paris, France

Site Status

Hôpital Saint-Louis

Paris, , France

Site Status

Klinikum der Universitaet Muenchen Campus Grosshadern

Munich, Bavaria, Germany

Site Status

Universitaetsklinikum Koeln

Cologne, North Rhine-Westphalia, Germany

Site Status

Charite Universitaetsmedizin Berlin - Campus Benjamin Franklin

Berlin, , Germany

Site Status

Charite-Campus Benjamin Franklin (CBF)

Berlin, , Germany

Site Status

Soroka University Medical Center

Beersheba, , Israel

Site Status

Rambam Health Care Campus

Haifa, , Israel

Site Status

Hadassah University Hospital - Ein Kerem

Jerusalem, , Israel

Site Status

Chaim Sheba Medical Center

Ramat Gan, , Israel

Site Status

Tel Aviv Sourasky Medical Center

Tel Aviv, , Israel

Site Status

Radboudumc

Nijmegen, , Netherlands

Site Status

Erasmus Medisch Centrum

Rotterdam, , Netherlands

Site Status

UMC Utrecht

Utrecht, , Netherlands

Site Status

Uniwersyteckie Centrum Kliniczne

Gdansk, , Poland

Site Status

SPZOZ Szpital Uniwersytecki w Krakowie

Krakow, , Poland

Site Status

Wojewodzki Szpital Specjalistyczny im. J. Korczaka

Słupsk, , Poland

Site Status

Instytut Hematologii i Transfuzjologii

Warsaw, , Poland

Site Status

Leningrad Regional Clinical Hospital

Saint Petersburg, , Russia

Site Status

FBI "Scientific Research Institute of Oncology n. a. N. N. Petrov"

Saint Petersburg, , Russia

Site Status

Pavlov First Saint Petersburg State Medical University

Saint Petersburg, , Russia

Site Status

SBEIHPE "NWSMU n. a. I.I Mechnikov" of MoH and SD of RH

Saint Petersburg, , Russia

Site Status

Asan Medical Center

Seoul, , South Korea

Site Status

Samsung Medical Center

Seoul, , South Korea

Site Status

The Catholic University of Korea, Seoul St. Mary's Hospital

Seoul, , South Korea

Site Status

Hospital Universitari Vall d'Hebron

Barcelona, , Spain

Site Status

Hospital Universitario Ramon y Cajal

Madrid, , Spain

Site Status

Hospital Universitario 12 de Octubre

Madrid, , Spain

Site Status

Hospital Universitari i Politecnic La Fe

Valencia, , Spain

Site Status

Siriraj Hospital

Bangkoknoi, Bangkok, Thailand

Site Status

King Chulalongkorn Memorial Hospital

Pathum Wan, Bangkok, Thailand

Site Status

Dicle University, Medical Faculty

Diyarbakır, , Turkey (Türkiye)

Site Status

Acibadem Atakent Hospital

Istanbul, , Turkey (Türkiye)

Site Status

Marmara University Pendik Research and Training Hospital

Istanbul, , Turkey (Türkiye)

Site Status

King's College Hospital

London, Greater London, United Kingdom

Site Status

Manchester Royal Infirmary

Manchester, Greater Manchester, United Kingdom

Site Status

Wythenshawe Hospital

Manchester, Wythenshawe, United Kingdom

Site Status

Bach Mai Hospital

Hanoi, , Vietnam

Site Status

National Lung Hospital

Hanoi, , Vietnam

Site Status

HCMC Hospital for Tropical Diseases

Ho Chi Minh City, , Vietnam

Site Status

Blood Transfusion Hematology Hospital

Ho Chi Minh City, , Vietnam

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Australia Belgium Brazil Egypt France Germany Israel Netherlands Poland Russia South Korea Spain Thailand Turkey (Türkiye) United Kingdom Vietnam

References

Explore related publications, articles, or registry entries linked to this study.

Maertens JA, Thompson GR 3rd, Spec A, Donovan FM, Hammond SP, Bruns AHW, Rahav G, Shoham S, Johnson R, Rijnders B, Schaenman J, Hoenigl M, Morrissey CO, Mehta SR, Heath CH, Koehler P, Paterson DL, Slavin MA, Fortun J, Nguyen MH, Patterson TF, Uspenskaya O, Van de Veerdonk FL, Verweij PE, Aoun M, Georgala A, Alexander BD, Chayakulkeeree M, Mehra V, Miceli MH, Sikka MK, Sole A, Walsh TJ, Aguado JM, Holland SM, Moussa M, Rautemaa-Richardson R, Bazaz R, Schwartz S, Walsh SR, Plate M, Yehudai-Ofir D, Bruggemann RJ, Cornely OA, Ostrosky-Zeichner L, Vazquez JA, White PL, Cornelissen K, Ross GG, Fitton L, Dane A, Zinzi D, Rex JH, Chen SC. Olorofim for the treatment of invasive fungal diseases in patients with few or no therapeutic options: a single-arm, open-label, phase 2b study. Lancet Infect Dis. 2025 Jun 17:S1473-3099(25)00224-5. doi: 10.1016/S1473-3099(25)00224-5. Online ahead of print.

Reference Type DERIVED
PMID: 40541222 (View on PubMed)

Provided Documents

Download supplemental materials such as informed consent forms, study protocols, or participant manuals.

Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

F901318/0032

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.

Evaluation of Immediate Release Tablet
NCT02808741 COMPLETED PHASE1