Trial Outcomes & Findings for Human Factors Study to Validate the User Interface of TOBI Podhaler Using Placebo Capsules (NCT NCT03502070)

NCT ID: NCT03502070

Last Updated: 2022-03-03

Results Overview

Critical use errors and close calls for the following: placing of capsule into the top of the mouthpiece, failure to replace mouthpiece, failure to adequately pierce capsule, failure to release before inhaling, multiple piercing of capsule, exhalation into mouthpiece, inadequate seal around mouthpiece, inadequate inhalation technique, failure to use reserve device when capsule not adequately pierced, failure to administer 4 capsules per dose, swallowing of capsule

Recruitment status

COMPLETED

Study phase

PHASE4

Target enrollment

47 participants

Primary outcome timeframe

1 Day

Results posted on

2022-03-03

Participant Flow

Participant milestones

Participant milestones
Measure
Open-Label Placebo
One dose (4 capsules) of placebo Placebo: One dose (4 capsules) of placebo Tobi Podhaler: The placebo capsule has to be released from the blister card and inserted into the Podhaler device. The device is then actuated and the study drug is inhaled according to the instructions for use
Overall Study
STARTED
47
Overall Study
COMPLETED
45
Overall Study
NOT COMPLETED
2

Reasons for withdrawal

Reasons for withdrawal
Measure
Open-Label Placebo
One dose (4 capsules) of placebo Placebo: One dose (4 capsules) of placebo Tobi Podhaler: The placebo capsule has to be released from the blister card and inserted into the Podhaler device. The device is then actuated and the study drug is inhaled according to the instructions for use
Overall Study
Withdrawal by Subject
1
Overall Study
Screen Failure
1

Baseline Characteristics

Human Factors Study to Validate the User Interface of TOBI Podhaler Using Placebo Capsules

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Open-Label Placebo
n=45 Participants
One dose (4 capsules) of placebo Placebo: One dose (4 capsules) of placebo Tobi Podhaler: The placebo capsule has to be released from the blister card and inserted into the Podhaler device. The device is then actuated and the study drug is inhaled according to the instructions for use
Age, Continuous
17.5 years
STANDARD_DEVIATION 12.55 • n=5 Participants
Sex: Female, Male
Female
21 Participants
n=5 Participants
Sex: Female, Male
Male
24 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
9 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
36 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
1 Participants
n=5 Participants
Race (NIH/OMB)
Asian
0 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
2 Participants
n=5 Participants
Race (NIH/OMB)
White
41 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
1 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants

PRIMARY outcome

Timeframe: 1 Day

Critical use errors and close calls for the following: placing of capsule into the top of the mouthpiece, failure to replace mouthpiece, failure to adequately pierce capsule, failure to release before inhaling, multiple piercing of capsule, exhalation into mouthpiece, inadequate seal around mouthpiece, inadequate inhalation technique, failure to use reserve device when capsule not adequately pierced, failure to administer 4 capsules per dose, swallowing of capsule

Outcome measures

Outcome measures
Measure
Open-Label Placebo
n=45 Participants
One dose (4 capsules) of placebo Placebo: One dose (4 capsules) of placebo Tobi Podhaler: The placebo capsule has to be released from the blister card and inserted into the Podhaler device. The device is then actuated and the study drug is inhaled according to the instructions for use
Number of Participants With Critical Use Errors and Close Calls Associated With the Simulated Inhalation of One Dose Using TOBI Podhaler
4 Participants

Adverse Events

Open-Label Placebo

Serious events: 0 serious events
Other events: 1 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Open-Label Placebo
n=45 participants at risk
One dose (4 capsules) of placebo Placebo: One dose (4 capsules) of placebo Tobi Podhaler: The placebo capsule has to be released from the blister card and inserted into the Podhaler device. The device is then actuated and the study drug is inhaled according to the instructions for use
Injury, poisoning and procedural complications
Subject Accidentally Kicked Himself Causing A Wart To Bleed On His Leg
2.2%
1/45 • Number of events 1 • Adverse events were collected from time of signing Informed Consent through completion of their study visit, 1 day
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Wart On Leg
2.2%
1/45 • Number of events 1 • Adverse events were collected from time of signing Informed Consent through completion of their study visit, 1 day
Injury, poisoning and procedural complications
Wart Bleed On Leg
2.2%
1/45 • Number of events 1 • Adverse events were collected from time of signing Informed Consent through completion of their study visit, 1 day

Additional Information

Keri L Vaughan

Director Global Clinical Operations, General Medicine

Phone: +1 267.980.5015

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place

Restriction type: LTE60