Post Marketing Surveillance on Long-term Use With Norditropin® (Short Stature Due to Noonan Syndrome)

NCT ID: NCT03435627

Last Updated: 2022-11-14

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Total Enrollment

71 participants

Study Classification

OBSERVATIONAL

Study Start Date

2018-02-26

Study Completion Date

2022-01-18

Brief Summary

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The purpose of this study is to collect information about safety and effectiveness for long term use of Norditropin®. Participants will attend the medical institution according to usual practice and receive medical care, as agreed with the study doctor.

Detailed Description

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Conditions

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Genetic Disorder Noonan Syndrome

Study Design

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Observational Model Type

COHORT

Study Time Perspective

PROSPECTIVE

Study Groups

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Norditropin® (naïve participants)

The treatment period of Norditropin® for naïve participants will be up to 208 weeks.

Somatropin

Intervention Type DRUG

Participants will be treated with commercially available Norditropin® (somatropin) according to routine clinical practice at the discretion of the treating physician.

Norditropin® (non-naïve participants)

The treatment period of Norditropin® for non-naïve participants will be up to 442 weeks.

Somatropin

Intervention Type DRUG

Participants will be treated with commercially available Norditropin® (somatropin) according to routine clinical practice at the discretion of the treating physician.

Interventions

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Somatropin

Participants will be treated with commercially available Norditropin® (somatropin) according to routine clinical practice at the discretion of the treating physician.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Signed informed consent obtained before any study-related activities (study-related activities are any procedure related to recording of data according to the protocol).
* The decision to initiate treatment with commercially available Norditropin® has been made by the patient/Legally Acceptable Representative (LAR) and the treating physician before and independently from the decision to include the patient in this study.
* For non-naïve patients; patients who were previously enrolled in study: GHLIQUID-4020.
* For naïve patients; short stature due to Noonan syndrome diagnosed by the physician and a decision to initiate treatment with Norditropin® has been made by the patient/parent and the physician. At study sites, all patients will be registered consecutively from the first patient after approval date (consecutively registered system).
* Male or female, 3 years old or over, bone age: less than 17 years old for male / less than 15 years old for female.

Exclusion Criteria

* Previous participation in this study. Participation is defined as having given informed consent in this study.
* Known or suspected allergy to study products or related products.
* In case of naïve patients, patients who have received growth hormone (GH) products for treatment of indication other than short stature due to Noonan syndrome before approval date of Noonan indication.
Minimum Eligible Age

3 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novo Nordisk A/S

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Reporting Anchor and Disclosure (1452)

Role: STUDY_DIRECTOR

Novo Nordisk A/S

Locations

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Novo Nordisk Investigational Site

Asahikawa, Hokkaido, , Japan

Site Status

Novo Nordisk Investigational Site

Fukuoka, , Japan

Site Status

Novo Nordisk Investigational Site

Kanagawa, , Japan

Site Status

Novo Nordisk Investigational Site

Kanagawa, , Japan

Site Status

Novo Nordisk Investigational Site

Kyoto, , Japan

Site Status

Novo Nordisk Investigational Site

Kyoto, , Japan

Site Status

Novo Nordisk Investigational Site

Maebashi-shi, Gunma, , Japan

Site Status

Novo Nordisk Investigational Site

Miyazaki, , Japan

Site Status

Novo Nordisk Investigational Site

Nagoya, Aichi, , Japan

Site Status

Novo Nordisk Investigational Site

Niigata-shi, Niigata, , Japan

Site Status

Novo Nordisk Investigational Site

Osaka, , Japan

Site Status

Novo Nordisk Investigational Site

Osaka, , Japan

Site Status

Novo Nordisk Investigational Site

Ōita, , Japan

Site Status

Novo Nordisk Investigational Site

Saitama-shi, Saitama, , Japan

Site Status

Novo Nordisk Investigational Site

Sapporo, Hokkaido, , Japan

Site Status

Novo Nordisk Investigational Site

Sendai-shi, Miyagi, , Japan

Site Status

Novo Nordisk Investigational Site

Shizuoka, , Japan

Site Status

Novo Nordisk Investigational Site

Tochigi, , Japan

Site Status

Novo Nordisk Investigational Site

Tokyo, , Japan

Site Status

Novo Nordisk Investigational Site

Tokyo, , Japan

Site Status

Novo Nordisk Investigational Site

Tokyo, , Japan

Site Status

Novo Nordisk Investigational Site

Tokyo, , Japan

Site Status

Countries

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Japan

Other Identifiers

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U1111-1191-3084

Identifier Type: OTHER

Identifier Source: secondary_id

GHLIQUID-4358

Identifier Type: -

Identifier Source: org_study_id

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