Study to Assess the Efficacy and Safety of ACT-541468 (Daridorexant) in Adult and Elderly Subjects Suffering From Difficulties to Sleep

NCT ID: NCT03575104

Last Updated: 2022-03-25

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

924 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-05-29

Study Completion Date

2020-05-14

Brief Summary

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The main purpose of this study is to assess efficacy and safety of ACT-541468 (daridorexant) in adult and elderly subjects with insomnia disorder. Efficacy will be evaluated on objective and subjective sleep parameters.

Detailed Description

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Conditions

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Insomnia Disorder

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Daridorexant 10 mg

Group Type EXPERIMENTAL

Daridorexant

Intervention Type DRUG

Daridorexant will be administered as tablets, orally, once daily in the evening.

Daridorexant 25 mg

Group Type EXPERIMENTAL

Daridorexant

Intervention Type DRUG

Daridorexant will be administered as tablets, orally, once daily in the evening.

Placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

Matching placebo will be administered as tablets, orally, once daily in the evening.

Interventions

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Daridorexant

Daridorexant will be administered as tablets, orally, once daily in the evening.

Intervention Type DRUG

Placebo

Matching placebo will be administered as tablets, orally, once daily in the evening.

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

* Signed informed consent prior to any study-mandated procedure;
* Male or female aged ≥ 18 years;
* Insomnia disorder according to DSM-5 criteria;
* Insomnia Severity Index score ≥ 15;
* Insufficient sleep quantity as collected subjectively in the sleep diary and validated objectively by polysomnography;
* Women of childbearing potential must have a negative and urine pregnancy test and use the contraception scheme up to at least 30 days after last study treatment intake.

Exclusion Criteria

* Body mass index below 18.5 or above 40.0 kg/m2;
* Any lifetime history of of related breathing disorder, periodic limb movement disorder, restless legs syndrome, circadian rhythm disorder, rapid eye movement (REM) behavior disorder, narcolepsy, or apnea/hypopnea;
* Cognitive behavioral therapy (CBT) only allowed if, the treatment started at least 1 month prior to Visit 3 and the subject agrees to continue this CBT throughout the study;
* Self-reported usual daytime napping ≥ 1 hour per day and ≥ 3 days per week;
* Acute or unstable psychiatric conditions diagnosed by the Mini International Neuropsychiatric Interview;
* Mini Mental State Examination (MMSE) score \< 25 in subjects ≥ 50 years;
* For female subjects: pregnant, lactating or planning to become pregnant during projected duration of the study;
* History or clinical evidence of any disease or medical condition or treatment, which may put the subject at risk of participation in the study or may interfere with the study assessments.
* Any circumstances or conditions, which, in the opinion of the investigator, may affect the subject's full participation in the study or compliance with the protocol.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Idorsia Pharmaceuticals Ltd.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Trials

Role: STUDY_DIRECTOR

Idorsia Pharmaceuticals Ltd.

Locations

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Pulmonary Associates, Pa

Glendale, Arizona, United States

Site Status

Noble Clinical Research

Tucson, Arizona, United States

Site Status

Baptist Health Center for Clinical Research

Little Rock, Arkansas, United States

Site Status

Woodland International Research Group

Little Rock, Arkansas, United States

Site Status

Core Healthcare Group

Cerritos, California, United States

Site Status

Artemis Institute For Clinical Research - Riverside

Riverside, California, United States

Site Status

Pacific Research Network

San Diego, California, United States

Site Status

Artemis Institute for Clinical Research

San Marcos, California, United States

Site Status

Santa Monica Clinical Trials

Santa Monica, California, United States

Site Status

Empire Clinical Research

Upland, California, United States

Site Status

Innovative Clinical Research

Lafayette, Colorado, United States

Site Status

Clinical Research of South Florida

Coral Gables, Florida, United States

Site Status

Fleming Island Center for Clinical Research

Fleming Island, Florida, United States

Site Status

Clinical Trials Research

Lincoln, Florida, United States

Site Status

Clinical Research Group of St. Petersburgh

St. Petersburg, Florida, United States

Site Status

Neurotrials Research Incorporated

Atlanta, Georgia, United States

Site Status

Sleep Practitioners, LLC

Macon, Georgia, United States

Site Status

Hawaii Pacific Neurosciences

Honolulu, Hawaii, United States

Site Status

Saltzer Clinical Research

Nampa, Idaho, United States

Site Status

Rowe Neurology Institute

Lenexa, Kansas, United States

Site Status

Sleep Disorders Center of the Mid-Atlantic

Glen Burnie, Maryland, United States

Site Status

Neurocare Inc.

Newton, Massachusetts, United States

Site Status

Precise Research Centers

Flowood, Mississippi, United States

Site Status

Garden City Asthma and Sleep Center

Garden City, New York, United States

Site Status

Research Carolina of Hickory

Hickory, North Carolina, United States

Site Status

Wake Research Associates

Raleigh, North Carolina, United States

Site Status

Clinical Trials of America - NC, LLC

Winston-Salem, North Carolina, United States

Site Status

CTI Clinical Research II

Cincinnati, Ohio, United States

Site Status

Ohio Sleep Medicine Institue

Dublin, Ohio, United States

Site Status

Cleveland Sleep Research Center

Middleburg Heights, Ohio, United States

Site Status

Robert V. Sibilia, MD, Inc.

Wooster, Ohio, United States

Site Status

Brian Abaluck LLC

Paoli, Pennsylvania, United States

Site Status

Wesley Neurology Clinic Pc (Multiple Sclerosis)

Cordova, Tennessee, United States

Site Status

FutureSearch Trials of Neurology, LP

Austin, Texas, United States

Site Status

InSite Clinical Research

DeSoto, Texas, United States

Site Status

Jacksonville Center for Clinical Research

Jacksonville, Texas, United States

Site Status

Dm Clinical Research / Martin Diagnostic Clinic

Tomball, Texas, United States

Site Status

HOSPITAL AZ SINT-JAN_Neurology department

Bruges, , Belgium

Site Status

Hospital Universitair Zieknhuis Brussel, Pneumology and Sleep Laboratory

Brussels, , Belgium

Site Status

University Hospital Gent, Department of General Internal Medicine and Center of neurophysiological Monitoring

Ghent, , Belgium

Site Status

Hospital UZ Leuven_ Pneumology Department

Leuven, , Belgium

Site Status

Acibadem City Clinic Tokuda Hospital EAD

Sofia, , Bulgaria

Site Status

Canadian Phase Onward Inc.

Toronto, Ontario, Canada

Site Status

Queensway Sleep Lab Sleep Clinic (MedSleep)- 5359 Dundas Street West, Suite 202, Etobicoke, ON M9B 1B1

Etobicoke, , Canada

Site Status

The Medical Arts Health Research Group

Kelowna, , Canada

Site Status

Somni Research Inc.

Markham, , Canada

Site Status

Somni Research, Calgary

Toronto, , Canada

Site Status

CANADIAN PHASE ONWARD INC. (Toronto)

Toronto, , Canada

Site Status

Nemocnice České Budějovice, Centrum pro poruchy spánku a spánkovou medicínu

České Budějovice, , Czechia

Site Status

Narodni Ustav Dusevniho Zdravi (National Institute of Mental Health)

Klecany, , Czechia

Site Status

Fakultní nemocnice Ostrava, Spánková laboratoř

Ostrava-Poruba, , Czechia

Site Status

Vitalmed Uniklinikka

Helsinki, , Finland

Site Status

Oivauni Oy - Kuopio

Kuopio, , Finland

Site Status

Oivauni Oy - Tampere

Tampere, , Finland

Site Status

Unitutkimusyksikkö, Turun Yliopisto

Turku, , Finland

Site Status

CHRU De Lille - Hospital Salengro - Neurophysiologie Clinique

Lille, , France

Site Status

Clinique beau soleil - Department Sleep and Neurology

Montpellier, , France

Site Status

CHU NIMES - Unité de Sommeil

Nîmes, , France

Site Status

Advanced Sleep Research GmbH

Berlin, , Germany

Site Status

Klinische Forschung Berlin-Mitte GmbH

Berlin, , Germany

Site Status

Charité - Universitätsmedizin Berlin - Campus Benjamin Franklin Kompetenzzentrum Schlafmedizin

Berlin, , Germany

Site Status

Synexus Clinical Research GmbH

Bochum, , Germany

Site Status

Klinische Forschung Dresden GmbH

Dresden, , Germany

Site Status

Synexus Clinical Research GmbH

Frankfurt, , Germany

Site Status

Klinische Forschung Hannover Mitte GmbH

Hanover, , Germany

Site Status

Interdisziplinäre Schlafmedizin, Pfalzklinikum

Klingenmünster, , Germany

Site Status

Zentrum für Integrative Psychiatrie (ZiP) Universität zu Lübeck

Lübeck, , Germany

Site Status

Central Insitute of Mental Health Sleep laboratory Medical Faculty Mannheim/Heidelberg University

Mannheim, , Germany

Site Status

Klinik und Poliklinik für Psychiatrie, Psychosomatik und Psychotherapie der Universität am Bezirksklinikum Regensburg

Regensburg, , Germany

Site Status

SOMNIBENE Institut für Medizinische Forschung und Schlafmedizin Schwerin GmbH

Schwerin, , Germany

Site Status

Magyar Honvédség Egészségügyi Központ, Neurológiai Osztály

Budapest, , Hungary

Site Status

Somnius Kft. SomnoCenter Szeged

Szeged, , Hungary

Site Status

Dong-A University Hospital

Busan, , South Korea

Site Status

4F Neuroimaging analysis laboratory, 56 Dalseong-ro, Jung-gu

Daegu, , South Korea

Site Status

Chungnam National University Hospital

Daejeon, , South Korea

Site Status

3F, 2nd Building, Psychiatry Outpatient, Family Counseling Room, 42 Jebong-ro, Donggu

Gwangju, , South Korea

Site Status

8F Sleep Lab, 1st Building,82, Gumi-ro 173 Beon-gil, Bundang-gu

Seongnam, , South Korea

Site Status

3F Sleep Medicine Center, 101 Daehak-Ro Jongno-Gu

Seoul, , South Korea

Site Status

1st CRC room, 2F, Jejoong building, 50-1 Yonsei-ro,, Seodaemun-gu

Seoul, , South Korea

Site Status

B2F, Clinical Trial Center, Konkuk University Medical Center 120-1, Neungdong-ro, Gwangjin-gu

Seoul, , South Korea

Site Status

B1F Neurological examination room, 892 Dongnam-ro, Gangdong-gu

Seoul, , South Korea

Site Status

2F Psychiatry Outpatient, 93, Jungbu-daero, Paldal-gu

Suwon, , South Korea

Site Status

Göteborgs Universitet, Centrum för sömn och vakenhetsstörningar

Gothenburg, , Sweden

Site Status

Universitetssjukhuset Örebro Neurokliniken, Sömnenheten

Örebro, , Sweden

Site Status

SOPHIAHEMMET (Stockholm)

Stockholm, , Sweden

Site Status

Sömnutredningsmottagningen, smärtcentrum Akademiska sjukhuset

Uppsala, , Sweden

Site Status

Countries

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United States Belgium Bulgaria Canada Czechia Finland France Germany Hungary South Korea Sweden

References

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Hudgens S, Phillips-Beyer A, Newton L, Seboek Kinter D, Benes H. Development and Validation of the Insomnia Daytime Symptoms and Impacts Questionnaire (IDSIQ). Patient. 2021 Mar;14(2):249-268. doi: 10.1007/s40271-020-00474-z. Epub 2020 Nov 1.

Reference Type BACKGROUND
PMID: 33131027 (View on PubMed)

Mignot E, Mayleben D, Fietze I, Leger D, Zammit G, Bassetti CLA, Pain S, Kinter DS, Roth T; investigators. Safety and efficacy of daridorexant in patients with insomnia disorder: results from two multicentre, randomised, double-blind, placebo-controlled, phase 3 trials. Lancet Neurol. 2022 Feb;21(2):125-139. doi: 10.1016/S1474-4422(21)00436-1.

Reference Type RESULT
PMID: 35065036 (View on PubMed)

Di Marco T, Djonlagic I, Dauvilliers Y, Sadeghi K, Little D, Datta AN, Hubbard J, Hajak G, Krystal A, Olivieri A, Parrino L, Puryear CB, Zammit G, Donoghue J, Scammell TE. Effect of daridorexant on sleep architecture in patients with chronic insomnia disorder: a pooled post hoc analysis of two randomized phase 3 clinical studies. Sleep. 2024 Nov 8;47(11):zsae098. doi: 10.1093/sleep/zsae098.

Reference Type DERIVED
PMID: 38644625 (View on PubMed)

Citrome L, Juday TR, Lundwall C. Lemborexant and Daridorexant for the Treatment of Insomnia: An Indirect Comparison Using Number Needed to Treat, Number Needed to Harm, and Likelihood to Be Helped or Harmed. J Clin Psychiatry. 2023 Oct 2;84(6):23m14851. doi: 10.4088/JCP.23m14851.

Reference Type DERIVED
PMID: 37796657 (View on PubMed)

Dutta S, Singhal S, Shah R, Charan J, Dhingra S, Haque M. Daridorexant as a novel pharmacotherapeutic approach in insomnia: a systematic review and meta-analysis. Expert Opin Drug Saf. 2023 Jul-Dec;22(12):1237-1251. doi: 10.1080/14740338.2023.2243217. Epub 2023 Aug 7.

Reference Type DERIVED
PMID: 37526060 (View on PubMed)

Heidenreich S, Ross M, Chua GN, Seboek Kinter D, Phillips-Beyer A. Preferences of patients for benefits and risks of insomnia medications using data elicited during two phase III clinical trials. Sleep. 2022 Nov 9;45(11):zsac204. doi: 10.1093/sleep/zsac204.

Reference Type DERIVED
PMID: 36054921 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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ID-078A302

Identifier Type: -

Identifier Source: org_study_id

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