A Study to Assess the Safety and Tolerability of AZD1390 Given With Radiation Therapy in Patients With Brain Cancer

NCT ID: NCT03423628

Last Updated: 2025-11-10

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE1

Total Enrollment

180 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-04-02

Study Completion Date

2026-09-16

Brief Summary

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This study will test an investigational drug called AZD1390 in combination with radiation therapy for the treatment of brain tumors. This is the first time AZD1390 is being given to patients. This study will test safety, tolerability and PK (how the drug is absorbed, distributed and eliminated) of ascending doses of AZD1390 in combination with distinct regimens of radiation therapy

Detailed Description

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This first time-in patients (FTIP), open-label, multicentre study of AZD1390 will be conducted in the United States, the United Kingdom and Japan. It consists of three treatment arms: Arm A, B, C. The Japan dose confirmation part (Japan part) is a sub-study of Arm A. Sites from Japan will only participate in the Japan part. This Phase 1 study will assess safety and tolerability of AZD1390 in combination with radiation therapy (RT) in brain malignancies. The combination cohorts have been designed to assess escalating cumulative doses of AZD1390 in settings with 3 different radiation treatment regimens:

* Arm A: 35 Gy over 2 weeks with intensity-modulated radiation therapy (IMRT) in patients with recurrent Glioblastoma Multiforme (GBM). Arm A will also include the food effect cohort
* Arms B: 30 Gy over two weeks with whole brain radiation therapy (WBRT)/ partial brain radiation therapy (PBRT) in patients with brain metastases. \*\*Arm B has now closed to recruitment\*\*
* Arm C: 60 Gy over 6 weeks (IMRT) in patients with primary GBM Each arm provides standard of care RT for the disease setting indicated with the experimental agent being administered in dose escalating cohorts.

Conditions

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Recurrent Glioblastoma Multiforme Primary Glioblastoma Multiforme Brain Neoplasms, Malignant Leptomeningeal Disease (LMD)

Keywords

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glioblastoma Ataxia-telangiectasia mutated kinase (ATM) inhibition radiation therapy

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

AZD1390 will be administered to patients in three different Arms (A, B and C), with each arm receiving standard of care radiation therapy (RT) for their disease setting.

In arms A and C, AZD1390 will be administered in three cycles: Cycle 0 (before RT), Cycle 1 (during RT) and Cycle 2 (after RT).

In arm B, AZD1390 will be administered in cycle 1 only (during RT). Within each arm, AZD1390 will be administered in dose escalating cohorts, first in an intermittent and then in a consecutive fashion, to achieve daily administration prior to RT.

\*\*Arm B has now closed to recruitment\*\*

For Arm A, there is an optional food effect assessment during cycle 0. \*Note: the food effect assessment is currently open to recruitment\*
Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Arm A: AZD1390 + Radiation Therapy

AZD1390 administration plus 35 Gy of Intensity-modulated radiation therapy (IMRT) administered at daily fractions of 3.5 Gy over 10 fractions (2 weeks)

Group Type EXPERIMENTAL

AZD1390

Intervention Type DRUG

AZD1390 Administered in 3 Cycles depending on arm:

Cycle 0: 1 dose prior to Radiation Therapy. Cycle 1: 2 weeks Intermittent or continuous dosing during Radiation Therapy. Cycle 2: 2 weeks adjuvant treatment after Radiation Therapy. For optional food effect assessment in Arm A, 2 doses prior to RT under both fed and fasted conditions. Note: the food effect assessment is currently open to recruitment.

Arm A includes the Japan part following the same dosing administration.

Radiation Therapy

Intervention Type RADIATION

35 Gy of Intensity-modulated radiation therapy (IMRT) administered at daily fractions of 3.5 Gy over 10 fractions (2 weeks)

Arm B: AZD1390 + Radiation Therapy

AZD1390 administration plus 30 Gy of whole brain radiation therapy (WBRT) or partial brain radiation therapy (PBRT) administered at daily fractions of 3 Gy over 10 fractions (2 weeks).

Group Type EXPERIMENTAL

Radiation Therapy

Intervention Type RADIATION

30 Gy of whole brain radiation therapy (WBRT) or partial brain radiation therapy (PBRT) administered at daily fractions of 3 Gy over 10 fractions (2 weeks).

AZD1390

Intervention Type DRUG

AZD1390 administered in 1 Cycle. AZD1390 administration concomitantly with RT (2 weeks). Cycle 1 also contains an additional 5 days (post completion of RT with AZD1390 administration). Arm is Closed.

Arm C: AZD1390 + Radiation Therapy

AZD1390 administration plus 60 Gy of intensity- modulated radiation therapy (IMRT) administered at daily fractions of 2 Gy over 30 fractions (6 weeks)

Group Type EXPERIMENTAL

Radiation Therapy

Intervention Type RADIATION

60 Gy of intensity- modulated radiation therapy (IMRT) administered at daily fractions of 2 Gy over 30 fractions (6 weeks)

AZD1390

Intervention Type DRUG

AZD1390 Administered in 3 Cycles depending on arm:

Cycle 0: 1 dose prior to Radiation Therapy. Cycle 1: 6 weeks Intermittent or continuous dosing during Radiation Therapy. Cycle 2: 2 weeks adjuvant treatment after Radiation Therapy. Arm is closed.

Interventions

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AZD1390

AZD1390 Administered in 3 Cycles depending on arm:

Cycle 0: 1 dose prior to Radiation Therapy. Cycle 1: 2 weeks Intermittent or continuous dosing during Radiation Therapy. Cycle 2: 2 weeks adjuvant treatment after Radiation Therapy. For optional food effect assessment in Arm A, 2 doses prior to RT under both fed and fasted conditions. Note: the food effect assessment is currently open to recruitment.

Arm A includes the Japan part following the same dosing administration.

Intervention Type DRUG

Radiation Therapy

30 Gy of whole brain radiation therapy (WBRT) or partial brain radiation therapy (PBRT) administered at daily fractions of 3 Gy over 10 fractions (2 weeks).

Intervention Type RADIATION

Radiation Therapy

60 Gy of intensity- modulated radiation therapy (IMRT) administered at daily fractions of 2 Gy over 30 fractions (6 weeks)

Intervention Type RADIATION

AZD1390

AZD1390 administered in 1 Cycle. AZD1390 administration concomitantly with RT (2 weeks). Cycle 1 also contains an additional 5 days (post completion of RT with AZD1390 administration). Arm is Closed.

Intervention Type DRUG

AZD1390

AZD1390 Administered in 3 Cycles depending on arm:

Cycle 0: 1 dose prior to Radiation Therapy. Cycle 1: 6 weeks Intermittent or continuous dosing during Radiation Therapy. Cycle 2: 2 weeks adjuvant treatment after Radiation Therapy. Arm is closed.

Intervention Type DRUG

Radiation Therapy

35 Gy of Intensity-modulated radiation therapy (IMRT) administered at daily fractions of 3.5 Gy over 10 fractions (2 weeks)

Intervention Type RADIATION

Other Intervention Names

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Radiotherapy Radiation treatment RT ATM inhibitor Radiotherapy Radiation treatment RT Radiotherapy Radiation treatment RT ATM inhibitor ATM inhibitor

Eligibility Criteria

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Inclusion Criteria

* Provision of formalin-fixed paraffin embedded tissue sample from primary or metastatic disease
* Karnofsky Performance Score of ≥60.

* Histologically proven diagnosis of GBM. Patients who have had RT for low-grade glioma (LGG) or grade 3 glioma and have subsequently relapsed to histologically confirmed GBM can be considered
* A radiological diagnosis of recurrent/relapsed or progressive disease according to RANO criteria.
* Completion of first-line radiation at least 6 months prior to Cycle 1 Day 1.
* Patients with tumor-induced seizures must be well controlled on a stable anti-epileptic treatment
* Willing to receive anti-epileptic prophylaxis for the duration of study drug administration.

\*\*Arm B has now closed to recruitment\*\*

* Histologically proven diagnosis of solid tumor malignancy and Magnetic Resonance (MR) imaging documenting brain lesions.
* Not eligible for Stereotactic Radiosurgery (SRS) treatment of brain tumor.
* Patient has not received any previous brain RT to the area that is to be irradiated. Prior PBRT may be allowed if there is not significant overlap between the prior and new radiation fields.
* Non-CNS malignant disease must be sufficiently controlled so that patients can be without additional systemic therapy for the required washout period before starting therapy until 5 days after the end of RT. Required washout period before starting the first dose of AZD1390 (Cycle 1) is 28 days for immune checkpoint inhibitors and 7 days for all other agents
* Not received radiation to the lung fields within the past 8 weeks.
* No history of seizures related to the brain metastases or LMD.
* Receiving PBRT (rather than WBRT) during Cycle 1 as standard of care for brain metastases

* Histologically proven primary diagnosis of GBM with unmethylated O6-methylguanine-DNA methyltransferase (MGMT). Grade 4 astrocytoma or histology with molecular features of GBM can be considered.
* Determination of MGMT promoter status by methylation-specific polymerase chain reaction (PCR) or pyrosequencing per local institutional guidelines is required to assess eligibility for this Arm.
* Patients will have to undergo mutational testing for Isocitrate dehydrogenase 1 (IDH1) on a tumor specimen before entering study. Patients are eligible for Arm C regardless of their IDH1 mutational status.
* No history of uncontrolled seizures after surgery for primary GBM (despite adequate antiepileptic therapy) or with need for concurrent administration of more than 2 antiepileptic drugs.
* Willing to receive anti-epileptic prophylaxis for the duration of study drug administration


* For the fed assessment portion: fast overnight (for at least 10 hours) prior to consuming a high-fat meal consisting of approximately 800 to 1000 calories, with around 54% of the calories coming from fat.
* For the fasted assessment portion: fast overnight (for at least 10 hours prior to dosing) and until 4 hours after dosing.

\*Note: the optional food effect assessment is currently open to enrolment\*

Exclusion Criteria

* Administration of chemotherapy or any investigational drug in the 28 days or carmustine (CCNU) or lomustine (BCNU) in the 6 weeks prior to receiving the first dose of treatment in Arms A and C. Administration of checkpoint inhibitors within 28 days prior to first dose of treatment and any other agent within 7 days of beginning study treatment in Arm B. Hormonal therapies are allowed during study treatment for patients in Arm B.
* History of severe brain-injury or stroke.
* Patient not eligible for sequential MRI evaluations are not eligible for this study.
* History of epileptic disorder or any seizure history unrelated to tumor
* Treatment with Strong inhibitors or inducers of CYP3A4 within 2 weeks prior to receiving study drug
* Concurrent therapy with other seizurogenic medications.
* Past medical history of interstitial lung disease (ILD), drug-induced ILD, radiation pneumonitis which required steroid treatment, or any evidence of clinically active ILD.
* Concurrent severe and/or uncontrolled medical condition (e.g., severe COPD).
* Prior treatment with pneumotoxic drugs, e.g. busulfan, bleomycin, within the past year. If prior therapy in lifetime, then excluded if history of pulmonary toxicities from administration. Patients who have received treatment with nitrosoureas (e.g., carmustine, lomustine) in the year before study entry without experiencing lung toxicity are allowed on study.
* History or presence of myopathy or raised creatine kinase (CK) \>5 x upper limit of normal (ULN) on 2 occasions at screening.
* Cardiac dysfunction defined as: Myocardial infarction within six months of study entry, NYHA (New York Heart Association) Class II/III/IV heart failure, unstable angina, unstable cardiac arrhythmias
* Evidence of severe pulmonary infections, as judged by the investigator (For Japan part only this includes active infection including tuberculosis, chronic active or uncontrolled Hep B or Hep C)
* Has previously received ATM inhibitor with concurrent RT


* Diabetes Type I, Type II, or steroid-induced diabetes.
* Undergoing systemic steroid treatment \*Note: the food effect assessment is currently open to enrolment\*
Minimum Eligible Age

18 Years

Maximum Eligible Age

130 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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AstraZeneca

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Patrick Wen

Role: PRINCIPAL_INVESTIGATOR

Dana-Farber Cancer Institute

Brandon Imber

Role: PRINCIPAL_INVESTIGATOR

Memorial Sloan Kettering Cancer Center

Mariza Daras

Role: PRINCIPAL_INVESTIGATOR

VCU Massey Cancer Center

Jan Drappatz

Role: PRINCIPAL_INVESTIGATOR

UPMC Hospital Radiation Oncology

Deborah Forst

Role: PRINCIPAL_INVESTIGATOR

Massachusetts General Hospital

Anthony Chalmers

Role: PRINCIPAL_INVESTIGATOR

Beatson West of Scotland Cancer Centre

Rajesh Jena

Role: PRINCIPAL_INVESTIGATOR

Cambridge University Hospitals NHS Foundation Trust

Louise Murray

Role: PRINCIPAL_INVESTIGATOR

University of Leeds

Yoshitaka Narita

Role: PRINCIPAL_INVESTIGATOR

National Cancer Center Hospital

Yoshiki Arakawa

Role: PRINCIPAL_INVESTIGATOR

Kyoto University Hospital

Kazuhiko Mishima

Role: PRINCIPAL_INVESTIGATOR

Saitama Medical University International Medical Center

Locations

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Research Site

Boston, Massachusetts, United States

Site Status RECRUITING

Research Site

Boston, Massachusetts, United States

Site Status RECRUITING

Research Site

New York, New York, United States

Site Status RECRUITING

Research Site

Pittsburgh, Pennsylvania, United States

Site Status RECRUITING

Research Site

Richmond, Virginia, United States

Site Status RECRUITING

Research Site

Chūōku, , Japan

Site Status RECRUITING

Research Site

Hidaka-shi, , Japan

Site Status RECRUITING

Research Site

Kyoto, , Japan

Site Status RECRUITING

Research Site

Cambridge, , United Kingdom

Site Status ACTIVE_NOT_RECRUITING

Research Site

Glasgow, , United Kingdom

Site Status COMPLETED

Research Site

Leeds, , United Kingdom

Site Status RECRUITING

Research Site

London, , United Kingdom

Site Status WITHDRAWN

Countries

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United States Japan United Kingdom

Central Contacts

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AstraZeneca Clinical Study Information Center

Role: CONTACT

Phone: 1-877-240-9479

Email: [email protected]

Other Identifiers

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135803

Identifier Type: REGISTRY

Identifier Source: secondary_id

2017-002451-28

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

D6940C00002

Identifier Type: -

Identifier Source: org_study_id